Safety and Pharmacokinetics of Intravenous and Oral APX001 in Patients With Acute Myeloid Leukemia (AML) and Neutropenia

NCT ID: NCT03333005

Last Updated: 2024-05-17

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-11-27

Study Completion Date

2018-10-26

Brief Summary

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An open-label, multi-center, Phase Ib study to determine the safety and pharmacokinetics of intravenous and oral APX001 in patients undergoing chemotherapy for Acute Myeloid Leukemia with neutropenia.

A total of 20 patients will be enrolled in this study. 10 patients in Cohort I, intravenous drug dosing and 10 patients will be enrolled in Cohort II, oral drug dosing.

All patients will receive chemotherapy for their AML according to local clinical standard of care as well as antifungal prophylaxis.

APX001 will be administered for 14 consecutive days, beginning on Study Day 3 after onset of chemotherapy

Detailed Description

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Conditions

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Acute Myeloid Leukemia

Study Design

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Allocation Method

NA

Intervention Model

SEQUENTIAL

The first 10 patients enrolled will be administered IV APX001. The second 10 patients enrolled will be administered oral APX001
Primary Study Purpose

OTHER

Blinding Strategy

NONE

Study Groups

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APX001 with Standard of Care Anti-fungal agent

Group Type EXPERIMENTAL

APX001 with Standard of Care anti-fungal agent

Intervention Type DRUG

safety assessment

Interventions

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APX001 with Standard of Care anti-fungal agent

safety assessment

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Provision of written consent
* Ages 18-75 inclusive, male or female
* Diagnosis of Acute Myeloid Leukemia
* Patients entering first induction treatment chemotherapy
* Expected to be neutropenic (\<500 ANC/ul) for \>/= 10 days

Exclusion Criteria

* Patients who received systemic antifungal therapy for proven or probable fungal infections within the last 12 months
* Current fever (\> 38 degrees Celsius)
* Concomitant use of rifampin, rifabutin, ergot alkaloids, terfenadine, astemizole, cisapride, pimozide, quinidine, long acting barbiturates, neostigmine and carbamazepine
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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The Clinical Trials Centre Cologne

OTHER

Sponsor Role collaborator

Basilea Pharmaceutica

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Marc Engelhardt

Role: STUDY_DIRECTOR

Basilea Pharmaceutica International Ltd, Allschwil

Locations

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University of Cologne, Center for Integrated Oncology (CIO)

Cologne, , Germany

Site Status

Johannes Gutenberg, University of Mainz

Mainz, , Germany

Site Status

University of Munich, Grosshadern Campus

Munich, , Germany

Site Status

Countries

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Germany

Other Identifiers

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APX001-103

Identifier Type: -

Identifier Source: org_study_id

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