A Trial to Investigate Efficacy, Safety and Tolerability of FE 201836 for Nocturia Due to Nocturnal Polyuria in Adults

NCT ID: NCT03201419

Last Updated: 2022-03-02

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

302 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-07-27

Study Completion Date

2019-10-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this trial was to investigate the efficacy, safety and tolerability of different oral doses of FE 201836, with desmopressin as a benchmark, during 12 weeks of treatment for nocturia due to nocturnal polyuria in adults

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Nocturia

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

The trial consisted of a 2 week period of screening/lifestyle changes during which no treatment was given, a 2 week enrichment period (including a 1 week single blind active run-in period \[FE 201836 500 µg\] and a 1 week washout period) followed by a 12 week randomized treatment period for each subject. Prior to the first interim analysis, the first 129 subjects were randomized to daily treatment with FE 201836 500 µg, placebo, or desmopressin (25 µg for females and 50 µg for males) in a 2:2:1 ratio. After the first interim analysis, subjects were randomized to daily treatment with FE 201836 (50 µg, 100 µg, 150 µg, 250 µg, 350 µg, or 500 µg), placebo, or desmopressin (25 µg for females and 50 µg for males) using response adaptive allocation probabilities.
Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators
Each subject will receive 2 medications (an oral solution and an orally disintegrating tablet (ODT) formulation) throughout the trial, in order to keep the treatment blinded.

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

FE 201836 500 μg (Randomized Treatment Period)

FE 201836 500 μg oral solution and placebo orally disintegrating tablet (ODT), administered once daily

Group Type EXPERIMENTAL

FE 201836

Intervention Type DRUG

Oral solution for daily intake

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

FE 201836 350 μg (Randomized Treatment Period)

FE 201836 350 μg oral solution and placebo ODT, administered once daily

Group Type EXPERIMENTAL

FE 201836

Intervention Type DRUG

Oral solution for daily intake

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

FE 201836 250 μg (Randomized Treatment Period)

FE 201836 250 μg oral solution and placebo ODT, administered once daily

Group Type EXPERIMENTAL

FE 201836

Intervention Type DRUG

Oral solution for daily intake

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

FE 201836 150 μg (Randomized Treatment Period)

FE 201836 150 μg oral solution and placebo ODT, administered once daily

Group Type EXPERIMENTAL

FE 201836

Intervention Type DRUG

Oral solution for daily intake

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

FE 201836 100 μg (Randomized Treatment Period)

FE 201836 100 μg oral solution and placebo ODT, administered once daily

Group Type EXPERIMENTAL

FE 201836

Intervention Type DRUG

Oral solution for daily intake

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

FE 201836 50 μg (Randomized Treatment Period)

FE 201836 50 μg oral solution and placebo ODT, administered once daily

Group Type EXPERIMENTAL

FE 201836

Intervention Type DRUG

Oral solution for daily intake

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

Placebo (Randomized Treatment Period)

Placebo oral solution and placebo ODT, administered once daily

Group Type EXPERIMENTAL

Placebo oral solution

Intervention Type DRUG

Manufactured to mimic experimental drug

Placebo ODT

Intervention Type DRUG

Manufactured to mimic experimental drug

Desmopressin 25 μg (Randomized Treatment Period)

Desmopressin 25 μg ODT and placebo oral solution, administered once daily (female subjects)

Group Type EXPERIMENTAL

Desmopressin

Intervention Type DRUG

Desmopressin Orally Disintegrating Tablet (ODT)

Placebo oral solution

Intervention Type DRUG

Manufactured to mimic experimental drug

Desmopressin 50 μg (Randomized Treatment Period)

Desmopressin 50 μg ODT and placebo oral solution, administered once daily (male subjects)

Group Type EXPERIMENTAL

Desmopressin

Intervention Type DRUG

Desmopressin Orally Disintegrating Tablet (ODT)

Placebo oral solution

Intervention Type DRUG

Manufactured to mimic experimental drug

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

FE 201836

Oral solution for daily intake

Intervention Type DRUG

Desmopressin

Desmopressin Orally Disintegrating Tablet (ODT)

Intervention Type DRUG

Placebo oral solution

Manufactured to mimic experimental drug

Intervention Type DRUG

Placebo ODT

Manufactured to mimic experimental drug

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Velmupressin NOCDURNA

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Adults ≥18 years of age (at the time of written consent)
* Medical history of, or subject reported nocturia symptoms during the 6 months prior to Visit 1
* ≥2 nocturnal voids (an average over 3 days) as documented in the 3-day e-Diary prior to Visit 2
* The largest single voided volume must be ≥200 mL (at least 1 void ≥200 mL) as documented in the 3-day e-Diary prior to Visit 2
* Nocturnal polyuria, defined as Nocturnal Polyuria index \>33%, a ratio of Nocturnal Urine Volume in excess of 33% of total daily (24-hour) urine volume as documented in the 3-day e-Diary prior to Visit 2
* ≥20% decrease in the nocturnal diuresis rate (mL/min) (that was recorded at Visit 2) as documented in the 3-day e-Diary prior to Visit 3

Exclusion Criteria

* Current diagnosis of Obstructive Sleep Apnoea (OSA)
* Restless Legs Syndrome (RLS)
* Bladder Outlet Obstruction (BOO) or urine flow \<5 mL/s, as confirmed by uroflowmetry upon suspicion during screening prior to Visit 2
* Urinary incontinence defined as an average of \>1 episode/day in the 3-day e-Diary prior to Visit 2 (occasional urge incontinence during daytime or at night on the way to void is not necessarily exclusionary)
* Any pelvic or lower urinary tract surgery and/or radio therapy or previous pelvic irradiation within the past 6 months prior to Visit 1. Including e.g., transurethral resection for Bladder Outlet Obstruction or Benign Prostatic Hyperplasia, hysterectomy or female incontinence procedures
* Genito-urinary tract pathology that can in the investigator's opinion be responsible for urgency or urinary incontinence e.g., symptomatic or recurrent urinary tract infections, interstitial cystitis, bladder-related pain, chronic pelvic pain syndrome, or stone in the bladder or urethra causing symptoms
* A history of cancer with the last date of disease activity/presence of malignancy within the last 12 months prior to Visit 1, except for adequately treated basal cell carcinoma of the skin
* History of any neurological disease affecting bladder function or muscle strength (e.g., Multiple Sclerosis, Parkinson's, spinal cord injury, spina bifida)
* Habitual (fluid intake \>3L per day) or psychogenic polydipsia
* Uncontrolled hypertension, as judged by the investigator
* Uncontrolled diabetes mellitus, as judged by the investigator
* Central or nephrogenic diabetes insipidus
* Known history of Syndrome of Inappropriate Antidiuretic Hormone (SIADH) secretion
* History of gastric retention
* Suspicion or evidence of congestive heart failure, (New York Heart Association (NYHA) class II, III, IV)
* Hyponatraemia:

* Serum sodium level \<135 mmol/L at Visit 1(re-tested, with results available within 7 days)
* Serum sodium level \<130 mmol/L at Visit 3 (re-tested, with results available within 7 days)
* Use of any prohibited therapy listed below:

* Current or former (within 3 months prior to screening) treatment with any other investigational medicinal product (IMP)
* Unstable electrostimulation or behavioural bladder training program less than 3 months prior to screening (stable electrostimulation or behavioural bladder training program started at least 3 months before screening are acceptable)
* Thiazide diuretics
* Antiarrhythmic agents
* V2-receptor antagonists/agonists (e.g., vaptans/desmopressin, vasopressin)
* Loperamide
* Botulinum toxin (cosmetic non-urological use is acceptable)
* Valproate
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Ferring Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Global Clinical Compliance

Role: STUDY_DIRECTOR

Ferring Pharmaceuticals

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Achieve Clinical Research, LLC

Birmingham, Alabama, United States

Site Status

Coastal Clinical Research, an AMR company

Mobile, Alabama, United States

Site Status

Clinical Trials Research

Lincoln, California, United States

Site Status

Tri Valley Urology Medical Group

Murrieta, California, United States

Site Status

San Diego Clinical Trials

San Diego, California, United States

Site Status

Advanced Rx Clinical Research Group, Inc.

Westminster, California, United States

Site Status

Downtown Women's Health Care

Denver, Colorado, United States

Site Status

Genitourinary Surgical Consultants, P.C.

Denver, Colorado, United States

Site Status

South Florida Medical Research

Aventura, Florida, United States

Site Status

Women's Medical Research Group, LLC

Clearwater, Florida, United States

Site Status

Tampa Bay Medical Research, Inc.

Clearwater, Florida, United States

Site Status

Clinical Research of South Florida

Coral Gables, Florida, United States

Site Status

Avail Clinical Research, LLC

DeLand, Florida, United States

Site Status

Finlay Medical Research Corp

Greenacres City, Florida, United States

Site Status

Pharmax Research Clinic

Miami, Florida, United States

Site Status

Doctors Research Institute Corporation

Miami, Florida, United States

Site Status

Sanitas Research

Miami, Florida, United States

Site Status

Bayside Clinical Research LLC

New Port Richey, Florida, United States

Site Status

Pines Care Research Center, Inc

Pembroke Pines, Florida, United States

Site Status

Clinical Research Center of Florida

Pompano Beach, Florida, United States

Site Status

Meridien Research, Inc.

St. Petersburg, Florida, United States

Site Status

American Health Network of Indiana, LLC

Avon, Indiana, United States

Site Status

American Health Network of Indiana, LLC

Greenfield, Indiana, United States

Site Status

Bay State Clinical Trials, Inc.

Watertown, Massachusetts, United States

Site Status

Beyer Research

Kalamazoo, Michigan, United States

Site Status

Remedica LLC

Rochester, Michigan, United States

Site Status

Quality Clinical Research Center, Inc.

Omaha, Nebraska, United States

Site Status

Clinical Research Consortium, an AMR company

Las Vegas, Nevada, United States

Site Status

Mid Hudson Medical Research, PLLC

New Windsor, New York, United States

Site Status

Premier Medical Group of the Hudson Valley, PC

Poughkeepsie, New York, United States

Site Status

American Health Research, Inc.

Charlotte, North Carolina, United States

Site Status

Medication Management, LLC

Greensboro, North Carolina, United States

Site Status

Peters Medical Research

High Point, North Carolina, United States

Site Status

PMG Research of Raleigh, LLC

Raleigh, North Carolina, United States

Site Status

PMG Research of Wilmington, LLC

Wilmington, North Carolina, United States

Site Status

HWC Women's Research Center

Englewood, Ohio, United States

Site Status

NECCR Primacare Research, LLC

Providence, Rhode Island, United States

Site Status

Coastal Carolina Research Center, Inc

Mt. Pleasant, South Carolina, United States

Site Status

PMG Research of Charleston, LLC

Mt. Pleasant, South Carolina, United States

Site Status

MCA Research - Partner

Houston, Texas, United States

Site Status

Ericksen Research & Development, LLC

Clinton, Utah, United States

Site Status

Advanced Research Institute

Ogden, Utah, United States

Site Status

Clinical Research Associates of Tidewater, an AMR company

Norfolk, Virginia, United States

Site Status

ULB Hopital Erasme

Brussels, , Belgium

Site Status

UZ Antwerpen

Edegem, , Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

AZ Groeninge - Campus Vercruysselaan

Kortrijk, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

Ultra-Med Inc.

Pointe-Claire, Quebec, Canada

Site Status

Milestone Research

London, , Canada

Site Status

SKDS Research Inc.

Newmarket, , Canada

Site Status

Clinique Médicale St-Louis (Recherche) inc d/b/a/ Centre de Recherche Saint-Louis

Québec, , Canada

Site Status

DIEX Recherche Quebec Inc.

Québec, , Canada

Site Status

Bluewater Health-Norman Site

Sarnia, , Canada

Site Status

CHUS - Hôpital Fleurimont

Sherbrooke, , Canada

Site Status

DIEX Recherche Sherbrooke Inc.

Sherbrooke, , Canada

Site Status

Ferring Investigational Site

Toronto, , Canada

Site Status

DIEX Recherche Victoriaville Inc.

Victoriaville, , Canada

Site Status

Urologie Benešov - Afimed s.r.o.

Benešov, , Czechia

Site Status

Fakultni nemocnice Brno, Dept of Klinika nemoci plicnich a tuberkulozy

Brno, , Czechia

Site Status

Krajska nemocnice Liberec, a.s.

Liberec, , Czechia

Site Status

Urocentrum Plzen

Pilsen, , Czechia

Site Status

Thomayerova nemocnice, PARENT

Prague, , Czechia

Site Status

Gemeinschaftspraxis fuer Urologie und Andrologie

Duisburg, , Germany

Site Status

Urologische Gemeinschaftspraxis

Emmendingen, , Germany

Site Status

Klinikum Weiden, Klinik f. Urologie, Andrologie und Kinderurologie

Weiden, , Germany

Site Status

Jahn Ferenc Del-pesti Korhaz es Rendelointezet

Budapest, , Hungary

Site Status

Synexus Magyarorszag Kft.

Budapest, , Hungary

Site Status

Bagoly Egeszseghaz

Kecskemét, , Hungary

Site Status

SzSzB Megyei Korhazak es Egyetemi Oktatokorhaz, Josa Andras Oktatokorhaz Urologia

Nyíregyháza, , Hungary

Site Status

Jasz-Nagykun-Szolnok Megyei Hetenyi Geza Korhaz-Rendelointezet

Szolnok, , Hungary

Site Status

Nasz Lekarz Osrodek Badan Klinicznych

Bydgoszcz, , Poland

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium Canada Czechia Germany Hungary Poland

References

Explore related publications, articles, or registry entries linked to this study.

Hudgens S, Howerter A, Polek E, Andersson FL. Psychometric validation and interpretation of the Nocturia Impact Diary in a clinical trial setting. Qual Life Res. 2022 Jun;31(6):1837-1848. doi: 10.1007/s11136-021-03060-4. Epub 2021 Dec 21.

Reference Type BACKGROUND
PMID: 34932192 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2016-003851-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

000233

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Daytime Impact Sleep Study
NCT01779466 TERMINATED PHASE2
Desmopressin Response in the Young
NCT00230594 COMPLETED PHASE3
Efficacy and Safety of VA106483 in Elderly Males
NCT00879138 COMPLETED PHASE1/PHASE2