Decoding Presymptomatic White Matter Changes in Huntington Disease

NCT ID: NCT03193099

Last Updated: 2020-02-18

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

NA

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-07-11

Study Completion Date

2019-12-30

Brief Summary

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WIN-HD is a monocentric longitudinal study comparing premanifest Huntingtin (HTT) mutation carriers and non HTT mutation carriers to determine that white-matter atrophy occurs far earlier than clinical onset in HD using Diffusion-weighted Nuclear Magnetic Resonance (N spectroscopy (DWS) and Diffusion Tensor Imaging (DTI).

The investigators will recruit up to 20 premanifest HTT mutation carriers (15 completed) and up to 20 non HTT mutation carriers (15 completed). It is important to have those 2 populations in order to compare our results and determine if there are significant white-matter changes far from the onset of HD. Therefore, non HTT mutation carriers will be age and gender matched to premanifest HTT mutation carriers.

In order to test the hypothesis, the study has 2 visits with a year interval.

This study is based on 4 principal criteria:

1. Imaging criteria
2. Clinical and neurological criteria
3. Psychological criteria
4. Behavioral criteria

Detailed Description

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Conditions

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Huntington Disease White Matter Alterations

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

OTHER

Blinding Strategy

NONE

Study Groups

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Premanifest HTT mutation carriers

Group Type OTHER

Brain imaging

Intervention Type OTHER

Volume, DWS and DTI

Neurological assessments

Intervention Type OTHER

UHDRS

Psychological assessments

Intervention Type BEHAVIORAL

STAI (Spielberger state and Trait Anxiety Inventory) A and B, BDI-II (Beck Depression Inventory), MINI (Mini-International Neuropsychiatric Interview) and MINI-SEA (mini Social cognitive and Emotional Assessment)

Behavioural assessments

Intervention Type BEHAVIORAL

Computerized game

non HTT mutation carriers

Group Type OTHER

Brain imaging

Intervention Type OTHER

Volume, DWS and DTI

Neurological assessments

Intervention Type OTHER

UHDRS

Psychological assessments

Intervention Type BEHAVIORAL

STAI (Spielberger state and Trait Anxiety Inventory) A and B, BDI-II (Beck Depression Inventory), MINI (Mini-International Neuropsychiatric Interview) and MINI-SEA (mini Social cognitive and Emotional Assessment)

Behavioural assessments

Intervention Type BEHAVIORAL

Computerized game

Interventions

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Brain imaging

Volume, DWS and DTI

Intervention Type OTHER

Neurological assessments

UHDRS

Intervention Type OTHER

Psychological assessments

STAI (Spielberger state and Trait Anxiety Inventory) A and B, BDI-II (Beck Depression Inventory), MINI (Mini-International Neuropsychiatric Interview) and MINI-SEA (mini Social cognitive and Emotional Assessment)

Intervention Type BEHAVIORAL

Behavioural assessments

Computerized game

Intervention Type BEHAVIORAL

Eligibility Criteria

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Inclusion Criteria

* For presymptomatic individuals:

* Genetic test available with CAG (Cytosine-Adenine-Guanine) repeat length \> 36 in HTT gene
* UHDRS score \<5
* Burden score \<250
* For controls:

\- Genetic test available with CAG repeat length ≤ 36 in HTT gene

* At least 18 years of age
* Capacity to consent
* Signature of the informed consent
* Covered by social security
* Ability to undergo MRI scanning


* Under the age of 18 years of age
* Contra-indications to MRI examination (metallic implant, pacemaker, artificial heart valve, brain vascular malformation, aneurysm clips, exposed by metallic fragments, artificial implants, peripheral or neuronal stimulator, insulin pump, intravenous catheter, epilepsy, person with an history of seizure, metallic contraceptive device, permanent eyelid make up, claustrophobia,…)
* Unwillingness to be informed in case of abnormal MRI (with a significant medical anomaly)
* History of severe head injury
* History of neurological disorder or presence of neurological disorder
* Participation in a drug trial or exclusion period of another study
* Pregnancy or breastfeeding
* Inability to understand information about the protocol
* Person deprived of their liberty by judicial or administrative decision
* Person under legal protection (legal guardianship, tutelage or maintenance of justice)
* Person without any protection and unable to consent
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

Yes

Sponsors

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University College, London

OTHER

Sponsor Role collaborator

Institut National de la Santé Et de la Recherche Médicale, France

OTHER_GOV

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Alexandra DURR, PU-PH

Role: PRINCIPAL_INVESTIGATOR

Institut National de la Santé Et de la Recherche Médicale, France

Locations

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Brain and Spine Institute

Paris, , France

Site Status

Countries

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France

Other Identifiers

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2017-A00589-44

Identifier Type: REGISTRY

Identifier Source: secondary_id

C16-115

Identifier Type: -

Identifier Source: org_study_id

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