A Study to Investigate the Efficacy and Safety of Canagliflozin in Children and Adolescents (>=10 to <18 Years) With Type 2 Diabetes Mellitus

NCT ID: NCT03170518

Last Updated: 2025-04-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

171 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-07-21

Study Completion Date

2023-09-20

Brief Summary

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The purpose of this study is to assess the effect of canagliflozin relative to placebo on glycated hemoglobin (HbA1c) after 26 weeks of treatment, and to assess the overall safety and tolerability of canagliflozin.

Detailed Description

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Conditions

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Diabetes Mellitus, Type 2

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Single-blind run-in Period: Placebo

Participants will receive 1 placebo tablet matching canagliflozin 100 milligram (mg) once-daily during the 2-week single-blind placebo run-in period.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Matching placebo tablet will be administered orally once-daily.

Double-blind Treatment Phase: Canagliflozin or Placebo

Canagliflozin 100 mg/matching placebo once-daily during first 12 weeks. At Week 13, participants who have glycated hemoglobin (HbA1c) of greater than or equal to (\>=)7.0 percent (%), estimated glomerular filtration rate (eGFR) \>=60 milliliter/minute/1.73 meter square (mL/min/1.73 m\^2) will be re-randomized to either remain on canagliflozin 100 mg/matching placebo or up-titrate to canagliflozin 300 mg/matching placebo till Week 52.

Group Type EXPERIMENTAL

Canagliflozin 100 mg

Intervention Type DRUG

Canagliflozin 100 mg tablet will be administered orally (by mouth) once-daily.

Canagliflozin 300 mg

Intervention Type DRUG

Canagliflozin 300 mg tablet will be administered orally once-daily.

Placebo

Intervention Type DRUG

Matching placebo tablet will be administered orally once-daily.

Interventions

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Canagliflozin 100 mg

Canagliflozin 100 mg tablet will be administered orally (by mouth) once-daily.

Intervention Type DRUG

Canagliflozin 300 mg

Canagliflozin 300 mg tablet will be administered orally once-daily.

Intervention Type DRUG

Placebo

Matching placebo tablet will be administered orally once-daily.

Intervention Type DRUG

Other Intervention Names

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JNJ-28431754 JNJ-28431754

Eligibility Criteria

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Inclusion Criteria

* Participants with a diagnosis of type 2 diabetes mellitus (T2DM)
* Random C-peptide at screening greater than (\>)0.6 nanogram/milliliter (ng/mL) (\>0.2 nanomole/liter \[nmol\]/L\])

1. On diet and exercise only for at least 4 weeks prior to screening
2. On diet and exercise and a stable dose of metformin monotherapy \>=1,000 mg per day or MTD per day for at least 8 weeks prior to screening
3. On diet and exercise and a stable insulin monotherapy regimen for at least 8 weeks prior to screening (stable dose is defined as no change in the insulin regimen \[that is, type{s} of insulin\] and \<=15% change in the total daily dose of insulin \[averaged over 1 week to account for day to day variability\])
4. On diet and exercise and a stable combination therapy with metformin and insulin for at least 8 weeks prior to screening

Exclusion Criteria

* History of diabetic ketoacidosis (DKA), type 1 diabetes mellitus (T1DM), pancreas or cell transplantation, or diabetes secondary to pancreatitis or pancreatectomy or maturity onset diabetes of the young (MODY)
* Participants on any antihyperglycemic agents (AHAs) other than metformin, or injectable insulin within 8 weeks of the first dose of study drug (that is Day 1)
* Repeated (2 or more over a 1-week period) fasting self-monitoring of blood glucose (SMBG) measurements \>270 milligram/deciliter (mg/dL) (\>15 millimole/liter \[mmol/L\]) during the pretreatment phase, despite reinforcement of diet and exercise counseling
* Severe hypoglycemia within 6 months prior to Day 1
* History of hereditary glucose-galactose malabsorption or primary renal glucosuria
* Alanine aminotransferase level \>5.0 times the upper limit of normal (ULN) or total bilirubin \>1.5 times the ULN at screening (for elevations in bilirubin: if, in the opinion of the investigator and agreed upon by the sponsor's medical officer, the elevation in bilirubin is consistent with Gilbert's disease, the subject may participate)
Minimum Eligible Age

10 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Janssen Research & Development, LLC

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Janssen Research & Development, LLC Clinical Trial

Role: STUDY_DIRECTOR

Janssen Research & Development, LLC

Locations

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Arkansas Childrens Hospital

Little Rock, Arkansas, United States

Site Status

Center of Excellence for Diabetes and Endocrinology (CEDE)

Sacramento, California, United States

Site Status

American Institute of Research

Whittier, California, United States

Site Status

University of Colorado School of Medicine/Children's Hospital Colorado

Aurora, Colorado, United States

Site Status

Nemours DuPont Hospital for Children

Wilmington, Delaware, United States

Site Status

TOPAZ Clinical Research

Apopka, Florida, United States

Site Status

Columbus Clinical Services LLC

Miami, Florida, United States

Site Status

Medical Research Center of Miami II Inc

Miami, Florida, United States

Site Status

Nicklaus Children's Hospital

Miami, Florida, United States

Site Status

Nemours Children's Hospital/Endocrinology

Orlando, Florida, United States

Site Status

Asclepes Research

Spring Hill, Florida, United States

Site Status

Johns Hopkins All Children's Hospital

St. Petersburg, Florida, United States

Site Status

Appalachian Clinical Research

Adairsville, Georgia, United States

Site Status

Endocrine Consultants Research

Columbus, Georgia, United States

Site Status

University of Iowa Hospitals and Clinics

Iowa City, Iowa, United States

Site Status

Capital Diabetes and Endocrine Associates

Camp Springs, Maryland, United States

Site Status

Floating Hospital For Children at Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Alas Viable Research

Henderson, Nevada, United States

Site Status

University of New Mexico

Albuquerque, New Mexico, United States

Site Status

SUNY Downstate Medical Center

Brooklyn, New York, United States

Site Status

Icahn School of Medicine at Mount Sinai

New York, New York, United States

Site Status

Carolinas Research Center, LLC

Charlotte, North Carolina, United States

Site Status

WakeMed Clinical Research Institute

Raleigh, North Carolina, United States

Site Status

PMG Research of Wilmington, LLC

Wilmington, North Carolina, United States

Site Status

Cleveland Clinic Center for Pediatric Endocrinology

Cleveland, Ohio, United States

Site Status

Buckeye Health and Research, LLC

Columbus, Ohio, United States

Site Status

Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

AM Diabetes & Endocrinology Center

Bartlett, Tennessee, United States

Site Status

LifeDoc Research, PLLC

Memphis, Tennessee, United States

Site Status

Avant Research Associates, LLC

Austin, Texas, United States

Site Status

Driscoll Children's Hospital

Corpus Christi, Texas, United States

Site Status

Amir Ali Hassan, MD, PA

Houston, Texas, United States

Site Status

Sante Clinical Research

Kerrville, Texas, United States

Site Status

Texas Institute for Kidney and Endocrine Disorders

Lufkin, Texas, United States

Site Status

Sun Research Institute

San Antonio, Texas, United States

Site Status

MultiCare Health System

Tacoma, Washington, United States

Site Status

Hospital Universitario Joao de Barros Barreto - UFPA

Belém, , Brazil

Site Status

Santa Casa de Misericordia de Belo Horizonte

Belo Horizonte, , Brazil

Site Status

Condominio Centro Clinico do Lago

Brasília, , Brazil

Site Status

Centro de Diabetes Curitiba Ltda

Curitiba, , Brazil

Site Status

Núcleo de Pesquisa Clinica

Porto Alegre, , Brazil

Site Status

Instituto da Criança com Diabetes do Rio Grande do Sul - ICDRS

Porto Alegre, , Brazil

Site Status

Ruschel Medicina e Pesquisa Clínica Ltda

Rio de Janeiro, , Brazil

Site Status

Hospital e Maternidade Dr Christovao da Gama S.A

Santo André, , Brazil

Site Status

IPEC - Instituto de Pesquisa Clínica Ltda

São Paulo, , Brazil

Site Status

Hospital Das Clinicas Da Faculdade De Medicina Da USP

São Paulo, , Brazil

Site Status

Santa Casa de Misericórdia de Votuporanga

Votuporanga, , Brazil

Site Status

Capital Institute of Pediatrics

Beijing, , China

Site Status

Xiangya Hospital Central South University

Changsha, , China

Site Status

The Childrens Hospital Zhejiang University School Of Medicine

Hangzhou, , China

Site Status

Jiangxi Provincial Children's Hospital

Nanchang, , China

Site Status

Jiangsu Province Hospital

Nanjing, , China

Site Status

Wuhan Union Hospital

Wuhan, , China

Site Status

Tongji Hospital Tongji Medical College of Huazhong University of Science and Technology

Wuhan, , China

Site Status

Chidren's Hospital of Zhengzhou

Zhengzhou, , China

Site Status

General Children's Hospital 'P. and A. Kyriakou'

Athens, , Greece

Site Status

Athens Medical Center

Athens, , Greece

Site Status

Diacon Hospital

Bangalore, , India

Site Status

Post Graduate Institute of Medical Education And Research PGIMER

Chandigarh, , India

Site Status

Kovai Diabetes Specialty Centre & Hospital

Coimbatore, , India

Site Status

Quality Care India Limited

Hyderabad, , India

Site Status

P D Hinduja National Hospital and Medical Research Center

Mumbai, , India

Site Status

Sir Ganga Ram Hospital

New Delhi, , India

Site Status

Jehangir Clinical Development Center Pvt Ltd

Pune, , India

Site Status

Jothydev's Diabetes Research Centre

Trivandrum, , India

Site Status

Hospital Sultanah Bahiyah

Alor Star, , Malaysia

Site Status

Hospital Pulau Pinang

George Town, , Malaysia

Site Status

Hospital Raja Permaisuri Bainun

Ipoh, , Malaysia

Site Status

Hospital Tuanku Fauziah

Kangar, , Malaysia

Site Status

Hospital University Sains Malaysia

Kubang Kerian, , Malaysia

Site Status

Investigación Biomédica para el Desarrollo de Fármacos S.A. de C.V.

Aguascalientes, , Mexico

Site Status

Instituto Nacional de Pediatría

Coyoacán, , Mexico

Site Status

Desarrollo Ético en Investigación Clínica S.C .

Guadalajara, , Mexico

Site Status

Centro de Estudios de Investigación Metabólicos y Cardiovasculares S.C.

Madero, , Mexico

Site Status

Bio Investigación AMARC, S.C.

Mexico City, , Mexico

Site Status

St Lucas Clinical Research Center

Mérida, , Mexico

Site Status

UBAM Unidad Biomédica Avanzada Monterrey

Monterrey, , Mexico

Site Status

Consultorio Medico

Puebla City, , Mexico

Site Status

Centro Integral Medico SJR, SC

San Juan del Río, , Mexico

Site Status

Centro De Investigacion Medica De Occidente, S.C.

Zapopan, , Mexico

Site Status

Chong Hua Hospital

Cebu City, , Philippines

Site Status

Norzel MedicaL and Diagnostic Clinic

Cebu City, , Philippines

Site Status

De La Salle Health Sciences Institute- DLSUMC

Dasmariñas, , Philippines

Site Status

Davao Doctors Hospital

Davao City, , Philippines

Site Status

Docbebet Diabetes Clinic

San Fernando City, , Philippines

Site Status

Gornoslaskie Centrum Zdrowia, SPSK nr 6 Slaskiego Uniwersytetu Medycznego w Katowicach

Katowice, , Poland

Site Status

WSS Dzieciecy prof.dr S.Popowskiego w Olsztynie,Od.Pediatryczny VI Reumatologiczno-Endokrynologiczny

Olsztyn, , Poland

Site Status

Gabinet Pediatryczny Artur Mazur

Rzeszów, , Poland

Site Status

Instytut 'Pomnik-Centrum Zdrowia Dziecka', Klinika Endokrynologii i Diabetologii

Warsaw, , Poland

Site Status

Uniwersytecki Szpital Kliniczny im Jana Mikulicza Radeckiego we Wroclawiu

Wroclaw, , Poland

Site Status

Specjalistyczna Praktyka Lekarska Aspiro

Wroclaw, , Poland

Site Status

Republic Children Clinical Hospital of the Ministry of Health of Udmurtskaya Republic

Izhevsk, , Russia

Site Status

Kirov Clinical Hospital #7 named after V.I. Yurlova

Kirov, , Russia

Site Status

Krasnoyarsk State Medical University

Krasnoyarsk, , Russia

Site Status

Natiolal Medical Research Center of Endocrinology

Moscow, , Russia

Site Status

Russian National Research Medical University named after N.I.Pirogov

Moscow, , Russia

Site Status

Children City Clinical Hospital #1

Novosibirsk, , Russia

Site Status

Omsk Regional Childrens Clinical Hospital

Omsk, , Russia

Site Status

City Children Clinical Outpatient Clinic #5

Perm, , Russia

Site Status

SBHI Children's City Multi-Profile Clinical Center named after K. A. Rauhfus

Saint Petersburg, , Russia

Site Status

Children Outpatient Clinic 45 Of Nevskiy Region

Saint Petersburg, , Russia

Site Status

Saint-Petersburg State Pediatric Medical Academy of RosZdrav, Clinical Diagnostic Center

Saint Petersburg, , Russia

Site Status

Samara Regional Children Clinical Hospital named after N.N. Ivanova

Samara, , Russia

Site Status

Siberian State Medical University

Tomsk, , Russia

Site Status

Tver Regional Clinical Hospital

Tver', , Russia

Site Status

Regional Pediatric Clinical Hospital No.1

Yekaterinburg, , Russia

Site Status

Countries

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United States Brazil China Greece India Malaysia Mexico Philippines Poland Russia

References

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Nadgir U, Ali SR, Gogate J, Shaw W, Antunes J, Fonseca S. Treatment With Canagliflozin Versus Placebo in Children and Adolescents With Type 2 Diabetes : A Randomized Clinical Trial. Ann Intern Med. 2025 Sep;178(9):1217-1226. doi: 10.7326/ANNALS-24-04017. Epub 2025 Aug 5.

Reference Type DERIVED
PMID: 40759025 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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28431754DIA3018

Identifier Type: OTHER

Identifier Source: secondary_id

2016-005223-88

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CR108298

Identifier Type: -

Identifier Source: org_study_id

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