HDL Acute Lipid Optimization in Homozygous Familial Hypercholesterolemia

NCT ID: NCT03135184

Last Updated: 2019-05-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

NA

Total Enrollment

6 participants

Study Classification

INTERVENTIONAL

Study Start Date

2018-01-26

Study Completion Date

2019-08-31

Brief Summary

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Assess the effect on coronary atheroma of serial infusions of autologous selectively delipidated HDL/preβ enriched plasma following use of HDL Therapeutics PDS-2™ System

Detailed Description

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The PDS-2™ System is intended to reduce coronary atheroma in patients with Homozygous Familial Hypercholesterolemia (HoFH). Subjects will receive serial infusions of autologous selectively delipidated HDL/preβ enriched plasma following use of HDL Therapeutics' PDS-2 System.

Conditions

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Homozygous Familial Hypercholesterolemia HoFH

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Prospective, unblinded, interventional study
Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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HDL Therapeutics PDS-2™ System

Serial infusions of autologous selectively delipidated HDL/preβ enriched plasma following use of HDL Therapeutics PDS-2™ System

Group Type EXPERIMENTAL

HDL Therapeutics PDS-2 System

Intervention Type DEVICE

Delipidation of plasma HDL to reduce coronary atheroma

Interventions

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HDL Therapeutics PDS-2 System

Delipidation of plasma HDL to reduce coronary atheroma

Intervention Type DEVICE

Eligibility Criteria

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Inclusion Criteria

* Clinical diagnosis of Homozygous Familial Hypercholesterolemia (HoFH) due to a defect in the LDL receptor, or the identification of a defect in apoB-100, or a gain of function of PCSK9, or a genetic defect resulting in the HoFH clinical phenotype
* No other condition that would preclude the subject from successfully completing the series of plasmapheresis visits in the investigator's opinion
* At least one (1) coronary artery study segment will be identified for each subject and all will remain constant throughout the study. The qualifying study segment(s) will have 20% to 40% stenosis.

Exclusion Criteria

* Planned change in current lipid lowering therapy
* Use of oral anticoagulants, unless the dose has been stable for 4 weeks
* LDL or plasma apheresis within 1 week prior to enrollment and through 8-week primary endpoint
* New York Heart Association (NYHA) class III or IV or last known left ventricular ejection fraction \< 30%
* Myocardial infarction, unstable angina, percutaneous coronary intervention (PCI), coronary artery bypass graft (CABG) or stroke within 3 months of enrollment
Minimum Eligible Age

12 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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MedStar Heart and Vascular Institute

UNKNOWN

Sponsor Role collaborator

HDL Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Cedars-Sinai Medical Center (CSMC)

Los Angeles, California, United States

Site Status

Countries

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United States

Other Identifiers

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HALO-FH

Identifier Type: -

Identifier Source: org_study_id

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