A Study to Evaluate Multiple Doses of GLPG2222 in Adult Subjects With Cystic Fibrosis

NCT ID: NCT03119649

Last Updated: 2018-11-16

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

59 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-03-18

Study Completion Date

2017-10-19

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a Phase IIa, multi-center, randomized, double-blind, placebo-controlled, parallel-group study to evaluate 4 different doses of GLPG2222 administered for 4 weeks to adult subjects with a confirmed diagnosis of CF and homozygous for the F508del Cystic Fibrosis Transmembrane conductance Regulator (CFTR) mutation.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Cystic Fibrosis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Cohort A: GLPG2222 50 mg once daily (QD)

Participants received a single GLPG2222 50 mg tablet and two matching placebo tablets orally, QD for 29 days.

Group Type EXPERIMENTAL

GLPG2222 50 mg

Intervention Type DRUG

Oral tablet(s) containing GLPG2222

Placebo

Intervention Type DRUG

Matching oral tablet(s) containing placebo

Cohort A: GLPG2222 100 mg QD

Participants received a single GLPG2222 100 mg tablet and two matching placebo tablets orally, QD for 29 days.

Group Type EXPERIMENTAL

GLPG2222 100 mg

Intervention Type DRUG

Oral tablet(s) containing GLPG2222

Placebo

Intervention Type DRUG

Matching oral tablet(s) containing placebo

Cohort B: GLPG2222 200 mg QD

Participants received two GLPG2222 100 mg tablets and one matching placebo tablet orally, QD for 29 days.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Matching oral tablet(s) containing placebo

GLPG2222 200 mg

Intervention Type DRUG

Oral tablet(s) containing GLPG2222

Cohort B: GLPG2222 400 mg QD

Participants received two GLPG2222 150 mg tablets and one GLPG2222 100 mg tablet orally, QD for 29 days.

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Matching oral tablet(s) containing placebo

GLPG2222 400 mg

Intervention Type DRUG

Oral tablet(s) containing GLPG2222

Cohort A Placebo

Participants received three matching placebo tablets, orally, QD for 29 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching oral tablet(s) containing placebo

Cohort B Placebo

Participants received three matching placebo tablets, orally, QD for 29 days.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching oral tablet(s) containing placebo

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

GLPG2222 50 mg

Oral tablet(s) containing GLPG2222

Intervention Type DRUG

GLPG2222 100 mg

Oral tablet(s) containing GLPG2222

Intervention Type DRUG

Placebo

Matching oral tablet(s) containing placebo

Intervention Type DRUG

GLPG2222 200 mg

Oral tablet(s) containing GLPG2222

Intervention Type DRUG

GLPG2222 400 mg

Oral tablet(s) containing GLPG2222

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

1. Male or female subject ≥ 18 years of age, on the day of signing the Informed Consent Form (ICF).
2. A confirmed clinical diagnosis of CF and homozygous for the F508del CFTR mutation
3. Weight ≥ 40 kg.
4. Stable concomitant treatment for at least 4 weeks (28 days) prior to baseline
5. Forced expiratory volume in 1 second (FEV1) ≥ 40% of predicted normal for age, gender and height at screening

Exclusion Criteria

1. History of clinically meaningful unstable or uncontrolled chronic disease that makes the subject unsuitable for inclusion in the study in the opinion of the investigator.
2. Unstable pulmonary status or respiratory tract infection requiring a change in therapy within 4 weeks of baseline.
3. Need for supplemental oxygen during the day, and \>2 liters per minute (LPM) while sleeping.
4. Use of CFTR modulator therapy (e.g. lumacaftor or ivacaftor) within 4 weeks prior to the first study drug administration.
5. History of hepatic cirrhosis with portal hypertension.
6. Abnormal liver function test at screening; defined as aspartate aminotransferase (AST) and/or alanine aminotransferase (ALT) and/ or alkaline phosphatase and/or gamma-glutamyl transferase (GGT) ≥ 3x the upper limit of normal (ULN); and/or total bilirubin (\>1.5 times ULN)
7. Estimated creatinine clearance \< 60 mL/min using the Cockcroft-Gault formula at screening.
Minimum Eligible Age

18 Years

Maximum Eligible Age

99 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Galapagos NV

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Olivier Van Steen, MD, MBA

Role: STUDY_DIRECTOR

Galapagos NV

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Child Health Research Unit at UAB

Chatom, Alabama, United States

Site Status

University of Arkansas for medical Sciences

Little Rock, Arkansas, United States

Site Status

Central Florida Pulmonary Group

Orlando, Florida, United States

Site Status

Cystic Fibrosis Center of Chicago

Glenview, Illinois, United States

Site Status

Maine Medical Center

Portland, Maine, United States

Site Status

John Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

UZ Antwerpen

Antwerp, , Belgium

Site Status

UZ Brussel

Brussels, , Belgium

Site Status

UZ Gent

Ghent, , Belgium

Site Status

UZ Leuven

Leuven, , Belgium

Site Status

AMC Amsterdam

Amsterdam, , Netherlands

Site Status

Erasmus medisch centrum

Rotterdam, , Netherlands

Site Status

Haga Ziekenhuis

The Hague, , Netherlands

Site Status

UMC Utrecht

Utrecht, , Netherlands

Site Status

Mother and child health institute of Serbia

New Belgrade, , Serbia

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitarii Plitecnic La Fe

Valencia, , Spain

Site Status

Papworth Hospital

Cambridge, , United Kingdom

Site Status

St James University Hospital

Leeds, , United Kingdom

Site Status

Liverpool Heart and Chest Hospital

Liverpool, , United Kingdom

Site Status

Southampton general Hospital

Southampton, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Belgium Netherlands Serbia Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Bell SC, Barry PJ, De Boeck K, Drevinek P, Elborn JS, Plant BJ, Minic P, Van Braeckel E, Verhulst S, Muller K, Kanters D, Bellaire S, de Kock H, Geller DE, Conrath K, Van de Steen O, van der Ent K. CFTR activity is enhanced by the novel corrector GLPG2222, given with and without ivacaftor in two randomized trials. J Cyst Fibros. 2019 Sep;18(5):700-707. doi: 10.1016/j.jcf.2019.04.014. Epub 2019 May 3.

Reference Type DERIVED
PMID: 31056441 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

GLPG2222-CL-202

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.