A Study to Evaluate the Efficacy and Safety of X0002 Spray in Subjects With Osteoarthritis Knee Pain

NCT ID: NCT03081806

Last Updated: 2024-03-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

399 participants

Study Classification

INTERVENTIONAL

Study Start Date

2021-09-24

Study Completion Date

2024-01-10

Brief Summary

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This is a Phase 3, Multicenter, 22-Week, double-blind and 30-Week open label Study to Evaluate the Efficacy and Safety of X0002 Spray in relief of pain of subjects with Osteoarthritis of the Knee.

Detailed Description

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The study comprises a 14-day Screening Period, a 22-week Double-blind Treatment Period, and a 30-week Open-label Treatment Period, with an additional 4-week Follow-up Visit. Subjects will be randomized into a low-dose or high-dose group receiving either active or placebo treatment during the DB period.

The WOMAC version 3.1 using the NRS will be used for the primary and secondary efficacy endpoints. Safety assessments will include assessment of AEs, vital signs (blood pressure, respiratory rate, pulse rate, and oral temperature), clinical laboratory tests, physical examination, skin irritation, and electrocardiograms (ECGs).

Conditions

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Pain Associated With Osteoarthritis of the Knee

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Group A

High dose group: X0002, BID (approximately every 12 hours; n=102); Placebo, BID(approximately every 12 hours; n=102)

Group Type EXPERIMENTAL

X0002

Intervention Type DRUG

Subjects will complete 22 weeks of double-blind treatment and then enter into 30 weeks open-label treatment.

Group B

Low dose group: X0002, BID (approximately every 12 hours; n=102); Placebo, BID(approximately every 12 hours; n=102)

Group Type PLACEBO_COMPARATOR

X0002

Intervention Type DRUG

Subjects will complete 22 weeks of double-blind treatment and then enter into 30 weeks open-label treatment.

Interventions

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X0002

Subjects will complete 22 weeks of double-blind treatment and then enter into 30 weeks open-label treatment.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Ability to read and provide written, personally signed, and dated informed consent to participate in the study, in accordance with the ICH GCP Guideline E6 and applicable regulations, before completing any study related procedures.
2. An understanding, ability, and willingness to fully comply with study procedures and restrictions.
3. Subject must be a male or female between 35 and 85 years of age, inclusive.
4. Female subjects must either not be of childbearing potential (defined as postmenopausal for at least 1 year or surgically sterile \[bilateral tubal ligation, bilateral oophorectomy, or hysterectomy\]) or be willing to Practice at least 1 of the following medically acceptable methods of birth control.
5. Subject must have a body mass index (BMI) between 18.5 and 45 kg/m2, inclusive.
6. Must have a history of clinically symptomatic OA of the knee for ≥6 months.
7. Must meet the American College of Rheumatology clinical classification criteria for knee OA. These criteria include the presence of knee pain in addition to at least 3 of the following 6 items:

* age of ≥50 years
* stiffness lasting \<30 minutes
* crepitus on knee motion
* Bony Tenderness
* Bony Enlargement
* No palpable warmth
8. A subject must have a Kellgren Lawrence Grade of 2,3 or 4 as determined by a central radiologist at the first screening visit. .
9. Subject must have had knee pain while standing, walking, and/or in motion for at least 14 days during the month prior to Screening.
10. Subject must have a knee pain score ≥4 and \<9 on 0-10 pain intensity NRS (without analgesic medication) on at least 7 of the 10 days prior to randomization.
11. Subject must be willing to discontinue any NSAIDs or other analgesic (eg, aspirin, acetaminophen) or potentially confounding concomitant treatments (eg, physiotherapy, acupuncture) starting on the first screening visit until completing participation in the study. (The use of ≤325 mg acetylsalicylic acid per day as cardiac prophylaxis is permitted.) The subject will be allowed to take rescue medication (acetaminophen) for pain during the study except during the 24 hours prior to the Second Screening Visit, Baseline (Day1), Week 2, Week 4, Week 8, Week 12, Week 22, Week 32, Week 42, and Week 52/EOS.
12. Subject must be willing to discontinue applying any topical preparations containing Vitamin A acids (including all trans retinoic acid (tretinoin), 13 cis retinoic acid \[isotretinoin\], 9 cis retinoic acid \[alitretinoin\], vitamin A \[retinol\], retinal, and their derivatives) to the lower limbs starting on the first screening visit until completing participation in the study. (Topical preparations containing Vitamin A acids or retinol may be applied to areas of the skin above the waist, but should not be applied to areas of the skin exposed to study medication.)
13. Subject must be willing to avoid unaccustomed physical activity (eg, starting a new weight lifting routine) for the duration of the study starting on the first screening visit.
14. With the exception of OA of the knee subjects with medical history must be stable as determined by the investigator.

Exclusion Criteria

1. Has worker's compensation injuries affecting the knee or back.
2. Has a history of or is currently in litigation regarding joint injuries.
3. Has secondary OA of the target knee or OA of lower limb joints other than the knee that, in the investigator's opinion, could interfere with pain and functional assessments related to the target knee.
4. Has a history of total or partial knee replacement, arthroplasty, or other knee surgery on the target knee.
5. In the investigator's opinion, has had significant injury involving the target knee within the 6 months before Screening.
6. Has skin lesions or wounds on or near the target knee at Screening or at Baseline (Day 1) that, in the investigator's opinion, would affect absorption of the medication.
7. Has used opiates (including tramadol or tapentadol) or systemic corticosteroids within 30 days before Screening or requires treatment with chronic opiates or systemic corticosteroids.
8. Subjects with a placebo response exceeding 25% improvement in the average Western Ontario and McMaster Osteoarthritis Index \[WOMAC\] pain subscale score from Screening Visit to Day 1 will be excluded.
9. Has used gabapentin, pregabalin, antiepileptics, or specific antidepressants (i.e., tricyclics, serotonin norepinephrine reuptake inhibitors, or selective serotonin reuptake inhibitors) to treat pain in the 14 days before Screening. Other uses not related to the pain treatment may be permitted at the medical monitor's discretion provided they have been at a stable dose for at least 90 days.
10. Has had intra articular (IA) injections of corticosteroids, hyaluronic acid, or viscosupplements (e.g., Synvisc®) to the target knee within the 12 weeks before Screening
11. Has had IA or intravenous (IV) stem cell therapy in the 6 months prior to Screening
12. Is receiving or is planning to receive concomitant nonpharmacologic treatments (e.g., physiotherapy, acupuncture) that in the investigator's opinion could confound efficacy assessments within 14 days of Day 1.
13. Has a history of significant hypersensitivity, intolerance, or allergy to ibuprofen or any other NSAIDs, aspirin, or acetaminophen.
14. Has had an active gastrointestinal (GI) ulceration in the 6 months prior to Screening or a history of GI bleeding within 5 years of Screening.
15. Has used an anticoagulant or antiplatelet agent (except aspirin up to 325 mg/day for cardiac prophylaxis) in the 30 days prior to Screening.
16. Has a documented history of chronic inflammatory disease (e.g., rheumatoid arthritis, psoriatic arthritis, inflammatory bowel disease, gouty arthritis) OR chronic pain condition (e.g., fibromyalgia), OR has other conditions that may affect the target joint for the functional and pain assessments (e.g., osteonecrosis, chondrocalcinosis).
17. Has uncontrolled depression or other uncontrolled psychiatric disorder (subjects with controlled depression or other psychiatric disorder, if using medication, must be on a stable dose of a medication other than an epileptic, tricyclic, serotonin norepinephrine reuptake inhibitor, or selective reuptake inhibitor for ≥12 weeks prior to Screening to participate in the study).
18. Has asthma requiring treatment with systemic corticosteroids in the last year prior to Screening. Asthmatic subjects using inhaled corticosteroids are eligible.
19. Has uncontrolled hypertension defined as systolic blood pressure \>170 mmHg and diastolic blood pressure \>90 mmHg at the Screening or Baseline Visit (may be repeated after 5 minutes rest to verify).
20. Is receiving systemic chemotherapy, has an active malignancy, lymphoproliferative disorder, or blood dyscrasia of any type, or has been diagnosed with cancer within 5 years before Screening. Subjects with completely excised squamous or basal cell carcinoma of the skin will be allowed.
21. Has any clinically significant unstable cardiac, respiratory, neurological, immunological, hematological, hepatic, or renal disease, or any other condition that, in the Investigator's opinion, could confound the study results, compromise the subject's welfare, interfere with the ability to communicate with the study staff, or otherwise contraindicate study participation.
22. Has any of the following conditions at Screening:

* Acute hepatitis
* Cirrhosis
* Stage 4 or 5 end-stage renal disease
23. Subject has any other clinically significant laboratory finding at Screening that in the investigator's opinion contraindicates study participation.
24. Has clinically significant abnormality at Screening or Baseline (Day 1) on 12-lead ECG, including a QT interval calculated using Fridericia's correction (QTcF) interval \>500 milliseconds (msec) or evidence of cardiac ischemia (i.e., Evident q waves: t wave inversion).
25. Is pregnant, planning to become pregnant during the study, or lactating. Has a positive serum and urine pregnancy test at Screening Visit, or a positive urine pregnancy test at Baseline (Day 1).
26. Has a positive urine drug screen for a nonprescribed drug prohibited by the protocol at Screening.
27. Has known alcohol or other substance abuse in the investigator's opinion.
28. Has participated in a previous clinical study with X0002.
29. Has participated in any other clinical trial within the past 30 days or within 5 half-lives of the study drug prior to Screening, whichever is longer.
30. Is a participating investigator, sub-investigator, study coordinator, or employee of a participating investigator, or is an immediate family member of the aforementioned.
31. Has any factor that, in the investigator's opinion, would jeopardize the evaluation or safety or be associated with poor adherence to the protocol.
32. Is without access to telephone and/or ability to gain technology access.
Minimum Eligible Age

35 Years

Maximum Eligible Age

85 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Techfields Pharma Co. Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Chongxi Yu, PhD

Role: STUDY_CHAIR

Techfields Inc

Locations

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Arizona Research Center

Phoenix, Arizona, United States

Site Status

Yuma Clinical Trials

Yuma, Arizona, United States

Site Status

Orange County Research Institute

Anaheim, California, United States

Site Status

Biosolutions Clinical Research Center

La Mesa, California, United States

Site Status

Velocity Clinical Research

North Hollywood, California, United States

Site Status

University Clinical Research-Deland

DeLand, Florida, United States

Site Status

Reliable Clinical Research

Hialeah, Florida, United States

Site Status

Health Awareness Inc.

Jupiter, Florida, United States

Site Status

Ascension Research

Pinellas Park, Florida, United States

Site Status

Conquest Research

Winter Park, Florida, United States

Site Status

Horizon Clinical Research

Newnan, Georgia, United States

Site Status

Pinnacle Trials Inc

Stockbridge, Georgia, United States

Site Status

Chicago Clinical Research Institute Inc

Chicago, Illinois, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Healthcare Research Network

Flossmoor, Illinois, United States

Site Status

Affinity Health Corp

Oak Brook, Illinois, United States

Site Status

DelRicht Research

New Orleans, Louisiana, United States

Site Status

DelRicht Research

Prairieville, Louisiana, United States

Site Status

DelRicht Research - Gulfport

Gulfport, Mississippi, United States

Site Status

Healthcare Research Network, LLC

Hazelwood, Missouri, United States

Site Status

AMR Kansas City

Kansas City, Missouri, United States

Site Status

Sundance Clinical Research, LLC

St Louis, Missouri, United States

Site Status

AMR: Las Vegas

Las Vegas, Nevada, United States

Site Status

Upstate Clinical Research Associates LLC

Williamsville, New York, United States

Site Status

Aventiv Research, Inc - Brice Road Location

Columbus, Ohio, United States

Site Status

DelRicht Research

Tulsa, Oklahoma, United States

Site Status

Altoona Center For Clinical Research

Duncansville, Pennsylvania, United States

Site Status

Tekton Research

Austin, Texas, United States

Site Status

Clinical Investigations of Texas

Plano, Texas, United States

Site Status

Quality Research Inc.

San Antonio, Texas, United States

Site Status

Wasatch Clinical Research LLC

Salt Lake City, Utah, United States

Site Status

Charlottesville Medical Research, LLC

Charlottesville, Virginia, United States

Site Status

Spectrum Medical, Inc

Danville, Virginia, United States

Site Status

Countries

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United States

Other Identifiers

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TF-X0002-31

Identifier Type: -

Identifier Source: org_study_id

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