Extension Study of NT-501 Ciliary Neurotrophic Factor (CNTF) Implant for Macular Telangiectasia (MacTel)

NCT ID: NCT03071965

Last Updated: 2025-05-09

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

70 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-05-12

Study Completion Date

2021-05-11

Brief Summary

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This was a prospective, multicenter, single-masked, sham-controlled extension study designed to provide long-term safety and efficacy follow-up data for subjects with MacTel who had NT-501 implanted intraocularly and/or underwent sham surgery in the respective precursor study (NTMT-01 or NTMT-02).

A substudy was conducted in which subjects enrolled in study (NTMT-02), who had 1 study-eligible eye that underwent sham surgery, were offered the option to have NT-501 implanted in the same study eye. Of the 19 subjects who had 1 study-eligible eye and underwent sham surgery in the Cohort 2 precursor study (NTMT-02), 16 subjects elected to have NT-501 implanted in the same study eye during the substudy

Detailed Description

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Conditions

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MacTel (Macular Telangiectasia) Type 2

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

SINGLE

Outcome Assessors

Study Groups

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Cohort 1

Participants completed protocol NTMT-01. All participants received surgery to implant NT-501. All participants received ciliary neurotrophic factor (CNTF).

Group Type EXPERIMENTAL

Ciliary neurotrophic factor (CNTF)

Intervention Type BIOLOGICAL

The investigational product is the NT-501 encapsulated cell system, which consists of cells encapsulated within a semi-permeable polymer membrane and supportive matrices. NT-501 contains NTC-201 cells that secrete recombinant human CNTF, which were derived from genetically modified NTC-200 cells.

Surgery

Intervention Type PROCEDURE

Surgery to implant device for NT-501

Cohort 2

Participants completed protocol NTMT-02. Participants for cohort 2 arm were either:

* NT-501 group: included subjects who each had 1 study-eligible eye that had NT-501 implanted and a fellow eye that did not undergo any study intervention.
* Sham group: included subjects who each had 1 study-eligible eye that underwent sham surgery and a fellow eye that did not undergo any study intervention.
* Sham+NT-501 group: included subjects who had both eyes that were study-eligible, and had NT-501 implanted in 1 eye and underwent sham surgery in the contralateral eye.

Group Type EXPERIMENTAL

Ciliary neurotrophic factor (CNTF)

Intervention Type BIOLOGICAL

The investigational product is the NT-501 encapsulated cell system, which consists of cells encapsulated within a semi-permeable polymer membrane and supportive matrices. NT-501 contains NTC-201 cells that secrete recombinant human CNTF, which were derived from genetically modified NTC-200 cells.

Surgery

Intervention Type PROCEDURE

Surgery to implant device for NT-501

Surgery

Intervention Type PROCEDURE

Sham surgery

Interventions

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Ciliary neurotrophic factor (CNTF)

The investigational product is the NT-501 encapsulated cell system, which consists of cells encapsulated within a semi-permeable polymer membrane and supportive matrices. NT-501 contains NTC-201 cells that secrete recombinant human CNTF, which were derived from genetically modified NTC-200 cells.

Intervention Type BIOLOGICAL

Surgery

Surgery to implant device for NT-501

Intervention Type PROCEDURE

Surgery

Sham surgery

Intervention Type PROCEDURE

Eligibility Criteria

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Inclusion Criteria

* Previously enrolled in the NTMT-01 or NTMT-02 protocol and received the NT-501 implant and/or underwent a Sham procedure
* Participant must be offered sufficient opportunity to review and to understand the informed consent form, agree to the form's contents, and provide written informed consent.
Minimum Eligible Age

21 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Neurotech Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Thomas Aaberg, Jr, MD

Role: STUDY_CHAIR

Neurotech Pharmaceuticals, LLC

Locations

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Stein Eye Institute / David Geffen School of Medicine

Los Angeles, California, United States

Site Status

University of Miami-Miller School of Medicine, Bascom Palmer Eye Institute

Miami, Florida, United States

Site Status

Emory University School of Medicine, Dept of Ophthalmology, Emory University Eye Center

Atlanta, Georgia, United States

Site Status

NIH Clinical Center

Rockville, Maryland, United States

Site Status

Massachusetts Eye and Ear Infirmary

Boston, Massachusetts, United States

Site Status

University of Michigan, Kellogg Eye Center

Ann Arbor, Michigan, United States

Site Status

Retina Associates of Cleveland, Inc

Cleveland, Ohio, United States

Site Status

University of Wisconsin-Madison, Department of Ophthalmology and Visual Sciences

Madison, Wisconsin, United States

Site Status

Sydney Eye Hospital

Sydney, New South Wales, Australia

Site Status

Centre for Eye Research Australia

East Melbourne, Victoria, Australia

Site Status

Lions Eye Institute

Nedlands, Western Australia, Australia

Site Status

Countries

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United States Australia

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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NTMT-01/02E

Identifier Type: -

Identifier Source: org_study_id

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