A Multiple Ascending Dose Study to Evaluate Safety and Tolerability of BFKB8488A in Participants With Type 2 Diabetes Mellitus and Participants With Non-Alcoholic Fatty Liver Disease

NCT ID: NCT03060538

Last Updated: 2020-03-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

154 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-03-05

Study Completion Date

2019-12-13

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a Phase Ib, randomized, blinded, placebo-controlled, multiple ascending-dose study of the safety, tolerability, pharmacokinetic (PK), and pharmacodynamic (PD) effects of BFKB8488A in participants with Type 2 diabetes mellitus (T2DM) and participants with non-alcoholic fatty liver disease(NAFLD). A maximum of approximately 160 participants will be enrolled across multiple sites in the United States. Participants will be randomly assigned to receive study drug (active BFKB8488A or placebo). The study will consist of a screening period (up to 8 weeks), a 12-week treatment period, and a 6-week follow-up period. Participants may come to clinic for an optional pre-screening visit.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Diabetes Mellitus, Type 2 Non-Alcoholic Fatty Liver Disease

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Multiple Ascending Dose BFKB8488A

Participants will be randomized to receive BFKB8488A. When adequate safety data are available, a review will be done for all participants to make a dose-escalation or dose and/or regimen modification decision. This will be repeated for each cohort.

Group Type EXPERIMENTAL

BFKB8488A

Intervention Type DRUG

Administered subcutaneously starting on Day 1 and according to dosing schedule.

Placebo

Participants will receive BFKB8488A-matching placebo.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Administered subcutaneously starting on Day 1 and according to dosing schedule.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

BFKB8488A

Administered subcutaneously starting on Day 1 and according to dosing schedule.

Intervention Type DRUG

Placebo

Administered subcutaneously starting on Day 1 and according to dosing schedule.

Intervention Type OTHER

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

RO7040551

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

For T2DM Cohort only:

* Body mass index (BMI) ≥ 27 kg/m2 and ≤ 40 kg/m2.
* A confirmed diagnosis of Type 2 diabetes ≥ 6 months at screening
* Current stable treatment (at least 3 months) for diabetes
* Hemoglobin A1c (HbA1c) ≥ 6.8% and ≤ 9.0%.
* For women of childbearing potential, agreement to remain abstinent or use reliable contraception during treatment period and for at least 42 days after last dose of study drug
* For men, agreement to remain abstinent or use reliable contraception and agree to refrain from donating sperm
* For NAFLD cohort only:
* BMI ≥ 25 kg/m2 and ≤ 40 kg/m2
* At screening, confirmed liver fat by ultrasound OR calculated Liver Fat ≥ 10% using variables from the NAFLD liver fat score
* Hepatic steatosis on magnetic resonance imaging (MRI; ≥ 10% average liver proton density fat fraction \[PDFF\]) prior to randomization.

Exclusion Criteria

* Pregnant, lactating, or intending to become pregnant within 42 days after the last dose of study drug is administered
* Suspected or confirmed diagnosis of Type 1 diabetes
* Significant cardiac disease
* Any psychiatric illness that increases the risk of participation in the study
* History of severe allergic, anaphylactic, or other hypersensitivity reactions, or severe systemic bacterial, fungal, or parasitic infections
* Poor peripheral venous access
* Received blood products within 2 months before dosing
* Donation or loss of blood within 30-56 days prior to study drug administration
* Positive for hepatitis C virus (HCV) antibody, hepatitis B surface antigen (HBsAg), or human immunodeficiency virus (HIV) antibody
* Liver enzymes greater than acceptable limits
* History of eating disorders or surgical procedures for weight loss
* Active participation in a structured weight loss or dietary program
* Treatment with investigational therapy or exposure to any biological therapy
* Illicit drug use, marijuana use, or alcohol abuse
* Current use of more than one pack of cigarettes a day or equivalent nicotine- containing products
* Any serious medical condition or abnormality in clinical laboratory tests
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Pinnacle Research Group Cullman

Anniston, Alabama, United States

Site Status

Pinnacle Research Group; Llc, Central

Anniston, Alabama, United States

Site Status

Southern California Research Center, Inc.

Coronado, California, United States

Site Status

Stanford Health Care

Stanford, California, United States

Site Status

Diabetes Research Center

Tustin, California, United States

Site Status

MD Clinical

Hallandale, Florida, United States

Site Status

Premier Research Associate, Inc

Miami, Florida, United States

Site Status

Agile Clinical Research Trials

Atlanta, Georgia, United States

Site Status

MidWest Clinical Research

Overland Park, Kansas, United States

Site Status

Hassman Research Institute

Berlin, New Jersey, United States

Site Status

Carolina Research Center at Jones Family Practice

Shelby, North Carolina, United States

Site Status

New Orleans Center for Clinical Research

Knoxville, Tennessee, United States

Site Status

Texas Clinical Research Institute, LLC

Arlington, Texas, United States

Site Status

Dallas Diabetes & Endocrine Center

Dallas, Texas, United States

Site Status

Clinical Trials of Texas Incorporated

San Antonio, Texas, United States

Site Status

Northeast Clinical Research of San Antonio LLC

San Antonio, Texas, United States

Site Status

Consano Clinical Research

Shavano Park, Texas, United States

Site Status

inVentiv Health Clinical

Montreal, Quebec, Canada

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada

References

Explore related publications, articles, or registry entries linked to this study.

Wong C, Dash A, Fredrickson J, Lewin-Koh N, Chen S, Yoshida K, Liu Y, Gutierrez J, Kunder R. Fibroblast growth factor receptor 1/Klothobeta agonist BFKB8488A improves lipids and liver health markers in patients with diabetes or NAFLD: A phase 1b randomized trial. Hepatology. 2023 Sep 1;78(3):847-862. doi: 10.1002/hep.32742. Epub 2022 Sep 12.

Reference Type DERIVED
PMID: 35993161 (View on PubMed)

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

GC39547

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.