Pharmacokinetic Characterization of the Hemophilia A Population in Spain Using myPKFiT®

NCT ID: NCT03006965

Last Updated: 2023-06-08

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

50 participants

Study Classification

OBSERVATIONAL

Study Start Date

2016-11-11

Study Completion Date

2022-12-22

Brief Summary

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The purpose of this study is to describe the pharmacokinetic profile of patients with hemophilia A in prophylaxis in Spain using myPKFit®

Detailed Description

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This pharmacokinetic profile will be obtained in only in patient using Advate® (INN-octocog alfa) or Adynovi® (INN- rurioctocog alfa pegol), both recombinant intravenous FVIII products, with myPKFiT®. This patients will be followed during the period of 12 months, and the pharmacokinetic will be measured collecting at least 2 blood samples, in which the presence of factor VIII will be determined by the usual clinical methods: chromogenic method or coagulative method.

Conditions

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Hemophilia A Hemophilia Factor VIII Deficiency

Study Design

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Observational Model Type

COHORT

Study Time Perspective

OTHER

Study Groups

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Hemophilia A patients

Group of patients in prophylactic treatment with Advate® (octocog alfa) or Adynovi® (rurioctocog alfa pegol), or patients using already myPKFit®.

Patients will be given a dose of octocog alfa or rurioctocog alfa pegol according to usual clinical practice, and two blood samples will be taken in case of octocog alfa: one sample will be extracted 3-4h postdose (+/- 30 minutes), and the second sample will be extracted 24-32h postdose (+/- 60 minutes). In case of rurioctocog alfa pegol, the first sample is taken in the same conditions than octocog alfa, and the second sample will be extracted 48h postdose (+/- 120 minutes), and other sample post 72h(+/- 120 minutes) optional.

octocog alfa

Intervention Type DRUG

Pharmacokinetic Characterization of the Hemophilia A Population in Spain using an standalone web-based software

rurioctocog alfa pegol

Intervention Type DRUG

Pharmacokinetic Characterization of the Hemophilia A Population in Spain using an standalone web-based software

Interventions

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octocog alfa

Pharmacokinetic Characterization of the Hemophilia A Population in Spain using an standalone web-based software

Intervention Type DRUG

rurioctocog alfa pegol

Pharmacokinetic Characterization of the Hemophilia A Population in Spain using an standalone web-based software

Intervention Type DRUG

Other Intervention Names

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Advate® recombinant intravenous factor VIII recombinant intravenous factor VIII

Eligibility Criteria

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Inclusion Criteria

* Male patients.
* Age between 1 and 65 years old.
* Patients diagnosed with Hemophilia A who are on prophylactic treatment with Advate® or Adynovi® or adjusted with myPKFIT.
* Patients older than 18 who have signed the informed consent form.
* In the case of mature minors, in addition to the consent signed by the legal guardian, an assent of the minor must be obtain.
* In the case of patients legally incapable for giving their consent, their primary caregiver will consent as the patient's legal guardian.

Exclusion Criteria

* Withdrawal of informed consent.
* Patients with any medical or psychological condition that according to the researcher's criteria prevents them from following the usual clinical practice procedures.
* Patients with concomitant diagnosis of other haemostasis disorders.
* Patients being treated for induction of immunologic tolerance at the time of inclusion.
Minimum Eligible Age

1 Year

Maximum Eligible Age

65 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Takeda

INDUSTRY

Sponsor Role collaborator

Instituto de Investigación Hospital Universitario La Paz

OTHER

Sponsor Role collaborator

Spanish Society of Thrombosis and Haemostasis

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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M Teresa Álvarez Román, MD,PhD

Role: PRINCIPAL_INVESTIGATOR

Hospital Universitario La Paz, IdiPAZ, Universidad Autónoma de Madrid

Locations

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Complexo Hospitalario Universitario A Coruña

A Coruña, A Coruña, Spain

Site Status

Hospital Universitario Son Espases

Palma, Balearic Islands, Spain

Site Status

Hospital Sant Joan de Deu

Esplugues de Llobregat, Barcelona, Spain

Site Status

Hospital Universitario Virgen de la Arrixaca

El Palmar, Murcia, Spain

Site Status

Hospital Virgen del Camino

Pamplona, Navarre, Spain

Site Status

Hospital Xeral de Vigo

Vigo, Pontevedra, Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, Principality of Asturias, Spain

Site Status

Hospital Universitario Cruces

Barakaldo, Vizcaya, Spain

Site Status

Hospital Vall D'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Regional Universitario de Málaga

Málaga, , Spain

Site Status

Hospital Materno-infantil de Málaga

Málaga, , Spain

Site Status

Hospital Universitario Virgen del Rocío

Seville, , Spain

Site Status

Hospital Universitari i Politècnic La Fe

Valencia, , Spain

Site Status

Countries

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Spain

Other Identifiers

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STH-OCT-2016-01

Identifier Type: OTHER

Identifier Source: secondary_id

PK HemoA-SP

Identifier Type: -

Identifier Source: org_study_id

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