A Study of Rucaparib Versus Physician's Choice of Therapy in Participants With Metastatic Castration-resistant Prostate Cancer and Homologous Recombination Gene Deficiency

NCT ID: NCT02975934

Last Updated: 2025-07-25

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

405 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-06-13

Study Completion Date

2024-08-08

Brief Summary

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The purpose of this study is to determine how participants with metastatic castration-resistant prostate cancer, and evidence of a homologous recombination gene deficiency, respond to treatment with rucaparib versus treatment with physician's choice of abiraterone acetate, enzalutamide, or docetaxel.

Detailed Description

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Conditions

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Metastatic Castration Resistant Prostate Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Rucaparib

Oral rucaparib (monotherapy).

Group Type EXPERIMENTAL

Rucaparib

Intervention Type DRUG

Rucaparib will be administered daily.

Abiraterone acetate or Enzalutamide or Docetaxel

Oral abiraterone acetate (monotherapy, given in combination with prednisone). Oral enzalutamide (monotherapy). Intravenous docetaxel (monotherapy, given in combination with prednisone or prednisolone).

Group Type ACTIVE_COMPARATOR

Abiraterone acetate or Enzalutamide or Docetaxel

Intervention Type DRUG

Abiraterone acetate and enzalutamide will be administered daily. Docetaxel will be administered every 3 weeks.

Interventions

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Rucaparib

Rucaparib will be administered daily.

Intervention Type DRUG

Abiraterone acetate or Enzalutamide or Docetaxel

Abiraterone acetate and enzalutamide will be administered daily. Docetaxel will be administered every 3 weeks.

Intervention Type DRUG

Other Intervention Names

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CO-338 Zytiga (abiraterone acetate) or Xtandi (enzalutamide) or Taxotere (docetaxel)

Eligibility Criteria

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Inclusion Criteria

* Be 18 years old at the time the informed consent is signed
* Have a histologically or cytologically confirmed adenocarcinoma or poorly differentiated carcinoma of the prostate that is metastatic
* Be surgically or medically castrated, with serum testosterone levels of ≤ 50 ng/dL (1.73 nM)
* Be eligible for treatment with physician's choice of comparator treatment (abiraterone acetate, enzalutamide or docetaxel)
* Experienced disease progression after having received 1 prior next generation androgen receptor-targeted therapy
* Have a deleterious mutation in a BRCA1/2 or ATM gene

Exclusion Criteria

* Active second malignancy, with the exception of curatively treated non melanoma skin cancer, carcinoma in situ, or superficial bladder cancer
* Prior treatment with any PARP inhibitor
* Prior treatment with chemotherapy for metastatic castration-resistant prostate cancer
* Symptomatic and/or untreated central nervous system metastases
* Pre-existing duodenal stent and/or any gastrointestinal disorder or defect that would, in the opinion of the investigator, interfere with absorption of study drug
Minimum Eligible Age

18 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Foundation Medicine

INDUSTRY

Sponsor Role collaborator

pharmaand GmbH

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Mayo Clinic - Arizona

Phoenix, Arizona, United States

Site Status

Arizona Oncology Associates - USOR

Tucson, Arizona, United States

Site Status

University of Southern California

Beverly Hills, California, United States

Site Status

Alliance Research Centers

Laguna Hills, California, United States

Site Status

VA Greater Los Angeles Healthcare System

Los Angeles, California, United States

Site Status

San Bernardino Urological Associates

San Bernardino, California, United States

Site Status

Sharp Memorial Hospital

San Diego, California, United States

Site Status

Pacific Hematology Oncology Associates

San Francisco, California, United States

Site Status

San Francisco VA Health Care System

San Francisco, California, United States

Site Status

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, United States

Site Status

St. Joseph Heritage Healthcare

Santa Rosa, California, United States

Site Status

Kaiser Permanente, Northern CA

Vallejo, California, United States

Site Status

Rocky Mountain Cancer Centers

Aurora, Colorado, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Medical Oncology Hematology Consultants - USOR

Newark, Delaware, United States

Site Status

Boca Raton Community Hospital, Inc.

Boca Raton, Florida, United States

Site Status

University of Florida Health Cancer Center

Orlando, Florida, United States

Site Status

Atlanta Urological Group

Atlanta, Georgia, United States

Site Status

Kaiser Permanente Medical Group

Honolulu, Hawaii, United States

Site Status

Ochsner Medical Center

New Orleans, Louisiana, United States

Site Status

University of Maryland Greenebaum Cancer Center

Baltimore, Maryland, United States

Site Status

Walter Reed National Military Medical Center

Bethesda, Maryland, United States

Site Status

Maryland Oncology Hematology P.A.

Columbia, Maryland, United States

Site Status

Massachusetts General Hospital

Boston, Massachusetts, United States

Site Status

VA Ann Arbor Healthcare System

Ann Arbor, Michigan, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Minnesota Oncology Hematology, P.A.

Minneapolis, Minnesota, United States

Site Status

Minnesota Veterans Research Institute

Minneapolis, Minnesota, United States

Site Status

University of Minnesota

Minneapolis, Minnesota, United States

Site Status

Mayo Clinic - Rochester, MN

Rochester, Minnesota, United States

Site Status

Alegent Health Bergan Mercy Hospital , GU Research Network

Omaha, Nebraska, United States

Site Status

Nebraska Cancer Specialists

Omaha, Nebraska, United States

Site Status

Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

Premier Urology Associates

Lawrenceville, New Jersey, United States

Site Status

Roswell Park

Buffalo, New York, United States

Site Status

NYU Perlmutter Cancer Center

New York, New York, United States

Site Status

Memorial Sloan Kettering CC

New York, New York, United States

Site Status

Weill Cornell Medical College

New York, New York, United States

Site Status

Premier Medical Group of the Hudson Valley PC

Poughkeepsie, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

SUNY Upstate Medical University

Syracuse, New York, United States

Site Status

University of North Carolina Lineberger Cancer Center

Chapel Hill, North Carolina, United States

Site Status

Carolina Urology Partners

Concord, North Carolina, United States

Site Status

Durham VA Medical Center

Durham, North Carolina, United States

Site Status

Oncology Hematology Care

Cincinnati, Ohio, United States

Site Status

The Urology Group

Cincinnati, Ohio, United States

Site Status

Kettering Medical Center

Kettering, Ohio, United States

Site Status

Clinical Research Solutions

Middleburg Heights, Ohio, United States

Site Status

VA Portland Health Care System

Portland, Oregon, United States

Site Status

Northwest Cancer Specialist DBA Compass Oncology

Portland, Oregon, United States

Site Status

Knight Cancer Institute

Portland, Oregon, United States

Site Status

Urology Associates Clinical Research

Nashville, Tennessee, United States

Site Status

Urology Clinics of North Texas

Dallas, Texas, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

UT Health Science Center

Houston, Texas, United States

Site Status

Texas Oncology Cancer Center-Round Rock

Round Rock, Texas, United States

Site Status

Urology of Virginia

Virginia Beach, Virginia, United States

Site Status

MultiCare Regional Cancer Center - Gig Harbor

Gig Harbor, Washington, United States

Site Status

VA Puget Sound HCS

Seattle, Washington, United States

Site Status

University of Washington Fred Hutchinson Cancer Research Center

Seattle, Washington, United States

Site Status

Southside Cancer Care Centre

Miranda, New South Wales, Australia

Site Status

Orange Health Service

Orange, New South Wales, Australia

Site Status

Northern Cancer Insitute, St. Leonards

Saint Leonards, New South Wales, Australia

Site Status

St John of God Hospital, Subiaco

Subiaco, Western Australia, Australia

Site Status

Peninsula & Southeast Oncology

Frankston, , Australia

Site Status

Barwon Health, University Hospital Geelong

Geelong, , Australia

Site Status

Royal Hobart Hospital

Hobart, , Australia

Site Status

Riverina Cancer Care Centre

Wagga Wagga, , Australia

Site Status

ZNA Middelheim

Antwerp, , Belgium

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AZ Groeninge

Kortrijk, , Belgium

Site Status

CHU Sart-Tilman

Liège, , Belgium

Site Status

Clinique et Maternité Sainte-Elisabeth

Namur, , Belgium

Site Status

Tom Baker Cancer Centre

Calgary, Alberta, Canada

Site Status

Cancer Care Manitoba

Winnipeg, Manitoba, Canada

Site Status

Centre Hospitalier Universitaire Dr-Georges-L.-Dumont

Moncton, New Brunswick, Canada

Site Status

London Health Sciences Centre

London, Ontario, Canada

Site Status

The Ottawa Hospital

Ottawa, Ontario, Canada

Site Status

Princess Margaret Cancer Centre

Toronto, Ontario, Canada

Site Status

Lakeridge Health Medical Specialty Medical Oncology

Oshawa, , Canada

Site Status

Sunnybrook Odette Cancer Centre

Toronto, , Canada

Site Status

Copenhagen University Hospital

Copenhagen, , Denmark

Site Status

Herlev Hospital

Herlev, , Denmark

Site Status

Vejle Sygehus

Vejle, , Denmark

Site Status

Centre Georges François Leclerc

Dijon, , France

Site Status

Clinique Victor Hugo Centre Jean Bernard

Le Mans, , France

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Hôpital Privé La Louvière

Lille, , France

Site Status

Centre Léon Bérard

Lyon, , France

Site Status

Polyclinique de Gentilly (Centre D'Oncologie De Gentilly)

Nancy, , France

Site Status

Institut Curie

Paris, , France

Site Status

Centre Armoricain de Radiotherapie, Imagerie medicale et Oncologie, CARIO

Plérin, , France

Site Status

CRLCC Eugene Marquis

Rennes, , France

Site Status

Institut Gustave-Roussy

Villejuif, , France

Site Status

Gemeinschaftspraxis für Hämatologie&Onkologie

Augsburg, , Germany

Site Status

Charite - Universitaetsmedizin Berlin

Berlin, , Germany

Site Status

Apotheke des Städtischen Klinikums Braunschweig

Braunschweig, , Germany

Site Status

Universitätsklinikum Köln

Cologne, , Germany

Site Status

University Hospital Carl Gustav Carus

Dresden, , Germany

Site Status

Universitatsklinikum Dusseldorf

Düsseldorf, , Germany

Site Status

Urologische Gemeinschaftspraxis

Emmendingen, , Germany

Site Status

Universitaetsklinikum Hamburg-Eppendorf (UKE)

Hamburg, , Germany

Site Status

Universitatsklinikum Jena

Jena, , Germany

Site Status

Universitätsklinikum Schleswig-Holstein

Lübeck, , Germany

Site Status

Medizinischen Fakultät Mannheim der Universität Heidelberg

Mannheim, , Germany

Site Status

Studienpraxis Urologie

Nürtingen, , Germany

Site Status

University of Tuebingen

Tübingen, , Germany

Site Status

Die GesundheitsUnion (DGU)

Wuppertal, , Germany

Site Status

Cork University Hospital

Cork, , Ireland

Site Status

Adelaide & Meath Hospital, Incorporating the National Children's Hospital

Dublin, , Ireland

Site Status

Mater Misericordiae University Hospital

Dublin, , Ireland

Site Status

Mater Private Hospital (MPH)

Dublin, , Ireland

Site Status

St James's Hospital

Dublin, , Ireland

Site Status

St. Vincent's University Hospital

Dublin, , Ireland

Site Status

Rambam Health Care Campus (RHCC), Rambam Medical Center

Haifa, , Israel

Site Status

Hadassah University Hospital

Jerusalem, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Rabin Medical Center-Beilinson Campus

Petah Tikva, , Israel

Site Status

The Tel Aviv Sourasky Medical Center (Ichilov Hospital)

Tel Aviv, , Israel

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Chaim Sheba Medical Center

Tel Litwinsky, , Israel

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Ospedale San Donato, Azienda USLSUDEST

Arezzo, , Italy

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Ospedale Santa Maria delle Croci

Faenza, , Italy

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Romagnolo per lo Studio e la Cura dei Tumori IRST-IRCCS - Oncologia medica

Meldola, , Italy

Site Status

IEO Instituto Europeo di Oncologia

Milan, , Italy

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University of Modena and Reggio Emilia

Modena, , Italy

Site Status

Azienda Ospedaliera San Camillo-Forlanini

Roma, , Italy

Site Status

Azienda Opsedaliera S. Maria di Terni

Terni, , Italy

Site Status

Presidio Ospedaliero Santa Chiara di Trento

Trento, , Italy

Site Status

Hospital Universitari Germans Trias i Pujol

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital General Universitario de Guadalajara

Guadalajara, , Spain

Site Status

Hospital Universitario Lucus Augusti.

Lugo, , Spain

Site Status

MD Anderson Cancer Center - Madrid

Madrid, , Spain

Site Status

Hospital Universitario Ramón y Cajal

Madrid, , Spain

Site Status

Hospital 12 de Octubre

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Clinico Universitario Virgen de la Victoria

Málaga, , Spain

Site Status

Hospital Universitario Central de Asturias

Oviedo, , Spain

Site Status

Corporacio Sanitaria Parc Tauli

Sabadell, , Spain

Site Status

Marques de Valdecilla University Hospital (HUMV)

Santander, , Spain

Site Status

Hospital Universitario Virgen del Rocío

Seville, , Spain

Site Status

Instituto Valenciano de Oncología

Valencia, , Spain

Site Status

Guy's and St Thomas' NHS Foundation Trust

London, England, United Kingdom

Site Status

Royal Marsden Hospital

London, England, United Kingdom

Site Status

Oxford Cancer Centre, Medical Oncology Unit

Oxford, England, United Kingdom

Site Status

Royal Preston Hospital

Preston, England, United Kingdom

Site Status

Wexham Park Hospital

Slough, England, United Kingdom

Site Status

Velindre Hospital

Cardiff, , United Kingdom

Site Status

Royal Marsden Hospital

London, , United Kingdom

Site Status

The Clatterbridge Cancer Centre NHS Foundation Trust

Metropolitan Borough of Wirral, , United Kingdom

Site Status

Musgrove Park Hospital

Taunton, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada Denmark France Germany Ireland Israel Italy Spain United Kingdom

References

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Fizazi K, Piulats JM, Reaume MN, Ostler P, McDermott R, Gingerich JR, Pintus E, Sridhar SS, Bambury RM, Emmenegger U, Lindberg H, Morris D, Nole F, Staffurth J, Redfern C, Saez MI, Abida W, Daugaard G, Heidenreich A, Krieger L, Sautois B, Loehr A, Despain D, Heyes CA, Watkins SP, Chowdhury S, Ryan CJ, Bryce AH; TRITON3 Investigators. Rucaparib or Physician's Choice in Metastatic Prostate Cancer. N Engl J Med. 2023 Feb 23;388(8):719-732. doi: 10.1056/NEJMoa2214676. Epub 2023 Feb 16.

Reference Type RESULT
PMID: 36795891 (View on PubMed)

Collins K, Cheng L. Reprint of: morphologic spectrum of treatment-related changes in prostate tissue and prostate cancer: an updated review. Hum Pathol. 2023 Mar;133:92-101. doi: 10.1016/j.humpath.2023.02.007. Epub 2023 Mar 8.

Reference Type DERIVED
PMID: 36898948 (View on PubMed)

Maia MC, Salgia M, Pal SK. Harnessing cell-free DNA: plasma circulating tumour DNA for liquid biopsy in genitourinary cancers. Nat Rev Urol. 2020 May;17(5):271-291. doi: 10.1038/s41585-020-0297-9. Epub 2020 Mar 17.

Reference Type DERIVED
PMID: 32203306 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-003163-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CO-338-063

Identifier Type: -

Identifier Source: org_study_id

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