Prospective ARNI vs ACE Inhibitor Trial to DetermIne Superiority in Reducing Heart Failure Events After MI

NCT ID: NCT02924727

Last Updated: 2023-06-22

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

5669 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-12-09

Study Completion Date

2021-02-26

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of LCZ696 titrated to a target dose of 200 mg twice daily, compared to ramipril titrated to a target dose of 5 mg twice daily.

Detailed Description

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The purpose of this study is to evaluate the efficacy and safety of LCZ696 titrated to a target dose of 200 mg twice daily, compared to ramipril titrated to a target dose of 5 mg twice daily, in addition to conventional post-AMI treatment, in reducing the occurrence of composite endpoint of CV death, HF hospitalization and outpatient HF (time-to-first event analysis) in post-AMI patients with evidence of LV systolic dysfunction and/or pulmonary congestion, with no known prior history of chronic HF.

Conditions

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Acute Myocardial Infarction

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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LCZ696 (sacubitril/valsartan)

Following randomization, patients will receive LCZ696 in titrated doses from level 1 up to level 3 (50, 100 and 200 mg twice daily).

Patients will be required to take a total of two pills, (one tablet from the LCZ696 pack and one capsule from ramipril matching placebo pack) twice a day for the duration of the study.

Patients randomized to LCZ who were previously treated with ACE inhibitors receiving the last dose of that agent during the last 36 hours prior to randomization will receive a valsartan bridge for one day. These patients will receive two doses of valsartan for 1 day in a blinded manner prior to beginning double-blind LCZ696 treatment.

Group Type EXPERIMENTAL

LCZ696 (sacubitril/valsartan)

Intervention Type DRUG

LCZ696 (sacubitril/valsartan) tablet will be available in 24/26 mg, 49/51 mg and 97/103 mg, respectively

Placebo of ramipril

Intervention Type DRUG

Matching placebo of ramipril capsule

Valsartan

Intervention Type DRUG

Valsartan (VAL489) 40 mg and 80 mg tablets, two doses for 1 day to patients who were previously treated with ACE inhibitors receiving the last dose of that agent during the last 36 hours prior to randomization

Ramipril

Following randomization, patients will receive the Ramipril in titrated doses from level 1 up to level 3 (1.25, 2.5 and 5 mg twice daily).

Patients will be required to take a total of two pills, (one capsule from the ramipril pack and one tablet from LCZ696 matching placebo pack) twice a day for the duration of the study.

Patients randomized to ramipril who were previously treated with ACE inhibitors receiving the last dose of that agent during the last 36 hours prior to randomization will immediately start on double-blind ramipril; however, to maintain double blind/double dummy of the valsartan bridge, these patients will receive two doses of matching valsartan placebo for 1 day in a blinded manner prior to beginning double-blind LCZ696 placebo.

Group Type ACTIVE_COMPARATOR

Ramipril

Intervention Type DRUG

Ramipril 1.25 mg, 2.5 mg, and 5 mg oral capsules

Placebo of LCZ696

Intervention Type DRUG

Matching placebo of LCZ696 tablets

Placebo of valsartan

Intervention Type DRUG

matching placebo of valsartan for one day to patients who will be randomized to received ramipril

Interventions

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LCZ696 (sacubitril/valsartan)

LCZ696 (sacubitril/valsartan) tablet will be available in 24/26 mg, 49/51 mg and 97/103 mg, respectively

Intervention Type DRUG

Ramipril

Ramipril 1.25 mg, 2.5 mg, and 5 mg oral capsules

Intervention Type DRUG

Placebo of LCZ696

Matching placebo of LCZ696 tablets

Intervention Type DRUG

Placebo of ramipril

Matching placebo of ramipril capsule

Intervention Type DRUG

Valsartan

Valsartan (VAL489) 40 mg and 80 mg tablets, two doses for 1 day to patients who were previously treated with ACE inhibitors receiving the last dose of that agent during the last 36 hours prior to randomization

Intervention Type DRUG

Placebo of valsartan

matching placebo of valsartan for one day to patients who will be randomized to received ramipril

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Male or female patients ≥ 18 years of age.
2. Diagnosis of spontaneous AMI based on the universal MI definition\* with randomization to occur between 12 hours and 7 days after index event presentation. (\*patients with spontaneous MI event determined to be secondary to another medical condition such as anemia, hypotension, or arrhythmia OR thought to be caused by coronary vasospasm with document normal coronary arteries are not eligible; patients with clinical presentation thought to be related to Takotsubo cardiomyopathy are also not eligible)
3. Evidence of LV systolic dysfunction and/or pulmonary congestion requiring intravenous treatment associated with the index MI event defined as:

* LVEF ≤40% after index MI presentation and prior to randomization and/or
* Pulmonary congestion requiring intravenous treatment with diuretics, vasodilators, vasopressors and/or inotropes, during the index hospitalization
4. At least one of the following 8 risk factors:

* Age ≥ 70 years
* eGFR \<60 mL/min/1.73 m\^2 based on MDRD formula at screening visit
* Type I or II diabetes mellitus
* Documented history of prior MI
* Atrial fibrillation as noted by ECG, associated with index MI
* LVEF \<30% associated with index MI
* Worst Killip class III or IV associated with index MI requiring intravenous treatment
* STEMI without reperfusion therapy within the first 24 hours after presentation
5. Hemodynamically stable defined as:

* SBP ≥ 100 mmHg at randomization for patients who received ACEi/ARB during the last 24 hours prior to randomization
* SBP ≥ 110 mmHg at randomization for patients who did not receive ACEi/ARB during the last 24 hours prior to randomization
* No IV treatment with diuretics, vasodilators, vasopressors and/or inotropes during the 24 hours prior to randomization

Exclusion Criteria

1. Known history of chronic HF prior to randomization
2. Cardiogenic shock within the last 24 hours prior to randomization
3. Persistent clinical HF at the time of randomization
4. Coronary artery bypass graft (CABG) performed or planned for index MI
5. Clinically significant right ventricular MI as index MI
6. Symptomatic hypotension at screening or randomization
7. Patients with a known history of angioedema
8. Stroke or transient ischemic attack within one month prior to randomization
9. Known or suspected bilateral renal artery stenosis
10. Clinically significant obstructive cardiomyopathy
11. Open-heart surgery performed within one month prior to randomization or planned cardiac surgery w/in the 3 months prior to randomization
12. eGFR \< 30 ml/min/1.73 m\^2 as measured by MDRD at screening
13. Serum potassium \> 5.2 mmol /L (or equivalent plasma potassium value) at randomization
14. Known hepatic impairment (as evidenced by total bilirubin \> 3.0 mg/dL or increased ammonia levels, if performed), or history of cirrhosis with evidence of portal hypertension such as esophageal varices
15. Previous use of LCZ696
16. History of malignancy of any organ system (other than localized basal cell carcinoma of the skin) within the past 3 years with a life expectancy of less than 1year.
17. History of hypersensitivity to the study drugs or drugs of similar chemical classes or known intolerance or contraindications to study drugs or drugs of similar chemical classes including ACE inhibitors, ARB or NEP inhibitors
18. Pregnant or nursing women or women of child-bearing potential unless they are using highly effective methods of contraception
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Novartis Pharmaceuticals

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Novartis Investigative Site

Birmingham, Alabama, United States

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Birmingham, Alabama, United States

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Huntsville, Alabama, United States

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Gilbert, Arizona, United States

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Bakersfield, California, United States

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Carmichael, California, United States

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Los Alamitos, California, United States

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Northridge, California, United States

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Orange, California, United States

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San Francisco, California, United States

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Sylmar, California, United States

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Brandon, Florida, United States

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Hollywood, Florida, United States

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Jacksonville Beach, Florida, United States

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Ocala, Florida, United States

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Cumming, Georgia, United States

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Johns Creek, Georgia, United States

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Thomasville, Georgia, United States

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Boise, Idaho, United States

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Coeur d'Alene, Idaho, United States

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Muncie, Indiana, United States

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Munster, Indiana, United States

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Richmond, Indiana, United States

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Iowa City, Iowa, United States

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Alexandria, Louisiana, United States

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Baton Rouge, Louisiana, United States

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Covington, Louisiana, United States

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Hammond, Louisiana, United States

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Slidell, Louisiana, United States

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Bangor, Maine, United States

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Hattiesburg, Mississippi, United States

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Medellín, Antioquia, Colombia

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Bucaramanga, Santander Department, Colombia

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Cali, Valle del Cauca Department, Colombia

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Barranquilla, , Colombia

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Zagreb, HRV, Croatia

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Aalborg, , Denmark

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Glostrup Municipality, , Denmark

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Jyväskylä, , Finland

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Augsburg, , Germany

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Freiburg im Breisgau, , Germany

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Gütersloh, , Germany

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Hennigsdorf, , Germany

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Kiel, , Germany

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Koeln-Nippes, , Germany

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Langen, , Germany

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Leverkusen, , Germany

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Ludwigshafen, , Germany

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Mönchengladbach, , Germany

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Neuwied, , Germany

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Riesa, , Germany

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Rüsselsheim am Main, , Germany

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Stadtlohn, , Germany

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Vechta, , Germany

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Villingen-Schwenningen, , Germany

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Witten, , Germany

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Würzburg, , Germany

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Alexandroupoli, Evros, Greece

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Larissa, GR, Greece

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Pécs, Baranya, Hungary

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Zalaegerszeg, Zala County, Hungary

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Budapest, , Hungary

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Debrecen, , Hungary

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Szeged, , Hungary

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Székesfehérvár, , Hungary

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Ahmedabad, Gujarat, India

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Karamsad, Gujarat, India

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United States Argentina Australia Austria Belgium Brazil Bulgaria Canada China Colombia Croatia Czechia Denmark Finland France Germany Greece Hungary India Israel Italy Mexico Netherlands Norway Peru Philippines Poland Portugal Romania Russia Singapore Slovakia South Africa South Korea Spain Sweden Switzerland Taiwan Thailand Turkey (Türkiye) United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Curtain JP, Pfeffer MA, Braunwald E, Claggett BL, Granger CB, Kober L, Lewis EF, Maggioni AP, Mann DL, Rouleau JL, Solomon SD, Steg PG, Finn PV, Fernandez A, Jering KS, McMurray JJV. Rates of Sudden Death After Myocardial Infarction-Insights From the VALIANT and PARADISE-MI Trials. JAMA Cardiol. 2024 Oct 1;9(10):928-933. doi: 10.1001/jamacardio.2024.2356.

Reference Type DERIVED
PMID: 39110471 (View on PubMed)

Mann DL, Nicolas J, Claggett B, Miao ZM, Granger CB, Kerkar P, Kober L, Lewis EF, McMurray JJV, Maggioni AP, Nunez J, Ntsekhe M, Rouleau JL, Sim D, Solomon SD, Steg PG, van der Meer P, Braunwald E, Pfeffer MA, Mehran R. Angiotensin Receptor-Neprilysin Inhibition in Patients With STEMI vs NSTEMI. J Am Coll Cardiol. 2024 Mar 5;83(9):904-914. doi: 10.1016/j.jacc.2024.01.002.

Reference Type DERIVED
PMID: 38418004 (View on PubMed)

Petrie MC, Rouleau JL, Claggett B, Jering K, van der Meer P, Kober L, Miao ZM, Lewis E, Granger C, De Pasqulae CG, Mann D, Steg PG, Maggioni A, Amir O, Lefkowitz M, Braunwald E, Solomon SD, McMurray JJV, Pfeffer MA. Pulmonary Congestion and Left Ventricular Dysfunction After Myocardial Infarction: Insights From the PARADISE-MI Trial. Circulation. 2024 Jan 23;149(4):335-338. doi: 10.1161/CIRCULATIONAHA.123.066163. Epub 2024 Jan 22. No abstract available.

Reference Type DERIVED
PMID: 38252738 (View on PubMed)

Wang X, Jering KS, Cikes M, Tokmakova MP, Mehran R, Han Y, East C, Mody FV, Wang Y, Lewis EF, Claggett B, McMurray JJV, Granger CB, Pfeffer MA, Solomon SD. Sex Differences in Clinical Characteristics and Outcomes After Myocardial Infarction With Low Ejection Fraction: Insights From PARADISE-MI. J Am Heart Assoc. 2023 Sep 5;12(17):e028942. doi: 10.1161/JAHA.122.028942. Epub 2023 Aug 23.

Reference Type DERIVED
PMID: 37609931 (View on PubMed)

Jering KS, Claggett BL, Pfeffer MA, Granger CB, Kober L, Lewis EF, Maggioni AP, Mann DL, McMurray JJV, Prescott MF, Rouleau JL, Solomon SD, Steg PG, von Lewinski D, Braunwald E. Prognostic Importance of NT-proBNP (N-Terminal Pro-B-Type Natriuretic Peptide) Following High-Risk Myocardial Infarction in the PARADISE-MI Trial. Circ Heart Fail. 2023 May;16(5):e010259. doi: 10.1161/CIRCHEARTFAILURE.122.010259. Epub 2023 May 1.

Reference Type DERIVED
PMID: 37125529 (View on PubMed)

Mehran R, Steg PG, Pfeffer MA, Jering K, Claggett B, Lewis EF, Granger C, Kober L, Maggioni A, Mann DL, McMurray JJV, Rouleau JL, Solomon SD, Ducrocq G, Berwanger O, De Pasquale CG, Landmesser U, Petrie M, Leng DSK, van der Meer P, Lefkowitz M, Zhou Y, Braunwald E. The Effects of Angiotensin Receptor-Neprilysin Inhibition on Major Coronary Events in Patients With Acute Myocardial Infarction: Insights From the PARADISE-MI Trial. Circulation. 2022 Dec 6;146(23):1749-1757. doi: 10.1161/CIRCULATIONAHA.122.060841. Epub 2022 Nov 2.

Reference Type DERIVED
PMID: 36321459 (View on PubMed)

Shah AM, Claggett B, Prasad N, Li G, Volquez M, Jering K, Cikes M, Kovacs A, Mullens W, Nicolau JC, Kober L, van der Meer P, Jhund PS, Ibram G, Lefkowitz M, Zhou Y, Solomon SD, Pfeffer MA. Impact of Sacubitril/Valsartan Compared With Ramipril on Cardiac Structure and Function After Acute Myocardial Infarction: The PARADISE-MI Echocardiographic Substudy. Circulation. 2022 Oct 4;146(14):1067-1081. doi: 10.1161/CIRCULATIONAHA.122.059210. Epub 2022 Sep 9.

Reference Type DERIVED
PMID: 36082663 (View on PubMed)

Pfeffer MA, Claggett B, Lewis EF, Granger CB, Kober L, Maggioni AP, Mann DL, McMurray JJV, Rouleau JL, Solomon SD, Steg PG, Berwanger O, Cikes M, De Pasquale CG, Fernandez A, Filippatos G, Jering K, Landmesser U, Menon V, Merkely B, Petrie MC, Petrov I, Schou M, Senni M, Sim D, van der Meer P, Lefkowitz M, Zhou Y, Wang Y, Braunwald E. Impact of Sacubitril/Valsartan Versus Ramipril on Total Heart Failure Events in the PARADISE-MI Trial. Circulation. 2022 Jan 4;145(1):87-89. doi: 10.1161/CIRCULATIONAHA.121.057429. Epub 2021 Nov 19. No abstract available.

Reference Type DERIVED
PMID: 34797725 (View on PubMed)

Pfeffer MA, Claggett B, Lewis EF, Granger CB, Kober L, Maggioni AP, Mann DL, McMurray JJV, Rouleau JL, Solomon SD, Steg PG, Berwanger O, Cikes M, De Pasquale CG, East C, Fernandez A, Jering K, Landmesser U, Mehran R, Merkely B, Vaghaiwalla Mody F, Petrie MC, Petrov I, Schou M, Senni M, Sim D, van der Meer P, Lefkowitz M, Zhou Y, Gong J, Braunwald E; PARADISE-MI Investigators and Committees. Angiotensin Receptor-Neprilysin Inhibition in Acute Myocardial Infarction. N Engl J Med. 2021 Nov 11;385(20):1845-1855. doi: 10.1056/NEJMoa2104508.

Reference Type DERIVED
PMID: 34758252 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-002154-20

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

CLCZ696G2301

Identifier Type: -

Identifier Source: org_study_id

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