Interferon-pegyle α2a Efficiency and Tolerance in Myelofibrosis

NCT ID: NCT02910258

Last Updated: 2018-09-21

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

62 participants

Study Classification

OBSERVATIONAL

Study Start Date

2012-09-30

Study Completion Date

2017-03-31

Brief Summary

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Patients who carried primary or secondary myelofibrosis from Philadelphia negative MPNs (PMF/SMF) and who are treated or are about to be treated with pegylated-interferon (mostly α2a) are eligible to this prospective study. Biological and clinical parameters will be collected from the beginning of the drug use until last news.

A non-opposition consent form need to be signed before entering this study.

Detailed Description

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In all centres interested, patients who were diagnosed for PMF/SMF can be treated with oral or sub-cutaneous drugs in order to reduce clinical symptoms and biological abnormalities belonging to these diseases.

Pegylated-interferon is one of the better weapons that can be used in these cases. These treatments are well known and used from many years in french hematological centres.

The investigators to collect clinical and biological data from patients treated with pegylated-interferon α2a (the most use) in case of PMF/SMF in order to assess efficacity and tolerance to this drug. The prescription of the product and the dose are under the responsibility of each practician.

Clinical data collected: disease and patients characteristics at the time of diagnosis and at the beginning of the drug use, spleen and liver size, presence of constitutive symptoms, transfusion needs.

Biological data collected: complete hemogram, CD34+ cells count, allele burden of JAK2V617F and calreticulin clones if DNA samples are collected.

These data will be collected avery 3 months during the two first years and every 6 months after.

The investigators also recorded adverse side effects if significative, the concomitant use of hematological drugs (cytoreductive treatments, ASE...), modalities of prescription of the drugs and the reason for stopping the drug and etiology of death if happened.

Conditions

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Myelofibrosis

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Eligibility Criteria

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Inclusion Criteria

* Primary or secondary Myelofibrosis
* Prescription of pegylated interferon α2a
* Age \> 18 years-old

Exclusion Criteria

* Other MPNs treated with pegylated interferon α2a
* Patients treated for PMF or SMF but without pegylated interferon
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University Hospital, Brest

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jean-Christophe Ianotto, MD

Role: STUDY_DIRECTOR

CHRU de Brest

Locations

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CHU d'Angers

Angers, , France

Site Status

Hopital du genevois

Annecy, , France

Site Status

CHRU de Brest

Brest, , France

Site Status

Centre Hospitalier du Mans

Le Mans, , France

Site Status

Centre Hospitalier de Lens

Lens, , France

Site Status

Institut Paoli Calmette

Marseille, , France

Site Status

CH des pays de Morlaix

Morlaix, , France

Site Status

Centre Hospitalier de Nice

Nice, , France

Site Status

AP-HP Hôpital Saint Louis

Paris, , France

Site Status

CHIC de Cornouaille

Quimper, , France

Site Status

Centre Hospitalier de Tours

Tours, , France

Site Status

CHU de Nancy

Vandœuvre-lès-Nancy, , France

Site Status

Countries

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France

References

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Ianotto JC, Chauveau A, Boyer-Perrard F, Gyan E, Laribi K, Cony-Makhoul P, Demory JL, de Renzis B, Dosquet C, Rey J, Roy L, Dupriez B, Knoops L, Legros L, Malou M, Hutin P, Ranta D, Benbrahim O, Ugo V, Lippert E, Kiladjian JJ. Benefits and pitfalls of pegylated interferon-alpha2a therapy in patients with myeloproliferative neoplasm-associated myelofibrosis: a French Intergroup of Myeloproliferative neoplasms (FIM) study. Haematologica. 2018 Mar;103(3):438-446. doi: 10.3324/haematol.2017.181297. Epub 2017 Dec 7.

Reference Type RESULT
PMID: 29217781 (View on PubMed)

Other Identifiers

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PEG-MF

Identifier Type: -

Identifier Source: org_study_id

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