A Study of the Safety and Efficacy of GDC-0853 in Participants With Moderate to Severe Active Systemic Lupus Erythematosus

NCT ID: NCT02908100

Last Updated: 2024-05-08

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

260 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-01-19

Study Completion Date

2019-07-16

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This is a study to evaluate the safety and efficacy of GDC-0853 in combination with standard of care therapy in participants with moderate to severe active systemic lupus erythematosus (SLE).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Systemic Lupus Erythematosus

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Placebo

Participants received matching placebo to GDC-0853 orally starting on Day 1 and ending at Week 48, in combination with background standard of care therapy.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Participants received matching placebo to GDC-0853 at dosages of 150 and 200mg as per the dosing schedules described above.

GDC-0853 (150mg) QD

Participants received GDC-0853 (150mg) orally once daily (QD) starting on Day 1 and ending at Week 48, in combination with background standard of care therapy.

Group Type EXPERIMENTAL

GDC-0853

Intervention Type DRUG

Participants received GDC-0853 at dosages of 150 or 200mg as per the dosing schedules described above.

GDC-0853 (200mg) BID

Participants received GDC-0853 (200mg) orally twice daily (BID) starting on Day 1 and ending at Week 48, in combination with background standard of care therapy.

Group Type EXPERIMENTAL

GDC-0853

Intervention Type DRUG

Participants received GDC-0853 at dosages of 150 or 200mg as per the dosing schedules described above.

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

GDC-0853

Participants received GDC-0853 at dosages of 150 or 200mg as per the dosing schedules described above.

Intervention Type DRUG

Placebo

Participants received matching placebo to GDC-0853 at dosages of 150 and 200mg as per the dosing schedules described above.

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

RO7010939

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Fulfillment of SLE classification criteria according to either American College of Rheumatology (ACR) or Systemic Lupus International Collaborating Clinics (SLICC) criteria at any time prior to or at screening
* At least one serologic marker of SLE at screening as follows: positive antinuclear antibody (ANA) test by immunofluorescent assay with titer \>/= 1:80; or positive anti-double-stranded DNA (anti-dsDNA) antibodies; or positive anti-Smith antibody
* At both screening and Day 1, moderate to severe active SLE, defined as meeting all of the following unless indicated otherwise: Systemic Lupus Erythematosus Disease Activity Index 2000 (SLEDAI-2K) score ≥ 8 (at screening only) with clinical SLEDAI-2K score \>/= 4.0 (at both screening and Day 1), Physician's Global Assessment \>/= 1.0 (out of 3), and currently receiving at least one standard oral treatment for SLE
* If on oral corticosteroids (OCS), the dose must be \</= 40 mg/day prednisone (or equivalent)
* Stable doses of anti-malarial or immunosuppressive therapies
* Participants must be willing to avoid pregnancy

Exclusion Criteria

* Proteinuria \> 3.5 g/24 h or equivalent using urine protein-to-creatinine ratio (uPCR) in a first morning void urine sample
* Active proliferative lupus nephritis (as assessed by the investigator) or histological evidence of active Class III or Class IV lupus nephritis on renal biopsy performed in the 6 months prior to screening (or during the screening period)
* History of having required hemodialysis or high dose corticosteroids (\>100 mg/d) prednisone or equivalent) for the management of lupus renal disease within 90 days of Day 1
* Neuropsychiatric or central nervous system lupus manifestations
* Serum creatinine \> 2.5 mg/dL, or estimated glomerular-filtration rate \< 30 milliliter per minute (mL/min) or on chronic renal replacement therapy
* History of receiving a solid organ transplant
* Evidence of active, latent, or inadequately treated infection with Mycobacterium tuberculosis (TB)
* Significant and uncontrolled medical disease within the 12 weeks prior to screening in any organ system (e.g., cardiac, neurologic, pulmonary, renal, hepatic, endocrine, metabolic, gastrointestinal, or psychiatric) not related to SLE, which, in the investigator's or Sponsor's opinion, would preclude study participation
* History of cancer, including hematological malignancy and solid tumors, within 10 years of screening
* Need for systemic anticoagulation with warfarin, other oral or injectable anticoagulants, or anti-platelet agents
* Evidence of chronic and/or active hepatitis B or C
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Genentech, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Valerius Medical Group & Research Ctr of Greater Long Beach

Los Alamitos, California, United States

Site Status

RASF-Clinical Research Center

Boca Raton, Florida, United States

Site Status

Bay Area Arthritis and Osteoporosis

Brandon, Florida, United States

Site Status

Omega Research Consultants

Orlando, Florida, United States

Site Status

Clinical Research of West Florida

Tampa, Florida, United States

Site Status

Institute of Arthritis Research

Idaho Falls, Idaho, United States

Site Status

Via Christi Research, a division of Via Christi Hospitals Wichita, Inc.

Wichita, Kansas, United States

Site Status

Ochsner Clinic Foundation

Baton Rouge, Louisiana, United States

Site Status

The Arthritis & Diabetes Clinic, Inc.; Research

Monroe, Louisiana, United States

Site Status

Albuquerque Clinical Trials

Albuquerque, New Mexico, United States

Site Status

Saint Lawrence Health System

Canton, New York, United States

Site Status

New York University School of Medicine

New York, New York, United States

Site Status

Shanahan Rheumatology & Immunology, PLLC

Raleigh, North Carolina, United States

Site Status

Ohio State University Clinical Trials Management Office

Columbus, Ohio, United States

Site Status

Tekton Research Inc

Austin, Texas, United States

Site Status

Accurate Clinical Research

Houston, Texas, United States

Site Status

Accurate Clinical Research

Houston, Texas, United States

Site Status

Arthritis Clinic Of Central Texas

San Marcos, Texas, United States

Site Status

Organizacion Medica de Investigacion

Buenos Aires, , Argentina

Site Status

APRILLUS

Buenos Aires, , Argentina

Site Status

Hospital Italiano de La Plata

La Plata, , Argentina

Site Status

CER San Juan Centro Polivalente de Asistencia e Investigacion Clinica

San Juan, , Argentina

Site Status

Centro Medico Privado de Reumatologia; Reumathology

San Miguel, , Argentina

Site Status

CEDOES - Diagnóstico e Pesquisa

Vitória, Espírito Santo, Brazil

Site Status

CIP - Centro Internacional de Pesquisa X; Pesquisa Clinica

Goiânia, Goiás, Brazil

Site Status

Hospital das Clinicas - UFMG

Belo Horizonte, Minas Gerais, Brazil

Site Status

CMiP - Centro Mineiro de Pesquisa*X*

Juiz de Fora, Minas Gerais, Brazil

Site Status

Edumed - Educação e Saúde SA

Curitiba, Paraná, Brazil

Site Status

Hospital Moinhos de Vento

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Centro de Pesquisas em Diabetes - CPD

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Clinica de Neoplasias Litoral

Itajaí, Santa Catarina, Brazil

Site Status

Faculdade de Medicina do ABC - FMABC

Santo André, São Paulo, Brazil

Site Status

Hospital Estadual Mario Covas

Santo André, São Paulo, Brazil

Site Status

Hospital Abreu Sodré - AACD

São Paulo, São Paulo, Brazil

Site Status

MHAT Plovdiv

Plovdiv, , Bulgaria

Site Status

Medical Center "Teodora", EOOD

Rousse, , Bulgaria

Site Status

Medical Center Excelsior OOD

Sofia, , Bulgaria

Site Status

UMHAT "Sv. Ivan Rilski", EAD

Sofia, , Bulgaria

Site Status

MC "Synexus - Sofia", EOOD

Sofia, , Bulgaria

Site Status

Medical Center "Nov Rehabilitatsionen Tsentar", EOOD

Stara Zagora, , Bulgaria

Site Status

CTR Estudios SPA

Providencia, , Chile

Site Status

Dermacross

Santiago, , Chile

Site Status

Centro de Estudios Reumatológicos

Santiago, , Chile

Site Status

SOMEAL

Santiago, , Chile

Site Status

Biomedica

Santiago, , Chile

Site Status

CEQUIN - Fundación Cardiomet Eje Cafetero

Armenia, , Colombia

Site Status

Centro Integral de Reumatologia del Caribe SAS CIRCARIBE SAS

Barranquilla, , Colombia

Site Status

Centro de Reumatologia y Ortopedia

Barranquilla, , Colombia

Site Status

Medicity S.A.S.

Bucaramanga, , Colombia

Site Status

Servimed S.A.S.

Bucaramanga, , Colombia

Site Status

Hospital Pablo Tobon Uribe

Medellín, , Colombia

Site Status

Charite Research Organisation GmbH; Phase - I Unit of Hematology and Oncology

Berlin, , Germany

Site Status

Centro de Investigacion Alberto Bazzoni S.A. de C.V.

Torreón, Coahuila, Mexico

Site Status

Unidad de Atencion Medica e Investigacion en Salud S.C.

Mérida, Yucatán, Mexico

Site Status

Consultorio Particular del Dr. Miguel Cortes Hernandez

Cuernavaca, , Mexico

Site Status

Hospital Angeles Lindavista

México, , Mexico

Site Status

Hospital Universitario de Saltillo

Saltillo, , Mexico

Site Status

Hospital Central Dr Ignacio Morones Prieto

San Luis Potosí City, , Mexico

Site Status

Konkuk University Medical Center

Seoul, , South Korea

Site Status

The Catholic University of Korea St.Mary's Hospital

Seoul, , South Korea

Site Status

Complejo Hospitalario Universitario A Coruña

A Coruña, LA Coruña, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status

Hospital Clinico Universitario de Valladolid; Servicio de Reumatologia

Valladolid, , Spain

Site Status

Kaohsiung Chang Gung Memorial Hospital

Kaohsiung City, , Taiwan

Site Status

National Taiwan University Hospital

Taipei, , Taiwan

Site Status

Chang Gung Memorial Hospital - Linkou

Taoyuan District, , Taiwan

Site Status

University College London Hospital

London, , United Kingdom

Site Status

Guy's Hospital; Louise Coote Lupus Unit

London, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Brazil Bulgaria Chile Colombia Germany Mexico South Korea Spain Taiwan United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Isenberg D, Furie R, Jones NS, Guibord P, Galanter J, Lee C, McGregor A, Toth B, Rae J, Hwang O, Desai R, Lokku A, Ramamoorthi N, Hackney JA, Miranda P, de Souza VA, Jaller-Raad JJ, Maura Fernandes A, Garcia Salinas R, Chinn LW, Townsend MJ, Morimoto AM, Tuckwell K. Efficacy, Safety, and Pharmacodynamic Effects of the Bruton's Tyrosine Kinase Inhibitor Fenebrutinib (GDC-0853) in Systemic Lupus Erythematosus: Results of a Phase II, Randomized, Double-Blind, Placebo-Controlled Trial. Arthritis Rheumatol. 2021 Oct;73(10):1835-1846. doi: 10.1002/art.41811. Epub 2021 Aug 24.

Reference Type DERIVED
PMID: 34042314 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2016-001039-11

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GA30044

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.