A Study to Evaluate the Efficacy and Safety of Pemigatinib (INCB054828) in Subjects With Urothelial Carcinoma - (FIGHT-201)

NCT ID: NCT02872714

Last Updated: 2025-08-14

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

263 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-01-12

Study Completion Date

2022-02-01

Brief Summary

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The purpose of this study is to evaluate the overall response rate (ORR) of pemigatinib as a monotherapy in the treatment of metastatic or surgically unresectable urothelial carcinoma harboring FGF/FGFR alterations.

Detailed Description

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Conditions

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UC (Urothelial Cancer)

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Cohort A-ID (Intermittent Dose) Pemigatinib

Pemigatinib in subjects with FGFR3 mutations or fusions.

Group Type EXPERIMENTAL

pemigatinib

Intervention Type DRUG

Pemigatinib once a day by mouth for 2 consecutive weeks and 1 week off therapy.

Cohort A-CD (Continuous Dose) Pemigatinib

Pemigatinib in subjects with FGFR3 mutations or fusions.

Group Type EXPERIMENTAL

pemigatinib

Intervention Type DRUG

Pemigatinib once a day by mouth continuously.

Cohort B Pemigatinib

Pemigatinib in subjects with other FGF/FGFR alterations.

Group Type EXPERIMENTAL

pemigatinib

Intervention Type DRUG

Pemigatinib once a day by mouth for 2 consecutive weeks and 1 week off therapy.

Interventions

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pemigatinib

Pemigatinib once a day by mouth for 2 consecutive weeks and 1 week off therapy.

Intervention Type DRUG

pemigatinib

Pemigatinib once a day by mouth continuously.

Intervention Type DRUG

Other Intervention Names

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INCB054828 INCB054828

Eligibility Criteria

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Inclusion Criteria

* 20 years and older in Japan
* Histologically documented metastatic or surgically unresectable urothelial carcinoma; may include primary site from urethra, ureters, upper tract, renal pelvis, and bladder.
* Eastern Cooperative Oncology Group (ECOG) performance status of 0-2.
* Life expectancy ≥ 12 weeks.
* Radiographically measurable per RECIST v1.1.
* Documented FGF/FGFR alteration and have either 1a) failed at least 1 previous treatment for their metastatic or surgically unresectable urothelial carcinoma (ie, chemotherapy, immunotherapy) or 1b) have not received chemotherapy due to poor ECOG status or 2) have insufficient renal function.

Exclusion Criteria

* Prior receipt of a selective FGFR inhibitor.
* Use of any potent CYP3A4 inhibitors or inducers within 14 days or 5 half-lives (whichever is shorter) before the first dose of study drug.
* Inability or unwillingness to swallow pemigatinib or significant gastrointestinal disorder(s) that could interfere with the absorption, metabolism, or excretion of pemigatinib.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Ekaterine Asatiani, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Arizona Oncology Associates (Wilmot)

Tucson, Arizona, United States

Site Status

Sharp Memorial Hospital

San Diego, California, United States

Site Status

UCSF Helen Diller Family Comprehensive Care Center

San Francisco, California, United States

Site Status

Rocky Mountain Cancer Centers

Boulder, Colorado, United States

Site Status

Calaway-Young Cancer Center at Valley View Hospital

Glenwood Springs, Colorado, United States

Site Status

Mount Sinai Medical Center

Miami Beach, Florida, United States

Site Status

Florida Hospital Cancer Institute

Orlando, Florida, United States

Site Status

Emory University School of Medicine

Atlanta, Georgia, United States

Site Status

University of Maryland, Greenebaum Cancer Center

Baltimore, Maryland, United States

Site Status

Lahey Clinic Inc. - PARENT ACCOUNT

Burlington, Massachusetts, United States

Site Status

Minnesota Oncology Hematology, P.A.

Woodbury, Minnesota, United States

Site Status

GU Research Network

Omaha, Nebraska, United States

Site Status

TRIO - Comprehensive Cancer Centers of Nevada

Las Vegas, Nevada, United States

Site Status

New York Oncology Hematology, P.C.

Albany, New York, United States

Site Status

Northwell Cancer Institute

New Hyde Park, New York, United States

Site Status

University of Rochester

Rochester, New York, United States

Site Status

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, United States

Site Status

Oncology Hematology Care, Inc.

Cincinnati, Ohio, United States

Site Status

Oregon Health & Science University

Portland, Oregon, United States

Site Status

Compass Oncology the Northwest Cancer Specialists

Tualatin, Oregon, United States

Site Status

St. Luke's Hospital

Bethlehem, Pennsylvania, United States

Site Status

VA Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, United States

Site Status

Carolina Urologic Research Center

Myrtle Beach, South Carolina, United States

Site Status

Vanderbilt University Medical Center

Nashville, Tennessee, United States

Site Status

Texas Oncology, P.A. - Austin

Austin, Texas, United States

Site Status

Texas Oncology - Baylor Charles A. Sammons

Dallas, Texas, United States

Site Status

Texas Oncology

Houston, Texas, United States

Site Status

Texas Oncology, P.A. - Sherman

Sherman, Texas, United States

Site Status

Baylor Scott & White Health

Temple, Texas, United States

Site Status

Huntsman Cancer Institute

Salt Lake City, Utah, United States

Site Status

Virginia Oncology Associates - Hampton

Norfolk, Virginia, United States

Site Status

Northwest Medical Specialties, PLLC

Tacoma, Washington, United States

Site Status

University of Wisconsic Hospital and Clinic

Madison, Wisconsin, United States

Site Status

Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

UZ Antwerpen

Edegem, , Belgium

Site Status

AZ Sint-Lucas - Campus Sint-Lucas

Ghent, , Belgium

Site Status

AZ Groeninge Campus Loofstraat

Kortrijk, , Belgium

Site Status

AZ Delta

Roeselare, , Belgium

Site Status

Rigshospitalet

Copenhagen, , Denmark

Site Status

CHU Besançon - Hôpital Jean Minjoz

Besançon, Doubs, France

Site Status

Groupe Hospitalier Saint André - Hôpital Saint André

Bordeaux, Gironde, France

Site Status

Institut Claudius Regaud-Oncopole

Toulouse, Haute Garonne, France

Site Status

ICO - Site René Gauducheau

Saint-Herblain, Loire Atlantique, France

Site Status

ICO - Site Paul Papin

Angers, Maine Et Loire, France

Site Status

Hopital Saint Louis

Paris, Paris, France

Site Status

Centre Leon Berard

Lyon, Rhone, France

Site Status

CHU Strasbourg - Nouvel Hôpital Civil

Strasbourg, Rhone, France

Site Status

Groupe Hospitalier Pitie-Salpetriere

Paris, , France

Site Status

Institut Gustave Roussy

Villejuif, , France

Site Status

Charite Universitaetsmedizin Berlin - Campus Benjamin Franklin

Berlin, , Germany

Site Status

Universitaetsklinikum Koeln

Cologne, , Germany

Site Status

Klinikum Dresden Standort Dresden-Friedrichstadt

Dresden, , Germany

Site Status

Universitaetsklinikum Carl Gustav Carus TU Dresden

Dresden, , Germany

Site Status

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Universitaetsmedizin der Johannes Gutenberg-Universitaet Mainz

Mainz, , Germany

Site Status

Universitaetsklinikum Muenster

Münster, , Germany

Site Status

Studienpraxis Urologie Drs. Feyerabend

Nürtingen, , Germany

Site Status

Universitaetsklinikum Tuebingen

Tübingen, , Germany

Site Status

Soroka University Medical Center

Beersheba, , Israel

Site Status

Assaf Harofeh Medical Center

Be’er Ya‘aqov, , Israel

Site Status

Meir Medical Center

Kfar Saba, , Israel

Site Status

Chaim Sheba Medical Center

Ramat Gan, , Israel

Site Status

Tel Aviv Sourasky Medical Center

Tel Aviv, , Israel

Site Status

Azienda Ospedaliera Universitaria Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status

Fondazione Del Piemonte Per L'Oncologia IRCC Candiolo

Candiolo, , Italy

Site Status

Fondazione IRCCS Istituto Nazionale dei Tumori

Milan, , Italy

Site Status

Azienda Ospedaliera Di Rilievo Nazionale A. Cardarellio

Napoli, , Italy

Site Status

Ospedale degli Infermi

Rimini, , Italy

Site Status

University Campus Bio-Medico di Roma

Rome, , Italy

Site Status

IRCCS Ospedale Casa Sollievo della Sofferenza

San Giovanni Rotondo, , Italy

Site Status

A.O.U. Senese Policlinico Santa Maria alle Scotte

Siena, , Italy

Site Status

San Camillo-Forlanini Hospital

Siena, , Italy

Site Status

Kyushu University Hospital

Fukuoka, , Japan

Site Status

Saitama Medical University International Medical Center

Hidaka-shi, , Japan

Site Status

Hirosaki University Hospital

Hirosaki-shi, , Japan

Site Status

Teikyo University Hospital

Itabashi-ku, , Japan

Site Status

Nihon University Itabashi Hospital

Itabashi-ku, , Japan

Site Status

Nara Medical University Hospital

Kashihara-shi, , Japan

Site Status

Osaka International Cancer Institute

Osaka, , Japan

Site Status

Saitama Cancer Center

Saitama, , Japan

Site Status

Osaka University Hospital

Suita-shi, , Japan

Site Status

Jichi Medical University Hospital

Tochigi, , Japan

Site Status

VU Medisch Centrum

Amsterdam, , Netherlands

Site Status

Zorgsaam Ziekenhuis

Terneuzen, , Netherlands

Site Status

HagaZiekenhuis Van Den Haag

The Hague, , Netherlands

Site Status

Viecuri Medisch Centrum

Venlo, , Netherlands

Site Status

Clinica Universidad de Navarra

Pamplona, Navarre, Spain

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

ICO Girona - Hospital Universitari de Girona Dr. Josep Trueta

Girona, , Spain

Site Status

Centro Integral Oncologico Clara Campal

Madrid, , Spain

Site Status

University College London Hospitals

London, Greater London, United Kingdom

Site Status

Guy's Hospital

London, Greater London, United Kingdom

Site Status

Charing Cross Hospital

London, Greater London, United Kingdom

Site Status

Nottingham University Hospitals City Campus

Nottingham, Nottinghamshire, United Kingdom

Site Status

Beatson West of Scotland Cancer Centre

Glasgow, Strathclyde, United Kingdom

Site Status

Queen Elizabeth Hospital

Birmingham, West Midlands, United Kingdom

Site Status

Countries

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United States Belgium Denmark France Germany Israel Italy Japan Netherlands Spain United Kingdom

References

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Zhang C, Huang MN, Shan JQ, Hu ZJ, Li ZW, Liu JY. Pemigatinib, a selective FGFR inhibitor overcomes ABCB1-mediated multidrug resistance in cancer cells. Biochem Biophys Res Commun. 2024 Jan 8;691:149314. doi: 10.1016/j.bbrc.2023.149314. Epub 2023 Nov 24.

Reference Type DERIVED
PMID: 38039831 (View on PubMed)

Necchi A, Pouessel D, Leibowitz R, Gupta S, Flechon A, Garcia-Donas J, Bilen MA, Debruyne PR, Milowsky MI, Friedlander T, Maio M, Gilmartin A, Li X, Veronese ML, Loriot Y. Pemigatinib for metastatic or surgically unresectable urothelial carcinoma with FGF/FGFR genomic alterations: final results from FIGHT-201. Ann Oncol. 2024 Feb;35(2):200-210. doi: 10.1016/j.annonc.2023.10.794. Epub 2023 Nov 11.

Reference Type DERIVED
PMID: 37956738 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2016-001321-14

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

INCB 54828-201

Identifier Type: -

Identifier Source: org_study_id

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