Darolutamide in Addition to Standard Androgen Deprivation Therapy and Docetaxel in Metastatic Hormone-Sensitive Prostate Cancer

NCT ID: NCT02799602

Last Updated: 2025-12-04

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1306 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-11-30

Study Completion Date

2023-04-11

Brief Summary

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The purpose of the study is to assess the efficacy and safety of BAY1841788 (darolutamide (ODM-201)) in combination with standard androgen deprivation therapy (ADT) and docetaxel in patients with metastatic hormone sensitive prostate cancer.

Detailed Description

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This is a randomized, double-blind, placebo-controlled, multicenter phase III study. The study population will consist of approximately 1300 subjects with metastatic hormone sensitive prostate cancer (mHSPC), who will be randomized (1:1 ratio) to receive 600 mg (2 x 300 mg tablets) of darolutamide (ODM-201)/placebo twice daily with food, equivalent to a total daily dose of 1200 mg, in addition to standard androgen deprivation therapy (ADT) and docetaxel. Subjects will be stratified at randomization for the extent of disease and for Alkaline Phosphatase levels. All subjects will be treated with ADT as standard therapy. Six cycles of docetaxel will be administered after randomization.

The subjects considered for inclusion in the study will have metastatic prostate cancer and will be candidates for ADT and docetaxel.

Treatment with darolutamide (ODM-201)/placebo will be administered until symptomatic progressive disease, change of antineoplastic therapy, unacceptable toxicity, until subject withdraws consent, withdrawal from the study at the discretion of the investigator or his/her designated associate(s), death, non-compliance, or if sponsor terminates the study.

Conditions

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Metastatic Hormone-sensitive Prostate Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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BAY1841788 /darolutamide (ODM-201)+standard ADT+Docetaxel

Co-administration of BAY 1841788 / darolutamide (ODM-201), standard ADT and docetaxel

Group Type EXPERIMENTAL

BAY1841788 / darolutamide (ODM-201)

Intervention Type DRUG

600mg (2 tablets of 300 mg) of darolutamide (ODM-201)/placebo twice daily with food, equivalent to a total a daily dose of 1200 mg in addition to standard ADT (luteinizing hormone releasing hormone (LHRH) agonist/antagonist or orchiectomy) and 6 cycles of docetaxel

Standard ADT (androgen deprivation therapy)

Intervention Type DRUG

As prescribed by the treating physician.

Docetaxel

Intervention Type DRUG

As prescribed by the treating physician.

Placebo + standard ADT + Docetaxel

Co-administration of Placebo matching BAY 1841788 / darolutamide (ODM-201) tablets, standard ADT and docetaxel

Group Type PLACEBO_COMPARATOR

Standard ADT (androgen deprivation therapy)

Intervention Type DRUG

As prescribed by the treating physician.

Docetaxel

Intervention Type DRUG

As prescribed by the treating physician.

Placebo

Intervention Type DRUG

Placebo matching darolutamide (ODM-201) tablets in appearance, bid orally with food, in addition to standard ADT (luteinizing hormone releasing hormone \[LHRH\] agonist/antagonist or orchiectomy) and 6 cycles of docetaxel.

Interventions

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BAY1841788 / darolutamide (ODM-201)

600mg (2 tablets of 300 mg) of darolutamide (ODM-201)/placebo twice daily with food, equivalent to a total a daily dose of 1200 mg in addition to standard ADT (luteinizing hormone releasing hormone (LHRH) agonist/antagonist or orchiectomy) and 6 cycles of docetaxel

Intervention Type DRUG

Standard ADT (androgen deprivation therapy)

As prescribed by the treating physician.

Intervention Type DRUG

Docetaxel

As prescribed by the treating physician.

Intervention Type DRUG

Placebo

Placebo matching darolutamide (ODM-201) tablets in appearance, bid orally with food, in addition to standard ADT (luteinizing hormone releasing hormone \[LHRH\] agonist/antagonist or orchiectomy) and 6 cycles of docetaxel.

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed adenocarcinoma of prostate.
* Metastatic disease
* Candidates for ADT and docetaxel.
* Started ADT with or without first generation anti androgen, but no longer than 12 weeks before randomization
* An Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1
* Adequate bone marrow, liver and renal function

Exclusion Criteria

* Prior treatment with: LHRH agonist/antagonists; second generation androgen receptor (AR) inhibitors such as enzalutamide, ARN-509, darolutamide (ODM-201), other investigational AR inhibitors; CYP17 enzyme inhibitor such as abiraterone acetate or oral ketoconazole as antineoplastic treatment for prostate cancer; chemotherapy or immunotherapy for prostate cancer prior to randomization.
* Treatment with radiotherapy/radiopharmaceuticals within 2 weeks before randomization.
* Had any of the following within 6 months before randomization: stroke, myocardial infarction, severe/unstable angina pectoris, coronary/peripheral artery bypass graft, congestive heart failure (New York Heart Association Class III or IV)
* Had a prior malignancy. Adequately treated basal cell or squamous cell carcinoma of skin or superficial bladder cancer that has not spread behind the connective tissue layer (i.e., pTis, pTa, and pT1) is allowed, as well as any other cancer for which treatment has been completed 5 years before randomization and from which the subject has been disease-free
* Gastrointestinal disorder or procedure which is expected to interfere significantly with absorption of study treatment.
* Inability to swallow oral medications
Minimum Eligible Age

18 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Orion Corporation, Orion Pharma

INDUSTRY

Sponsor Role collaborator

Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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Charleston, South Carolina, United States

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Greenville, South Carolina, United States

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Myrtle Beach, South Carolina, United States

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North Charleston, South Carolina, United States

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Dallas, Texas, United States

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Temple, Texas, United States

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Salt Lake City, Utah, United States

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Charlottesville, Virginia, United States

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Falls Church, Virginia, United States

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Richmond, Virginia, United States

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Everett, Washington, United States

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Milwaukee, Wisconsin, United States

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Sydney, New South Wales, Australia

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Sydney, New South Wales, Australia

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Adelaide, South Australia, Australia

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Kurralta Park, South Australia, Australia

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Fitzroy, Victoria, Australia

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Wilrijk, Antwerpen, Belgium

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Antwerp, , Belgium

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Brussels, , Belgium

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Bruxelles - Brussel, , Belgium

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Ghent, , Belgium

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Gilly, , Belgium

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Namur, , Belgium

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Cachoeiro de Itapemirim, Espírito Santo, Brazil

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Salvador, Estado de Bahia, Brazil

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Belo Horizonte, Minas Gerais, Brazil

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Belo Horizonte, Minas Gerais, Brazil

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Curitiba, Paraná, Brazil

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Natal, Rio Grande do Norte, Brazil

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Porto Alegre, Rio Grande do Sul, Brazil

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Santo André, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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São Paulo, São Paulo, Brazil

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Rio de Janeiro, , Brazil

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Rio de Janeiro, , Brazil

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São Paulo, , Brazil

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Gabrovo, , Bulgaria

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Pleven, , Bulgaria

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Plovdiv, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Varna, , Bulgaria

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Vratsa, , Bulgaria

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Calgary, Alberta, Canada

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Edmonton, Alberta, Canada

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Toronto, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Hefei City, Anhui Province, Anhui, China

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Beijing, Beijing Municipality, China

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Beijing, Beijing Municipality, China

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Beijing, Beijing Municipality, China

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Xiamen, Fujian, China

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Guangzhou, Guangdong, China

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Shijiazhuang, Hebei, China

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Zhengzhou, Henan, China

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Wuhan, Hubei, China

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Wuhan, Hubei, China

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Changsha, Hunan, China

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Nanjing, Jiangsu, China

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Nanjing, Jiangsu, China

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Nanchang, Jiangxi, China

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Changchun, Jilin, China

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Shengyang, Liaoning, China

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Shenyang, Liaoning, China

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Jinan, Shandong, China

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Jinan, Shandong, China

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Yantai, Shandong, China

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Xi’an, Shanxi, China

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Hangzhou, Zhejiang, China

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Hangzhou, Zhejiang, China

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Wenzhou, Zhejiang, China

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Beijing, , China

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Beijing, , China

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Beijing, , China

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Chongqing, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Shanghai, , China

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Tianjin, , China

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Tianjin, , China

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Brno, , Czechia

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Brno, , Czechia

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Hradec Králové, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Helsinki, Uusimaa, Finland

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Jyväskylä, , Finland

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Kuopio, , Finland

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Mikkeli, , Finland

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Oulu, , Finland

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Tampere, , Finland

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Turku, , Finland

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Angers, , France

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Besançon, , France

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Bordeaux, , France

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Brest, , France

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Cergy-Pontoise, , France

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Clermont-Ferrand, , France

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Créteil, , France

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Dijon, , France

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Marseille, , France

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Montpellier, , France

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Nancy, , France

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Paris, , France

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Pierre-Bénite, , France

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Poitiers, , France

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Reims, , France

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Saint-Grégoire, , France

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Saint-Herblain, , France

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Saint-Mandé, , France

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Strasbourg, , France

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Villejuif, , France

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Freiburg im Breisgau, Baden-Wurttemberg, Germany

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Nürtingen, Baden-Wurttemberg, Germany

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Tübingen, Baden-Wurttemberg, Germany

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Ulm, Baden-Wurttemberg, Germany

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Erlangen, Bavaria, Germany

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Braunschweig, Lower Saxony, Germany

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Rostock, Mecklenburg-Vorpommern, Germany

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Düsseldorf, North Rhine-Westphalia, Germany

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Münster, North Rhine-Westphalia, Germany

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Dresden, Saxony, Germany

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Magdeburg, Saxony-Anhalt, Germany

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Jena, Thuringia, Germany

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Berlin, , Germany

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Beersheba, , Israel

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Haifa, , Israel

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Holon, , Israel

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Jerusalem, , Israel

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Petah Tikva, , Israel

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Safed, , Israel

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Tel Aviv, , Israel

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Ẕerifin, , Israel

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Bologna, Emilia-Romagna, Italy

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Parma, Emilia-Romagna, Italy

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Rome, Lazio, Italy

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Milan, Lombardy, Italy

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Novara, Piedmont, Italy

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Turin, Piedmont, Italy

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Trento, Trentino-Alto Adige, Italy

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Cortona, Tuscany, Italy

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Padua, Veneto, Italy

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Verona, Veneto, Italy

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Nagoya, Aichi-ken, Japan

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Hirosaki, Aomori, Japan

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Asahi, Chiba, Japan

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Chiba, Chiba, Japan

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Kashiwa, Chiba, Japan

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Sakura, Chiba, Japan

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Matsuyama, Ehime, Japan

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Sapporo, Hokkaido, Japan

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Kobe, Hyōgo, Japan

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Kanazawa, Ishikawa-ken, Japan

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Kanazawa, Ishikawa-ken, Japan

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Kita-gun, Kagawa-ken, Japan

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Yokohama, Kanagawa, Japan

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Yokohama, Kanagawa, Japan

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Tsu, Mie-ken, Japan

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Sendai, Miyagi, Japan

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Kashihara, Nara, Japan

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Okayama, Okayama-ken, Japan

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Osaka, Osaka, Japan

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Sakai, Osaka, Japan

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Suita, Osaka, Japan

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Hamamatsu, Shizuoka, Japan

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Shimotsuke, Tochigi, Japan

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Utsunomiya, Tochigi, Japan

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Bunkyo-Ku, Tokyo, Japan

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Bunkyo-ku, Tokyo, Japan

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Bunkyo-ku, Tokyo, Japan

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Koto-ku, Tokyo, Japan

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Meguro-ku, Tokyo, Japan

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Minato-ku, Tokyo, Japan

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Mitaka, Tokyo, Japan

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Nakano-ku, Tokyo, Japan

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Shinjuku-ku, Tokyo, Japan

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Shinjuku-ku, Tokyo, Japan

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Yonago, Tottori, Japan

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Ube, Yamaguchi, Japan

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Chiba, , Japan

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Fukuoka, , Japan

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Gifu, , Japan

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Kumamoto, , Japan

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Miyazaki, , Japan

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Nagasaki, , Japan

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Osaka, , Japan

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Tokushima, , Japan

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Wakayama, , Japan

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Mexico City, Mexico City, Mexico

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México, D. F., Mexico City, Mexico

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Cuernavaca, Morelos, Mexico

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Monterrey, Nuevo León, Mexico

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Querétaro City, Querétaro, Mexico

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Mazatlán, Sinaloa, Mexico

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Durango, , Mexico

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Amsterdam, , Netherlands

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Amsterdam, , Netherlands

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Dordrecht, , Netherlands

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Geleen, , Netherlands

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Hilversum, , Netherlands

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Hoofddorp, , Netherlands

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Nijmegen, , Netherlands

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The Hague, , Netherlands

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Tilburg, , Netherlands

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Lodz, , Poland

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Lublin, , Poland

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Poznan, , Poland

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Rybnik, , Poland

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Siedlce, , Poland

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Waliszew, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Barnaul, , Russia

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Chelyabinsk, , Russia

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Chelyabinsk, , Russia

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Moscow, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Omsk, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Gwangju, Gwangju Gwang''yeogsi, South Korea

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Guri-si, Gyeonggi-do, South Korea

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Seongnam-si, Gyeonggido, South Korea

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Seoul, Seoul Teugbyeolsi, South Korea

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Seoul, Seoul Teugbyeolsi, South Korea

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Seoul, Seoul Teugbyeolsi, South Korea

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Seoul, Seoul Teugbyeolsi, South Korea

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Busan, , South Korea

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Daegu, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Sabadell, Barcelona, Spain

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Palma de Mallorca, Illes Baleares, Spain

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Málaga, Málaga, Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Cáceres, , Spain

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Córdoba, , Spain

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Lugo, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Madrid, , Spain

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Valencia, , Spain

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Gothenburg, , Sweden

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Lund, , Sweden

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Stockholm, , Sweden

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Umeå, , Sweden

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Uppsala, , Sweden

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Kaohsiung City, Kaohsiung, Taiwan

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Kaohsiung City, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taoyuan District, , Taiwan

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Colchester, Essex, United Kingdom

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Romford, Essex, United Kingdom

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Middlesbrough, Yorkshire, United Kingdom

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Belfast, , United Kingdom

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Glasgow, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Chandler, Arizona, United States

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Tucson, Arizona, United States

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Beverly Hills, California, United States

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Duarte, California, United States

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Los Angeles, California, United States

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Palo Alto, California, United States

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Denver, Colorado, United States

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Washington D.C., District of Columbia, United States

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Boca Raton, Florida, United States

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Gainesville, Florida, United States

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Miami Beach, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Chicago, Illinois, United States

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Peoria, Illinois, United States

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Louisville, Kentucky, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Towson, Maryland, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Boston, Massachusetts, United States

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Detroit, Michigan, United States

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Billings, Montana, United States

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Omaha, Nebraska, United States

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Lebanon, New Hampshire, United States

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Camden, New Jersey, United States

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Englewood, New Jersey, United States

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Hackensack, New Jersey, United States

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Albuquerque, New Mexico, United States

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Buffalo, New York, United States

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New York, New York, United States

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Poughkeepsie, New York, United States

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Rochester, New York, United States

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The Bronx, New York, United States

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Concord, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cleveland, Ohio, United States

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Columbus, Ohio, United States

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Gahanna, Ohio, United States

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Kettering, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Bala-Cynwyd, Pennsylvania, United States

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Camp Hill, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Charleston, South Carolina, United States

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Countries

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United States Australia Belgium Brazil Bulgaria Canada China Czechia Finland France Germany Israel Italy Japan Mexico Netherlands Poland Russia South Korea Spain Sweden Taiwan United Kingdom

References

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Hussain M, Tombal B, Saad F, Fizazi K, Sternberg CN, Crawford ED, Shore N, Kopyltsov E, Kalebasty AR, Bogemann M, Ye D, Cruz F, Suzuki H, Kapur S, Srinivasan S, Verholen F, Kuss I, Joensuu H, Smith MR. Darolutamide Plus Androgen-Deprivation Therapy and Docetaxel in Metastatic Hormone-Sensitive Prostate Cancer by Disease Volume and Risk Subgroups in the Phase III ARASENS Trial. J Clin Oncol. 2023 Jul 10;41(20):3595-3607. doi: 10.1200/JCO.23.00041. Epub 2023 Feb 16.

Reference Type DERIVED
PMID: 36795843 (View on PubMed)

Smith MR, Hussain M, Saad F, Fizazi K, Sternberg CN, Crawford D, Manarite J, Muslin D, Farrington T, Tombal B. Darolutamide and survival in metastatic, hormone-sensitive prostate cancer: a patient and caregiver perspective and plain language summary of the ARASENS trial. Future Oncol. 2022 Jul;18(21):2585-2597. doi: 10.2217/fon-2022-0433. Epub 2022 Jun 3.

Reference Type DERIVED
PMID: 35656777 (View on PubMed)

Smith MR, Hussain M, Saad F, Fizazi K, Sternberg CN, Crawford ED, Kopyltsov E, Park CH, Alekseev B, Montesa-Pino A, Ye D, Parnis F, Cruz F, Tammela TLJ, Suzuki H, Utriainen T, Fu C, Uemura M, Mendez-Vidal MJ, Maughan BL, Joensuu H, Thiele S, Li R, Kuss I, Tombal B; ARASENS Trial Investigators. Darolutamide and Survival in Metastatic, Hormone-Sensitive Prostate Cancer. N Engl J Med. 2022 Mar 24;386(12):1132-1142. doi: 10.1056/NEJMoa2119115. Epub 2022 Feb 17.

Reference Type DERIVED
PMID: 35179323 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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https://clinicaltrials.bayer.com/study/17777

Click here to find further information and, after study completion, the study results according to Bayer's transparency standards

http://www.clinicaltrialsregister.eu/

Click here to find information about studies related to Bayer Healthcare products conducted in Europe

Other Identifiers

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2015-002590-38

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

17777

Identifier Type: -

Identifier Source: org_study_id

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