Factor Product Utilization and Health Outcomes in Patients With Hemophilia

NCT ID: NCT02796222

Last Updated: 2021-04-28

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Total Enrollment

61 participants

Study Classification

OBSERVATIONAL

Study Start Date

2016-04-30

Study Completion Date

2021-04-26

Brief Summary

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Recombinant factor VIII Fc (rFVIIIFc) and recombinant factor IX Fc (rFIXFc) are extended half-life coagulation factors approved by Health Canada in 2014 for the treatment of severe hemophilia A and B, respectively. The objectives of this observational study is to describe the change in annual factor consumption, clinical and patient-reported outcomes for patients who switch from recombinant factor VIII (rFVIII) and recombinant factor IX (rFIX) to rFVIIIFc/ rFIXFc in Canada, and to explore clinicians' and patients' reasons for switching or not switching.

Detailed Description

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Conditions

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Hemophilia A, Congenital Hemophilia B, Congenital

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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Hemophilia A patients on rFVIIIFc

Patients with hemophilia A who switch from on-demand or prophylactic treatment with rFVIII to rFVIIIFc

No interventions assigned to this group

Hemophilia A patients on rFVIII

Patients with hemophilia A who remain on on-demand or prophylactic treatment with rFVIII

No interventions assigned to this group

Hemophilia B patients on rFIXFc

Patients with hemophilia B who switch from on-demand or prophylactic treatment with rFIX to rFIXFc

No interventions assigned to this group

Hemophilia A patients on rFIX

Patients with hemophilia B who remain on on-demand or prophylactic treatment with rFIX

No interventions assigned to this group

Eligibility Criteria

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Inclusion Criteria

1. Males ≥12 years of age with severe and moderate congenital hemophilia A or B (baseline factor activity\<5%)
2. Ability to understand the purpose and risks of the study and provide signed and dated informed consent or assent and authorization to use protected health information (PHI) in accordance with national and local privacy regulations.

Exclusion Criteria

1. Unable or unwilling to provide informed consent
2. Patients with an existing bleeding disorder other than hemophilia A or B
3. History of hypersensitivity or severe allergic reactions to factor products
4. Patients currently participating in a phase 1-3 study with another factor replacement product
5. Unable to adhere to the study requirements based on the judgment of the Prescribing Physician (e.g. unable to enter accurate and timely infusion and bleeding records)
Minimum Eligible Age

12 Years

Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Biogen

INDUSTRY

Sponsor Role collaborator

University of British Columbia

OTHER

Sponsor Role lead

Responsible Party

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Shannon Jackson

Clinical Associate Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Shannon Jackson, MD

Role: PRINCIPAL_INVESTIGATOR

Division of Hematology, Department of Medicine, University of British Columbia

Robert Klaassen, MD

Role: STUDY_CHAIR

Division of Hematology/Oncology, Department of Pediatrics, University of Ottawa

Man-Chiu Poon, MD

Role: STUDY_CHAIR

Division of Hematology, Department of Medicine, University of Calgary

Sue Robinson, MD

Role: STUDY_CHAIR

Division of Hematology, Department of Medicine, Dalhousie University

John Wu, MD

Role: STUDY_CHAIR

BC Children's hospital, Division of Hematology, Department of Medicine, University of British Columbia

Alfonso Iorio, MD

Role: STUDY_CHAIR

Hemophilia Program, Hamilton Health Services Program, McMaster University

Michelle Sholzberg, MD

Role: STUDY_CHAIR

Hemophilia Program, St. Michael's Hospital, University of Toronto

Locations

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BC Hemophilia Adult Program

Vancouver, British Columbia, Canada

Site Status

Countries

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Canada

Other Identifiers

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CAN-FAB-15-10911

Identifier Type: -

Identifier Source: org_study_id

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