Fc factOrs and Real-World hemophiliA Patient-ReporteD Outcomes

NCT ID: NCT02392156

Last Updated: 2020-12-19

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Total Enrollment

3 participants

Study Classification

OBSERVATIONAL

Study Start Date

2015-07-31

Study Completion Date

2015-12-31

Brief Summary

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The primary objective of the study is to evaluate the effectiveness of prophylactic treatment with recombinant Factor VIII Fc fusion protein (rFVIIIFc) and recombinant Factor IX Fc fusion protein (rFIXFc) therapy as assessed by patient treatment burden and health economic outcomes while maintaining disease control in males with hemophilia A or B.

Detailed Description

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Conditions

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Hemophilia A Hemophilia B

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Study Groups

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rFVIIIFc for hemophilia A

Administered based on the clinical judgment of the Prescribing Physician and according to the local approved drug label

rFVIIIFc

Intervention Type BIOLOGICAL

As described in the treatment arm

non-Fc (fusion protein) replacement products for hemophilia A

Administered based on the clinical judgment of the Prescribing Physician and according to the local approved drug label

rFVIIIFc

Intervention Type BIOLOGICAL

As described in the treatment arm

non-Fc FVIII replacement products

Intervention Type DRUG

Standard plasma-derived (pd) or recombinant (r) FVIII concentrate and other traditional treatment options

rFIXFc for hemophilia B

Administered based on the clinical judgment of the Prescribing Physician and according to the local approved drug label

rFIXFc

Intervention Type BIOLOGICAL

As described in the treatment arm

non-Fc factor replacement products for hemophilia B

Administered based on the clinical judgment of the Prescribing Physician and according to the local approved drug label

rFIXFc

Intervention Type BIOLOGICAL

As described in the treatment arm

non-Fc FIX replacement products

Intervention Type DRUG

Standard plasma-derived (pd) or recombinant (r) FIX concentrate and other traditional treatment options

Interventions

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rFVIIIFc

As described in the treatment arm

Intervention Type BIOLOGICAL

rFIXFc

As described in the treatment arm

Intervention Type BIOLOGICAL

non-Fc FVIII replacement products

Standard plasma-derived (pd) or recombinant (r) FVIII concentrate and other traditional treatment options

Intervention Type DRUG

non-Fc FIX replacement products

Standard plasma-derived (pd) or recombinant (r) FIX concentrate and other traditional treatment options

Intervention Type DRUG

Other Intervention Names

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antihemophilic factor (recombinant) Fc fusion protein Eloctate recombinant coagulation factor VIII Fc fusion protein efmoroctocog alfa BIIB031 coagulation factor IX (recombinant) Fc fusion protein Alprolix BIIB029 rFVIII pdFVIII rFIX pdFIX

Eligibility Criteria

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Inclusion Criteria

* Have a medically documented diagnosis of hemophilia A or B that is being treated prophylactically with a factor replacement product not designed to have a prolonged half-life and satisfy a therapeutic indication for rFVIIIFc/rFIXFc per the approved local label
* Have at least 50 prior exposure days (EDs) to any combination of factor replacement products
* Have documented pre-study data available that confirm fulfillment of the eligibility criteria
* Have no measurable inhibitor activity in a sample obtained within 4 weeks prior to the Baseline visit, and absence of clinical signs or symptoms of decreased response to the current factor replacement product

Exclusion Criteria

* Have a diagnosis of any bleeding disorder other than hemophilia A or hemophilia B or an additional coagulation disorder(s) in addition to hemophilia A or hemophilia B
* Have a prior history of anaphylaxis associated with any factor VIII (FVIII)/ factor IX (FIX) or intravenous immunoglobin administration
* Had an inhibitor within 5 years before the Baseline visit. Note: A family history of inhibitors will not exclude the patient.
* Past or current treatment with any factor replacement product with a prolonged half-life, including an Fc product, for the treatment of hemophilia
Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Swedish Orphan Biovitrum

INDUSTRY

Sponsor Role collaborator

Bioverativ Therapeutics Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Medical Director

Role: STUDY_DIRECTOR

Bioverativ Therapeutics Inc.

Locations

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Research Site

Los Angeles, California, United States

Site Status

Research Site

East Lansing, Michigan, United States

Site Status

Countries

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United States

Other Identifiers

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997HA401

Identifier Type: -

Identifier Source: org_study_id