A Study to Assess the Efficacy and Safety of PT009 Compared to PT005 on COPD Exacerbations Over a 52-Week Period in Subjects With Moderate to Very Severe COPD (Sophos)

NCT ID: NCT02727660

Last Updated: 2019-09-26

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

1876 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-04-29

Study Completion Date

2018-04-04

Brief Summary

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This is a Phase III randomized, double-blind, parallel group, multi-center, 52-week COPD exacerbation and lung function study with PT009 320/9.6 μg, PT009 160/9.6 μg and PT005 9.6 μg, all administered BID.

Detailed Description

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This is a Phase III randomized, double-blind, parallel group, multi-center, 52-week COPD exacerbation and lung function study. Subjects will undergo a 1- to 4-week Screening Period. Subjects who successfully complete the Screening Period will be randomized to one of the following three treatment groups: PT009 320/9.6 μg, PT009 160/9.6 μg and PT005 9.6 μg, all administered BID. Following randomization, subjects will enter the Treatment Period and undergo additional treatment visits over 52 weeks.

Conditions

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Chronic Obstructive Pulmonary Disorder

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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BFF MDI (PT009) 320/9.6 μg

Budesonide and Formoterol Fumarate Inhalation Aerosol - 160/4.8 μg per actuation MDI/120 inhalations Taken as 2 inhalations BID

Group Type EXPERIMENTAL

BFF MDI (PT009) 320/9.6 μg

Intervention Type DRUG

Blinded Treatment

BFF MDI (PT009) 160/9.6 μg

Budesonide and Formoterol Fumarate Inhalation Aerosol - 80/4.8 μg per actuation MDI/120 inhalations Taken as 2 inhalations BID

Group Type EXPERIMENTAL

BFF MDI (PT009) 160/9.6 μg

Intervention Type DRUG

Blinded Treatment

FF MDI (PT005) 9.6 μg

Formoterol Fumarate Inhalation Aerosol - 4.8 μg per actuation MDI/120 inhalations Taken as 2 inhalations BID

Group Type EXPERIMENTAL

FF MDI (PT005) 9.6 μg

Intervention Type DRUG

Blinded Treatment

Interventions

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BFF MDI (PT009) 320/9.6 μg

Blinded Treatment

Intervention Type DRUG

BFF MDI (PT009) 160/9.6 μg

Blinded Treatment

Intervention Type DRUG

FF MDI (PT005) 9.6 μg

Blinded Treatment

Intervention Type DRUG

Other Intervention Names

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Budesonide and Formoterol Fumarate Inhalation Aerosol Budesonide and Formoterol Fumarate Inhalation Aerosol Formoterol Fumarate Inhalation

Eligibility Criteria

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Inclusion Criteria

1. Give their signed written informed consent to participate
2. At least 40 years of age and no older than 80 years of age
3. COPD patients who are symptomatic
4. Must be receiving one or more inhaled bronchodilators as maintenance therapy
5. Must have a documented history of COPD exacerbations

Exclusion Criteria

1. Current diagnosis of asthma
2. COPD due to α1-Antitrypsin Deficiency
3. Known active tuberculosis, lung cancer, cystic fibrosis, and significant bronchiectasis, Pulmonary resection or Lung Volume Reduction Surgery during the past 6 months.
4. Long-term-oxygen therapy (≥ 15 hours a day).
Minimum Eligible Age

40 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pearl Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Dothan, Alabama, United States

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Huntsville, Alabama, United States

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Sheffield, Alabama, United States

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Flagstaff, Arizona, United States

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Costa Mesa, California, United States

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Gold River, California, United States

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Lincoln, California, United States

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Long Beach, California, United States

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Palo Alto, California, United States

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San Diego, California, United States

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San Diego, California, United States

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San Diego, California, United States

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Upland, California, United States

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Yorba Linda, California, United States

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Boulder, Colorado, United States

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Denver, Colorado, United States

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New Haven, Connecticut, United States

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Boynton Beach, Florida, United States

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Chiefland, Florida, United States

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Clearwater, Florida, United States

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Daytona Beach, Florida, United States

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Hialeah, Florida, United States

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Kissimmee, Florida, United States

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Leesburg, Florida, United States

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Lehigh Acres, Florida, United States

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Merritt Island, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Ormond Beach, Florida, United States

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Port Orange, Florida, United States

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Sarasota, Florida, United States

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Tampa, Florida, United States

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Tampa, Florida, United States

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Winter Park, Florida, United States

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Atlanta, Georgia, United States

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Dacula, Georgia, United States

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Decatur, Georgia, United States

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Snellville, Georgia, United States

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Stockbridge, Georgia, United States

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Aurora, Illinois, United States

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Chicago, Illinois, United States

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Peoria, Illinois, United States

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Brownsburg, Indiana, United States

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Evansville, Indiana, United States

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Valparaiso, Indiana, United States

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Iowa City, Iowa, United States

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Olathe, Kansas, United States

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Topeka, Kansas, United States

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Hazard, Kentucky, United States

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Metairie, Louisiana, United States

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Sunset, Louisiana, United States

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Biddeford, Maine, United States

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Rochester, Minnesota, United States

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Chesterfield, Missouri, United States

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Kansas City, Missouri, United States

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Saint Charles, Missouri, United States

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St Louis, Missouri, United States

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Lincoln, Nebraska, United States

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Reno, Nevada, United States

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Toms River, New Jersey, United States

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Brooklyn, New York, United States

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New York, New York, United States

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Syracuse, New York, United States

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The Bronx, New York, United States

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Gastonia, North Carolina, United States

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Hickory, North Carolina, United States

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Hickory, North Carolina, United States

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Lenoir, North Carolina, United States

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Tabor City, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Canton, Ohio, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Marion, Ohio, United States

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Wooster, Ohio, United States

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Edmond, Oklahoma, United States

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Medford, Oregon, United States

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Portland, Oregon, United States

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Johnstown, Pennsylvania, United States

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Scottdale, Pennsylvania, United States

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Wyomissing, Pennsylvania, United States

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Cumberland, Rhode Island, United States

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East Providence, Rhode Island, United States

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Warwick, Rhode Island, United States

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Anderson, South Carolina, United States

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Gaffney, South Carolina, United States

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Gaffney, South Carolina, United States

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Lancaster, South Carolina, United States

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Orangeburg, South Carolina, United States

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Rock Hill, South Carolina, United States

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Seneca, South Carolina, United States

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Spartanburg, South Carolina, United States

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Franklin, Tennessee, United States

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Knoxville, Tennessee, United States

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Smyrna, Tennessee, United States

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Amarillo, Texas, United States

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Austin, Texas, United States

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Baytown, Texas, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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Kerrville, Texas, United States

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Lewisville, Texas, United States

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Lufkin, Texas, United States

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McKinney, Texas, United States

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McKinney, Texas, United States

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Plano, Texas, United States

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Port Arthur, Texas, United States

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Sherman, Texas, United States

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Spring, Texas, United States

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Waco, Texas, United States

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Salt Lake City, Utah, United States

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Manassas, Virginia, United States

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Everett, Washington, United States

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Renton, Washington, United States

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Milwaukee, Wisconsin, United States

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Buenos Aires, , Argentina

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CABA, , Argentina

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CABA, , Argentina

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CABA, , Argentina

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CABA, , Argentina

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Ciudad Autonomade Buenos Aires, , Argentina

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Ciudad Autónoma de Buenos Aire, , Argentina

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Ciudad de Buenos Aires, , Argentina

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Concepción del Uruguay, , Argentina

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Córdoba, , Argentina

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Mar del Plata, , Argentina

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Mar del Plata, , Argentina

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Mar del Plata, , Argentina

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Mendoza, , Argentina

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Mendoza, , Argentina

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Nueve de Julio, , Argentina

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Ranelagh, , Argentina

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Rosario, , Argentina

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San Fernando, , Argentina

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San Juan Bautista, , Argentina

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San Miguel de Tucumán, , Argentina

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Bludenz, , Austria

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Feldbach, , Austria

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Hallein, , Austria

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Linz, , Austria

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Brussels, , Belgium

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Erpent, , Belgium

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Gilly, , Belgium

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Jambes, , Belgium

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Liège, , Belgium

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Roeselare, , Belgium

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Botucatu, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Santo André, , Brazil

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São Bernardo do Campo, , Brazil

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São Paulo, , Brazil

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Sorocaba, , Brazil

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Uberlândia, , Brazil

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Vitória, , Brazil

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Ajax, Ontario, Canada

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Windsor, Ontario, Canada

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Windsor, Ontario, Canada

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Québec, Quebec, Canada

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Québec, Quebec, Canada

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Saint-Charles-Borromée, Quebec, Canada

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Trois-Rivières, Quebec, Canada

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Curicó, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Talca, , Chile

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Talcahuano, , Chile

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Aalborg, , Denmark

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Aarhus N, , Denmark

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Hvidovre, , Denmark

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Kolding, , Denmark

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København NV, , Denmark

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Odense C, , Denmark

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Roskilde, , Denmark

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Silkeborg, , Denmark

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Cologne, , Germany

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Cottbus, , Germany

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Frankfurt, , Germany

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Leipzig, , Germany

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Lübeck, , Germany

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Rodgau-Dudenhofen, , Germany

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Bari, , Italy

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Catania, , Italy

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Ferrara, , Italy

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Legnago, , Italy

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Monza, , Italy

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Napoli, , Italy

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Padua, , Italy

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Pavia, , Italy

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Riccione, , Italy

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Rimini, , Italy

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Roma, , Italy

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Roma, , Italy

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Sassari, , Italy

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Durango, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Mexico City, , Mexico

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Minatitlán, , Mexico

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Monterrey, , Mexico

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Sonora, , Mexico

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Villahermosa, , Mexico

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Arendal, , Norway

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Hønefoss, , Norway

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Kråkeroy, , Norway

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Stavanger, , Norway

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Svelvik, , Norway

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Trondheim, , Norway

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Chancay, , Peru

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Cusco, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Piura, , Peru

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Ponce, , Puerto Rico

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San Juan, , Puerto Rico

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Izhevsk, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Novosibirsk, , Russia

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Omsk, , Russia

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Penza, , Russia

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Perm, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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StPetersburg, , Russia

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Ulyanovsk, , Russia

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Yekaterinburg, , Russia

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Bloemfontein, , South Africa

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Cape Town, , South Africa

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Cape Town, , South Africa

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Cape Town, , South Africa

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Durban, , South Africa

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Johannesburg, , South Africa

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KwaDukuza, , South Africa

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Lenasia Ext8, , South Africa

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Mowbray, , South Africa

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Parow, , South Africa

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Pretoria, , South Africa

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Alicante, , Spain

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Alzira (Valencia), , Spain

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Benalmádena (Málaga), , Spain

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Cáceres, , Spain

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Jerez de la Frontera, , Spain

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Laredo, , Spain

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Loja (Granada), , Spain

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Marbella (Málaga), , Spain

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Málaga, , Spain

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Palma de Mallorca, , Spain

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Sagunto(Valencia), , Spain

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Sant Boi de Llobregat, , Spain

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Lund, , Sweden

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Lund, , Sweden

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Malmo, , Sweden

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Stockholm, , Sweden

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Uppsala, , Sweden

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Bradford, , United Kingdom

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Chertsey, , United Kingdom

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Chester, , United Kingdom

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Doncaster, , United Kingdom

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Lancaster, , United Kingdom

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Sheffield, , United Kingdom

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Wishaw, , United Kingdom

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Countries

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United States Argentina Austria Belgium Brazil Canada Chile Denmark Germany Italy Mexico Norway Peru Puerto Rico Russia South Africa Spain Sweden United Kingdom

References

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Singh D, Hurst JR, Martinez FJ, Rabe KF, Bafadhel M, Jenkins M, Salazar D, Dorinsky P, Darken P. Predictive modeling of COPD exacerbation rates using baseline risk factors. Ther Adv Respir Dis. 2022 Jan-Dec;16:17534666221107314. doi: 10.1177/17534666221107314.

Reference Type DERIVED
PMID: 35815359 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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PT009003

Identifier Type: -

Identifier Source: org_study_id

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