A Study of Ramucirumab (LY3009806) or Merestinib (LY2801653) in Advanced or Metastatic Biliary Tract Cancer

NCT ID: NCT02711553

Last Updated: 2025-08-03

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

ACTIVE_NOT_RECRUITING

Clinical Phase

PHASE2

Total Enrollment

309 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-05-19

Study Completion Date

2026-12-31

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The main purpose of this study is to evaluate the efficacy and safety of ramucirumab or merestinib or placebo plus cisplatin and gemcitabine in participants with advanced or metastatic biliary tract cancer.

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Biliary Tract Cancer Metastatic Cancer Advanced Cancer

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

8 mg/kg Ramucirumab + 25 mg/m² Cisplatin + 1000 mg/m² Gemcitabine

Participants received 8 mg/kg ramucirumab plus 25 mg/square meter (mg/m²) cisplatin and 1000 mg/m² gemcitabine intravenously (IV) on days 1 and 8, every 21 days (1 cycle). Participants may continue on study drug for up to 8 cycles (for cisplatin and gemcitabine therapy) or until disease progression, unacceptable toxicity, or other withdrawal criterion is met (for ramucirumab therapy).

Group Type EXPERIMENTAL

Ramucirumab

Intervention Type DRUG

Administered IV

Cisplatin

Intervention Type DRUG

Administered IV

Gemcitabine

Intervention Type DRUG

Administered IV

Placebo IV + 25 mg/m² Cisplatin + 1000 mg/m² Gemcitabine

Participants received placebo (indistinguishable and equivalent volume to ramucirumab) plus 25 mg/m² cisplatin and 1000 mg/m² gemcitabine IV on days 1 and 8, every 21 days (1 cycle). Participants may continue on study drug for up to 8 cycles (for cisplatin and gemcitabine therapy) or until disease progression, unacceptable toxicity, or other withdrawal criterion is met (for placebo therapy).

Group Type PLACEBO_COMPARATOR

Cisplatin

Intervention Type DRUG

Administered IV

Gemcitabine

Intervention Type DRUG

Administered IV

Placebo IV

Intervention Type DRUG

Administered IV

80 mg Merestinib + 25 mg/m² Cisplatin + 1000 mg/m² Gemcitabine

Participants received 80 mg merestinib orally each day, plus 25 mg/m² cisplatin and 1000 mg/m² gemcitabine IV on Days 1 and 8, every 21 days (1 cycle). Participants may continue on study drug for up to 8 cycles (for cisplatin and gemcitabine therapy) or until disease progression, unacceptable toxicity, or other withdrawal criterion is met (for merestinib therapy).

Group Type EXPERIMENTAL

Merestinib

Intervention Type DRUG

Administered orally

Cisplatin

Intervention Type DRUG

Administered IV

Gemcitabine

Intervention Type DRUG

Administered IV

Placebo Oral + 25 mg/m² Cisplatin + 1000 mg/m² Gemcitabine

Participants received placebo (indistinguishable to merestinib) orally each day, plus 25 mg/m² cisplatin and 1000 mg/m² gemcitabine IV on Days 1 and 8, every 21 days. Participants may continue on study drug for up to 8 cycles (for cisplatin and gemcitabine therapy) or until disease progression, unacceptable toxicity, or other withdrawal criterion is met (for placebo therapy).

Group Type PLACEBO_COMPARATOR

Cisplatin

Intervention Type DRUG

Administered IV

Gemcitabine

Intervention Type DRUG

Administered IV

Placebo Oral

Intervention Type DRUG

Administered orally

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Ramucirumab

Administered IV

Intervention Type DRUG

Merestinib

Administered orally

Intervention Type DRUG

Cisplatin

Administered IV

Intervention Type DRUG

Gemcitabine

Administered IV

Intervention Type DRUG

Placebo Oral

Administered orally

Intervention Type DRUG

Placebo IV

Administered IV

Intervention Type DRUG

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

LY3009806 LY2801653 LY188011

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* Have an Eastern Cooperative Oncology Group performance status of 0 or 1.
* Have a histologically or cytologically confirmed diagnosis of non-resectable, recurrent, or metastatic biliary tract adenocarcinoma (intrahepatic or extrahepatic cholangiocarcinoma, gallbladder cancer, or Ampulla of Vater) .
* Have measurable disease by Response Evaluation Criteria in Solid Tumors (RECIST).
* Have adequate biliary drainage.
* Have adequate organ function.
* Males and females are sterile, postmenopausal, or compliant with a highly effective contraceptive method.
* Female participants of childbearing potential must have a negative serum pregnancy test within 7 days prior to first dose.
* Are willing to provide blood/serum/plasma and tumor tissue samples for research purposes. Submission of blood/serum/plasma and tumor tissue samples is mandatory for participation in this study, unless restricted per local regulations.

Exclusion Criteria

* Previous systemic therapy for locally advanced or metastatic disease is not allowed.
* Have a history of or have current hepatic encephalopathy of any grade, or ascites of Grade \>1, or cirrhosis with Child-Pugh Stage B or higher.
* Have ongoing or recent (≤6 months) hepatorenal syndrome.
* Have had a major surgical procedure or significant traumatic injury including nonhealing wound, peptic ulcer, or bone fracture ≤28 days prior to randomization.
* Anticipate having a major surgical procedure during the course of the study.
* Has documented brain metastases, leptomeningeal disease, or uncontrolled spinal cord compression.
* Within 6 months prior to randomization, have had any arterial thrombotic event, including myocardial infarction, unstable angina, cerebrovascular accident, or transient ischemic attack.
* Have an uncontrolled arterial hypertension with systolic blood pressure ≥150 or diastolic blood pressure ≥90 millimeters of mercury (mm Hg) despite standard medical management.
* Have a previous malignancy within 5 years of study entry or a concurrent malignancy.
* Have a history of gastrointestinal perforation and/or fistulae within 6 months prior to randomization.
* Have a known allergy or hypersensitivity reaction to any of the treatment components.
* Have a history of uncontrolled hereditary or acquired thrombotic disorder.
* Have uncontrolled metabolic disorders or other nonmalignant organ or systemic diseases or secondary effects of cancer that induce a high medical risk and/or make assessment of survival uncertain.
* Have mixed hepatocellular biliary tract cancer histology.
* Have a corrected QT interval \>470 milliseconds as calculated by the Fridericia equation.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Eli Lilly and Company

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Call 1-877-CTLILLY (1-877-285-4559) or 1-317-615-4559 Mon - Fri 9 AM - 5 PM Eastern time (UTC/GMT - 5 hours, EST)

Role: STUDY_DIRECTOR

Eli Lilly and Company

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

The University of Arizona Cancer Center

Tucson, Arizona, United States

Site Status

UCSF Medical Center at Mission Bay

San Francisco, California, United States

Site Status

Georgetown University Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of Florida School of Medicine

Gainesville, Florida, United States

Site Status

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

Washington University Medical School

City of Saint Peters, Missouri, United States

Site Status

Washington University Medical School

Creve Coeur, Missouri, United States

Site Status

Washington University Medical School

St Louis, Missouri, United States

Site Status

Washington University Medical School

St Louis, Missouri, United States

Site Status

Thomas Jefferson University

Philadelphia, Pennsylvania, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Florida Cancer Specialists

Nashville, Tennessee, United States

Site Status

Tennessee Oncology PLLC

Nashville, Tennessee, United States

Site Status

Alexander Fleming

CABA, BS, Argentina

Site Status

Hospital de Gastroenterologia Udaondo

Capital Federal, Buenos Aires, Argentina

Site Status

Fundacion Ars Medica

San Salvador de Jujuy, Jujuy Province, Argentina

Site Status

Clinica Viedma

Viedma, Río Negro Province, Argentina

Site Status

Centro Medico San Roque

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Fundacion Favaloro

Ciudad de Buenos Aires, , Argentina

Site Status

Fundación CORI para la Investigación y Prevención del Cáncer

La Rioja, , Argentina

Site Status

Centro Polivalente de Asistencia e Inv. Clinica CER-San Juan

San Juan, , Argentina

Site Status

Calvary Mater Newcastle

Waratah, New South Wales, Australia

Site Status

Royal Adelaide Hospital

Adelaide, South Australia, Australia

Site Status

Austin Health

Heidelberg, Victoria, Australia

Site Status

Landesklinikum Wr. Neustadt

Wiener Neustadt, Lower Austria, Austria

Site Status

Universitätsklinikum Salzburg

Salzburg, , Austria

Site Status

KH der Barmherzigen Brüder Wien

Vienna, , Austria

Site Status

Cliniques universitaires Saint-Luc

Brussels, Brussels Capital, Belgium

Site Status

Universitair Ziekenhuis Gent

Ghent, , Belgium

Site Status

Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg

Leuven, , Belgium

Site Status

Masarykuv onkologicky ustav

Brno, Brno-město, Czechia

Site Status

Fakultni nemocnice Hradec Kralove

Hradec Králové, , Czechia

Site Status

Fakultni Nemocnice v Motole

Prague, , Czechia

Site Status

Aarhus Universitetshospital, Aarhus Sygehus

Aarhus C, , Denmark

Site Status

Odense Universitetshospital

Odense C, , Denmark

Site Status

Centre Leon Berard

Lyon, Auvergne-Rhône-Alpes, France

Site Status

CHU de Bordeaux Hop St ANDRE

Bordeaux, Gironde, France

Site Status

CHU de Besancon Hopital Jean Minjoz

Besançon, , France

Site Status

Hôpital C. HURIEZ

Lille, , France

Site Status

CHRU de Montpellier-Hopital St Eloi

Montpellier, , France

Site Status

Centre Antoine-Lacassagne

Nice, , France

Site Status

Gustave Roussy

Villejuif, , France

Site Status

Universitätsklinikum Tübingen

Tübingen, Baden-Wurttemberg, Germany

Site Status

Universitätsklinikum Ulm

Ulm, Baden-Wurttemberg, Germany

Site Status

Universitätsklinikum Erlangen

Erlangen, Bavaria, Germany

Site Status

Medizinische Hochschule Hanover

Hanover, Lower Saxony, Germany

Site Status

HELIOS Klinikum Berlin-Buch

Berlin, , Germany

Site Status

Universitaetsklinikum Hamburg-Eppendorf

Hamburg, , Germany

Site Status

Debreceni Egyetem Klinikai Kozpont Onkologiai Tanszek

Debrecen, Hajdú-Bihar, Hungary

Site Status

Del-pesti Centrumkorhaz - Orszagos Hematologiai es Infektologiai Intezet

Budapest, , Hungary

Site Status

Arke Estudios Clinicos S.A. de C.V.

Mexico City, Mexico City, Mexico

Site Status

Centro de Alta Especialidad Reumatologia Inv del Potosi SC

San Luis Potosí City, , Mexico

Site Status

Russian Scientific Center of Radiology and Surgical Technologies

Saint Petersburg, Sankt-Peterburg, Russia

Site Status

Arkhangelsk Clinical Oncological Dispensary

Arkhangelsk, , Russia

Site Status

Blokhin Cancer Research Center

Moscow, , Russia

Site Status

Saint-Petersburg City Clinical Oncology Dispensary

Saint Petersburg, , Russia

Site Status

Asan Medical Center

Seoul, Korea, South Korea

Site Status

Seoul National University Hospital

Seoul, Seoul, Korea, South Korea

Site Status

Severance Hospital, Yonsei University Health System

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Duran I Reynals

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Hospital Clínico Universitario de Valencia

Barcelona, , Spain

Site Status

Hospital General Universitario Gregorio Marañon

Madrid, , Spain

Site Status

Hospital Clinico de San Carlos

Madrid, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

Skåne universitetssjukhus

Malmo, , Sweden

Site Status

Karolinska Universitetssjukhuset i Solna

Stockholm, , Sweden

Site Status

Chang Gung Memorial Hospital - Kaohsiung Branch

Kaohsiung City, , Taiwan

Site Status

China Medical University Hospital

Taichung, , Taiwan

Site Status

National Cheng-Kung Uni. Hosp.

Tainan City, , Taiwan

Site Status

Taipei Veterans General Hospital

Taipei, , Taiwan

Site Status

Chang Gung Memorial Hospital - Linkou

Taoyuan, , Taiwan

Site Status

Baskent University Dr. Turgut Noyan Research and Training Center

Adana, , Turkey (Türkiye)

Site Status

Hacettepe University Faculty of Medicine

Ankara, , Turkey (Türkiye)

Site Status

Akdeniz University Medical Faculty

Antalya, , Turkey (Türkiye)

Site Status

Trakya University

Edirne, , Turkey (Türkiye)

Site Status

Istanbul Universitesi-Cerrahpasa Cerrahpasa Tip Fakultesi Yerleskesi

Istanbul, , Turkey (Türkiye)

Site Status

University College Hospital - London

London, Greater London, United Kingdom

Site Status

The Christie NHS Foundation Trust

Manchester, Greater Manchester, United Kingdom

Site Status

Hammersmith Hospital

Acton, London, United Kingdom

Site Status

The Clatterbridge Cancer Centre

Bebbington, Merseyside, United Kingdom

Site Status

Royal Marsden Hospital

Sutton, Surrey, United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Australia Austria Belgium Czechia Denmark France Germany Hungary Mexico Russia South Korea Spain Sweden Taiwan Turkey (Türkiye) United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Valle JW, Vogel A, Denlinger CS, He AR, Bai LY, Orlova R, Van Cutsem E, Adeva J, Chen LT, Obermannova R, Ettrich TJ, Chen JS, Wasan H, Girvan AC, Zhang W, Liu J, Tang C, Ebert PJ, Aggarwal A, McNeely SC, Moser BA, Oliveira JM, Carlesi R, Walgren RA, Oh DY. Addition of ramucirumab or merestinib to standard first-line chemotherapy for locally advanced or metastatic biliary tract cancer: a randomised, double-blind, multicentre, phase 2 study. Lancet Oncol. 2021 Oct;22(10):1468-1482. doi: 10.1016/S1470-2045(21)00409-5.

Reference Type DERIVED
PMID: 34592180 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

Access external resources that provide additional context or updates about the study.

https://trials.lillytrialguide.com/en-US/trial/3MKeCKU0hiwqg4gsAMgAEs

A Study of Ramucirumab (LY3009806) or Merestinib (LY2801653) in Advanced or Metastatic Biliary Tract Cancer

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

I3O-MC-JSBF

Identifier Type: OTHER

Identifier Source: secondary_id

2015-004699-31

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

16329

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.