A Phase III Safety Study of Ferumoxytol Compared to Ferric Carboxymaltose for the Treatment of Iron Deficiency Anemia (IDA)

NCT ID: NCT02694978

Last Updated: 2023-07-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

2014 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-02-29

Study Completion Date

2017-07-17

Brief Summary

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To evaluate the safety of 1.020 grams (g) of intravenous (IV) ferumoxytol compared to 1.500 g of IV ferric carboxymaltose (FCM).

Detailed Description

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Conditions

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Iron Deficiency Anemia

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Ferumoxytol

Participants received an IV infusion of ferumoxytol 510 milligram (mg) diluted (17 milliliter \[mL\]) in 233 mL 0.9% sodium chloride injection, United States Pharmacopeia (USP) (normal saline) (final volume 250 mL) over at least 15 minutes with a second dose 7-8 days after the first dose, for a total cumulative dose of 1.020 g.

Group Type EXPERIMENTAL

Ferumoxytol

Intervention Type DRUG

FCM

Participants received an IV infusion of FCM 750 mg diluted (15 mL) in 235 mL 0.9% sodium chloride injection, USP (normal saline) (final volume 250 mL) over at least 15 minutes with a second dose 7-8 days after the first dose, for a total cumulative dose of 1.500 g.

Group Type ACTIVE_COMPARATOR

FCM

Intervention Type DRUG

Interventions

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Ferumoxytol

Intervention Type DRUG

FCM

Intervention Type DRUG

Other Intervention Names

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Feraheme Injectafer, Ferinject

Eligibility Criteria

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Inclusion Criteria

* Participants with IDA and in whom IV iron treatment is indicated and defined as:

* Participants with documented hemoglobin \<12.0 g per deciliter (dL) for females and \<14.0 g/dL for males within 60 days of dosing And
* Participants with documented transferrin saturation (TSAT) ≤20% or Ferritin ≤100 nanograms (ng) per mL within 60 days of dosing
* Documented history of unsatisfactory oral iron therapy or in whom oral iron cannot be tolerated, or for whom oral iron is considered medically inappropriate (as per oral iron history questionnaire)
* All participants (male and female) of childbearing potential who are sexually active who agree to routinely use adequate contraception from randomization throughout the duration of the study

Exclusion Criteria

* Known hypersensitivity reaction to any component of ferumoxytol or FCM
* History of allergy to an IV iron
* History of multiple drug allergies
* Participants with dialysis-dependent chronic kidney disease
* Hemoglobin ≤7.0 g/dL
* Female participants who are pregnant, intend to become pregnant, are breastfeeding, have a positive serum/urine pregnancy test or not willing to use effective contraceptive precautions during the study (including females of childbearing potential who are partners of male participants)
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AMAG Pharmaceuticals, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Huntsville, Alabama, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Anaheim, California, United States

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Chula Vista, California, United States

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Corona, California, United States

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Encino, California, United States

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Fountain Valley, California, United States

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Granada Hills, California, United States

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La Mesa, California, United States

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Orange, California, United States

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Oxnard, California, United States

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Riverside, California, United States

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San Diego, California, United States

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West Hollywood, California, United States

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Westminster, California, United States

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Bristol, Connecticut, United States

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Norwalk, Connecticut, United States

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Clearwater, Florida, United States

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Gainesville, Florida, United States

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Lauderdale Lakes, Florida, United States

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Lauderdale Lakes, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Lakes, Florida, United States

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North Miami, Florida, United States

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South Miami, Florida, United States

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West Palm Beach, Florida, United States

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Winter Haven, Florida, United States

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Atlanta, Georgia, United States

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Augusta, Georgia, United States

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Savannah, Georgia, United States

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Thomasville, Georgia, United States

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Elk Grove Village, Illinois, United States

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Evergreen Park, Illinois, United States

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Hazel Crest, Illinois, United States

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Skokie, Illinois, United States

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Skokie, Illinois, United States

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Wichita, Kansas, United States

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Crestview Hills, Kentucky, United States

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Metairie, Louisiana, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Bethesda, Maryland, United States

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AMAG Pharmaceuticals, Inc.

Waltham, Massachusetts, United States

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Bay City, Michigan, United States

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Flint, Michigan, United States

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Saginaw, Michigan, United States

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Saginaw, Michigan, United States

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Chesterfield, Missouri, United States

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Kansas City, Missouri, United States

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Kirksville, Missouri, United States

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Las Vegas, Nevada, United States

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East Setauket, New York, United States

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Flushing, New York, United States

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New York, New York, United States

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Rosedale, New York, United States

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Asheville, North Carolina, United States

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Asheville, North Carolina, United States

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Charlotte, North Carolina, United States

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Greensboro, North Carolina, United States

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Hickory, North Carolina, United States

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Jacksonville, North Carolina, United States

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Morehead City, North Carolina, United States

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Raleigh, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cincinnati, Ohio, United States

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Cincinnati, Ohio, United States

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Marion, Ohio, United States

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Norman, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Tulsa, Oklahoma, United States

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Jenkintown, Pennsylvania, United States

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Levittown, Pennsylvania, United States

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Scottdale, Pennsylvania, United States

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Smithfield, Pennsylvania, United States

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Upland, Pennsylvania, United States

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Greenville, South Carolina, United States

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Greenville, South Carolina, United States

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Greer, South Carolina, United States

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Rapid City, South Dakota, United States

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Germantown, Tennessee, United States

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Kingsport, Tennessee, United States

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Memphis, Tennessee, United States

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Austin, Texas, United States

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Fort Sam Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Houston, Texas, United States

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Longview, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Schertz, Texas, United States

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Orem, Utah, United States

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Fredericksburg, Virginia, United States

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Norfolk, Virginia, United States

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Seattle, Washington, United States

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Sault Ste. Marie, Ontario, Canada

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Vaughan, Ontario, Canada

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Montreal, Quebec, Canada

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Budapest, , Hungary

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Debrecen, , Hungary

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Komárom, , Hungary

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Szekszárd, , Hungary

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Vác, , Hungary

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Jelgava, , Latvia

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Krāslava, , Latvia

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Liepāja, , Latvia

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Riga, , Latvia

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Riga, , Latvia

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Riga, , Latvia

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Ventspils, , Latvia

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Kaunas, , Lithuania

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Kaunas, , Lithuania

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Kaunas, , Lithuania

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Klaipėda, , Lithuania

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Šiauliai, , Lithuania

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Utena, , Lithuania

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Vilnius, , Lithuania

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Bialystok, , Poland

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Bialystok, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Ponce, , Puerto Rico

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Countries

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United States Canada Hungary Latvia Lithuania Poland Puerto Rico

References

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Adkinson NF, Strauss WE, Macdougall IC, Bernard KE, Auerbach M, Kaper RF, Chertow GM, Krop JS. Comparative safety of intravenous ferumoxytol versus ferric carboxymaltose in iron deficiency anemia: A randomized trial. Am J Hematol. 2018 May;93(5):683-690. doi: 10.1002/ajh.25060. Epub 2018 Feb 24.

Reference Type BACKGROUND
PMID: 29417614 (View on PubMed)

Adkinson NF, Strauss WE, Bernard K, Kaper RF, Macdougall IC, Krop JS. Comparative safety of intravenous Ferumoxytol versus Ferric Carboxymaltose for the Treatment of Iron Deficiency Anemia: rationale and study design of a randomized double-blind study with a focus on acute hypersensitivity reactions. J Blood Med. 2017 Sep 26;8:155-163. doi: 10.2147/JBM.S142236. eCollection 2017.

Reference Type BACKGROUND
PMID: 29033620 (View on PubMed)

Wolf M, Chertow GM, Macdougall IC, Kaper R, Krop J, Strauss W. Randomized trial of intravenous iron-induced hypophosphatemia. JCI Insight. 2018 Dec 6;3(23):e124486. doi: 10.1172/jci.insight.124486.

Reference Type DERIVED
PMID: 30518682 (View on PubMed)

Other Identifiers

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AMAG-FER-IDA-304

Identifier Type: -

Identifier Source: org_study_id

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