Phase 2 Study of Ruxolitinib Versus Anagrelide in Subjects With Essential Thrombocythemia Who Are Resistant to or Intolerant of Hydroxyurea (RESET-272)

NCT ID: NCT03123588

Last Updated: 2021-11-19

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

12 participants

Study Classification

INTERVENTIONAL

Study Start Date

2017-11-14

Study Completion Date

2020-08-03

Brief Summary

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The purpose of this study is to evaluate the efficacy and safety of ruxolitinib versus anagrelide in subjects with essential thrombocythemia who are resistant to or intolerant of hydroxyurea.

Detailed Description

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Conditions

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MPN (Myeloproliferative Neoplasms)

Keywords

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Essential thrombocythemia hydroxyurea-resistant hydroxyurea-intolerant ruxolitinib anagrelide

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Group A : Ruxolitinib and anagrelide placebo

Ruxolitinib or placebo will be administered orally twice a day at a starting dose of 10 mg.

Group Type EXPERIMENTAL

Ruxolitinib

Intervention Type DRUG

Ruxolitinib administered orally twice daily (BID) at the protocol-defined starting dose.

Placebo

Intervention Type DRUG

Anagrelide-placebo administered orally BID

Group B : Anagrelide and Ruxolitinib PLacebo

Anagrelide or placebo will be administered orally twice a day at a starting dose of 1 mg. Use of anagrelide will be consistent with approved prescribing information.

Group Type ACTIVE_COMPARATOR

Anagrelide

Intervention Type DRUG

Anagrelide administered orally at a starting dose of 1 mg BID.

Placebo

Intervention Type DRUG

Ruxolitinib-placebo administered orally BID.

Interventions

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Ruxolitinib

Ruxolitinib administered orally twice daily (BID) at the protocol-defined starting dose.

Intervention Type DRUG

Anagrelide

Anagrelide administered orally at a starting dose of 1 mg BID.

Intervention Type DRUG

Placebo

Anagrelide-placebo administered orally BID

Intervention Type DRUG

Placebo

Ruxolitinib-placebo administered orally BID.

Intervention Type DRUG

Other Intervention Names

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Jakafi INCB018424

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of essential thrombocythemia according to revised World Health Organization (WHO) 2016 criteria.
* Resistant to or intolerant of hydroxyurea, that is, fulfilling at least 1 of the following criteria:

* Platelet count \> 600 × 10\^9/L after 3 months of at least 2 g/day of hydroxyurea (2.5 g/day in subjects with a body weight over 80 kg) OR at the subject's maximally tolerated dose if that dose is \< 2 g/day.
* Platelet count \> 400 × 10\^9/L and WBC count \< 2.5 × 10\^9/L or hemoglobin \< 10 g/dL at any dose of hydroxyurea.
* Presence of leg ulcers or other unacceptable mucocutaneous manifestations at any dose of hydroxyurea.
* Hydroxyurea-related fever.
* Platelet count ≥ 650 × 10\^9/L at screening.
* WBC ≥ 11.0 × 10\^9/L at screening.

* Inadequate liver function at screening and Day 1 (before drug administration) as demonstrated by:

* Total bilirubin \> 1.5 × upper limit of normal (ULN)
* Aspartate aminotransferase or alanine aminotransferase \> 1.5 × ULN
* Hepatocellular disease (eg, cirrhosis)
* Inadequate renal function at screening as demonstrated by creatinine clearance \< 40 mL/min calculated by Cockcroft-Gault equation.

Exclusion Criteria

* Subjects previously treated with anagrelide or Hydroxyurea (HU).

1. Prior anagrelide use is allowed provided the reason for discontinuation is not AE-related and anagrelide is stopped at least 28 days before the start of study medications (ie, Day 1).
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Albert Assad, MD

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Mayo Clinic

Phoenix, Arizona, United States

Site Status

Pacific Shores Medical Group

Long Beach, California, United States

Site Status

University of Southern California

Los Angeles, California, United States

Site Status

Ventura County Hematology-Oncology Specialists

Oxnard, California, United States

Site Status

Compassionate Cancer Care Medical Group

Riverside, California, United States

Site Status

Innovative Clinical Research Institute

Whittier, California, United States

Site Status

Bond Clinic, PA

Winter Haven, Florida, United States

Site Status

Tift Regional

Tifton, Georgia, United States

Site Status

Edward Cancer Center

Naperville, Illinois, United States

Site Status

North Shore Cancer Research Association-Skokie

Skokie, Illinois, United States

Site Status

Southern Illinois University

Springfield, Illinois, United States

Site Status

Clinical Trials of SWLA LLC

Lake Charles, Louisiana, United States

Site Status

St. Agnes Hospital

Baltimore, Maryland, United States

Site Status

Washington University School of Medicine

St Louis, Missouri, United States

Site Status

Summit Medical Group

Morristown, New Jersey, United States

Site Status

Columbia Weill Cornell Cancer Centers - Herbert Irving Comprehensive Cancer Center (HICCC)

New York, New York, United States

Site Status

Montefiore Medical Center

The Bronx, New York, United States

Site Status

Waverly Hem Onc

Cary, North Carolina, United States

Site Status

Vidant Medical Center

Greenville, North Carolina, United States

Site Status

Gabrail Cancer Center- Canton Facility

Canton, Ohio, United States

Site Status

INTEGRIS Southwest Medical Center

Oklahoma City, Oklahoma, United States

Site Status

INTEGRIS Cancer Institute Proton Campus

Oklahoma City, Oklahoma, United States

Site Status

Kaiser Permanente Northwest

Portland, Oregon, United States

Site Status

Geisinger - Knapper Clinic

Danville, Pennsylvania, United States

Site Status

Prairie Lakes Health Care System Inc.

Watertown, South Dakota, United States

Site Status

Renovatio Clinical

The Woodlands, Texas, United States

Site Status

Countries

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United States

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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INCB 18424-272 (RESET-272)

Identifier Type: -

Identifier Source: org_study_id