Phase IIb Study of IFN-K in Systemic Lupus Erythematosus

NCT ID: NCT02665364

Last Updated: 2020-04-09

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE2

Total Enrollment

185 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-09-23

Study Completion Date

2020-02-04

Brief Summary

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The safety and immunogenicity of the IFNα-Kinoid (IFN-K) have been evaluated in a phase I clinical study conducted in subjects with Systemic Lupus Erythematosus (SLE). Preliminary results showed acceptable safety profile and patients developped antibodies response.

The principal aim of the present study is to confirm the neutralization of the interferon gene signature and the clinical efficacy of IFN-K in subjects with SLE. In addition, the immune responses and the safety elicited by IFN-K will also be evaluated.

Detailed Description

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Conditions

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Systemic Lupus Erythematosus

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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IFNα-Kinoid

IFNα-Kinoid (IFN-K) adjuvanted with ISA 51 VG via intramuscular injection. 1 administration of 240 μg at W0, W1, W4 and 1 administration of 120 μg at month 3 (W12) and month 6 (W24) in addition to standard of care treatment.

Group Type EXPERIMENTAL

IFNα-Kinoid

Intervention Type BIOLOGICAL

ISA 51 VG

Intervention Type OTHER

Placebo

Placebo normal saline (0.9% Sodium Chloride) adjuvanted with ISA 51 VG via intramuscular injection. 1 administration of 240 μg at week (W)0, W1, W4 and 1 administration of 120 μg at month 3 (W12) and month 6 (W24) in addition to standard of care treatment.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

ISA 51 VG

Intervention Type OTHER

Interventions

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IFNα-Kinoid

Intervention Type BIOLOGICAL

Placebo

Intervention Type OTHER

ISA 51 VG

Intervention Type OTHER

Eligibility Criteria

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Inclusion Criteria

* Has had a diagnosis of SLE according to current American College of Rheumatology (ACR) criteria (4 of 11 ACR criteria)
* Has SLEDAI-2K ≥ 6
* Has at least 1 BILAG A and/or at least 2 BILAG B
* Has a positive IFN gene signature by reverse transcription quantitative polymerase chain reaction (RT-qPCR)
* Has anti-nuclear antibodies (ANA) ≥ 1:160 and/or anti-dsDNA antibodies ≥ 7.0 IU/mL
* Currently receiving at least one treatment for SLE

Exclusion Criteria

* Has active, severe lupus nephritis as defined either by the immediate need for cyclophosphamide treatment or by renal BILAG A
* Has active, severe, neuropsychiatric SLE, defined as neuropsychiatric BILAG A
* Has been treated with corticosteroids (CS) at a dose of \>20 mg of prednisone equivalent/day for \> 7 consecutive days
* Is currently receiving or has received pulse dose CS (≥ 250 mg prednisone equivalent/day)
* Has received potent immunosuppressive drugs
* Has received abatacept, sifalimumab, rontalizumab, anifrolumab, belimumab, tumor necrosis factor (TNF) antagonists or another registered or investigational biological therapy
* Has received anti-B-cell therapy (e.g., rituximab, epratuzumab)
* Has frequent recurrences of oral or genital herpes simplex lesions
* Is at high risk of significant infection and/or has any current signs or symptoms of infection at entry or has received intravenous antibiotics
* Has received any live vaccine
* Has used any investigational or non-registered product or any investigational or non-registered vaccine
* Is high-risk human papilloma virus (HPV) positive by rRT-qPCR on a cervical swab
* Has cytological abnormalities ≥ high grade squamous intraepithelial lesions (HSIL) on a cervical swab
Minimum Eligible Age

18 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Neovacs

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Frédéric Houssiau, MD, PhD

Role: STUDY_CHAIR

Head of Rhumatology, UCL, Brussels, Belgium

Locations

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Little Rock, Arkansas, United States

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La Jolla, California, United States

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Los Angeles, California, United States

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Fort Lauderdale, Florida, United States

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Fort Myers, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Orlando, Florida, United States

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Tampa, Florida, United States

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Charlotte, North Carolina, United States

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Oklahoma City, Oklahoma, United States

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Austin, Texas, United States

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Buenos Aires, , Argentina

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Brussels, , Belgium

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Medellín, Antioquia, Colombia

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Barranquilla, , Colombia

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Bogotá, , Colombia

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Bogotá, , Colombia

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Bucaramanga, , Colombia

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Zipaquirá, , Colombia

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Zagreb, , Croatia

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Pessac, Bordeaux, France

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Lille, , France

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Marseille, , France

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Montpellier, , France

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Paris, , France

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Strasbourg, , France

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Tbilisi, , Georgia

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Bad Nauheim, , Germany

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Berlin, , Germany

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Hanover, , Germany

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Mainz, , Germany

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Munich, , Germany

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Rome, Roma, Italy

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Bologna, , Italy

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Milan, , Italy

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Pavia, , Italy

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Pisa, , Italy

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Verona, , Italy

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Cuernavaca, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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León, , Mexico

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México, , Mexico

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México, , Mexico

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Chisinau, , Moldova

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Chisinau, , Moldova

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Lima, , Peru

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Cebu, , Philippines

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Davao City, , Philippines

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Manila, , Philippines

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Quezon, , Philippines

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Bytom, , Poland

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Krakow, , Poland

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Poznan, , Poland

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Sosnowiec, , Poland

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Szczecin, , Poland

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Warsaw, , Poland

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Wroclaw, , Poland

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Chelyabinsk, , Russia

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Kemerovo, , Russia

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Kemerovo, , Russia

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Moscow, , Russia

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Omsk, , Russia

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Omsk, , Russia

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Orenburg, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saratov, , Russia

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Yekaterinburg, , Russia

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Seoul, , South Korea

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Seoul, , South Korea

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Lausanne, , Switzerland

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Taichung, , Taiwan

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Taichung, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Taipei, , Taiwan

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Bangkok, , Thailand

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Bangkok, , Thailand

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Sfax, , Tunisia

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Sousse, , Tunisia

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Sousse, , Tunisia

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Tunis, , Tunisia

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Tunis, , Tunisia

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Countries

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United States Argentina Belgium Chile Colombia Croatia France Georgia Germany Italy Mexico Moldova Peru Philippines Poland Russia South Korea Switzerland Taiwan Thailand Tunisia

References

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Hannon CW, McCourt C, Lima HC, Chen S, Bennett C. Interventions for cutaneous disease in systemic lupus erythematosus. Cochrane Database Syst Rev. 2021 Mar 9;3(3):CD007478. doi: 10.1002/14651858.CD007478.pub2.

Reference Type DERIVED
PMID: 33687069 (View on PubMed)

Houssiau FA, Thanou A, Mazur M, Ramiterre E, Gomez Mora DA, Misterska-Skora M, Perich-Campos RA, Smakotina SA, Cerpa Cruz S, Louzir B, Croughs T, Tee ML. IFN-alpha kinoid in systemic lupus erythematosus: results from a phase IIb, randomised, placebo-controlled study. Ann Rheum Dis. 2020 Mar;79(3):347-355. doi: 10.1136/annrheumdis-2019-216379. Epub 2019 Dec 23.

Reference Type DERIVED
PMID: 31871140 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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IFN-K-002

Identifier Type: -

Identifier Source: org_study_id

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