Sustained Effect of Droxidopa in Symptomatic Neurogenic Orthostatic Hypotension

NCT ID: NCT02586623

Last Updated: 2023-08-23

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

453 participants

Study Classification

INTERVENTIONAL

Study Start Date

2016-02-11

Study Completion Date

2022-09-09

Brief Summary

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To evaluate the time to treatment intervention in patients with Parkinson's Disease (PD), Multiple System Atrophy (MSA), Pure Autonomic Failure (PAF), Non-Diabetic Autonomic Neuropathy (NDAN) or Dopamine Beta Hydroxylase (DBH) Deficiency who have been previously stabilized with droxidopa therapy for symptoms of neurogenic orthostatic hypotension (NOH) (dizziness, light-headedness, or feelings that they are about to black out)

Detailed Description

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This is a multi-site, placebo-controlled, double-blind, randomized withdrawal, time to intervention study with a duration of up to 36 weeks, consisting of 5 periods:

Screening Period: up to 4 weeks duration; Open-Label Titration Period (Titration Period): up to 4 weeks duration; Open-Label Treatment Period (Open-Label Period): 12 weeks duration; Double-Blind Treatment Period (Double-Blind Period): 12 weeks duration; Safety Follow-Up Period: 4 weeks duration

Conditions

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Symptomatic Neurogenic Orthostatic Hypotension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Open Label Period

Active droxidopa 100, 200, 300, 400, 500, or 600 mg three times daily (TID) orally. During the Open Label Titration Period, patients will first receive 100 mg TID and their dose will be raised (in 100 mg increments) at subsequent visits until optimal dose is determined. During the Open Label Treatment Period, patients will receive active droxidopa100, 200, 300, 400, 500, or 600 mg three times daily (TID) orally (equal to the patient's individual dose at the end of the Open-Label Titration Period).

Group Type EXPERIMENTAL

Droxidopa capsules

Intervention Type DRUG

100, 200 or 300 mg

Randomized Period

Active droxidopa 100, 200, 300, 400, 500, or 600 mg three times daily (TID) orally (equal to patients individual dose at the end of the Open-Label Period) or matching placebo.

Group Type PLACEBO_COMPARATOR

Droxidopa capsules

Intervention Type DRUG

100, 200 or 300 mg

Placebo capsules

Intervention Type DRUG

Interventions

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Droxidopa capsules

100, 200 or 300 mg

Intervention Type DRUG

Placebo capsules

Intervention Type DRUG

Other Intervention Names

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Northera Placebo

Eligibility Criteria

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Inclusion Criteria

* 18 years or older and able to stand (with or without limited assistance)
* Clinical diagnosis of symptomatic orthostatic hypotension associated with Primary Autonomic Failure (PD, MSA or PAF) or NDAN or DBH Deficiency
* Score of at least 4 or greater on Orthostatic Hypotension Symptom Assessment (OHSA) Item #1 (measured at Screening \[Visit 1\] and the first Titration Visit \[Visit 2a\] prior to dosing)
* A documented drop of at least 20 millimeters of mercury (mmHg) in SBP, within 3 minutes of standing. This can either be documented in the patient history or assessed during Screening prior to the first Titration Visit (Visit 2a)
* Provide written informed consent to participate in the study and understand that they may withdraw their consent at any time without prejudice to their future medical care



* The patient's Visit 1 OHSA Item #1 score is ≥ 7 AND the prescribed dose is ≤ 300 mg three times daily (TID); OR
* The patient's Visit 1 OHSA Item #1 score is ≤6 AND worsens by ≥ 2 units when retested after washing out of droxidopa for at least 3 days

Exclusion Criteria

* In the investigator's opinion, the patient is not able to understand or cooperate with study procedures
* Known or suspected alcohol or substance use disorder within the past 12 months (DSM-5 criteria)
* Women who are pregnant or breastfeeding
* Women of childbearing potential (WOCP) who are not using at least one method of contraception with their partner
* Sustained supine hypertension greater than or equal to 180 mmHg systolic or 110 mmHg diastolic. Sustained is defined as the average of 3 observations each at least 10 minutes apart with the patient having been supine and at rest for at least 5 minutes prior to each measurement.
* Untreated closed angle glaucoma
* Diagnosis of hypertension that requires treatment with antihypertensive medications (short-acting antihypertensives to treat nocturnal supine hypertension are allowed in this study)
* Any significant uncontrolled cardiac arrhythmia
* History of myocardial infarction or stroke, within the past 2 years
* Current unstable angina
* Congestive heart failure (NYHA Class 3 or 4)
* Diabetic autonomic neuropathy
* History of cancer within the past 2 years other than a successfully treated, non-metastatic cutaneous squamous cell or basal cell carcinoma or cervical cancer in situ
* Any major surgical procedure within the past 30 days
* Currently receiving any investigational drug or have received an investigational drug within the past 28 days
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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H. Lundbeck A/S

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Email contact via H. Lundbeck A/S

Role: STUDY_DIRECTOR

[email protected]

Locations

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MDFirst Research - Chandler

Chandler, Arizona, United States

Site Status

21st Century Neurology

Phoenix, Arizona, United States

Site Status

Movement Disorders Center of Arizona

Scottsdale, Arizona, United States

Site Status

Center For Neurosciences

Tucson, Arizona, United States

Site Status

Movement Disorder Clinic - The University of Arizona

Tucson, Arizona, United States

Site Status

University of Arizona Health Sciences Center, Department Of Neurology

Tucson, Arizona, United States

Site Status

Arkansas Cardiology Clinic

Little Rock, Arkansas, United States

Site Status

East Bay Physicians Medical Group

Berkeley, California, United States

Site Status

Sutter East Bay Medical Foundation

Berkeley, California, United States

Site Status

The Parkinson's and Movement Disorder Institute

Fountain Valley, California, United States

Site Status

Behavioral Research Specialists, LLC

Glendale, California, United States

Site Status

Loma Linda University Medical Center

Loma Linda, California, United States

Site Status

University Of Southern California

Los Angeles, California, United States

Site Status

Parkinson's Institute and Clinical Center

Mountain View, California, United States

Site Status

Diverse Research Solutions, LLC

Oxnard, California, United States

Site Status

Focilmed

Oxnard, California, United States

Site Status

Parkinsons Disease & Movement Disorder of Silicon Valley

Palo Alto, California, United States

Site Status

Neurosearch, Inc. - Pasedena

Pasadena, California, United States

Site Status

Neurosearch, Inc. - Ventura

Pasadena, California, United States

Site Status

SC3 Research Group

Pasadena, California, United States

Site Status

Neurosearch, Inc. - Reseda

Reseda, California, United States

Site Status

Radiological Associates of Sacramento

Sacramento, California, United States

Site Status

Sutter Neuroscience

Sacramento, California, United States

Site Status

The Parkinson's Institute and Clinical Center

Sunnyvale, California, United States

Site Status

Neurosearch Inc. - Torrance

Torrance, California, United States

Site Status

Colorado Springs Neurological Associates

Colorado Springs, Colorado, United States

Site Status

Associated Neurologists, P.C.

Danbury, Connecticut, United States

Site Status

Associated Neurologists of Southern Connecticut, P.C.

Fairfield, Connecticut, United States

Site Status

Eastern Connecticut Neurology Specialists, LLC

Manchester, Connecticut, United States

Site Status

Yale-New Haven Hospital

New Haven, Connecticut, United States

Site Status

Yale Neurology / Hypertension Program

New Haven, Connecticut, United States

Site Status

Yale University School Of Medicine

New Haven, Connecticut, United States

Site Status

Christiana Care Neurology Specialists

Newark, Delaware, United States

Site Status

Georgetown University

Washington D.C., District of Columbia, United States

Site Status

MedStar Georgetown-MedStar Georgetown Transplant Institute University Hospital (MGUH)

Washington D.C., District of Columbia, United States

Site Status

Neurology Offices Of South Florida

Boca Raton, Florida, United States

Site Status

Parkinson's Disease And Movement Disorders Center of Boca Raton

Boca Raton, Florida, United States

Site Status

South Florida Neurology Associates, P.A.

Boca Raton, Florida, United States

Site Status

Innovative Research of West Florida

Clearwater, Florida, United States

Site Status

UF Center for Movement Disorders and Neurorestoration

Gainesville, Florida, United States

Site Status

Galiz Research

Hialeah, Florida, United States

Site Status

SIH Research

Kissimmee, Florida, United States

Site Status

Neurology Associates

Maitland, Florida, United States

Site Status

Future Clinical Research

Miami, Florida, United States

Site Status

Project 4 Research

Miami, Florida, United States

Site Status

Premium Medical Research, Corp

Miami, Florida, United States

Site Status

University Of Miami - Jackson Memorial Hospital, Dept. of Neurology

Miami, Florida, United States

Site Status

Coral Way Research

Miami, Florida, United States

Site Status

Florida Research Center

Miami, Florida, United States

Site Status

Anchor Medical Research, LLC

Miami, Florida, United States

Site Status

Novel Clinical Research Center, LLC

Miami, Florida, United States

Site Status

Pro-Care Research Center, Corporation

Miami Gardens, Florida, United States

Site Status

New Life Medical Research Center

Miami Lakes, Florida, United States

Site Status

Neurostudies, Inc.

Port Charlotte, Florida, United States

Site Status

Parkinson's Disease Treatment Center of Southwest Florida

Port Charlotte, Florida, United States

Site Status

Eminance Medical & Clinical Research

Tampa, Florida, United States

Site Status

University Of South Florida

Tampa, Florida, United States

Site Status

USF Parkinson's & Movement Disorders Center

Tampa, Florida, United States

Site Status

Vero Neurology

Vero Beach, Florida, United States

Site Status

Geodyssey Research, LLC

Vero Beach, Florida, United States

Site Status

Emory University

Atlanta, Georgia, United States

Site Status

Georgia Regents University

Augusta, Georgia, United States

Site Status

Neurological Center of North Georgia

Gainesville, Georgia, United States

Site Status

The Neurological Center of North Georgia

Gainesville, Georgia, United States

Site Status

Hawaii Pacific Neuroscience

Honolulu, Hawaii, United States

Site Status

Northwestern Medical Group

Chicago, Illinois, United States

Site Status

Cardio Specialists Group, Ltd., Rush University Medical Center

Chicago, Illinois, United States

Site Status

Rush University Medical Center - Department Of Cardiology

Chicago, Illinois, United States

Site Status

Rush University Medical Center, Department of Neurology

Chicago, Illinois, United States

Site Status

NorthShore Neurological Institute

Glenview, Illinois, United States

Site Status

Central Dupage Hospital

Winfield, Illinois, United States

Site Status

Northwestern Medicine Central DuPage Hospital

Winfield, Illinois, United States

Site Status

American Health Network of Indiana

Avon, Indiana, United States

Site Status

Fort Wayne Neurological Center

Fort Wayne, Indiana, United States

Site Status

Franciscan Physician Network Indiana Heart Physicians

Indianapolis, Indiana, United States

Site Status

Mid America Cardiology - University of Kansas

Kansas City, Kansas, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Louisiana Heart Center

Covington, Louisiana, United States

Site Status

Maine Medical Partners Technology

Scarborough, Maine, United States

Site Status

Mir Neurology

Hagerstown, Maryland, United States

Site Status

Tufts Medical Center

Boston, Massachusetts, United States

Site Status

Massachusetts General Hospital - Movement Disorders Clinic

Boston, Massachusetts, United States

Site Status

Movement Disorders Clinic

Boston, Massachusetts, United States

Site Status

Autonomic and Movement Disorders

Boston, Massachusetts, United States

Site Status

Brigham and Women's Faulkner Hospital (BWFH) - Brigham & Women's Foot & Ankle Center

Boston, Massachusetts, United States

Site Status

Michigan State University, Department of Neurology

East Lansing, Michigan, United States

Site Status

Detroit Clinical Research Center

Farmington Hills, Michigan, United States

Site Status

Michigan Center of Medical Research

Farmington Hills, Michigan, United States

Site Status

Northern Michigan Neurology

Traverse City, Michigan, United States

Site Status

Nothern Michigan Neurology

Traverse City, Michigan, United States

Site Status

Henry Ford West Bloomfield Hospital

West Bloomfield, Michigan, United States

Site Status

Platte Valley Medical Group

Kearney, Nebraska, United States

Site Status

Methodist Physicians Clinic - Heart Consultants

Omaha, Nebraska, United States

Site Status

MPC Heart Consultants

Omaha, Nebraska, United States

Site Status

University Of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

The Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, United States

Site Status

JFK Neuroscience Institution

Edison, New Jersey, United States

Site Status

Neuroscience Research Institute, LLC

Toms River, New Jersey, United States

Site Status

SUNY Downstate Medical Center

Brooklyn, New York, United States

Site Status

David L. Kreitzman MD, PC

Commack, New York, United States

Site Status

Office of David L. Kreitzman, M.D., P.C.

Commack, New York, United States

Site Status

Neurology Associates of West Chester

Hawthorne, New York, United States

Site Status

Parker Jewish Institute for Health Care & Rehabilitation

New Hyde Park, New York, United States

Site Status

Weill Cornell Medical College, Dept. of Neurology

New York, New York, United States

Site Status

The Bendheim Parkinson and Movement Disorders Center

New York, New York, United States

Site Status

Columbia University Medical Center

New York, New York, United States

Site Status

Project 4 Research, Inc., The Neurological Institute at Columbia University Medical Center

New York, New York, United States

Site Status

The Neurological Institute at Columbia University Medical Center

New York, New York, United States

Site Status

Parker Jewish Institute For Healthcare And Rehabilitation

New York, New York, United States

Site Status

Island Neurological Associates

Plainview, New York, United States

Site Status

Alpha Neurology

Staten Island, New York, United States

Site Status

Helen Hayes Hospital

West Haverstraw, New York, United States

Site Status

UBMD Neurology

Williamsville, New York, United States

Site Status

Peak Clinical Trials

Apex, North Carolina, United States

Site Status

The Neurological Institute, PA

Charlotte, North Carolina, United States

Site Status

Neurosciences Institute

Charlotte, North Carolina, United States

Site Status

Carolinas HealthCare System Neurosciences Institute

Charlotte, North Carolina, United States

Site Status

Insight Neuroscience, LLC

Bellevue, Ohio, United States

Site Status

Dayton Center for Neurological Disorders

Centerville, Ohio, United States

Site Status

Riverhills Healthcare, Inc.

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic - Taussig Cancer Institute

Cleveland, Ohio, United States

Site Status

Ohio Health Research Institute

Columbus, Ohio, United States

Site Status

Ohio State University, Department of Neurology

Columbus, Ohio, United States

Site Status

The Ohio State University

Columbus, Ohio, United States

Site Status

Gardner-McMaster Parkinson Center - The University of Toledo

Toledo, Ohio, United States

Site Status

Medical College of Ohio, Department of Neurology

Toledo, Ohio, United States

Site Status

Baha Abu-Esheh, MD

Ardmore, Oklahoma, United States

Site Status

CardioVoyage, LLC

Ardmore, Oklahoma, United States

Site Status

COR Clinical Research, LLC

Oklahoma City, Oklahoma, United States

Site Status

Legacy / Oregon Clinic Neurology

Portland, Oregon, United States

Site Status

The Oregon Clinic

Portland, Oregon, United States

Site Status

St. Luke's Neurology Associates

Bethlehem, Pennsylvania, United States

Site Status

Penn State Hershey Children's Hospital

Hershey, Pennsylvania, United States

Site Status

Penn State Milton S. Hershey Medical Center

Hershey, Pennsylvania, United States

Site Status

Drexel Neurosciences Institute

Philadelphia, Pennsylvania, United States

Site Status

University of Pennsylvania, Parkinson's Disease & Movement Disorders Center

Philadelphia, Pennsylvania, United States

Site Status

University of Pittsburgh, Department of Neurology

Pittsburgh, Pennsylvania, United States

Site Status

Dr. Umer Akbar MD, Office of

Providence, Rhode Island, United States

Site Status

Rhode Island Hospital

Providence, Rhode Island, United States

Site Status

Vanderbilt University Autonomic Dysfunction Center - Clinical Trials Center

Nashville, Tennessee, United States

Site Status

iMD Medical Center

Carrollton, Texas, United States

Site Status

Sunbeam Clinical Research

Carrollton, Texas, United States

Site Status

UT Southwestern Medical Center

Dallas, Texas, United States

Site Status

Elite Primary Care

Greenville, Texas, United States

Site Status

Sunbeam Clinical Research

Greenville, Texas, United States

Site Status

University of Texas Health Science Center at Houston

Houston, Texas, United States

Site Status

Texas Institute of Cardiology, The Heartbeat Clinic

McKinney, Texas, United States

Site Status

The Heartbeat Clinic

McKinney, Texas, United States

Site Status

Sunbeam Clinical Research, LLC.

Prosper, Texas, United States

Site Status

Central Texas Neurology Consultants

Round Rock, Texas, United States

Site Status

Christus Research Institute

Tyler, Texas, United States

Site Status

Clear Lake Specialties

Webster, Texas, United States

Site Status

Bateman Home Center

Salt Lake City, Utah, United States

Site Status

Inova Health Systems

Alexandria, Virginia, United States

Site Status

Integrated Neurology Services, PLLC

Falls Church, Virginia, United States

Site Status

Health Research of Hampton Roads-Norfolk, Inc

Norfolk, Virginia, United States

Site Status

Sentara Neurology Specialists

Norfolk, Virginia, United States

Site Status

Henrico Doctors Neurology Associates, LLC

Richmond, Virginia, United States

Site Status

Carilion Clinic

Roanoke, Virginia, United States

Site Status

Booth Gardner Parkinson's Care Center

Kirkland, Washington, United States

Site Status

Northwest Neurology, Premier Clinical Research

Spokane, Washington, United States

Site Status

Premeir Clinical Research

Spokane, Washington, United States

Site Status

Aurora Medical Center

Grafton, Wisconsin, United States

Site Status

Grafton Medical Office

Grafton, Wisconsin, United States

Site Status

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, United States

Site Status

Medical College of Wisconsin, Department of Neurology

Milwaukee, Wisconsin, United States

Site Status

Aurora Sinai Medical Center-Arrhythmia Center

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

References

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Hauser RA, Favit A, Hewitt LA, Lindsten A, Gorny S, Kymes S, Isaacson SH. Durability of the Clinical Benefit of Droxidopa for Neurogenic Orthostatic Hypotension During 12 Weeks of Open-Label Treatment. Neurol Ther. 2022 Mar;11(1):459-469. doi: 10.1007/s40120-021-00317-5. Epub 2022 Feb 2.

Reference Type DERIVED
PMID: 35107750 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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NOH402

Identifier Type: OTHER

Identifier Source: secondary_id

16306A

Identifier Type: -

Identifier Source: org_study_id

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