High-dose Chemotherapy and ASCT or Consolidating Conventional Chemotherapy in Primary CNS Lymphoma

NCT ID: NCT02531841

Last Updated: 2015-08-25

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

UNKNOWN

Clinical Phase

PHASE3

Total Enrollment

250 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-07-31

Study Completion Date

2019-12-31

Brief Summary

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In the presently planned multicentre Phase III trial the two therapies will be compared: Patients will be randomized after intensified induction treatment with 4 cycles rituximab, methotrexate, cytarabine and thiotepa (MATRix) between first-line high-dose chemotherapy against conventional consolidating therapy with 2 cycles of conventional chemotherapy with R-DeVIC (rituximab, dexamethasone, etoposide, ifosfamide, carboplatin).

Detailed Description

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Trial purpose and rationale Primary central nervous system lymphoma (PCNSL) is a highly aggressive disease with rising incidence over the past 30 years. Similar to other hematological diseases, the rationale for consolidation in PCNSL is the elimination of minimal residual disease. The efficacy of WBRT, which is the current standard for consolidation after HD-MTX-based systemic treatment, is being compared to HDT-ASCT in the ongoing IELSG-32 trial.

High-dose chemotherapy with carmustine or busulfan and thiotepa followed by autologous stem cell transplantation has been shown to be feasible and highly effective in newly diagnosed eligible patients, but also in the salvage situation.

The question we aim to answer is whether HDT-ASCT is superior to conventional therapy as consolidation after intensified immunochemotherapy in newly diagnosed PCNSL.

Rationale for this study:

Based on previously obtained good results from the treatment of recurrent or refractory PCNSL the DeVIC protocol was chosen for conventional consolidation treatment. This protocol, originally designed as a salvage protocol for aggressive NHL, crosses the blood-brain barrier and consists of multidrug resistant unrelated agents.

Treatment plan and procedure

Interventions

Induction treatment 4 cycles (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d 0,5)
* Methotrexate 3,5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4)

Patients with PD after two cycles, SD/PD after four cycles of induction therapy or insufficient stem-cell harvest after three cycles are ineligible for randomization.

Consolidation Arm A 2 cycles of R-DeVIC (every 3 weeks):

* Rituximab 375 mg/m²/d i.v. (d0)
* Dexamethasone 40 mg/d i.v. (d1-3)
* Etoposide 100 mg/m²/d i.v. (d1-3)
* Ifosfamide 1500 mg/m²/d i.v. (d1-3)
* Carboplatin 300 mg/m² i.v. (d1)

Consolidation Arm B

High-dose chemotherapy (HDT-ASCT):

* Carmustine\* 400 mg/m² i.v. (d-6)
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

\* if carmustine is not available at the investigation site, busulfan can be administered instead:
* Busulfan 3,2 mg/kg/d (d-8-(-7))
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

Conditions

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Diffuse Large B-cell-lymphoma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Arm A

Induction Treatment 4 cycles MATRix (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d0,5)
* Methotrexate 3.5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4)

Consolidation Treatment 2 cycles of R-DeVIC (every 3 weeks):

* Rituximab 375 mg/m²/d i.v. (d0)
* Dexamethasone 40 mg/d i.v. (d1-3)
* Etoposide 100 mg/m²/d i.v. (d1-3)
* Ifosfamide 1500 mg/m²/d i.v. (d1-3)
* Carboplatin 300 mg/m² i.v. (d1)

Group Type ACTIVE_COMPARATOR

Arm A (Fortecortin®-ETOPOPHOS®-IFO-cell®-CARBO-cell®)

Intervention Type DRUG

Arm A 4 cycles MATRix (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d0,5)
* Methotrexate 3.5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4) Consolidation 2 cycles of R-DeVIC (every 3 weeks):
* Rituximab 375 mg/m²/d i.v. (d0)
* Dexamethasone 40 mg/d i.v. (d1-3)
* Etoposide 100 mg/m²/d i.v. (d1-3)
* Ifosfamide 1500 mg/m²/d i.v. (d1-3)
* Carboplatin 300 mg/m² i.v. (d1)

Arm B

Induction Treatment 4 cycles MATRix (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d0,5)
* Methotrexate 3.5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4)

Consolidation Treatment High-dose chemotherapy

* Carmustine\* 400 mg/m² i.v. (d-6)
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

\*if not available at study site, Busulfan can be administered instead:
* Busulfan 3,2 mg/kg/d i.v. (d-8-(-7))
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

Group Type ACTIVE_COMPARATOR

Arm B (TEPADINA®-CARMUBRIS®-Busilvex®)

Intervention Type DRUG

4 cycles MATRix (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d0,5)
* Methotrexate 3.5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4) Consolidation

High-dose chemotherapy (HDT-ASCT):

* Carmustine\* 400 mg/m² i.v. (d-6)
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

\* if carmustine is not available at the investigation site, busulfan can be administered instead:
* Busulfan 3,2 mg/kg/d (d-8-(-7))
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

Interventions

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Arm A (Fortecortin®-ETOPOPHOS®-IFO-cell®-CARBO-cell®)

Arm A 4 cycles MATRix (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d0,5)
* Methotrexate 3.5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4) Consolidation 2 cycles of R-DeVIC (every 3 weeks):
* Rituximab 375 mg/m²/d i.v. (d0)
* Dexamethasone 40 mg/d i.v. (d1-3)
* Etoposide 100 mg/m²/d i.v. (d1-3)
* Ifosfamide 1500 mg/m²/d i.v. (d1-3)
* Carboplatin 300 mg/m² i.v. (d1)

Intervention Type DRUG

Arm B (TEPADINA®-CARMUBRIS®-Busilvex®)

4 cycles MATRix (every 3 weeks), stem-cell harvest after 2nd cycle:

* Rituximab 375 mg/m²/d i.v. (d0,5)
* Methotrexate 3.5 g/m² i.v. (d1)
* Cytarabine 2 x 2 g/m²/d i.v. (d2-3)
* Thiotepa 30 mg/m² i.v. (d4) Consolidation

High-dose chemotherapy (HDT-ASCT):

* Carmustine\* 400 mg/m² i.v. (d-6)
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

\* if carmustine is not available at the investigation site, busulfan can be administered instead:
* Busulfan 3,2 mg/kg/d (d-8-(-7))
* Thiotepa 2 x 5 mg/kg/d i.v. (d-5-(-4))
* Autologous Stem Cell Transplantation (d0)

Intervention Type DRUG

Other Intervention Names

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Fortecortin®-ETOPOPHOS®-IFO-cell®-CARBO-cell® TEPADINA®-CARMUBRIS®-Busilvex®

Eligibility Criteria

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Inclusion Criteria

1. Immunocompetent patients with newly-diagnosed primary central nervous system B-cell lymphoma
2. Age 18-65 years irrespective of ECOG or 66-70 years (with ECOG Performance Status ≤2)
3. Histologically or cytologically assessed diagnosis of B-cell lymphoma by local pathologist.
4. Diagnostic sample obtained by stereotactic or surgical biopsy, CSF cytology examination or vitrectomy
5. Disease exclusively located in the CNS
6. At least one measurable lesion
7. Previously untreated patients (previous or ongoing steroid treatment admitted)
8. Sexually active patients of childbearing potential who agree to take adequate contraceptive measures during study participation
9. Written informed consent obtained according to international guidelines and local laws by patient or authorized legal representative in case patient is temporarily legally not competent due to his or her disease

ADDITIONAL RANDOMIZATION CRITERIA

1. Sufficient stem cell harvest (≥ 5 x 106 CD34+ cells/kg of body weight)
2. Complete remission, unconfirmed complete remission or partial remission
3. Central pathology results confirming local results

Exclusion Criteria

1. Congenital or acquired immunodeficiency
2. Systemic lymphoma manifestation (outside the CNS)
3. Isolated ocular lymphoma without manifestation in the brain parenchyma or spinal cord
4. Previous or concurrent malignancies with the exception of surgically cured carcinoma in-situ of the cervix, carcinoma of the skin or other kinds of cancer without evidence of disease for at least 5 years
5. Previous Non-Hodgkin lymphoma at any time
6. Inadequate bone marrow (platelet count decreased ≥CTC grade 1, anemia ≥CTC grade 1, neutrophil count decreased ≥CTC grade 1), renal (creatinine clearance \<60 ml/min), cardiac (ejection fraction decreased ≥CTC grade 2), or hepatic function (blood bilirubin increased ≥CTC grade 2, alanine aminotransferase increased ≥CTC grade 2, aspartate aminotransferase increased ≥CTC grade 2 or gamma-GT increased ≥CTC grade 2)
7. HBsAg, anti-HBc or HCV positivity
8. HIV infection, previous organ transplantation or other clinical evident form of immunodeficiency
9. Concurrent treatment with other experimental drugs or participation in a clinical trial within the last thirty days before the start of this study
10. Symptomatic coronary artery disease, cardiac arrhythmias uncontrolled with medication or myocardial infarction within the last 6 months (New York Heart Association Class III or IV heart disease)
11. Severe non-compensated pulmonary disease (IVC \<55%, DLCO \<40%)
12. Third space fluid accumulation \>500 ml
13. Hypersensitivity to study treatment or any component of the formulation
14. Taking any medications likely to cause interactions with the study medication
15. Known or persistent abuse of medication, drugs or alcohol
16. Patient without legal capacity and who is unable to understand the nature, significance and consequences of the study and without designated legal representative
17. Persons who are in a relationship of dependency/employment to the sponsor and/ or investigator
18. Any familial, sociological or geographical condition potentially hampering compliance with the study protocol and follow-up schedule
19. Concurrent (or planned) pregnancy or lactation
20. Fertile patients refusing to use safe contraceptive methods during the study
Minimum Eligible Age

18 Years

Maximum Eligible Age

70 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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German Federal Ministry of Education and Research

OTHER_GOV

Sponsor Role collaborator

International Extranodal Lymphoma Study Group (IELSG)

OTHER

Sponsor Role collaborator

University Hospital Freiburg

OTHER

Sponsor Role lead

Responsible Party

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Elisabeth Schorb

Medical Trial Coordinator

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Gerald Illerhaus, PhD

Role: PRINCIPAL_INVESTIGATOR

Representative of Sponsor

Locations

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University Hospital Freiburg - Department for Hematology, Oncology and Stem cell Transplantion

Freiburg im Breisgau, Baden-Wurttemberg, Germany

Site Status RECRUITING

Klinikum Stuttgart, Clinic of Hematology, Oncology and Palliative Care, Stuttgart Cancer Center / Tumor Center Eva Mayr-Stihl

Stuttgart, Baden-Wurttemberg, Germany

Site Status RECRUITING

Countries

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Germany

Central Contacts

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Elisabeth Schorb, PhD

Role: CONTACT

0049761270 ext. 33210

Elvira Burger

Role: CONTACT

0049761270 ext. 73780

Facility Contacts

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Juergen Finke, PhD

Role: primary

+49761270 ext. 34080

Elisabeth Schorb, PhD

Role: backup

+49761270 ext. 33210

Gerald Illerhaus, PhD

Role: primary

+49 711 278 ext. 30400

Kristina Mikesch, PhD

Role: backup

+49 711 278 ext. 30403

References

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Illerhaus G, Marks R, Ihorst G, Guttenberger R, Ostertag C, Derigs G, Frickhofen N, Feuerhake F, Volk B, Finke J. High-dose chemotherapy with autologous stem-cell transplantation and hyperfractionated radiotherapy as first-line treatment of primary CNS lymphoma. J Clin Oncol. 2006 Aug 20;24(24):3865-70. doi: 10.1200/JCO.2006.06.2117. Epub 2006 Jul 24.

Reference Type RESULT
PMID: 16864853 (View on PubMed)

Illerhaus G, Muller F, Feuerhake F, Schafer AO, Ostertag C, Finke J. High-dose chemotherapy and autologous stem-cell transplantation without consolidating radiotherapy as first-line treatment for primary lymphoma of the central nervous system. Haematologica. 2008 Jan;93(1):147-8. doi: 10.3324/haematol.11771.

Reference Type RESULT
PMID: 18166803 (View on PubMed)

Kasenda B, Schorb E, Fritsch K, Finke J, Illerhaus G. Prognosis after high-dose chemotherapy followed by autologous stem-cell transplantation as first-line treatment in primary CNS lymphoma--a long-term follow-up study. Ann Oncol. 2012 Oct;23(10):2670-2675. doi: 10.1093/annonc/mds059. Epub 2012 Apr 3.

Reference Type RESULT
PMID: 22473593 (View on PubMed)

Soussain C, Hoang-Xuan K, Taillandier L, Fourme E, Choquet S, Witz F, Casasnovas O, Dupriez B, Souleau B, Taksin AL, Gisselbrecht C, Jaccard A, Omuro A, Sanson M, Janvier M, Kolb B, Zini JM, Leblond V; Societe Francaise de Greffe de Moelle Osseuse-Therapie Cellulaire. Intensive chemotherapy followed by hematopoietic stem-cell rescue for refractory and recurrent primary CNS and intraocular lymphoma: Societe Francaise de Greffe de Moelle Osseuse-Therapie Cellulaire. J Clin Oncol. 2008 May 20;26(15):2512-8. doi: 10.1200/JCO.2007.13.5533. Epub 2008 Apr 14.

Reference Type RESULT
PMID: 18413641 (View on PubMed)

Motomura K, Natsume A, Fujii M, Ito M, Momota H, Wakabayashi T. Long-term survival in patients with newly diagnosed primary central nervous system lymphoma treated with dexamethasone, etoposide, ifosfamide and carboplatin chemotherapy and whole-brain radiation therapy. Leuk Lymphoma. 2011 Nov;52(11):2069-75. doi: 10.3109/10428194.2011.596967. Epub 2011 Jul 12.

Reference Type RESULT
PMID: 21745167 (View on PubMed)

Schorb E, Finke J, Ferreri AJ, Ihorst G, Mikesch K, Kasenda B, Fritsch K, Fricker H, Burger E, Grishina O, Valk E, Zucca E, Illerhaus G. High-dose chemotherapy and autologous stem cell transplant compared with conventional chemotherapy for consolidation in newly diagnosed primary CNS lymphoma--a randomized phase III trial (MATRix). BMC Cancer. 2016 Apr 21;16:282. doi: 10.1186/s12885-016-2311-4.

Reference Type DERIVED
PMID: 27098429 (View on PubMed)

Other Identifiers

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DRKS00005503

Identifier Type: -

Identifier Source: org_study_id

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