A Registry for Adolescent and Pediatric Participants Who Received a Gilead Hepatitis C Virus Direct Acting Antiviral (DAA) in Gilead-Sponsored Chronic Hepatitis C Infection Trials

NCT ID: NCT02510300

Last Updated: 2023-01-27

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

TERMINATED

Total Enrollment

461 participants

Study Classification

OBSERVATIONAL

Study Start Date

2015-10-21

Study Completion Date

2023-01-06

Brief Summary

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This Registry will enroll adolescent and pediatric participants who received at least one Gilead Hepatitis C Virus (HCV) direct acting antiviral (DAA) while participating in a Gilead-sponsored chronic hepatitis C clinical trial. The primary objective of this Registry is to determine the long-term safety of anti-HCV regimens in the pediatric population. Secondary objectives of this Registry are to determine whether subsequent detection of HCV RNA in participants who relapse following sustained virologic response (SVR) represents the re-emergence of pre-existing virus, the development of resistance mutations, or whether it is due to re-infection, and to characterize resistance mutations and the persistence of resistance mutations in pediatric participants who did not achieve SVR. Once enrolled, participants will be followed for up to 5 years.

Detailed Description

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Conditions

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Hepatitis C Virus Infection

Study Design

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Observational Model Type

COHORT

Study Time Perspective

PROSPECTIVE

Interventions

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Sofosbuvir (SOF)

Exposure of interest for participants who received a SOF-based regimen in previous Gilead-sponsored chronic hepatitis C infection trials

Intervention Type DRUG

Ledipasvir/Sofosbuvir (LDV/SOF)

Exposure of interest for participants who received a LDV/SOF-based regimen in previous Gilead-sponsored chronic hepatitis C infection trials

Intervention Type DRUG

Sofosbuvir/Velpatasvir (SOF/VEL)

Exposure of interest for participants who received a SOF/VEL-based regimen in previous Gilead-sponsored chronic hepatitis C infection trials

Intervention Type DRUG

Sofosbuvir/Velpatasvir/Voxilaprevir (SOF/VEL/VOX)

Exposure of interest for participants who received a SOF/VEL/VOX-based regimen in previous Gilead-sponsored chronic hepatitis C infection trials

Intervention Type DRUG

Other Intervention Names

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Sovaldi® GS-7977 PSI-7977 Harvoni® GS-5885/GS-7977 Epclusa® GS-7977/GS-5816 Vosevi® GS-7977/GS-5816/GS-9857

Eligibility Criteria

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Inclusion Criteria

* Have previously participated in a Gilead-sponsored chronic hepatitis C study as an adolescent or pediatric participant and received at least one Gilead HCV direct acting antiviral
* Parent or legal guardian able to provide written informed consent OR individual is able to provide written informed consent prior to any study procedures and willing to comply with study requirements as determined by institutional review board (IRB)/independent ethics committee(IEC)/local requirements and Investigator's discretion.
* Individual is able to provide written assent, if they have the ability to read and write, as determined by IRB/IEC/local requirements and Investigator's discretion

Exclusion Criteria

* Individual is currently receiving or plans to initiate a new course of hepatitis C therapy including any investigational drug or device during the course of the follow-up Registry.
* History of clinically-significant illness or any other major medical disorder that may interfere with the individual's follow-up, assessments or compliance with the protocol.
Minimum Eligible Age

3 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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Phoenix Children's Hospital

Phoenix, Arizona, United States

Site Status

Children's Hospital Los Angeles, Div. of Research Immunology/BMT

Los Angeles, California, United States

Site Status

University of California San Francisco

San Francisco, California, United States

Site Status

Children's Hospital of Colorado

Aurora, Colorado, United States

Site Status

Children's National Medical Center

Washington D.C., District of Columbia, United States

Site Status

University of Florida

Gainesville, Florida, United States

Site Status

AdventHealth Orlando

Orlando, Florida, United States

Site Status

Children's Healthcare of Atlanta at Egleston

Atlanta, Georgia, United States

Site Status

Riley Hospital for Children

Indianapolis, Indiana, United States

Site Status

University of Louisville School of Medicine

Louisville, Kentucky, United States

Site Status

Johns Hopkins University School of Medicine

Baltimore, Maryland, United States

Site Status

Boston Children's Hospital

Boston, Massachusetts, United States

Site Status

Children's Mercy Hospital and Clinics

Kansas City, Missouri, United States

Site Status

Saint Louis University School of Medicine

St Louis, Missouri, United States

Site Status

University of Nebraska Medical Center

Omaha, Nebraska, United States

Site Status

Mount Sinai Medical Center

New York, New York, United States

Site Status

UNC Pediatrics/NC Children's Hospital

Chapel Hill, North Carolina, United States

Site Status

Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States

Site Status

Nationwide Children's Hospital

Columbus, Ohio, United States

Site Status

The Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Monroe Carell Jr. Children's Hospital at Vanderbilt

Nashville, Tennessee, United States

Site Status

Children's Medical Center Dallas

Dallas, Texas, United States

Site Status

Cook Children's Health Care System

Fort Worth, Texas, United States

Site Status

Texas Children's Hospital

Houston, Texas, United States

Site Status

Texas Liver Institute

San Antonio, Texas, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

West Virginia University Children's Hospital

Morgantown, West Virginia, United States

Site Status

John Hunter Children's Hospital (JHCH)

New Lambton Heights, New South Wales, Australia

Site Status

The Children's Hospital at Westmead

Westmead, New South Wales, Australia

Site Status

The Royal Children's Hospital

Parkville, Victoria, Australia

Site Status

Cliniques Universitaires Saint- LUC UCL

Brussels, , Belgium

Site Status

Charité Universitätsmedizin Berlin - Campus Virchow-Klinikum

Berlin, , Germany

Site Status

Helios Klinikum Wuppertal

Wuppertal, , Germany

Site Status

Ospedale Casa Sollievo della Sofferenza

San Giovanni Rotondo, Foggia, Italy

Site Status

Policlinico Sant'Orsola Malpighi

Bologna, , Italy

Site Status

Azienda Ospedaliero Universitaria - Ospedale Pediatrico Meyer

Florence, , Italy

Site Status

Polo Universitario - L'Azienda Ospedaliera Luigi Sacco

Milan, , Italy

Site Status

Azienda Ospedaliera Universitaria Federico II

Napoli, , Italy

Site Status

Azienda Ospedaliero-Universitaria di Padova

Padua, , Italy

Site Status

Azienda Ospedaliero-Universitaria Citta della Salute e della Scienza di Torino

Torino, , Italy

Site Status

Auckland Clinical Studies

Auckland, , New Zealand

Site Status

Wojewódzki Szpital Obserwacyjno-Zakaźny im. Tadeusza Browicza, Klinika Chorób Zakaźnych i Hepatologii Wieku Rozwojowego

Bydgoszcz, , Poland

Site Status

MED. POLONIA Sp. z.o.o.

Poznan, , Poland

Site Status

Federal Budget Institution of Science-Central Scientific and Research Institute of Epidemiology

Moscow, , Russia

Site Status

Federal Government Institution "Republican Clinical Infectious Hospital"

Saint Petersburg, , Russia

Site Status

Scientific-Research Institute of Children's Infections of Federal Medico- Biological Agency

Saint Petersburg, , Russia

Site Status

Ltd Medical Company "Hepatolog"

Tolyatti, , Russia

Site Status

Birmingham Childrens Hospital NHS Trust

Birmingham, , United Kingdom

Site Status

Royal Hospital for Sick Children Glasgow

Glasgow, , United Kingdom

Site Status

Leeds Teaching Hospitals NHS Trust

Leeds, , United Kingdom

Site Status

King's College Hospital

London, , United Kingdom

Site Status

Countries

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United States Australia Belgium Germany Italy New Zealand Poland Russia United Kingdom

References

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Gonzalez-Peralta RP, Wen JW, Hardikar W, Karnsakul WW, Whitworth S, Lin CH, Indolfi G, Rosenthal P, Balistreri W, Schwarz KB, Honegger JR, Zhang X, Svarovskaia EC, Suri V, Kersey K, Leung DH. Long-term efficacy and safety of sofosbuvir-based direct-acting antiviral regimens in paediatric patients with hepatitis C virus infection: an international registry study. Lancet Child Adolesc Health. 2025 Apr;9(4):248-254. doi: 10.1016/S2352-4642(25)00028-8.

Reference Type DERIVED
PMID: 40113366 (View on PubMed)

Related Links

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Other Identifiers

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2014-004674-42

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

GS-US-334-1113

Identifier Type: -

Identifier Source: org_study_id

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