PORtopulmonary Hypertension Treatment wIth maCitentan - a randOmized Clinical Trial

NCT ID: NCT02382016

Last Updated: 2025-03-30

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE4

Total Enrollment

85 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-06-23

Study Completion Date

2018-10-31

Brief Summary

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24-week study to evaluate the efficacy and safety of macitentan for the treatment of portopulmonary hypertension.

Detailed Description

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Conditions

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Portopulmonary Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Investigational treatment

Macitentan film-coated tablet 10 mg once daily.

Group Type EXPERIMENTAL

Macitentan

Intervention Type DRUG

Macitentan film-coated tablet 10 mg once daily.

Placebo

Matching placebo tablet once daily.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type OTHER

Matching placebo tablet once daily.

Interventions

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Macitentan

Macitentan film-coated tablet 10 mg once daily.

Intervention Type DRUG

Placebo

Matching placebo tablet once daily.

Intervention Type OTHER

Other Intervention Names

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ACT-064992

Eligibility Criteria

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Inclusion Criteria

* Male or female of at least 18 years of age
* Confirmed diagnosis of portopulmonary hypertension

Exclusion Criteria

* Severe hepatic impairment
* Severe obstructive or restrictive lung disease
* Pulmonary veno-occlusive disease
* Systolic blood pressure (SBP) \< 90 mmHg at Screening
* ALT/AST \>= 3 x ULN
* Bilirubin \>= 3 mg/dL at Screening
* Any known factor or disease that might interfere with treatment compliance, study conduct, or interpretation of results
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Actelion

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Loïc Perchenet, PhD

Role: STUDY_DIRECTOR

Actelion

Locations

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Mayo Clinic -Clinical Studies Unit

Phoenix, Arizona, United States

Site Status

UCSD

La Jolla, California, United States

Site Status

David Geffen School of Medicine, UCLA

Los Angeles, California, United States

Site Status

Keck School of Medicine

Los Angeles, California, United States

Site Status

UCSF

San Francisco, California, United States

Site Status

University of Colorado Health Sciences Center Aurora

Aurora, Colorado, United States

Site Status

University of Florida - Divison of Pulmonary Critical Care & Sleep

Gainesville, Florida, United States

Site Status

University of Florida College of Medicine

Jacksonville, Florida, United States

Site Status

Mayo Clinic Florida - Pulmonary Dept.

Jacksonville, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

South Miami Hospital

South Miami, Florida, United States

Site Status

Emory Healthcare

Atlanta, Georgia, United States

Site Status

Piedmont Healthcare

Austell, Georgia, United States

Site Status

Northwestern University

Chicago, Illinois, United States

Site Status

Indiana University

Indianapolis, Indiana, United States

Site Status

Kentuckiana Pulmonary Associates

Louisville, Kentucky, United States

Site Status

Boston University

Boston, Massachusetts, United States

Site Status

Henry Ford Hospital

Detroit, Michigan, United States

Site Status

Mayo Clinic

Rochester, Minnesota, United States

Site Status

University of New Mexico Health Science Center

Albuquerque, New Mexico, United States

Site Status

University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic - Department of Cardiovascular Medicine

Cleveland, Ohio, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

UPMC Montefiore

Pittsburgh, Pennsylvania, United States

Site Status

Baylor University Medical Center

Dallas, Texas, United States

Site Status

University of Texas Southwestern Medical Center Division of NeuroCritical Care 75390-8550

Dallas, Texas, United States

Site Status

Methodist Hospital

Houston, Texas, United States

Site Status

Methodist Hospital

San Antonio, Texas, United States

Site Status

University of Wisconsin-Madison

Madison, Wisconsin, United States

Site Status

Servico de Hipertensao Pulmonar - Complexo Hospitalar Santa Casa Irmandade Santa de Misericordia de Porto Alegre

Porto Alegre, , Brazil

Site Status

Hospital das Clinicas da Faculdade de Medicina da Universidade de Sao Paulo (HC-FMUSP)

São Paulo, , Brazil

Site Status

Lékařská fakulta a Všeobecná fakultní nemocnice v Praze, II. Interní klinika kardiologie a angiologie U

Prague, , Czechia

Site Status

IKEM (Institut klinické a experimentální medicíny, Institute for Clinical and Experimental Medicine)

Prague, , Czechia

Site Status

CHRU de Grenoble, Hôpital Albert Michallon

Grenoble, Auvergne-Rhône-Alpes, France

Site Status

CHRU Hôpital Cavale Blanche Brest

Brest, Brittany Region, France

Site Status

CHU Côte de Nacre, Service de Pneumologie

Caen, , France

Site Status

Hôpital cardiologique, Service de cardiologie 59037 Lille Cedex"

Lille, , France

Site Status

Hôpital Cardiologique et Pneumologique Louis Pradel 69677 Bron cedex"

Lyon, , France

Site Status

Hôpital Kremlin Bicêtre Service de Pneumologie

Paris, , France

Site Status

Hôpital Pontchaillou - CHU Rennes Service de Cardiologie et des Maladies Vasculaires Rennes Cedex 9 35033"

Rennes, , France

Site Status

CHU Rouen

Rouen, , France

Site Status

CHU Toulouse - Hôpital Larrey Hôpital de Jour et Semaine

Toulouse, , France

Site Status

Universitätsklinikum Carl Gustav Carus an der Technischen Universität Dresden

Dresden, , Germany

Site Status

Universitätsklinikum Giessen und Marburg GmbH Justus-Liebig Universität Giessen 35392

Giessen, , Germany

Site Status

Medizinische Hochschule Hannover, Abteilung Pneumologie

Hanover, , Germany

Site Status

Thoraxklinik des Universitätsklinikums Heidelberg Zentrum für pulmonale Hypertonie Studienkoordination

Heidelberg, , Germany

Site Status

Universitätsklinikum Leipzig, Department Innere Medizin, Abteilung Pneumologie

Leipzig, , Germany

Site Status

Hospital Clinico i Provincial Servicio de Neumología

Barcelona, , Spain

Site Status

Hospital Universitario12 Octubre

Madrid, , Spain

Site Status

NHS Greater Glasgow and Clyde Trust

Glasgow, Scotland, United Kingdom

Site Status

The Royal Free Hospital/ Cardiology Department

London, , United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust Royal Hallamshire Hospital

Sheffield, , United Kingdom

Site Status

Countries

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United States Brazil Czechia France Germany Spain United Kingdom

References

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Raevens S, Fallon MB. PORTICO: First Randomized Controlled Trial of Vasomodulator Therapy in Portopulmonary Hypertension. Hepatology. 2020 May;71(5):1870-1872. doi: 10.1002/hep.31166. No abstract available.

Reference Type DERIVED
PMID: 32031690 (View on PubMed)

Sitbon O, Bosch J, Cottreel E, Csonka D, de Groote P, Hoeper MM, Kim NH, Martin N, Savale L, Krowka M. Macitentan for the treatment of portopulmonary hypertension (PORTICO): a multicentre, randomised, double-blind, placebo-controlled, phase 4 trial. Lancet Respir Med. 2019 Jul;7(7):594-604. doi: 10.1016/S2213-2600(19)30091-8. Epub 2019 Jun 6.

Reference Type DERIVED
PMID: 31178422 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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AC-055-404

Identifier Type: -

Identifier Source: org_study_id

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