Phase 1 Pediatric Pharmacokinetics/Pharmacodynamics (PK/PD) Study

NCT ID: NCT02303431

Last Updated: 2023-10-11

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

66 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-11-05

Study Completion Date

2021-09-16

Brief Summary

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This is the first evaluation of edoxaban in pediatric subjects. In this Phase 1 study, a single dose of edoxaban will be given to pediatric subjects who require anticoagulant therapy to see what the body does to the drug (pharmacokinetics) and what the drug does to the body (pharmacodynamics), and to compare if these effects are similar to those observed in adults.

Detailed Description

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Phase 1, open-label, multiple-center study in pediatric patients from 0 to \< 18 years of age. Patients will receive a single dose of edoxaban to match either the 30 mg (low dose) or the 60 mg (high dose) exposure in adults. Exact doses will be selected during the study on the basis of PK modeling of emerging data. If unanticipated exposures are observed, the target doses may be modified to best match expected exposure response relationships observed in adults.

Enrollment in the study will start with the low dose, highest age group (adolescents) and will continue from low to high dose in each age group and from higher to lower age groups. Enrollment in the next dose/age cohort will begin after 50% of the subjects have completed the previous dose/age cohort.

Age cohorts and dose groups: (6 participants each in low and high dose groups, for a total of 12 participants per age cohort)

* 12 to \< 18 years of age
* 6 to \<12 years of age
* 2 to \<6 years of age
* 6 months to \<2 years of age
* 0 to \<6 months of age

Conditions

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Deep Vein Thrombosis Venous Thromboembolism

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

SINGLE_GROUP

Primary Study Purpose

BASIC_SCIENCE

Blinding Strategy

NONE

Study Groups

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Cohort 1a

12 to \< 18 years of age: edoxaban low dose group

Group Type EXPERIMENTAL

Edoxaban low dose

Intervention Type DRUG

Edoxaban low dose

Cohort 1b

12 to \< 18 years of age: edoxaban high dose group

Group Type EXPERIMENTAL

Edoxaban high dose

Intervention Type DRUG

Edoxaban high dose

Cohort 2a

6 to \< 12 years of age: edoxaban low dose group

Group Type EXPERIMENTAL

Edoxaban low dose

Intervention Type DRUG

Edoxaban low dose

Cohort 2b

6 to \< 12 years of age: edoxaban high dose group

Group Type EXPERIMENTAL

Edoxaban high dose

Intervention Type DRUG

Edoxaban high dose

Cohort 3a

2 to \< 6 years of age: edoxaban low dose group

Group Type EXPERIMENTAL

Edoxaban low dose

Intervention Type DRUG

Edoxaban low dose

Cohort 3b

2 to \< 6 years of age: edoxaban high dose group

Group Type EXPERIMENTAL

Edoxaban high dose

Intervention Type DRUG

Edoxaban high dose

Cohort 4a

6 months to \<2 years of age: edoxaban low dose group

Group Type EXPERIMENTAL

Edoxaban low dose

Intervention Type DRUG

Edoxaban low dose

Cohort 4b

6 months to \<2 years of age: edoxaban high dose group

Group Type EXPERIMENTAL

Edoxaban high dose

Intervention Type DRUG

Edoxaban high dose

Cohort 5a

0 to 6 months of age: edoxaban low dose group

Group Type EXPERIMENTAL

Edoxaban low dose

Intervention Type DRUG

Edoxaban low dose

Cohort 5b

0 to 6 months: edoxaban high dose group

Group Type EXPERIMENTAL

Edoxaban high dose

Intervention Type DRUG

Edoxaban high dose

Interventions

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Edoxaban low dose

Edoxaban low dose

Intervention Type DRUG

Edoxaban high dose

Edoxaban high dose

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Is a pediatric subject requiring anticoagulant therapy
* Will abstain from the use of nonsteroidal anti-inflammatory drugs (such as ibuprofen), and other antiplatelet and anticoagulant agents (except for aspirin) from 24 hours prior to edoxaban dose until after the last PK sample is collected
* Will follow food and concomitant medication restrictions

Exclusion Criteria

* Any major or clinically relevant unexplained bleeding during prior anticoagulant therapy
* History of abnormal bleeding or coagulation within last 6 months prior to study drug administration
* Renal function with glomerular filtration rate (GFR) less than 50% of normal for age and size
* Malabsorption disorders (e.g., cystic fibrosis or short bowel syndrome)
* Hepatic disease associated with coagulopathy leading to a clinically relevant bleeding risk, alanine transaminase (ALT) \> 5 times the upper limit of normal (ULN) or total bilirubin \> 2 times the ULN with direct bilirubin \> 20% of the total
Minimum Eligible Age

0 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Daiichi Sankyo

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Global Clinical Leader

Role: STUDY_DIRECTOR

Daiichi Sankyo

Locations

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University of California, Los Angeles (UCLA)

Los Angeles, California, United States

Site Status

Lucile Packard Children's Hospital Stanford University

Palo Alto, California, United States

Site Status

University of Colorado Denver

Denver, Colorado, United States

Site Status

Ann and Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States

Site Status

Indiana Hemophilia and Thrombosis Center

Indianapolis, Indiana, United States

Site Status

University of Louisville ; Kosair Charities Pediatric Clincial Research Unit

Louisville, Kentucky, United States

Site Status

Duke University Medical Center (DUMC)

Durham, North Carolina, United States

Site Status

University Hospitals Case Medical Center - Rainbow Babies and Children's Hospital

Cleveland, Ohio, United States

Site Status

The Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States

Site Status

Hasbro Children's Hospital

Providence, Rhode Island, United States

Site Status

St. Jude Children's Research Hospital, Inc.

Memphis, Tennessee, United States

Site Status

Children's Hospital of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

McMaster Children's Hospital

Hamilton, Ontario, Canada

Site Status

Childrens Hospital of Eastern Ontario

Ottawa, , Canada

Site Status

Hopital Arnaud de Villeneuve

Montpellier, , France

Site Status

CHU Bordeaux - Hopital Haut-Leveque

Pessac, , France

Site Status

Nirmal Hospital Pvt. Ltd

Gujrāt, , India

Site Status

Institute of Child Health

Kolkata, , India

Site Status

Christian Medical College and Hospital

Ludhiāna, , India

Site Status

Istituto Giannina Gaslini - UOSD Emostasi e Trombosi

Genova, , Italy

Site Status

A O Universita degli Studi di Padova ; Dipartimento di Salute della Donna e del Bambino-Universita di Padova

Padua, , Italy

Site Status

Bambino Gesu Hospital

Rome, , Italy

Site Status

Hotel Dieu De France

Beirut, , Lebanon

Site Status

Hammoud Hospital University Medical Center

Saida, , Lebanon

Site Status

Hospital Universitario Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario Reina Sofia

Córdoba, , Spain

Site Status

Hospital Clinico San Carlos

Madrid, , Spain

Site Status

Hospital Universitario La Paz

Madrid, , Spain

Site Status

Hospital Universitario Araba

Vitoria-Gasteiz, , Spain

Site Status

Ege University Medical Faculty - Department of Pediatric Hematology

Izmir, , Turkey (Türkiye)

Site Status

Leeds General Infirmary

Leeds, , United Kingdom

Site Status

Glenfield Hospital

Leicester, , United Kingdom

Site Status

Guy's and St Thomas Hospital NHS Trust

London, , United Kingdom

Site Status

Royal Brompton Hospital

London, , United Kingdom

Site Status

Southampton General Hospital

Southampton, , United Kingdom

Site Status

Countries

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United States Canada France India Italy Lebanon Spain Turkey (Türkiye) United Kingdom

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Other Identifiers

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2015-005732-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

DU176b-A-U157

Identifier Type: -

Identifier Source: org_study_id

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