Open-Label Study of Leuco-methylthioninium Bis(Hydromethanesulfonate) (LMTM) in Subjects With Alzheimer's Disease or Behavioral Variant Frontotemporal Dementia (bvFTD)

NCT ID: NCT02245568

Last Updated: 2023-05-24

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

913 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-08-31

Study Completion Date

2017-05-31

Brief Summary

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The purpose of this study is to provide subjects who have completed participation in a Phase 2 or Phase 3 trial of LMTM continued access to therapy and to evaluate the long-term safety of LMTM.

Detailed Description

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Conditions

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Alzheimer's Disease Behavioral Variant Frontotemporal Dementia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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LMTM

Group Type EXPERIMENTAL

LMTM

Intervention Type DRUG

The initial LMTM dose was 200 mg/day (one 100-mg tablet twice daily), except in subjects with bvFTD who were taking a reduced dose (i.e., 100 mg/day) upon entering this extension study. The dose could be increased (after at least 13 weeks of treatment) or decreased (at any time at or after 2 weeks of treatment) by the Investigator in 100-mg increments or decrements. The maximum allowable dose was 300 mg/day (or in those countries where limited by a Competent Authority or Ethics Committee, 200 mg/day).

Interventions

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LMTM

The initial LMTM dose was 200 mg/day (one 100-mg tablet twice daily), except in subjects with bvFTD who were taking a reduced dose (i.e., 100 mg/day) upon entering this extension study. The dose could be increased (after at least 13 weeks of treatment) or decreased (at any time at or after 2 weeks of treatment) by the Investigator in 100-mg increments or decrements. The maximum allowable dose was 300 mg/day (or in those countries where limited by a Competent Authority or Ethics Committee, 200 mg/day).

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Subjects with all cause dementia and probable Alzheimer's disease at enrollment and who completed participation in one of the following three TauRx studies (inclusive of the 4-week post-treatment follow-up visit): TRx-237-005, TRx-237-008, or TRx-237-015.
* Subjects with a diagnosis of probable bvFTD at enrollment and who completed participation in TauRx study TRx-237-007 through Visit 9 (Week 52).
* Females, if of child-bearing potential, must practice true abstinence or continue to use adequate contraception and agree to maintain this throughout the study
* Subject, and/or, in the case of reduced decision-making capacity, legally acceptable representative(s) consistent with national law and ethics approval is/are able to read, understand, and provide written informed consent
* Has an identified adult caregiver who is willing to provide written informed consent for his/her own participation; is able to read, understand, and speak the designated language at the study site; either lives with the subject or sees the subject for ≥1 hour/day ≥3 days/week; agrees to accompany the subject to each study visit; and is able to verify daily compliance with study drug
* Able to comply with the study procedures

Exclusion Criteria

* History of swallowing difficulties
* Pregnant or breastfeeding
* Clinically significant laboratory, pulse co-oximetry, electrocardiogram, or imaging abnormality (in originating study) or emergent intercurrent illness that, in the judgment of the principal investigator, could result in the risk of participation outweighing the potential benefit
* Current participation in, or intent to enroll in, another clinical trial of a drug, biologic, device, or medical food
* In Germany, subjects mandated to reside in a continuous care or assisted living facility or those whose willingness to participate in the clinical trial may be unduly influenced
Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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TauRx Therapeutics Ltd

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Locations

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Xenoscience, Inc / 21st Century Neurology

Phoenix, Arizona, United States

Site Status

Southern California Research, LLC

Fountain Valley, California, United States

Site Status

Feldman, Robert MD

Laguna Hills, California, United States

Site Status

Collaborative Neuroscience Network

Long Beach, California, United States

Site Status

The Shankle Clinic

Newport Beach, California, United States

Site Status

Neuro-Therapeutics, Inc.

Pasadena, California, United States

Site Status

Pacific Research Network

San Diego, California, United States

Site Status

San Francisco Clinical Research Center

San Francisco, California, United States

Site Status

Memory and Aging Centre

San Francisco, California, United States

Site Status

Schuster Medical Research Institute

Sherman Oaks, California, United States

Site Status

Mile High Research Center

Denver, Colorado, United States

Site Status

Institute for Neurodegenerative Disorders

New Haven, Connecticut, United States

Site Status

Yale University School of Medicine

New Haven, Connecticut, United States

Site Status

Coastal Connecticut Research, LLC

New London, Connecticut, United States

Site Status

JEM Research

Atlantis, Florida, United States

Site Status

Bradenton Research Center

Bradenton, Florida, United States

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Meridien Research

Brooksville, Florida, United States

Site Status

Brain Matters Research

Delray Beach, Florida, United States

Site Status

MD Clinical

Hallandale, Florida, United States

Site Status

Mayo Clinic

Jacksonville, Florida, United States

Site Status

CNS Healthcare, Inc

Jacksonville, Florida, United States

Site Status

Miami Research Associates

Miami, Florida, United States

Site Status

Compass Research, LLC

Orlando, Florida, United States

Site Status

The Roskamp Institute, Inc.

Sarasota, Florida, United States

Site Status

Axiom Clinical Research of Florida

Tampa, Florida, United States

Site Status

University of South Florida

Tampa, Florida, United States

Site Status

Compass Research, LLC - North Clinic

The Villages, Florida, United States

Site Status

iResearch Atlanta

Decatur, Georgia, United States

Site Status

Neurostudies.net

Decatur, Georgia, United States

Site Status

Alexian Brothers Neurosciences Institute

Elk Grove Village, Illinois, United States

Site Status

Ruan Neurology Clinic and Research Center

Des Moines, Iowa, United States

Site Status

ActivMed Practices & Research

Methuen, Massachusetts, United States

Site Status

Mayo Clinic, Alzheimer's Disease Research Center

Rochester, Minnesota, United States

Site Status

Neurological Research Center - Hattiesburg Clinic

Hattiesburg, Mississippi, United States

Site Status

Millennium Psychiatric Associates

Creve Coeur, Missouri, United States

Site Status

Memory Enhancement Center of America, Inc

Eatontown, New Jersey, United States

Site Status

The Atlantic Neuroscience Institute

Springfield, New Jersey, United States

Site Status

Advanced Memory Research Institute of NJ PC

Toms River, New Jersey, United States

Site Status

Neurological Associates of Albany, P. C.

Albany, New York, United States

Site Status

SPRI

Brooklyn, New York, United States

Site Status

Columbia University Taub Institute

New York, New York, United States

Site Status

Research Foundation for Mental Hygiene, Inc.

Orangeburg, New York, United States

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UNC Department of Neurology, Physicians Office Building

Chapel Hill, North Carolina, United States

Site Status

Clinical Trials of America, Inc

Winston-Salem, North Carolina, United States

Site Status

Neurobehavioral Clinical Research

Canton, Ohio, United States

Site Status

University Hospitals Case Medical Center, Neurology Clinical Trials Unit

Cleveland, Ohio, United States

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Rivus Wellness and Research Institute

Oklahoma City, Oklahoma, United States

Site Status

The Clinical Trial Center, LLC

Jenkintown, Pennsylvania, United States

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Hospital of the University of Pennsylvania, Department of Neurology

Philadelphia, Pennsylvania, United States

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RI Hospital

Providence, Rhode Island, United States

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Neurology Clinic, P.C.

Cordova, Tennessee, United States

Site Status

Clinical Neuroscience Solutions CNS Healthcare

Memphis, Tennessee, United States

Site Status

FutureSearch Trials of Neurology

Austin, Texas, United States

Site Status

Senior Adults Specialty Research, Inc.

Austin, Texas, United States

Site Status

FutureSearch Trials of Dallas, LP

Dallas, Texas, United States

Site Status

University of Virginia Adult Neurology, Primary Care Center

Charlottesville, Virginia, United States

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Independent Psychiatric Consultants

Waukesha, Wisconsin, United States

Site Status

Frontotemporal Research Group

Camperdown, New South Wales, Australia

Site Status

Division of Rehabilitation and Aged Care

Hornsby, New South Wales, Australia

Site Status

Southern Neurology Pty Limited

Kogarah, New South Wales, Australia

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Discipline of Psychiatry, University of Queensland

Herston, Queensland, Australia

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Royal Adelaide Hospital Memory Trials Centre

Adelaide, South Australia, Australia

Site Status

Box Hill Hospital

Box Hill, Victoria, Australia

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Medical and Cognitive Research Unit, Austin Health Heidelberg Repatriation Hospital

Heidelberg West, Victoria, Australia

Site Status

McCusker Alzheimer's Research Foundation Inc

Nedlands, Western Australia, Australia

Site Status

Neurodegenerative Disorders Research Pty Ltd

Subiaco, Western Australia, Australia

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University Hospital Ghent Department of Neurology

Ghent, , Belgium

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Jessa Hospital

Hasselt, , Belgium

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GZA Sint-Augustinus

Wilrijk, , Belgium

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Heritage Medical Research Clinic

Calgary, Alberta, Canada

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Okanagan Clinical Trials

Kelowna, British Columbia, Canada

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University of British Columbia Hospital, Clinic for Alzheimer Disease and Related Disorders

Vancouver, British Columbia, Canada

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Vancouver Island Health Authority

Victoria, British Columbia, Canada

Site Status

True North Clinical Research Halifax Inc

Halifax, Nova Scotia, Canada

Site Status

True North Clinical Research Kentville Inc

Kentville, Nova Scotia, Canada

Site Status

Geriatric Clinical Trials Group, St. Joseph's Health Care, Parkwood Hospital Site

London, Ontario, Canada

Site Status

Toronto Memory Program

Toronto, Ontario, Canada

Site Status

Jewish General Hospital

Montreal, Quebec, Canada

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McGill Centre for Studies in Aging, Alzheimer Disease Research Unit

Verdun, Quebec, Canada

Site Status

University Hospital Centre Zagreb, Department of Neurology

Zagreb, , Croatia

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University Psychiatric Hospital Vrapče

Zagreb, , Croatia

Site Status

University of Eastern Finland, Brain Research Unit Mediteknia

Kuopio, , Finland

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Clinical Research Services Turku (CRST)

Turku, , Finland

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Hôpitaux Civils de Colmar

Colmar, Cedex, France

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Centre de Recherche Clinique

Toulouse, , France

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Hôpital de Charpennes

Villeurbanne, , France

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Charité, University Medicine Berlin, CBF, Neurology

Berlin, , Germany

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Arzeneimittelforschung Leipzig GmbH

Leipzig, , Germany

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University Kuala Lumpur Royal College of Medicine

Ipoh, , Malaysia

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Hospital Sultan Ismail

Johor Bahru, , Malaysia

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University Malaya Medical Centre

Kuala Lumpur, , Malaysia

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Erasmus University Medical Center

Rotterdam, , Netherlands

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Psychiatry Hospital "Dr. Gheorghe Preda", Department of Psychiatry III

Sibiu, , Romania

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Non-governmental Healthcare Institution "Central Clinical Hospital #6 of the JSC "Russian Railways"

Moscow, , Russia

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Mental Health Research Center of the Russian Academy of Medical Sciences, Gerontopsychiatry department

Moscow, , Russia

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Mental Health Research Center of the Russian Academy of Medical Sciences

Moscow, , Russia

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City Clinical Hospital #34, City Scientific Practical Neurological Center

Novosibirsk, , Russia

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City Geriatric Medical and Social Center

Saint Petersburg, , Russia

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Saint Petersburg Psychoneurological Research Institute n. a. V.M. Bekhterev

Saint Petersburg, , Russia

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State Budgetary Healthcare Institution of Sverdlovsk region "Sverdlovsk Regional Clinical Psychiatric Hospital"

Yekaterinburg, , Russia

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National University Hospital (NUH)

Singapore, , Singapore

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National Neuroscience Institute (NNI)

Singapore, , Singapore

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Dong-A University Hospital

Busan, , South Korea

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Gachon University Gil Medical Center

Incheon, , South Korea

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Samsung Medical Center

Seoul, , South Korea

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Seoul National University Boramae Medical Center

Seoul, , South Korea

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Seoul National University Hospital

Seoul, , South Korea

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Fundació ACE

Barcelona, , Spain

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Hospital Clinico San Carlos

Madrid, , Spain

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Hospital Universitario La Paz

Madrid, , Spain

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Hospital Viamed Montecanal

Zaragoza, , Spain

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Chang Gung Memorial Hospital, Kaohsiung

Kaohsiung City, , Taiwan

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China Medical University Hospital

Taichung, , Taiwan

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National Taiwan University Hospital

Taipei, , Taiwan

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Taipei Veterans General Hospital

Taipei, , Taiwan

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Chang Gung Memorial Hospital, Linkou

Taoyuan District, , Taiwan

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Grampian NHS, Royal Cornhill Hospital

Aberdeen, , United Kingdom

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RICE - The Research Institute for the Care of Older People

Bath, , United Kingdom

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Belfast Health and Social Care Trust (BHSCT)

Belfast, , United Kingdom

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The Barberry Centre

Birmingham, , United Kingdom

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MAC Clinical Research Ltd

Blackpool, , United Kingdom

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MAC Clinical Research Ltd

Cannock, , United Kingdom

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Sussex Partnership NHS Foundation Trust, Cognitive Treatment and Research Unit

Crowborough, , United Kingdom

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St Margaret's Hospital Mental Health Unit

Epping, , United Kingdom

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Cognition Health Ltd

Guildford, , United Kingdom

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MAC Clinical Research Ltd

Leeds, , United Kingdom

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Cognition Health Ltd.

London, , United Kingdom

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Imperial College Healthcare NHS Trust - Charing Cross Hospital

London, , United Kingdom

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Leonard Wolfson Experimental Neurology Centre

London, , United Kingdom

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MAC Clinical Research Ltd

Manchester, , United Kingdom

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Nuffield Department of Clinical Neurosciences

Oxford, , United Kingdom

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Redwoods Centre

Shrewsbury, , United Kingdom

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Wessex Neurological Centre, Southampton General Hospital

Southampton, , United Kingdom

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Memory Assessment and Research Centre (MARC)

Southampton, , United Kingdom

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Kingshill Research Centre, Victoria Hospital

Swindon, , United Kingdom

Site Status

Countries

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United States Australia Belgium Canada Croatia Finland France Germany Malaysia Netherlands Romania Russia Singapore South Korea Spain Taiwan United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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TRx-237-020

Identifier Type: -

Identifier Source: org_study_id

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