Trial Outcomes & Findings for Adherence in Pediatric Multiple Sclerosis (NCT NCT02234713)

NCT ID: NCT02234713

Last Updated: 2020-01-18

Results Overview

Objective measures included: (A) pharmacy refill data provided by site coordinators for 12 months prior to study entry and for 6 months post-study entry and (B) the MEMS cap, an EM device (MEMS, AARDEX) that captures each time the patient discards a needle from their injection or opens their pill bottle. Adherence information from MEMS caps is downloaded and stored on a secured web-platform (medAmigo™). These data were used to compile drug-dosing history data and to calculate medication adherence during the course of the study.

Recruitment status

COMPLETED

Study phase

NA

Target enrollment

71 participants

Primary outcome timeframe

Baseline, 3 months, 6 months

Results posted on

2020-01-18

Participant Flow

Participants were assigned to a study arm after completion of the enrollment visit. Thus, any participants who consented but did not complete the enrollment visit were not assigned to a study arm.

Participant milestones

Participant milestones
Measure
Behavioural Intervention/Feedback
The behavioral interventionist will contact the patient and parent by email and telephone to schedule a telephone call to review the downloaded adherence information and discuss barriers experienced by the patient/parent using a standard script. The behavioral feedback will be administered three times: at 1-, 2- and 3-months post-baseline. Motivational Interview
Video Attention Control
The patients in this arm of the study will be emailed a link to an educational video about Pediatric MS and therapy for MS at three time points: 1-, 2-, and 3-months post-baseline. Video Attention Control
Overall Study
STARTED
31
32
Overall Study
COMPLETED
25
27
Overall Study
NOT COMPLETED
6
5

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Adherence in Pediatric Multiple Sclerosis

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Behavioural Intervention/Feedback
n=25 Participants
The behavioral interventionist will contact the patient and parent by email and telephone to schedule a telephone call to review the downloaded adherence information and discuss barriers experienced by the patient/parent using a standard script. The behavioral feedback will be administered three times: at 1-, 2- and 3-months post-baseline. Motivational Interview
Video Attention Control
n=27 Participants
The patients in this arm of the study will be emailed a link to an educational video about Pediatric MS and therapy for MS at three time points: 1-, 2-, and 3-months post-baseline. Video Attention Control
Total
n=52 Participants
Total of all reporting groups
Age, Categorical
<=18 years
25 Participants
n=5 Participants
27 Participants
n=7 Participants
52 Participants
n=5 Participants
Age, Categorical
Between 18 and 65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Categorical
>=65 years
0 Participants
n=5 Participants
0 Participants
n=7 Participants
0 Participants
n=5 Participants
Age, Continuous
16.32 years
STANDARD_DEVIATION 1.81 • n=5 Participants
15.76 years
STANDARD_DEVIATION 2.52 • n=7 Participants
16.03 years
STANDARD_DEVIATION 2.20 • n=5 Participants
Sex: Female, Male
Female
18 Participants
n=5 Participants
16 Participants
n=7 Participants
34 Participants
n=5 Participants
Sex: Female, Male
Male
7 Participants
n=5 Participants
11 Participants
n=7 Participants
18 Participants
n=5 Participants
Race/Ethnicity, Customized
White
12 participants
n=5 Participants
11 participants
n=7 Participants
23 participants
n=5 Participants
Race/Ethnicity, Customized
Other
13 participants
n=5 Participants
16 participants
n=7 Participants
29 participants
n=5 Participants
Region of Enrollment
Canada
13 participants
n=5 Participants
10 participants
n=7 Participants
23 participants
n=5 Participants
Region of Enrollment
United States
12 participants
n=5 Participants
17 participants
n=7 Participants
29 participants
n=5 Participants

PRIMARY outcome

Timeframe: Baseline, 3 months, 6 months

Population: Behavioural Intervention /Feedback and Video Attention Control Arms were combined to look at changes in adherence over time (baseline, 3-months and 6-months)

Objective measures included: (A) pharmacy refill data provided by site coordinators for 12 months prior to study entry and for 6 months post-study entry and (B) the MEMS cap, an EM device (MEMS, AARDEX) that captures each time the patient discards a needle from their injection or opens their pill bottle. Adherence information from MEMS caps is downloaded and stored on a secured web-platform (medAmigo™). These data were used to compile drug-dosing history data and to calculate medication adherence during the course of the study.

Outcome measures

Outcome measures
Measure
Baseline
n=51 Participants
3-month Follow up
n=52 Participants
6-month Follow up
n=49 Participants
Change in Level of Adherence in Subjects (Objective Measure)
Pharmacy refill adherence
0.95 Proportion of doses (actual vs expected)
Standard Deviation 0.12
0.86 Proportion of doses (actual vs expected)
Standard Deviation 0.20
0.85 Proportion of doses (actual vs expected)
Standard Deviation 0.22
Change in Level of Adherence in Subjects (Objective Measure)
MEMs cap adherence
0.81 Proportion of doses (actual vs expected)
Standard Deviation 0.22
0.82 Proportion of doses (actual vs expected)
Standard Deviation 0.18
0.66 Proportion of doses (actual vs expected)
Standard Deviation 0.32

PRIMARY outcome

Timeframe: Baseline, 3 months, 6 months

Population: Behavioural Intervention /Feedback and Video Attention Control Arms were combined to look at changes in adherence over time (baseline, 3-months and 6-months)

Multiple Sclerosis Treatment Adherence Questionnaire (MSTAQ): Assesses missed doses, side effects and barriers of taking DMTs, and behavioral coping strategies used (e.g., icing the injection site, taking pain medication) over the past four weeks. We adapted the MSTAQ to include both oral and injectable medications. We used a standardized scoring algorithm (0-100), where higher scores reflected higher numbers of missed doses, side effects, barriers, or behavioral coping strategies. Subjects completed only the barriers items, and the parent completed all items.

Outcome measures

Outcome measures
Measure
Baseline
n=47 Participants
3-month Follow up
n=45 Participants
6-month Follow up
n=47 Participants
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): MSTAQ
Parent MSTAQ missed doses
0.06 Score on a scale
Standard Deviation 0.18
0.07 Score on a scale
Standard Deviation 0.19
0.07 Score on a scale
Standard Deviation 0.22
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): MSTAQ
Parent MSTAQ behavioural coping strategies
49.64 Score on a scale
Standard Deviation 9.58
49.24 Score on a scale
Standard Deviation 8.28
49.33 Score on a scale
Standard Deviation 10.76
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): MSTAQ
Parent MSTAQ side effects
50.03 Score on a scale
Standard Deviation 9.63
49.48 Score on a scale
Standard Deviation 9.58
49.04 Score on a scale
Standard Deviation 10.63
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): MSTAQ
Parent MSTAQ barriers
50.12 Score on a scale
Standard Deviation 10.42
48.66 Score on a scale
Standard Deviation 8.60
49.31 Score on a scale
Standard Deviation 9.74
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): MSTAQ
Patient MSTAQ barriers
48.88 Score on a scale
Standard Deviation 9.22
50.40 Score on a scale
Standard Deviation 9.57
50.09 Score on a scale
Standard Deviation 10.90

PRIMARY outcome

Timeframe: Baseline, 3 months, 6 months

Population: Behavioural Intervention /Feedback and Video Attention Control Arms were combined to look at changes in adherence over time (baseline, 3-months and 6-months)

Morisky Adherence Scale (Morisky): A widely used 8-item patient-/parent-reported measure with documented reliability and validity. Total scores range from 0 to 8.The following scoring algorithm was used: 8 = high adherence, 6-7 = medium adherence, and \<6=low adherence.

Outcome measures

Outcome measures
Measure
Baseline
n=52 Participants
3-month Follow up
n=48 Participants
6-month Follow up
n=49 Participants
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): Morisky
Parent Morisky
6.28 Score on a scale
Standard Deviation 1.46
6.40 Score on a scale
Standard Deviation 1.50
6.20 Score on a scale
Standard Deviation 1.85
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): Morisky
Patient Morisky
5.93 Score on a scale
Standard Deviation 1.74
6.00 Score on a scale
Standard Deviation 1.82
5.94 Score on a scale
Standard Deviation 1.91

PRIMARY outcome

Timeframe: Baseline, 3 months, 6 months

Population: Behavioural Intervention /Feedback and Video Attention Control Arms were combined to look at changes in adherence over time (baseline, 3-months and 6-months)

Parental involvement in DMT administration (Parental Involvement): Percentage of time the parent reported (1) reminding the child to take her/his DMT; (2) being present when the child took her/his DMT; and (3) administering the child's DMT.

Outcome measures

Outcome measures
Measure
Baseline
n=51 Participants
3-month Follow up
n=48 Participants
6-month Follow up
n=49 Participants
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): Parental Involvement
Parent remind
44.61 Percentage of time
Standard Deviation 38.83
37.50 Percentage of time
Standard Deviation 37.90
33.16 Percentage of time
Standard Deviation 34.76
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): Parental Involvement
Parent present
65.20 Percentage of time
Standard Deviation 37.11
55.21 Percentage of time
Standard Deviation 39.26
57.14 Percentage of time
Standard Deviation 39.53
Change in Level of Adherence in Subjects (Parent- and Patient-Reported): Parental Involvement
Parent administer
36.27 Percentage of time
Standard Deviation 41.33
32.81 Percentage of time
Standard Deviation 41.95
30.10 Percentage of time
Standard Deviation 40.82

SECONDARY outcome

Timeframe: Baseline, 3 months, 6 months

Population: The number analyzed may differ from the overall number analyzed when not all participants completed each measure.

Pediatric Quality of Life Inventory (PedsQL): A 23-item tool with subscales for physical, social, emotional, and school functioning. The PedsQL has documented reliability and validity, and has been used in a large number of pediatric quality-of-life studies. Subscale scores range from 0 to 100 with higher scores representing better functioning.

Outcome measures

Outcome measures
Measure
Baseline
n=52 Participants
3-month Follow up
n=48 Participants
6-month Follow up
n=49 Participants
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Parent: PedsQL physical functioning
80.39 Score on a scale
Standard Deviation 22.32
76.69 Score on a scale
Standard Deviation 24.60
80.93 Score on a scale
Standard Deviation 21.34
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Parent: PedsQL emotional functioning
73.04 Score on a scale
Standard Deviation 21.61
73.23 Score on a scale
Standard Deviation 19.03
72.30 Score on a scale
Standard Deviation 20.09
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Parent: PedsQL social functioning
82.35 Score on a scale
Standard Deviation 18.56
84.27 Score on a scale
Standard Deviation 17.74
84.72 Score on a scale
Standard Deviation 20.06
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Parent: PedsQL school functioning
68.24 Score on a scale
Standard Deviation 16.27
68.13 Score on a scale
Standard Deviation 18.24
68.27 Score on a scale
Standard Deviation 19.75
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Patient: PedsQL physical functioning
82.23 Score on a scale
Standard Deviation 17.85
81.51 Score on a scale
Standard Deviation 15.95
79.21 Score on a scale
Standard Deviation 20.64
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Patient: PedsQL emotional functioning
71.15 Score on a scale
Standard Deviation 20.52
69.57 Score on a scale
Standard Deviation 21.44
66.63 Score on a scale
Standard Deviation 20.50
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): PedsQL
Patient: PedsQL social functioning
83.56 Score on a scale
Standard Deviation 15.85
80.63 Score on a scale
Standard Deviation 19.34
82.65 Score on a scale
Standard Deviation 20.36

SECONDARY outcome

Timeframe: Baseline, 3 months, 6 months

Population: The number analyzed may differ from the overall number analyzed when not all participants completed each measure.

Multiple Sclerosis Neuropsychological Screening Assessment Questionnaire (MSNQ): Neurocognitive Functioning will be assessed using the informant-report version of the Multiple Sclerosis Neuropsychological Screening Assessment Questionnaire (MSNQ). This 15-item tool has documented high test-retest stability, predictive validity, and construct validity. Informant reports are documented to be reliably correlated with cognitive dysfunction and be less biased by patient depression. Total scores range from 0 to 60 with a higher score indicating worse cognitive functioning.

Outcome measures

Outcome measures
Measure
Baseline
n=49 Participants
3-month Follow up
n=47 Participants
6-month Follow up
n=49 Participants
Quality of Life and Psychosocial Outcomes (Parent- and Patient-Reported): MSNQ
17.90 Score on a scale
Standard Deviation 13.42
17.55 Score on a scale
Standard Deviation 12.41
20.24 Score on a scale
Standard Deviation 14.60

OTHER_PRE_SPECIFIED outcome

Timeframe: baseline, three months, and six months

Autonomy and Environmental Mastery subscale scores (Ryff Scales of Psychological Well-Being) will be compared at baseline, three months, and six months between the two study arms.

Outcome measures

Outcome data not reported

Adverse Events

Behavioural Intervention/Feedback

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Video Attention Control

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Adverse event data not reported

Additional Information

Dr. Ann Yeh

Hospital for Sick Children

Phone: 416-813-7353

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place