A Clinical Study to Evaluate Symbicort Turbuhaler Used 'as Needed' in Adults and Adolescents With Asthma

NCT ID: NCT02224157

Last Updated: 2019-11-25

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

4215 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-11-28

Study Completion Date

2017-08-16

Brief Summary

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The purpose of this study is to test if Symbicort (budesonide/formoterol) Turbuhaler is effective in treating asthma when used 'as needed' in patients with milder asthma. The efficacy of Symbicort 'as needed' will be compared with Pulmicort (budesonide) Turbuhaler twice daily plus terbutaline Turbuhaler 'as needed'

Detailed Description

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A 52-week, double-blind, randomised, multi-centre, phase III, parallel-group study in patients 12 years and older with asthma, evaluating the efficacy and safety of Symbicort (budesonide/formoterol) Turbuhaler 160/4.5 μg 'as needed' compared with Pulmicort (budesonide) Turbuhaler 200 μg twice daily plus terbutaline Turbuhaler 0.4 mg 'as needed'

Conditions

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Asthma

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Symbicort "as needed"+placebo Pulmicort bid

Symbicort (budesonide/formoterol) Turbuhaler 160/4.5 μg 'as needed' + Placebo Pulmicort Turbuhaler 200 μg bid

Group Type EXPERIMENTAL

budesonide/formoterol 'as needed' + budesonide placebo bid

Intervention Type DRUG

Symbicort (budesonide/ formoterol) 160/4.5 μg powder for inhalation 'as needed' plus Pulmicort placebo 200 μg powder for inhalation, 1 inhalation twice daily (morning and evening), 52-week treatment

Pulmicort bid + terbutaline "as needed"

Pulmicort 200 μg Turbuhaler bid + terbutaline 0.4 mg Turbuhaler 'as needed'

Group Type ACTIVE_COMPARATOR

budesonode bid + terbutaline 'as needed'

Intervention Type DRUG

Pulmicort (budesonide) 200 μg powder for inhalation, 1 inhalation twice daily (morning and evening) plus terbutaline 0.4 mg powder for inhalation 'as needed', 52-week treatment

Interventions

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budesonide/formoterol 'as needed' + budesonide placebo bid

Symbicort (budesonide/ formoterol) 160/4.5 μg powder for inhalation 'as needed' plus Pulmicort placebo 200 μg powder for inhalation, 1 inhalation twice daily (morning and evening), 52-week treatment

Intervention Type DRUG

budesonode bid + terbutaline 'as needed'

Pulmicort (budesonide) 200 μg powder for inhalation, 1 inhalation twice daily (morning and evening) plus terbutaline 0.4 mg powder for inhalation 'as needed', 52-week treatment

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

1. Provision of informed consent prior to any study specific procedures. For patients under-age, signed informed consent from both the patient and the patient's parent/legal guardian is required
2. Male or Female, ≥12 years of age
3. Documented diagnosis of asthma for at least 6 months prior to Visit 1
4. Patients who are in need of GINA step 2 treatment
5. Patients treated with a short acting inhaled bronchodilator(s) only should have pre-bronchodilator FEV1 ≥ 60 % of predicted normal (PN) and post-bronchodilator FEV1 ≥ 80 % PN
6. Patients treated with low stable dose of ICS or leukotriene antagonists in addition to short acting inhaled bronchodilator(s) should have pre-bronchodilator FEV1 ≥80 % PN
7. Patients should have reversible airway obstruction
8. To be randomized patients must have used Bricanyl Turbuhaler as needed on at least 3 separate days during the last week of the run in period

Exclusion Criteria

1. Patient has a history of life-threatening asthma including intubation and intensive care unit admission
2. Patient has had an asthma worsening requiring change in treatment other than short acting inhaled bronchodilator(s) within 30 days prior to Visit 1 and from Visit 1 until randomization
3. Patient has required treatment with oral, rectal or parenteral GCS within 30 days and/or depot parenteral GCS within 12 weeks prior to Visit 1
4. Current or previous smoker with a smoking history of ≥ 10 pack years
5. Pregnancy, breast-feeding or planned pregnancy during the study
Minimum Eligible Age

12 Years

Maximum Eligible Age

130 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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AstraZeneca

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Carin Jorup, MD

Role: STUDY_DIRECTOR

AstraZeneca Research & Development

Locations

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Sydney, , Australia

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Botucatu, , Brazil

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Florianópolis, , Brazil

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Goiânia, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Porto Alegre, , Brazil

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Salvador, , Brazil

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Santo André, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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São Paulo, , Brazil

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Sorocaba, , Brazil

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Blagoevgrad, , Bulgaria

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Pernik, , Bulgaria

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Petrich, , Bulgaria

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Pleven, , Bulgaria

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Razlog, , Bulgaria

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Sliven, , Bulgaria

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Smolyan, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Sofia, , Bulgaria

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Stara Zagora, , Bulgaria

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Varna, , Bulgaria

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Veliko Tarnovo, , Bulgaria

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Vidin, , Bulgaria

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Yambol, , Bulgaria

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Curicó, , Chile

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Quillota, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Santiago, , Chile

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Talca, , Chile

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Viña del Mar, , Chile

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Barranquilla, , Colombia

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Bogotá, , Colombia

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Bogotá, , Colombia

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Bogotá, , Colombia

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Medellín, , Colombia

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Česká Lípa, , Czechia

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Kladno, , Czechia

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Kralupy nad Vltavou, , Czechia

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Kutná Hora, , Czechia

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Liberec, , Czechia

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Neratovice, , Czechia

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Ostrava, , Czechia

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Ostrava, , Czechia

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Pardubice, , Czechia

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Pilsen, , Czechia

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Pilsen, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Prague, , Czechia

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Rokycany, , Czechia

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Rudna U Prahy, , Czechia

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Tábor, , Czechia

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Teplice, , Czechia

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Žatec, , Czechia

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Brii-sous-forges, , France

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Colmar, , France

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Joué-lès-Tours, , France

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Nantes, , France

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Nîmes, , France

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Rezé, , France

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Bad Lippspringe, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Berlin, , Germany

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Cottbus, , Germany

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Frankfurt am Main, , Germany

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Geesthacht, , Germany

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Großhansdorf, , Germany

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Hamburg, , Germany

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Hanover, , Germany

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Leipzig, , Germany

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Lübeck, , Germany

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Oldenburg, , Germany

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Reinfeld, , Germany

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Rüdersdorf, , Germany

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Schleswig, , Germany

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Warendorf, , Germany

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Aszód, , Hungary

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Balassagyarmat, , Hungary

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Berettyóújfalu, , Hungary

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Budapest, , Hungary

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Cegléd, , Hungary

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Érd, , Hungary

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Gödöllő, , Hungary

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Gyula, , Hungary

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Gyula, , Hungary

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Hajdúnánás, , Hungary

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Létavértes, , Hungary

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Makó, , Hungary

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Miskolc, , Hungary

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Mórahalom, , Hungary

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Pécs, , Hungary

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Siófok, , Hungary

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Szeged, , Hungary

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Szombathely, , Hungary

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Vásárosnamény, , Hungary

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Chihuahua City, , Mexico

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Guadalajara, , Mexico

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Guadalajara, , Mexico

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Mexico City, , Mexico

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Mérida, , Mexico

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México, , Mexico

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San Juan del Río, , Mexico

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Tlanepantla, , Mexico

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Villahermosa, , Mexico

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Zapopan, , Mexico

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Christchurch, , New Zealand

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Christchurch Central, , New Zealand

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Grafton, , New Zealand

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Hamilton West, , New Zealand

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Maroubra, , New Zealand

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New Lambton, , New Zealand

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Newtown, , New Zealand

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Rotorua, , New Zealand

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South Brisbane, , New Zealand

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Tauranga, , New Zealand

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Wellington, , New Zealand

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Chancay, , Peru

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Lima, , Peru

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Lima Cercado, , Peru

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Miraflores, , Peru

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Santa Beatriz, , Peru

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Lipa City, , Philippines

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Manila, , Philippines

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Pasig, , Philippines

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Quezon City, , Philippines

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Quezon City, , Philippines

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Bialystok, , Poland

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Bialystok, , Poland

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Giżycko, , Poland

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Kościan, , Poland

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Krakow, , Poland

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Lublin, , Poland

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Mrągowo, , Poland

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Ostrowiec Świętokrzyski, , Poland

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Ostrów Wielkopolski, , Poland

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Pabianice, , Poland

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Piła, , Poland

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Poznan, , Poland

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Poznan, , Poland

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Proszowice, , Poland

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Rzeszów, , Poland

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Warsaw, , Poland

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Zabrze, , Poland

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Bragadiru, , Romania

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Brasov, , Romania

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Brasov, , Romania

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Bucharest, , Romania

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Constanța, , Romania

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Constanța, , Romania

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Deva, , Romania

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Iași, , Romania

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Piteşti, , Romania

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Chelyabinsk, , Russia

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Gatchina, , Russia

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Ivanovo, , Russia

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Izhevsk, , Russia

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Kazan', , Russia

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Kemerovo, , Russia

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Kemerovo, , Russia

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Kemerovo, , Russia

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Moscow, , Russia

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Novosibirsk, , Russia

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Omsk, , Russia

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Penza, , Russia

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Perm, , Russia

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Pskov, , Russia

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Saint Petersburg, , Russia

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Saint Petersburg, , Russia

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Saratov, , Russia

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Saratov, , Russia

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Tomsk, , Russia

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Tver', , Russia

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Ufa, , Russia

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Ulyanovsk, , Russia

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Vladikavkaz, , Russia

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Volgograd, , Russia

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Vsevolozhsk, , Russia

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Yaroslavl, , Russia

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Yekaterinburg, , Russia

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Dhahran, , Saudi Arabia

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Jeddah, , Saudi Arabia

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Jeddah, , Saudi Arabia

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Riyadh, , Saudi Arabia

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Riyadh, , Saudi Arabia

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Kežmarok, , Slovakia

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Komárno, , Slovakia

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Košice, , Slovakia

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Košice, , Slovakia

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Levice, , Slovakia

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Liptovský Mikuláš, , Slovakia

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Lučenec, , Slovakia

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Nitra, , Slovakia

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Nové Zámky, , Slovakia

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Poprad, , Slovakia

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Poprad, , Slovakia

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Rimavská Sobota, , Slovakia

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Ružomberok, , Slovakia

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Skalica, , Slovakia

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Šurany, , Slovakia

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Topoľčany, , Slovakia

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Trebišov, , Slovakia

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Zvolen, , Slovakia

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Žilina, , Slovakia

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Bellville, , South Africa

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Boksburg North, , South Africa

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Cape Town, , South Africa

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Cape Town, , South Africa

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Durban, , South Africa

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Durban, , South Africa

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Durban, , South Africa

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Durban, , South Africa

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Johannesburg, , South Africa

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Johannesburg, , South Africa

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Lenasia, , South Africa

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Mowbray, , South Africa

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Panorama, , South Africa

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Phoenix, , South Africa

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Verulam, , South Africa

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Busan, , South Korea

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Cheongju-si, , South Korea

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Daegu, , South Korea

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Incheon, , South Korea

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Seongnam-si, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Seoul, , South Korea

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Suwon, , South Korea

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Uijeongbu-si, , South Korea

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Wŏnju, , South Korea

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Alicante, , Spain

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Badalona, , Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Bilbao (Vizcaya), , Spain

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Madrid, , Spain

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Madrid, , Spain

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Marbella (Málaga), , Spain

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Málaga, , Spain

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Oviedo, , Spain

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Seville, , Spain

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Seville, , Spain

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Terrassa (Barcelona), , Spain

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Valencia, , Spain

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Borås, , Sweden

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Lund, , Sweden

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Malmo, , Sweden

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Stockholm, , Sweden

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Värnamo, , Sweden

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Västra Frölunda, , Sweden

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Bangkok, , Thailand

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Chon Buri, , Thailand

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Hat Yai, , Thailand

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Khon Kaen, , Thailand

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Muang,, , Thailand

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Nonthaburi, , Thailand

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Pathum Thani, , Thailand

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Cherkasy, , Ukraine

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Chernihiv, , Ukraine

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Chernivtsi, , Ukraine

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Dnipro, , Ukraine

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Ivano-Frankivsk, , Ukraine

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Kharkiv, , Ukraine

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Kharkiv, , Ukraine

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Kharkiv, , Ukraine

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Kharkiv, , Ukraine

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Kherson, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Kyiv, , Ukraine

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Lutsk, , Ukraine

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Lviv, , Ukraine

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Odesa, , Ukraine

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Odesa, , Ukraine

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Ternopil, , Ukraine

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Uzhhorod, , Ukraine

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Uzhhorod, , Ukraine

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Uzhhorod, , Ukraine

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Vinnytsia, , Ukraine

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Zaporizhzhya, , Ukraine

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Zaporizhzhya, , Ukraine

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Can Tho, , Vietnam

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Hanoi, , Vietnam

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Hà Nội, , Vietnam

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Ho Chi Minh City, , Vietnam

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Hochiminh, , Vietnam

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Huế, , Vietnam

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Countries

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Australia Brazil Bulgaria Chile Colombia Czechia France Germany Hungary Mexico New Zealand Peru Philippines Poland Romania Russia Saudi Arabia Slovakia South Africa South Korea Spain Sweden Thailand Ukraine Vietnam

References

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FitzGerald JM, O'Byrne PM, Bateman ED, Barnes PJ, Zheng J, Ivanov S, Lamarca R, Larsdotter U, Emerath U, Jansen G, Puu M, Alagappan VKT, Surmont F, Reddel HK. Safety of As-Needed Budesonide-Formoterol in Mild Asthma: Data from the Two Phase III SYGMA Studies. Drug Saf. 2021 Apr;44(4):467-478. doi: 10.1007/s40264-020-01041-z. Epub 2021 Feb 6.

Reference Type DERIVED
PMID: 33548020 (View on PubMed)

Bateman ED, Reddel HK, O'Byrne PM, Barnes PJ, Zhong N, Keen C, Jorup C, Lamarca R, Siwek-Posluszna A, FitzGerald JM. As-Needed Budesonide-Formoterol versus Maintenance Budesonide in Mild Asthma. N Engl J Med. 2018 May 17;378(20):1877-1887. doi: 10.1056/NEJMoa1715275.

Reference Type DERIVED
PMID: 29768147 (View on PubMed)

O'Byrne PM, FitzGerald JM, Zhong N, Bateman E, Barnes PJ, Keen C, Almqvist G, Pemberton K, Jorup C, Ivanov S, Reddel HK. The SYGMA programme of phase 3 trials to evaluate the efficacy and safety of budesonide/formoterol given 'as needed' in mild asthma: study protocols for two randomised controlled trials. Trials. 2017 Jan 10;18(1):12. doi: 10.1186/s13063-016-1731-4.

Reference Type DERIVED
PMID: 28069068 (View on PubMed)

Reddel HK, Busse WW, Pedersen S, Tan WC, Chen YZ, Jorup C, Lythgoe D, O'Byrne PM. Should recommendations about starting inhaled corticosteroid treatment for mild asthma be based on symptom frequency: a post-hoc efficacy analysis of the START study. Lancet. 2017 Jan 14;389(10065):157-166. doi: 10.1016/S0140-6736(16)31399-X. Epub 2016 Nov 30.

Reference Type DERIVED
PMID: 27912982 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Related Links

Other Identifiers

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2013-004473-28

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

D589SC00003

Identifier Type: -

Identifier Source: org_study_id

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