Bay98-7196, Dose Finding / POC Study

NCT ID: NCT02203331

Last Updated: 2023-11-07

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

319 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-10-16

Study Completion Date

2016-10-24

Brief Summary

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Purpose of the study is to test efficacy and safety of BAY98-7196 intravaginal ring as a new treatment option for patients with endometriosis-associated pelvic pain

Detailed Description

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Conditions

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Endometriosis

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Placebo

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Levonorgestrel

Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Levonorgestrel

Intervention Type DRUG

Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Anastrozole 300 µg/d + Levonorgestrel

Anastrozole 300 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Anastrozole

Intervention Type DRUG

Participants received Anastrozole 300 µg/d or 600 µg/d or 1050 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Anastrozole 600 µg/d + Levonorgestrel

Anastrozole 600 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Anastrozole

Intervention Type DRUG

Participants received Anastrozole 300 µg/d or 600 µg/d or 1050 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Anastrozole 1050 µg/d + Levonorgestrel

Anastrozole 1050 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Group Type EXPERIMENTAL

Placebo

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Anastrozole

Intervention Type DRUG

Participants received Anastrozole 300 µg/d or 600 µg/d or 1050 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Lupron / Leuprolide acetate

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Lupron / Leuprolide acetate 11.25 mg 3-months depot intramuscular injection

Group Type ACTIVE_COMPARATOR

Placebo

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Lupron / Leuprolide acetate

Intervention Type DRUG

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Lupron / Leuprolide acetate 11.25 mg 3-months depot intramuscular injection

Interventions

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Placebo

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Intervention Type DRUG

Levonorgestrel

Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Intervention Type DRUG

Anastrozole

Participants received Anastrozole 300 µg/d or 600 µg/d or 1050 µg/d + Levonorgestrel 40 µg/d intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Placebo 3-months depot intramuscular injection

Intervention Type DRUG

Lupron / Leuprolide acetate

Placebo intravaginal ring (treatment for 84 days, 28 days wearing period for each ring) and Lupron / Leuprolide acetate 11.25 mg 3-months depot intramuscular injection

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Premenopausal women18 years and above at the time of screening.
* Women with endometriosis confirmed by laparoscopy or laparotomy within the last ten years but not less than 8 weeks before the screening visit In Japan, diagnosis based on imaging (transvaginal ultrasound or MRI) also qualifies for inclusion.
* Moderate to severe endometriosis-associated pelvic pain (EAPP) of ≥5 in the last 28 days before screening visit 1 measured on the numeric rating scale (NRS; i.e. 4-week recall period).
* At randomization: Adherence to the study procedures during the screening period, at least 24 diary entries of ESD item 1 during the last 28 consecutive days before the randomization visit, and a sum of the available ESD item 1 ('worst pain' on the daily NRS) entries during this period of at least 98 (corresponding to an average score of ≥ 3.5).
* Willingness to use only ibuprofen as rescue pain medication for EAPP, if needed according to investigator's instruction.
* Use of a non-hormonal barrier method (i.e. spermicide-coated condoms) for contraception from screening visit until the end of the study. This is not required if adequate contraception is achieved by vasectomy of the partner

Exclusion Criteria

* Pregnancy or lactation (less than three months since delivery, abortion, or lactation before start of treatment)
* Any diseases or conditions that can compromise the function of the body systems and could result in altered absorption, excessive accumulation, impaired metabolism, or altered excretion of the study drug
* Any diseases or conditions that might interfere with the conduct of the study or the interpretation of the results.
* Any disease or condition that may worsen under hormonal treatment according to the assessment and opinion of the investigator.
* Undiagnosed abnormal genital bleeding
* Wish for pregnancy during the study
* Regular use of pain medication due to other underlying diseases
* Non-responsiveness of endometriosis associated pelvic pain (EAPP) to GnRH-a or surgery (partial response is not exclusionary).
Minimum Eligible Age

18 Years

Eligible Sex

FEMALE

Accepts Healthy Volunteers

No

Sponsors

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Bayer

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Bayer Study Director

Role: STUDY_DIRECTOR

Bayer

Locations

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San Diego, California, United States

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San Francisco, California, United States

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Gainesville, Florida, United States

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New Port Richey, Florida, United States

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Atlanta, Georgia, United States

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Sandy Springs, Georgia, United States

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Chicago, Illinois, United States

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Palos Heights, Illinois, United States

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Wichita, Kansas, United States

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Marrero, Louisiana, United States

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Canton, Michigan, United States

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Detroit, Michigan, United States

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Saginaw, Michigan, United States

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Lincoln, Nebraska, United States

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Neptune City, New Jersey, United States

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Plainsboro, New Jersey, United States

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Durham, North Carolina, United States

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Greensboro, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Columbus, Ohio, United States

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Dayton, Ohio, United States

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Philadelphia, Pennsylvania, United States

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Chattanooga, Tennessee, United States

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Seattle, Washington, United States

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Madison, Wisconsin, United States

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Villach, Carinthia, Austria

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Innsbruck, Tyrol, Austria

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Linz, Upper Austria, Austria

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Vienna, , Austria

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Bruxelles - Brussel, , Belgium

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Bruxelles - Brussel, , Belgium

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Edegem, , Belgium

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Ghent, , Belgium

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Hamilton, Ontario, Canada

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Ottawa, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Québec, , Canada

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Brno, , Czechia

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Brno, , Czechia

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České Budějovice, , Czechia

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Hradec Králové, , Czechia

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Olomouc, , Czechia

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Pilsen, , Czechia

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Písek, , Czechia

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Prague, , Czechia

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Tábor, , Czechia

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Aarhus N, , Denmark

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Copenhagen, , Denmark

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Odense C, , Denmark

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Espoo, , Finland

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Helsinki, , Finland

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Hyvinkää, , Finland

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Jyväskylä, , Finland

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Kuopio, , Finland

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Oulu, , Finland

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Turku, , Finland

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Karlsruhe, Baden-Wurttemberg, Germany

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Mannheim, Baden-Wurttemberg, Germany

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Erlangen, Bavaria, Germany

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München, Bavaria, Germany

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Aachen, North Rhine-Westphalia, Germany

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Cologne, North Rhine-Westphalia, Germany

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Dippoldiswalde, Saxony, Germany

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Dresden, Saxony, Germany

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Bernburg, Saxony-Anhalt, Germany

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Blankenburg, Saxony-Anhalt, Germany

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Jena, Thuringia, Germany

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Berlin, , Germany

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Berlin, , Germany

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Hamburg, , Germany

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Hamburg, , Germany

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Kitakyushu, Fukuoka, Japan

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Sapporo, Hokkaido, Japan

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Sapporo, Hokkaido, Japan

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Sapporo, Hokkaido, Japan

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Sapporo, Hokkaido, Japan

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Kawanishi, Hyōgo, Japan

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Kanazawa, Ishikawa-ken, Japan

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Kurashiki, Okayama-ken, Japan

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Sayama, Osaka, Japan

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Hamamatsu, Shizuoka, Japan

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Bunkyo-ku, Tokyo, Japan

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Minatoku, Tokyo, Japan

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Shinagawa-ku, Tokyo, Japan

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Kumamoto, , Japan

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Nagano, , Japan

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Osaka, , Japan

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Almere Stad, , Netherlands

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Groningen, , Netherlands

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Nieuwegein, , Netherlands

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Zwolle, , Netherlands

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Asker, , Norway

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Stokmarknes, , Norway

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Tromsø, , Norway

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Trondheim, , Norway

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Tønsberg, , Norway

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Bialystok, , Poland

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Katowice, , Poland

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Krakow, , Poland

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Lodz, , Poland

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Lublin, , Poland

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Szczecin, , Poland

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Łęczna, , Poland

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Aravaca, Madrid, Spain

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Collado Villalba, Madrid, Spain

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Pozuelo de Alarcón, Madrid, Spain

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Barcelona, , Spain

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Barcelona, , Spain

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Seville, , Spain

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Valencia, , Spain

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Valencia, , Spain

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Vitoria-Gasteiz, Álava, Spain

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Lausanne, Canton of Vaud, Switzerland

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Bern, , Switzerland

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Frauenklinik, , Switzerland

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Lucerne, , Switzerland

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Countries

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United States Austria Belgium Canada Czechia Denmark Finland Germany Japan Netherlands Norway Poland Spain Switzerland

Related Links

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https://www.clinicaltrialsregister.eu/

Click here to find information about studies related to Bayer AG products conducted in Europe.

Other Identifiers

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2013-005090-53

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

15832

Identifier Type: -

Identifier Source: org_study_id

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