Efficacy, Safety, and Tolerability of Selonsertib (GS-4997) in Participants With Diabetic Kidney Disease

NCT ID: NCT02177786

Last Updated: 2019-11-05

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

334 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-06-30

Study Completion Date

2016-08-31

Brief Summary

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The primary objective of this study is to determine the effect of selonsertib (formerly GS-4997) on estimated glomerular filtration rate (eGFR) decline in participants with diabetic kidney disease (DKD). Participants will be randomized with a 1:1:1:1 allocation to receive 1 of 3 doses of selonsertib (2 mg, 6 mg, or 18 mg) or matching placebo.

Detailed Description

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Conditions

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Diabetic Kidney Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Selonsertib 2 mg

Participants will receive selonsertib 2 mg for 48 weeks.

Group Type EXPERIMENTAL

Selonsertib

Intervention Type DRUG

Tablets administered orally once daily

Selonsertib 6 mg

Participants will receive selonsertib 6 mg for 48 weeks.

Group Type EXPERIMENTAL

Selonsertib

Intervention Type DRUG

Tablets administered orally once daily

Selonsertib 18 mg

Participants will receive selonsertib 18 mg for 48 weeks.

Group Type EXPERIMENTAL

Selonsertib

Intervention Type DRUG

Tablets administered orally once daily

Placebo to match selonsertib

Participants will receive placebo to match selonsertib for 48 weeks.

Group Type PLACEBO_COMPARATOR

Placebo to match selonsertib

Intervention Type DRUG

Tablets administered orally once daily

Interventions

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Selonsertib

Tablets administered orally once daily

Intervention Type DRUG

Placebo to match selonsertib

Tablets administered orally once daily

Intervention Type DRUG

Other Intervention Names

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GS-4997

Eligibility Criteria

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Inclusion Criteria

* Adult male or females with prior diagnosis of Diabetic Kidney Disease
* Type 2 diabetes mellitus diagnosis for at least 6 months
* eGFR (MDRD) at screening ≥ 15 mL/min/1.73m\^2 to \< 60 mL/min/1.73m\^2
* Urine albumin to creatinine ratio (UACR) as follows:

* Stage/Stratum 3a: eGFR range 45 to \< 60 mL/min; UACR ≥ 600 mg/g
* Stage/Stratum 3b: eGFR range 30 to \< 45 mL/min; UACR ≥ 300 mg/g
* Stage/Stratum 4: eGFR range 15 to \< 30 mL/min; UACR ≥ 150 mg/g
* Receiving angiotensin-converting-enzyme inhibitor (ACEi) or angiotensin receptor blockers (ARB) at a minimum dose deemed appropriate for the individual by the investigator and be at a stable dose for the last three months

* Individuals not on ACEi/ARB may be screened if there is documented intolerance to ACE inhibitor and/or ARB

Exclusion Criteria

* Type 1 diabetes mellitus
* HbA1c \> 9.5%
* Non-diabetic kidney disease
* UACR \> 5000 mg/g on any measurement during screening
* End stage renal disease (ESRD; receiving peritoneal dialysis, hemodialysis, or status post renal transplantation) or anticipated to occur within the treatment period
* Unstable cardiovascular disease
* Pregnant or lactating females
Minimum Eligible Age

18 Years

Maximum Eligible Age

75 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Gilead Sciences

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Gilead Study Director

Role: STUDY_DIRECTOR

Gilead Sciences

Locations

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The University of Alabama at Birmingham (UAB)

Birmingham, Alabama, United States

Site Status

Chase Medcare

Huntsville, Alabama, United States

Site Status

Choice Medicine

Toney, Alabama, United States

Site Status

Akdhc Medical Research Services, Llc

Peoria, Arizona, United States

Site Status

Akdhc Medical Research Services, Llc

Phoenix, Arizona, United States

Site Status

Akdhc Medical Research Services, Llc

Phoenix, Arizona, United States

Site Status

Akdhc Medical Research Services, Llc

Prescott, Arizona, United States

Site Status

Robert J. Bloomberg, MD

Tempe, Arizona, United States

Site Status

AKDHC East Office

Tucson, Arizona, United States

Site Status

Clinical Research Connections, LLC

Harrisburg, Arkansas, United States

Site Status

North America Research Institute

Azusa, California, United States

Site Status

California Institute of Renal Research

Chula Vista, California, United States

Site Status

California Institute of Renal Research Inc.

El Centro, California, United States

Site Status

Renal Consultants Medical Group Granada Hills

Granada Hills, California, United States

Site Status

Torrance Clinical Research

Lomita, California, United States

Site Status

IMD Medical Group

Los Angeles, California, United States

Site Status

Academic Medical Research Institute

Los Angeles, California, United States

Site Status

Kidney Research Center

Lynwood, California, United States

Site Status

Apex Research of Riverside

Riverside, California, United States

Site Status

San Francisco General Hospital

San Francisco, California, United States

Site Status

Clearview Medical Research, LLC

Santa Clarita, California, United States

Site Status

American Institute of Research

Whittier, California, United States

Site Status

Omega Research Consultants

DeBary, Florida, United States

Site Status

Creekside Medical Research

DeLand, Florida, United States

Site Status

Riverside Clinical Research

Edgewater, Florida, United States

Site Status

ASA Clinical Research

Jupiter, Florida, United States

Site Status

FPA Clinical Research

Kissimmee, Florida, United States

Site Status

The Chappel Group LLC

Kissimmee, Florida, United States

Site Status

South Florida Research Institute

Lauderdale Lakes, Florida, United States

Site Status

Prestige Clinical Research Center Inc

Miami, Florida, United States

Site Status

International Physicians Research / Nephrology Associates of South Miami

Miami, Florida, United States

Site Status

Tellus Clinical Research, Inc

Miami, Florida, United States

Site Status

Coral Research Clinic Corp

Miami, Florida, United States

Site Status

Suncoast Clinical Research, Inc.

New Port Richey, Florida, United States

Site Status

Discovery Medical Research Group

Ocala, Florida, United States

Site Status

Central Florida Internists

Orlando, Florida, United States

Site Status

Sunset Point Medical Associates DBA

Palm Harbor, Florida, United States

Site Status

Pines Clinical Research Inc.

Pembroke Pines, Florida, United States

Site Status

Central Florida Internists

Saint Cloud, Florida, United States

Site Status

Florida Pulmonary Research Institute

Winter Park, Florida, United States

Site Status

Rockdale Medical Research Associates

Conyers, Georgia, United States

Site Status

John H. Stroger Jr. Hospital Of Cook County

Chicago, Illinois, United States

Site Status

Midwest Endocrinology

Crystal Lake, Illinois, United States

Site Status

Beacon Medical Group Kidney and Hypertension Center

Mishawaka, Indiana, United States

Site Status

West Broadway Clinic

Council Bluffs, Iowa, United States

Site Status

Hutchinson Clinic, P.A

Hutchinson, Kansas, United States

Site Status

Kansas Nephrology Research Institute, LLC

Wichita, Kansas, United States

Site Status

L-MARC Research Center

Louisville, Kentucky, United States

Site Status

Four Rivers Clinical Research

Paducah, Kentucky, United States

Site Status

Research Nurse Specialists, LLc

Lafayette, Louisiana, United States

Site Status

Crescent City Clinical Research Center

Metairie, Louisiana, United States

Site Status

Tulane University

New Orleans, Louisiana, United States

Site Status

Internal Medicine Specialists

New Orleans, Louisiana, United States

Site Status

Green Clinic LLC

Ruston, Louisiana, United States

Site Status

Northwest Louisiana Nephrology

Shreveport, Louisiana, United States

Site Status

Southern Clinical Research

Zachary, Louisiana, United States

Site Status

Johns Hopkins Hospital/University

Baltimore, Maryland, United States

Site Status

A. Kaldun Nossuli MD Research

Bethesda, Maryland, United States

Site Status

Wayne State University

Detroit, Michigan, United States

Site Status

Apex Medical Research.Com

Flint, Michigan, United States

Site Status

Elite Clinical Research

Flint, Michigan, United States

Site Status

Troy Internal Medicine, PC

Troy, Michigan, United States

Site Status

VA Medical Center

Kansas City, Missouri, United States

Site Status

Mercury Street Medical Group, PLLC, Big Sky Clinical Research, LLC

Butte, Montana, United States

Site Status

Alegent Creighton Health

Omaha, Nebraska, United States

Site Status

Creighton Diabetes Center

Omaha, Nebraska, United States

Site Status

Nephrology and Hypertension Associates of New Jersey

Voorhees Township, New Jersey, United States

Site Status

Albuquerque Clinical Trials

Albuquerque, New Mexico, United States

Site Status

Nephrology Associates, PC

Flushing, New York, United States

Site Status

Mountain Kidney and Hypertension Associates

Asheville, North Carolina, United States

Site Status

Boice-Willis Clinic

Rocky Mount, North Carolina, United States

Site Status

Carolina Research Center

Shelby, North Carolina, United States

Site Status

Hightop Medical Research Center

Cincinnati, Ohio, United States

Site Status

Craig S Thompson MD LLC

Marion, Ohio, United States

Site Status

Your Diabetes Endocrine Nutrition Group Inc

Mentor, Ohio, United States

Site Status

Chris Sholer, MD, PC

Oklahoma City, Oklahoma, United States

Site Status

Bend Memorial Clinic

Bend, Oregon, United States

Site Status

Southeast Renal Research Institute

Chattanooga, Tennessee, United States

Site Status

Knoxville Kidney Center

Knoxville, Tennessee, United States

Site Status

Arlington Nephrology

Arlington, Texas, United States

Site Status

MW Clinical Research Center

Beaumont, Texas, United States

Site Status

Padre Coast Clinical Research

Corpus Christi, Texas, United States

Site Status

Corsicana Medical Research, PLLC

Corsicana, Texas, United States

Site Status

Texas Tech Univ. Health Sciences Center

El Paso, Texas, United States

Site Status

TVC Clinical Research

Gonzales, Texas, United States

Site Status

Diagnostic Clinic of Houston

Houston, Texas, United States

Site Status

Mercury Clinical Research

Houston, Texas, United States

Site Status

Lakewood Family Practice

Houston, Texas, United States

Site Status

Southwest Clinical Trials

Houston, Texas, United States

Site Status

Southwest Houston Research, Ltd.

Houston, Texas, United States

Site Status

HMRI CCAT Pearland

Pearland, Texas, United States

Site Status

Clinical Advancement Center, PLLC

San Antonio, Texas, United States

Site Status

Briggs Clinical Research, LLC

San Antonio, Texas, United States

Site Status

San Antonio Kidney Disease Center Physicians Group, P.L.L.C.

San Antonio, Texas, United States

Site Status

University of Texas Health Science Center at San Antonio

San Antonio, Texas, United States

Site Status

Val R. Hansen, M.D.

Bountiful, Utah, United States

Site Status

Fletcher Allen Health Care

Burlington, Vermont, United States

Site Status

University of Virginia

Charlottesville, Virginia, United States

Site Status

University of Wisconsin

Madison, Wisconsin, United States

Site Status

Zablocki VAMC

Milwaukee, Wisconsin, United States

Site Status

BC Diabetes

Vancouver, British Columbia, Canada

Site Status

Co-Medica Research Network

Courtice, Ontario, Canada

Site Status

Clinical Research Solutions, Inc.

Kitchener, Ontario, Canada

Site Status

OTT Healthcare Inc.

Scarborough Village, Ontario, Canada

Site Status

Toronto East General Medical Centre

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Chertow GM, Pergola PE, Chen F, Kirby BJ, Sundy JS, Patel UD; GS-US-223-1015 Investigators. Effects of Selonsertib in Patients with Diabetic Kidney Disease. J Am Soc Nephrol. 2019 Oct;30(10):1980-1990. doi: 10.1681/ASN.2018121231. Epub 2019 Sep 10.

Reference Type RESULT
PMID: 31506292 (View on PubMed)

Tesch GH, Ma FY, Han Y, Liles JT, Breckenridge DG, Nikolic-Paterson DJ. ASK1 Inhibitor Halts Progression of Diabetic Nephropathy in Nos3-Deficient Mice. Diabetes. 2015 Nov;64(11):3903-13. doi: 10.2337/db15-0384. Epub 2015 Jul 15.

Reference Type DERIVED
PMID: 26180085 (View on PubMed)

Other Identifiers

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GS-US-223-1015

Identifier Type: -

Identifier Source: org_study_id

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