Extension Study Evaluating the Safety and Efficacy of Subcutaneous Tocilizumab (RoActemra/Actemra) Administration in Systemic and Polyarticular-Course Juvenile Idiopathic Arthritis

NCT ID: NCT02165345

Last Updated: 2022-02-23

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

82 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-07-16

Study Completion Date

2021-11-24

Brief Summary

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This open-label extension of the JIGSAW studies (WA28117 \[NCT01904279\] and WA28118 \[NCT01904292\]) is designed to evaluate the long-term safety and efficacy of subcutaneous (SC) tocilizumab treatment in participants with polyarticular-course and systemic juvenile idiopathic arthritis (pJIA and sJIA). Participants from the 2 JIGSAW studies will continue to receive 162 milligrams (mg) of SC tocilizumab with treatment schedule according to arthritis subtype and body weight. Participants will receive the treatment until commercial availability of the drug or for a maximum of 5 years, whichever is earlier.

Detailed Description

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Conditions

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Juvenile Idiopathic Arthritis

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Tocilizumab

Participants will receive tocilizumab until the commercial availability of the drug or up to 5 years, whichever is earlier.

Group Type EXPERIMENTAL

Tocilizumab

Intervention Type DRUG

162 mg tocilizumab will be administered by SC injection at the following intervals: pJIA participants less than (\<) 30 kilograms (kg): every 3 weeks; pJIA participants greater than or equal to (\>=) 30 kg: every 2 weeks; sJIA participants \<30 kg: every 2 weeks; sJIA participants \>/= 30 kg: once weekly

Interventions

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Tocilizumab

162 mg tocilizumab will be administered by SC injection at the following intervals: pJIA participants less than (\<) 30 kilograms (kg): every 3 weeks; pJIA participants greater than or equal to (\>=) 30 kg: every 2 weeks; sJIA participants \<30 kg: every 2 weeks; sJIA participants \>/= 30 kg: once weekly

Intervention Type DRUG

Other Intervention Names

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RoActemra, Actemra

Eligibility Criteria

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Inclusion Criteria

* Completion of either of the JIGSAW studies, study WA28117 (for participants with pJIA) or study WA28118 (for participants with sJIA)
* Adequate disease control with the use of SC tocilizumab(TCZ)(comparable to the use of IV TCZ, if received prior to enrollment in the JIGSAW study), per clinical judgment of the investigator
* For participants of reproductive potential: agreement to remain abstinent or use of effective contraception as defined by the study protocol

Exclusion Criteria

* Prior discontinuation of SC tocilizumab because of inadequate clinical response during participation in a JIGSAW study
* Poorly controlled disease (in opinion of treating physician) despite treatment with SC tocilizumab in the JIGSAW study
* Prior discontinuation of intravenous tocilizumab because of inadequate clinical response or safety events (including hypersensitivity)
* Therapy with biologic agents (except tocilizumab) in the period between completion of the JIGSAW study and screening for the current study
* Concurrent treatment with disease-modifying anti-rheumatic drugs (DMARDs) (including methotrexate), nonsteroidal anti-inflammatory drugs (NSAIDs), and oral corticosteroids is permitted at the discretion of the investigator
* Use of live or attenuated vaccines and immunosuppressants, such as cyclosporine and cyclophosphamide
* Any significant concurrent medical or surgical conditions or findings that would jeopardize the participant's safety or ability to complete the study, including but not limited to disease of the nervous, renal, hepatic, cardiac, pulmonary, gastric, or endocrine system or any infection
* History of alcohol, drug, or chemical abuse within 6 months prior to screening
* History of atypical tuberculosis (TB) or active TB requiring treatment within 2 years prior to screening
* Known human immunodeficiency virus infection or other acquired forms of immune compromise or inborn conditions characterized by a compromised immune system
* Clinical signs or symptoms of acute or chronic viral hepatitis or chronic autoimmune hepatitis arising since enrollment in the JIGSAW study
* History of concurrent serious gastrointestinal disorders, such as ulcer or inflammatory bowel disease, Crohn's disease, ulcerative colitis, or other symptomatic lower gastrointestinal conditions
* History of or current cancer or lymphoma
* Uncontrolled diabetes mellitus with elevated glycosylated hemoglobin (HbA1c), defined with the use of age-specific standards
* Any abnormal laboratory values, an elevation of hepatic transaminases (\[aspartate aminotransferase \[AST\] or alanine aminotransferase \[ALT\]), lowering of neutrophil count, or thrombocytopenia attributed to tocilizumab use by investigator at screening, the participant may be enrolled; however, the initial tocilizumab dose may be delayed to adhere to the protocol risk mitigation strategy or per the investigator's clinical judgment
* Prior stem cell transplant at any time
Minimum Eligible Age

2 Years

Maximum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Hoffmann-La Roche

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Trials

Role: STUDY_DIRECTOR

Hoffmann-La Roche

Locations

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Arkansas Children's Hospital Research Institute

Little Rock, Arkansas, United States

Site Status

University of Chicago Hospital

Chicago, Illinois, United States

Site Status

Hackensack University Medical Center; Pediatric Rheumatology

Hackensack, New Jersey, United States

Site Status

Duke University

Durham, North Carolina, United States

Site Status

Cincinnati Children'S Hospital Medical Center; Division of Rheumatology

Cincinnati, Ohio, United States

Site Status

Cleveland Clinic Fndn

Cleveland, Ohio, United States

Site Status

Healthcare Research Consultants

Tulsa, Oklahoma, United States

Site Status

University of Utah; Immunology/Rheumatology/Allergy

Salt Lake City, Utah, United States

Site Status

Seattle Children's Hospital

Seattle, Washington, United States

Site Status

Hospital Gral de Niños Pedro Elizalde

Buenos Aires, , Argentina

Site Status

Hospital de Ninos de la Santisima Trinidad; Hematología

Córdoba, , Argentina

Site Status

Westmead Hospital; Paediatric Rheumatology

Westmead, New South Wales, Australia

Site Status

Royal Children'S Hospital; Paediatric Rheumatology

Parkville, Victoria, Australia

Site Status

Universidade Federal de Sao Paulo - UNIFES

São Paulo, São Paulo, Brazil

Site Status

Hospital das Clinicas - FMUSP

São Paulo, São Paulo, Brazil

Site Status

Alberta Children'S Hospital

Calgary, Alberta, Canada

Site Status

The Hospital for Sick Children

Toronto, Ontario, Canada

Site Status

CH de Bicêtre; Pediatrie Generale

Le Kremlin-Bicêtre, , France

Site Status

Charité Campus; Virchow Klinikum Berlin

Berlin, , Germany

Site Status

Uniklinikum Freiburg Zentrum für Kinder- und Jugendmedizin; Pädiatrische Infektio- u. Rheumatologie

Freiburg im Breisgau, , Germany

Site Status

Asklepios Klinik; Zentrum für Allgemeine Pädiatrie und Neonatologie

Sankt Augustin, , Germany

Site Status

Irccs Ospedale Pediatrico Bambin Gesu - Dip. Di Medicina

Rome, Lazio, Italy

Site Status

Hospital Infantil de México "Federico Gomez"; Rheumatology

México, , Mexico

Site Status

Hospital Universitario Dr. Jose Eleuterio Gonzalez; Pediatria

Monterrey, , Mexico

Site Status

SI Sceintific children health center RAMS

Moscow, , Russia

Site Status

Hospital Sant Joan De Deu; Servicio de Reumatologia Pediatrica

Esplugas de Llobregat, Barcelona, Spain

Site Status

Hospital Ramon y Cajal ; Servicio de Reumatologia

Madrid, , Spain

Site Status

Hospital de La Paz; Unidad de Reumatologia Pediatrica

Madrid, , Spain

Site Status

Hospital Universitario la Fe: Servicio de Reumatologia Pediatrica

Valencia, , Spain

Site Status

Bristol Royal Hospital for Children; Rheumatology Department

Bristol, , United Kingdom

Site Status

Alder Hey Children's NHS Foundation Trust

Liverpool, , United Kingdom

Site Status

Countries

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United States Argentina Australia Brazil Canada France Germany Italy Mexico Russia Spain United Kingdom

References

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Brunner HI, Ruperto N, Ramanan AV, Horneff G, Minden K, Calvo Penades I, Alexeeva E, Cleary G, Stern SM, Kone-Paut I, Maldonado Velazquez MDR, Rabinovich CE, Remesal A, Silva CA, Nikishina I, Zucchetto M, Brockwell L, Gordon O, Nagel S, De Benedetti F; PRINTO and PRCSG Investigators. Long-term efficacy and safety of subcutaneous tocilizumab in clinical trials of polyarticular or systemic juvenile idiopathic arthritis. Rheumatology (Oxford). 2024 Sep 1;63(9):2535-2546. doi: 10.1093/rheumatology/keae180.

Reference Type DERIVED
PMID: 38552315 (View on PubMed)

Other Identifiers

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2013-005212-98

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

WA29231

Identifier Type: -

Identifier Source: org_study_id

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