Study of Ruxolitinib in Pancreatic Cancer Patients (Janus 1)

NCT ID: NCT02117479

Last Updated: 2019-03-26

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

321 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-03-31

Study Completion Date

2016-12-31

Brief Summary

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Determining the efficacy, based upon overall survival, of ruxolitinib added to capecitabine for the treatment of advanced or metastatic pancreatic cancer.

Detailed Description

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This was a randomized, double-blinded, placebo-controlled, Phase 3 study, in which approximately 310 participants with advanced or metastatic adenocarcinoma of the pancreas who have failed, or were intolerant to first-line chemotherapy, were to be randomized (1:1) to one of the following treatment groups:

* Treatment A (N = 155): Capecitabine + ruxolitinib
* Treatment B (N = 155): Capecitabine + placebo

Treatment consisted of repeating 21-day cycles. Capecitabine was self-administered for the first 14 days of each cycle, and ruxolitinib/placebo was self-administered daily for each cycle. Treatment for all participants continued as long as the regimen was tolerated, and the participant did not meet discontinuation criteria. Participants who discontinued study treatment before study termination were monitored for safety up to 30-35 days from the end of treatment. All participants were followed for survival until study termination or the safety follow-up visit.

Conditions

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Pancreatic Cancer

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

DOUBLE

Participants Investigators

Study Groups

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Ruxolitinib plus capecitabine

Group Type EXPERIMENTAL

Ruxolitinib

Intervention Type DRUG

5 mg tablets to be administered by mouth twice daily (BID)

Capecitabine

Intervention Type DRUG

150 and 500 mg tablets to be administered by mouth twice daily (BID)

Placebo plus capecitabine

Group Type ACTIVE_COMPARATOR

Placebo

Intervention Type DRUG

5 mg tablets to be administered by mouth twice daily (BID)

Capecitabine

Intervention Type DRUG

150 and 500 mg tablets to be administered by mouth twice daily (BID)

Interventions

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Ruxolitinib

5 mg tablets to be administered by mouth twice daily (BID)

Intervention Type DRUG

Placebo

5 mg tablets to be administered by mouth twice daily (BID)

Intervention Type DRUG

Capecitabine

150 and 500 mg tablets to be administered by mouth twice daily (BID)

Intervention Type DRUG

Other Intervention Names

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Jakafi ® Jakavi ®

Eligibility Criteria

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Inclusion Criteria

* Histologically or cytologically confirmed adenocarcinoma of the pancreas.
* Advanced adenocarcinoma of the pancreas that is inoperable or metastatic.
* Eastern Cooperative Oncology Group (ECOG) performance status 0 to 2
* Received 1 prior chemotherapy regimen for advanced or metastatic disease (not including neoadjuvant and/or adjuvant therapy).
* ≥ 2 weeks elapsed from the completion of previous treatment regimen and participants must have recovered or be at a new stable baseline from any related toxicities.
* Radiographically measurable or evaluable disease
* Modified Glasgow Prognostic Score (mGPS) of 1 or 2 as defined below:

1. mGPS of 1: C-reactive protein \>10 mg/L and albumin ≥35 g/L
2. mGPS of 2: C-reactive protein \>10 mg/L and albumin \<35 g/L

Exclusion Criteria

* Received more than 1 prior regimen for advanced or metastatic disease.
* Ongoing radiation therapy, radiation therapy administered within 30 days of enrollment.
* Concurrent anticancer therapy (eg, chemotherapy, radiation therapy, surgery, immunotherapy, biologic therapy, hormonal therapy, investigational therapy, or tumor embolization).
* Prior severe reaction to fluoropyrimidines, known dihydropyrimidine dehydrogenase deficiency (DPD), or other known hypersensitivity to active substances, including fluorouracil (5-FU), or ruxolitinib, or any of their excipients.
* Prior treatment with a JAK inhibitor for any indication.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Incyte Corporation

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Fitzroy Dawkins, M.D.

Role: STUDY_DIRECTOR

Incyte Corporation

Locations

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Avondale, Arizona, United States

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Chandler, Arizona, United States

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Gilbert, Arizona, United States

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Glendale, Arizona, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Scottsdale, Arizona, United States

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Surprise, Arizona, United States

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Tucson, Arizona, United States

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Hot Springs, Arkansas, United States

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Jonesboro, Arkansas, United States

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Anaheim, California, United States

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Bakersfield, California, United States

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Berkeley, California, United States

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Beverly Hills, California, United States

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Chula Vista, California, United States

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Covina, California, United States

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Downey, California, United States

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El Cajon, California, United States

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Fullerton, California, United States

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Gilroy, California, United States

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Glendale, California, United States

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La Mesa, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Lynwood, California, United States

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Modesto, California, United States

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Montebello, California, United States

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Northridge, California, United States

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Oceanside, California, United States

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Orange, California, United States

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Redondo Beach, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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San Luis Obispo, California, United States

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Santa Ana, California, United States

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Santa Maria, California, United States

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Santa Monica, California, United States

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Torrance, California, United States

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Whittier, California, United States

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Aurora, Colorado, United States

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Boulder, Colorado, United States

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Colorado Springs, Colorado, United States

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Denver, Colorado, United States

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Grand Junction, Colorado, United States

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Longmont, Colorado, United States

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Thornton, Colorado, United States

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New Britain, Connecticut, United States

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New Haven, Connecticut, United States

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Southington, Connecticut, United States

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Trumbull, Connecticut, United States

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Newark, Delaware, United States

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Boca Raton, Florida, United States

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Hollywood, Florida, United States

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Miami, Florida, United States

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Pembroke Pines, Florida, United States

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Atlanta, Georgia, United States

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Austell, Georgia, United States

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Carrollton, Georgia, United States

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Cartersville, Georgia, United States

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Douglasville, Georgia, United States

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Marietta, Georgia, United States

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Newnan, Georgia, United States

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Rome, Georgia, United States

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Thomasville, Georgia, United States

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Arlington Heights, Illinois, United States

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Chicago, Illinois, United States

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Hinsdale, Illinois, United States

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Niles, Illinois, United States

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Urbana, Illinois, United States

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Goshen, Indiana, United States

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Indianapolis, Indiana, United States

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Topeka, Kansas, United States

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Ashland, Kentucky, United States

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Louisville, Kentucky, United States

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Metairie, Louisiana, United States

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New Orleans, Louisiana, United States

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Scarborough, Maine, United States

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Annapolis, Maryland, United States

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Baltimore, Maryland, United States

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Bethesda, Maryland, United States

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Rockville, Maryland, United States

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Worcester, Massachusetts, United States

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Ann Arbor, Michigan, United States

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Detroit, Michigan, United States

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Kalamazoo, Michigan, United States

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Lansing, Michigan, United States

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Woodbury, Minnesota, United States

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Bolivar, Missouri, United States

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Kansas City, Missouri, United States

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St Louis, Missouri, United States

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Kalispell, Montana, United States

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Hastings, Nebraska, United States

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Omaha, Nebraska, United States

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Papillion, Nebraska, United States

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Las Vegas, Nevada, United States

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Lebanon, New Hampshire, United States

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East Orange, New Jersey, United States

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Farmington, New Mexico, United States

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Binghamton, New York, United States

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Fresh Meadows, New York, United States

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Hudson, New York, United States

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Johnson City, New York, United States

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New York, New York, United States

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Nyack, New York, United States

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Rochester, New York, United States

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The Bronx, New York, United States

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Durham, North Carolina, United States

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Wake Forest, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Canton, Ohio, United States

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Columbus, Ohio, United States

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Middletown, Ohio, United States

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Oregon, Ohio, United States

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Toledo, Ohio, United States

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Eugene, Oregon, United States

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Portland, Oregon, United States

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Springfield, Oregon, United States

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Tualatin, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Charleston, South Carolina, United States

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Seneca, South Carolina, United States

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Spartanburg, South Carolina, United States

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Chattanooga, Tennessee, United States

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Knoxville, Tennessee, United States

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Memphis, Tennessee, United States

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Nashville, Tennessee, United States

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Arlington, Texas, United States

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Austin, Texas, United States

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Beaumont, Texas, United States

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Bedford, Texas, United States

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Cedar Park, Texas, United States

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Dallas, Texas, United States

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Denton, Texas, United States

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El Paso, Texas, United States

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Fort Worth, Texas, United States

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Houston, Texas, United States

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Plano, Texas, United States

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Round Rock, Texas, United States

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San Antonio, Texas, United States

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Temple, Texas, United States

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Tyler, Texas, United States

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Waco, Texas, United States

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Ogden, Utah, United States

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Salt Lake City, Utah, United States

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Blacksburg, Virginia, United States

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Richmond, Virginia, United States

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Roanoke, Virginia, United States

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Salem, Virginia, United States

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Wytheville, Virginia, United States

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Seattle, Washington, United States

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Vancouver, Washington, United States

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Madison, Wisconsin, United States

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Australian Capital Territory, , Australia

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New South Wales, , Australia

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South Australia, , Australia

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Victoria, , Australia

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Aalst, , Belgium

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Bruges, , Belgium

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Brussels, , Belgium

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Edegem, , Belgium

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Ghent, , Belgium

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Gilly, , Belgium

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Kortrijk, , Belgium

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Leuven, , Belgium

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Calgary, Alberta, Canada

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Oshawa, Ontario, Canada

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Sault Ste. Marie, Ontario, Canada

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Toronto, Ontario, Canada

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Greenfield Park, Quebec, Canada

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Laval, Quebec, Canada

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Montreal, Quebec, Canada

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Aschaffenburg, , Germany

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Berlin, , Germany

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Bochum, , Germany

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Cologne, , Germany

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Essen, , Germany

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Frankford, , Germany

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Velbert, , Germany

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Aviano, , Italy

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Bari, , Italy

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Bergamo, , Italy

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Brescia, , Italy

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Cremona, , Italy

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Florence, , Italy

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Genova, , Italy

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Lido di Camaiore, , Italy

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Milan, , Italy

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Napoli, , Italy

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Pisa, , Italy

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Rimini, , Italy

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Roma, , Italy

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Auckland, , New Zealand

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Christchurch, , New Zealand

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Hamilton, , New Zealand

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Hwasun-gun, , South Korea

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Seongnam-si, , South Korea

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Seoul, , South Korea

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Badajoz, , Spain

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Barcelona, , Spain

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Madrid, , Spain

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Málaga, , Spain

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Seville, , Spain

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Taichung, , Taiwan

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Tainan City, , Taiwan

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Taipei, , Taiwan

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Patumwan, , Thailand

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Ratchathewi, , Thailand

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Seetatarom, , Thailand

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Aberdeen, , United Kingdom

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Bangor, , United Kingdom

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Birmingham, , United Kingdom

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Boston, , United Kingdom

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Bristol, , United Kingdom

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Cardiff, , United Kingdom

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Glasgow, , United Kingdom

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Guildford, , United Kingdom

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Harlow, , United Kingdom

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Huddersfield, , United Kingdom

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Lancaster, , United Kingdom

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Leeds, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Metropolitan Borough of Wirral, , United Kingdom

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Newcastle upon Tyne, , United Kingdom

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Nottingham, , United Kingdom

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Plymouth, , United Kingdom

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Southampton, , United Kingdom

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Sutton, , United Kingdom

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Welwyn Garden City, , United Kingdom

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Countries

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United States Australia Belgium Canada Germany Italy New Zealand South Korea Spain Taiwan Thailand United Kingdom

References

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Hurwitz H, Van Cutsem E, Bendell J, Hidalgo M, Li CP, Salvo MG, Macarulla T, Sahai V, Sama A, Greeno E, Yu KH, Verslype C, Dawkins F, Walker C, Clark J, O'Reilly EM. Ruxolitinib + capecitabine in advanced/metastatic pancreatic cancer after disease progression/intolerance to first-line therapy: JANUS 1 and 2 randomized phase III studies. Invest New Drugs. 2018 Aug;36(4):683-695. doi: 10.1007/s10637-018-0580-2. Epub 2018 Mar 6.

Reference Type DERIVED
PMID: 29508247 (View on PubMed)

Other Identifiers

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INCB 18424-362

Identifier Type: -

Identifier Source: org_study_id

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