Evaluation of the Efficacy and Safety of Azeliragon (TTP488) in Patients With Mild Alzheimer's Disease

NCT ID: NCT02080364

Last Updated: 2021-05-07

Study Results

Results available

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Basic Information

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Recruitment Status

TERMINATED

Clinical Phase

PHASE3

Total Enrollment

880 participants

Study Classification

INTERVENTIONAL

Study Start Date

2015-04-30

Study Completion Date

2018-06-01

Brief Summary

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This is a study to evaluate the efficacy and safety of azeliragon in patients with mild Alzheimer's disease. Patients will receive either azeliragon or placebo with a patient's participation lasting approximately 18 months.

Detailed Description

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Conditions

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Alzheimer's Disease

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Azeliragon 5mg

Azeliragon (TTP488) 5mg orally once daily for 18 months

Group Type EXPERIMENTAL

Azeliragon

Intervention Type DRUG

Azeliragon 5mg administered orally, once daily for 18 months

Placebo

Placebo orally once daily for 18 months

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo administered orally, once daily for 18 months

Interventions

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Azeliragon

Azeliragon 5mg administered orally, once daily for 18 months

Intervention Type DRUG

Placebo

Placebo administered orally, once daily for 18 months

Intervention Type DRUG

Other Intervention Names

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TTP488

Eligibility Criteria

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Inclusion Criteria

* Diagnosis of probable Alzheimer Disease (AD) with documented evidence of progression of disease
* Mini Mental State Examination (MMSE) score of 21-26, inclusive
* Clinical Dementia Rating global score of 0.5 or 1
* Rosen-Modified Hachinski Ischemia Score less than or equal to 4
* Brain magnetic resonance imaging (MRI) consistent with the diagnosis of probable AD
* Concurrent use of cholinesterase inhibitor or memantine with stable dose for at least 3 months prior to randomization
* Caregiver willing to participate and be able to attend clinic visits with patient
* Ability to ingest oral medications

Exclusion Criteria

* Significant neurological or psychiatric disease other than Alzheimer's disease
* Participants with evidence or history of severe drug allergies (resulting in dyspnea or severe rash).
* Any contraindications to MRI (e.g., clinically significant claustrophobia, non-removable ferromagnetic implants). Patients with contraindications to MRI may undergo computed tomography (CT) on approval by sponsor.
* Any contraindications to the FDG-PET study (e.g. allergy to any component of the FDG dose) in the cohort undergoing a PET scan.
* Previous exposure to investigational or non-investigational therapies for Alzheimer's disease within 6 months of screening
* History of cancer within the last 5 years except adequately treated cervical carcinoma in-situ, cutaneous basal cell or squamous cell cancer, or non-progressive prostate cancer not requiring treatment
* Women of childbearing potential
* Uncontrolled blood pressure and/or blood pressure above 160/100
* Prescription medical food intended for dietary management of the metabolic processes associated with Alzheimer's disease.
* Diagnosis or history of cerebrovascular stroke, severe carotid stenosis, cerebral hemorrhage, intracranial tumor, subarachnoid hemorrhage.
* Patients with unstable, uncontrolled diabetes (HbA1c \> 7.7%) and those requiring insulin.
Minimum Eligible Age

50 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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vTv Therapeutics

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Aaron H Burstein, PharmD

Role: STUDY_DIRECTOR

vTv Therapeutics

Locations

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Tucson, Arizona, United States

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Bellflower, California, United States

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Costa Mesa, California, United States

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Fullerton, California, United States

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Glendale, California, United States

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Imperial, California, United States

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Irvine, California, United States

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Laguna Hills, California, United States

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Long Beach, California, United States

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Long Beach, California, United States

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Orange, California, United States

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Riverside, California, United States

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San Bernardino, California, United States

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San Francisco, California, United States

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Santa Ana, California, United States

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Atlantis, Florida, United States

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Brooksville, Florida, United States

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Delray Beach, Florida, United States

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Hallandale, Florida, United States

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Hialeah, Florida, United States

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Jacksonville, Florida, United States

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Lake Worth, Florida, United States

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Leesburg, Florida, United States

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Miami, Florida, United States

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Miami, Florida, United States

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Miami Beach, Florida, United States

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Miami Lakes, Florida, United States

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Miami Lakes, Florida, United States

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Orlando, Florida, United States

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Pensacola, Florida, United States

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Sarasota, Florida, United States

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Sunrise, Florida, United States

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Atlanta, Georgia, United States

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Columbus, Georgia, United States

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Chicago, Illinois, United States

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Fairway, Kansas, United States

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Prairie Village, Kansas, United States

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Lexington, Kentucky, United States

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Baltimore, Maryland, United States

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Newton, Massachusetts, United States

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Plymouth, Massachusetts, United States

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Quincy, Massachusetts, United States

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Hattiesburg, Mississippi, United States

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Creve Coeur, Missouri, United States

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Princeton, New Jersey, United States

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Albuquerque, New Mexico, United States

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Albany, New York, United States

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Lake Success, New York, United States

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New York, New York, United States

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Staten Island, New York, United States

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Charlotte, North Carolina, United States

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Raleigh, North Carolina, United States

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Wilmington, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Canton, Ohio, United States

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Shaker Heights, Ohio, United States

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Oklahoma City, Oklahoma, United States

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Oklahoma City, Oklahoma, United States

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Portland, Oregon, United States

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Portland, Oregon, United States

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Media, Pennsylvania, United States

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Norristown, Pennsylvania, United States

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Plains, Pennsylvania, United States

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East Providence, Rhode Island, United States

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East Providence, Rhode Island, United States

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Charleston, South Carolina, United States

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Mt. Pleasant, South Carolina, United States

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Cordova, Tennessee, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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San Antonio, Texas, United States

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San Antonio, Texas, United States

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Wichita Falls, Texas, United States

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Murray, Utah, United States

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Kirkland, Washington, United States

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Richland, Washington, United States

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Southport, Queensland, Australia

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Caulfield, Victoria, Australia

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Geelong, Victoria, Australia

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Heidelberg West, Victoria, Australia

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Nedlands, Western Australia, Australia

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West Perth, Western Australia, Australia

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Calgary, Alberta, Canada

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Medicine Hat, Alberta, Canada

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Kentville, Nova Scotia, Canada

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Chatham, Ontario, Canada

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London, Ontario, Canada

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Toronto, Ontario, Canada

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Gatineau, Quebec, Canada

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Greenfield Park, Quebec, Canada

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Cork, , Ireland

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Dublin, , Ireland

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Galway, , Ireland

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Christchurch, Canterbury, New Zealand

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Christchurch, Canterbury, New Zealand

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Cape Town, , South Africa

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Cape Town, , South Africa

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Johannesburg, , South Africa

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Saint George, , South Africa

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Glasgow, , United Kingdom

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London, , United Kingdom

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London, , United Kingdom

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Manchester, , United Kingdom

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Northampton, , United Kingdom

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Oxford, , United Kingdom

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Penarth, , United Kingdom

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Preston, , United Kingdom

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Sheffield, , United Kingdom

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Southhampton, , United Kingdom

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Swindon, , United Kingdom

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Warrington, , United Kingdom

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Countries

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United States Australia Canada Ireland New Zealand South Africa United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

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Other Identifiers

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TTP488-301

Identifier Type: -

Identifier Source: org_study_id

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