Efficacy and Safety of Allogeneic Mesenchymal Precursor Cells (Rexlemestrocel-L) for the Treatment of Heart Failure.

NCT ID: NCT02032004

Last Updated: 2022-01-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

566 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-02-14

Study Completion Date

2020-05-29

Brief Summary

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The primary objective of this study is to determine whether transendocardial delivery of allogeneic human bone marrow-derived mesenchymal precursor cells (MPCs \[rexlemestrocel-L\]) is effective in the treatment of chronic heart failure (HF) due to left ventricular (LV) systolic dysfunction.

Detailed Description

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The purpose of this study is to evaluate the efficacy and safety of a single transendocardial delivery in the cardiac catheterization laboratory of human bone marrow-derived allogeneic MPCs (rexlemestrocel-L) for improvement in clinical outcomes (heart failure major adverse cardiac events \[HF-MACE\]), preventing further adverse cardiac remodeling (left ventricular end systolic volume \[LVESV\] and left ventricular end-diastolic volume \[LVEDV\]), and increasing exercise capacity (six-minute walking test \[6MWT\]) in patients with chronic HF due to LV systolic dysfunction of either ischemic or nonischemic etiology who have received optimal medical/revascularization therapy.

Conditions

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Chronic Heart Failure

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Investigators Outcome Assessors

Study Groups

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Allogeneic Mesenchymal Precursor Cells

Participants randomly assigned to treatment will undergo a single index cardiac catheterization involving transendocardial delivery of rexlemestrocel-L into the myocardium at a cell injection center by an interventional cardiology team not involved with review or assessment of subsequent study results.

Group Type EXPERIMENTAL

Allogeneic Mesenchymal Precursor Cells (MPCs)

Intervention Type BIOLOGICAL

Rexlemestrocel-L consists of human bone marrow-derived allogeneic MPCs isolated from bone mononuclear cells with anti-STRO-3 antibodies, expanded ex vivo, and cryopreserved

Control Treatment

Participants randomly assigned to control treatment will undergo a single cardiac catheterization involving a scripted sham cardiac mapping and cell delivery procedure at a cell injection center by an interventional cardiology team not involved with review or assessment of subsequent study results.

Group Type SHAM_COMPARATOR

Sham Comparator

Intervention Type OTHER

The sham procedure will be staged to script and will not include actual cardiac mapping or delivery of rexlemestrocel-L.

Interventions

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Allogeneic Mesenchymal Precursor Cells (MPCs)

Rexlemestrocel-L consists of human bone marrow-derived allogeneic MPCs isolated from bone mononuclear cells with anti-STRO-3 antibodies, expanded ex vivo, and cryopreserved

Intervention Type BIOLOGICAL

Sham Comparator

The sham procedure will be staged to script and will not include actual cardiac mapping or delivery of rexlemestrocel-L.

Intervention Type OTHER

Other Intervention Names

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MPCs rexlemestrocel-L

Eligibility Criteria

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Inclusion Criteria

* The patient is 18 to 80 years of age, inclusive; both men and women will be enrolled.
* The patient has a diagnosis of chronic HF of ischemic or nonischemic etiology for at least 6 months
* The patient is on stable, optimally tolerated dosages of HF therapies including beta-blockers (approved for country-specific usage), angiotensin-converting enzyme (ACE) inhibitors or angiotensin-receptor blockers (ARBs), and/or aldosterone antagonists, without change in dose for at least 1 month before study intervention
* The patient is on a stable, outpatient, oral diuretic dosing regimen in which the patient remains clinically stable during screening.
* Other Criteria apply, please contact the investigator

Exclusion Criteria

* The patient has NYHA Functional Class I or Functional Class IV symptoms.
* Other Criteria apply, please contact the investigator
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Mesoblast, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Fred Grossman, DO

Role: STUDY_DIRECTOR

Mesoblast, Ltd.

Locations

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Mesoblast Investigational Site 10757 - Cardiology, P.C.

Birmingham, Alabama, United States

Site Status

Mesoblast Investigational Site 13262 - University of Alabama at Birmingham Hospital

Birmingham, Alabama, United States

Site Status

Mesoblast Investigational Site 10779 - Mercy Gilbert Medical Center

Gilbert, Arizona, United States

Site Status

Mesoblast Investigational Site 10786 - Cardiovascular Associates of Mesa

Mesa, Arizona, United States

Site Status

Mesoblast Investigational Site 10756 - Mayo Clinic

Phoenix, Arizona, United States

Site Status

Mesoblast Investigational Site 13023 - University of Arizona Medical Center

Tucson, Arizona, United States

Site Status

Mesoblast Investigational Site 10754 - University of California, San Diego

La Jolla, California, United States

Site Status

Mesoblast Investigational Site 10759 - Scripps Clinic

La Jolla, California, United States

Site Status

Mesoblast Investigational Site 13265 - University of California, Los Angeles

Los Angeles, California, United States

Site Status

Mesoblast Investigational Site 10775 - Cedars-Sinai Medical Care Foundation

Los Angeles, California, United States

Site Status

Mesoblast Investigational Site 10778 - Orange County Cardiology

Orange, California, United States

Site Status

Mesoblast Investigational Site 13031 - St. John's Regional Medical Center

Oxnard, California, United States

Site Status

Mesoblast Investigational Site 13275 - Stanford University Hospital

Stanford, California, United States

Site Status

Mesoblast Investigational Site 13267 - Bethesda Heart Hospital

Boynton Beach, Florida, United States

Site Status

Mesoblast Investigational Site 10780 - Morton Plant Hospital

Clearwater, Florida, United States

Site Status

Mesoblast Investigational Site 10760 - Shands Hospital, University of Florida

Gainesville, Florida, United States

Site Status

Mesoblast Investigational Site 13273 - University of Florida Health

Jacksonville, Florida, United States

Site Status

Mesoblast Investigational Site 10768 - University of Miami

Miami, Florida, United States

Site Status

Mesoblast Investigational Site 13280

Orlando, Florida, United States

Site Status

Mesoblast Investigational Site 13264 - Florida Hospital Pepin Heart Institute

Tampa, Florida, United States

Site Status

Mesoblast Investigational Site 13027 - Emory University School of Medicine

Atlanta, Georgia, United States

Site Status

Mesoblast Investigational Site 10765 - Georgia Regents University

Augusta, Georgia, United States

Site Status

Mesoblast Investigational Site 10772 - University Cardiologist, Rush University Medical Center

Chicago, Illinois, United States

Site Status

Mesoblast Investigational Site 13030 - University of Iowa

Iowa City, Iowa, United States

Site Status

Mesoblast Investigational Site 10783 - Gill Heart Institute, University of Kentucky

Lexington, Kentucky, United States

Site Status

Mesoblast Investigational Site 13022 - University of Louisville

Louisville, Kentucky, United States

Site Status

Mesoblast Investigational Site 13266

New Orleans, Louisiana, United States

Site Status

Mesoblast Investigational Site 10782

Boston, Massachusetts, United States

Site Status

Mesoblast Investigational Site 10766 - Michigan Cardiovascular Institute

Saginaw, Michigan, United States

Site Status

Mesoblast Investigational Site 10762 - Minneapolis Heart Institute

Minneapolis, Minnesota, United States

Site Status

Mesoblast Investigational Site 10761 - Mayo Clinic

Rochester, Minnesota, United States

Site Status

Mesoblast Investigational Site 13281

Las Vegas, Nevada, United States

Site Status

Mesoblast Investigational Site 13263 - RWJ Barnabas Heart Center

Newark, New Jersey, United States

Site Status

Mesoblast Investigational Site 10776 - Columbia University Medical Center

New York, New York, United States

Site Status

Mesoblast Investigational Site 13026 - Sanger Heart and Vascular Institute, Carolinas Healthcare System

Charlotte, North Carolina, United States

Site Status

Mesoblast Investigational Site 10781 - Duke University

Durham, North Carolina, United States

Site Status

Mesoblast Investigational Site 10758 - The Christ Hospital

Cincinnati, Ohio, United States

Site Status

Mesoblast Investigational Site 10770 - University of Cincinnati

Cincinnati, Ohio, United States

Site Status

Mesoblast Investigational Site 10773

Cleveland, Ohio, United States

Site Status

Mesoblast Investigational Site 13278 - OhioHealth Research Institute

Columbus, Ohio, United States

Site Status

Mesoblast Investigational Site 10785 - Lehigh Valley Hospital

Allentown, Pennsylvania, United States

Site Status

Mesoblast Investigational Site 13261 - University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

Mesoblast Investigational Site 10767 - Temple University Hospital

Philadelphia, Pennsylvania, United States

Site Status

Mesoblast Investigational Site 13277

Philadelphia, Pennsylvania, United States

Site Status

Mesoblast Investigational Site 10774 - University of Pittsburgh

Pittsburgh, Pennsylvania, United States

Site Status

Mesoblast Investigational Site 10777 - Stern Cardiovascular Foundation

Germantown, Tennessee, United States

Site Status

Mesoblast Investigational Site 13024 - Austin Heart, PLLC

Austin, Texas, United States

Site Status

Mesoblast Investigational Site 13274 - Soltero CV Research Center, Baylor Scott & White Research Institute

Dallas, Texas, United States

Site Status

Mesoblast Investigational Site 10755 - Texas Heart Institute

Houston, Texas, United States

Site Status

Mesoblast Investigational Site 13268 - Houston Methodist Hospital

Houston, Texas, United States

Site Status

Mesoblast Investigational Site 10763 - University Hospital

Salt Lake City, Utah, United States

Site Status

Mesoblast Investigational Site 10771 - Heart & Vascular Research, Swedish Medical Center

Seattle, Washington, United States

Site Status

Mesoblast Investigational Site 10764 - University of Wisconsin

Madison, Wisconsin, United States

Site Status

Mesoblast Investigational Site 10769 - Aurora Healthcare

Milwaukee, Wisconsin, United States

Site Status

Mesoblast Investigational Site 13279

Milwaukee, Wisconsin, United States

Site Status

Mesoblast Investigational Site 10789 - Aspirus Research Institute

Wausau, Wisconsin, United States

Site Status

Mesoblast Investigational Site 11027

Edmonton, Alberta, Canada

Site Status

Mesoblast Investigational Site 11024 - Victoria Heart Institute Foundation

Victoria, British Columbia, Canada

Site Status

Mesoblast Investigational Site 11025 - St. Michael's Hospital

Toronto, Ontario, Canada

Site Status

Countries

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United States Canada

References

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Borow KM, Yaroshinsky A, Greenberg B, Perin EC. Phase 3 DREAM-HF Trial of Mesenchymal Precursor Cells in Chronic Heart Failure. Circ Res. 2019 Jul 19;125(3):265-281. doi: 10.1161/CIRCRESAHA.119.314951. Epub 2019 Jul 18.

Reference Type DERIVED
PMID: 31318648 (View on PubMed)

Other Identifiers

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MSB-MPC-CHF001

Identifier Type: -

Identifier Source: org_study_id

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