Bone Marrow Derived Adult Stem Cells for Dilated Cardiomyopathy

NCT ID: NCT01302171

Last Updated: 2013-11-15

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

60 participants

Study Classification

INTERVENTIONAL

Study Start Date

2010-08-31

Study Completion Date

2013-07-31

Brief Summary

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A randomised, double-blind, placebo-controlled trial to evaluate the role of intracoronary injection of progenitor cells compared to placebo injection in patients with Dilated Cardiomyopathy who have been pre-treated with G-CSF (Granocyte™) injections for 5 days, and patients treated with a 5 day course of G-CSF (Granocyte™) injection only compared to placebo injection

Detailed Description

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Conditions

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Dilated Cardiomyopathy

Keywords

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dilated cardiomyopathy adult stem cells bone marrow progenitor cells bone marrow stem cells autologous granulocyte-colony stimulating factor intracoronary injection left ventricular function To determine if patient's own bone marrow derived stem cells can be used to improve cardiac function

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Peripheral

Half the patients will be randomised to the non-interventional part of the trial. In this subgroup of patients will be randomised 1:1 to 5 day course of subcutaneous placebo injections or a 5 day course of G-CSF(Granocyte™) subcutaneous injections

Group Type EXPERIMENTAL

granulocyte colony stimulating factor (GCSF)

Intervention Type DRUG

10mcg/kg per day 5 days

Interventional arm

In the subgroup of the interventional arm patients will be randomised 1:1 to receive a 5 day course of subcutaneous G-CSF (Granocyte™) injections and bone marrow aspiration at day 5, they will then receive either stem cells or placebo via intracoronary injection

Group Type EXPERIMENTAL

bone marrow mononuclear cells

Intervention Type PROCEDURE

intra coronary injection of stem cells or placebo

Interventions

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granulocyte colony stimulating factor (GCSF)

10mcg/kg per day 5 days

Intervention Type DRUG

bone marrow mononuclear cells

intra coronary injection of stem cells or placebo

Intervention Type PROCEDURE

Other Intervention Names

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Lenograstim, Granocyte™, Chugai Pharma UK, Limited

Eligibility Criteria

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Inclusion Criteria

* Symptomatic patients with a confirmed diagnosis of dilated cardiomyopathy (NYHA II-III) attending their local 'Heart Failure clinic' who are on optimal heart failure treatment, under supervision from their physician or heart failure nurse specialist, and have no other treatment options
* Patients who are NYHA II that have been hospitalised with a dilated cardiomyopathy related condition
* Coronary angiography will be performed where necessary to confirm the diagnosis and ensure no other conventional treatment options are indicated
* Prior to recruitment to the study patients at risk of ventricular arrhythmia will have undergone electrophysiological assessment and appropriate clinical management (including implantable defibrillator insertion) where indicated (as per NICE guidelines)

Exclusion Criteria

* NYHA I
* Referral hospitals most recent documented ejection fraction of \>45% (any imaging modality)
* The presence of cardiogenic shock
* The presence of acute left and/or right sided pump failure as judged by the presence of pulmonary oedema and/or new peripheral oedema
* Known severe pre-existent left ventricular dysfunction (with a documented ejection fraction of \<10% from referral hospital) prior to randomisation
* Congenital cardiac disease
* Cardiomyopathy secondary to a reversible cause that has not been treated e.g. thyroid disease, alcohol abuse, hypophosphataemia, hypocalcaemia, cocaine abuse, selenium toxicity \& chronic uncontrolled tachycardia
* Cardiomyopathy in association with a neuromuscular disorder e.g. Duchenne's progressive muscular dystrophy
* Previous cardiac surgery
* Contra-indication for bone marrow aspiration
* Known active infection
* Known infection with human immunodeficiency virus (HIV), hepatitis B virus (HBV), hepatitis C virus (HCV), HTLV or syphilis.
* Chronic inflammatory disease requiring ongoing medication
* Serious known concomitant disease with a life expectancy of less than one year
* Follow-up impossible (no fixed abode, etc)
* Patients with an irregular heart rhythm (AF allowed if paced in a regular rhythm)
* Patients with renal impairment (Creatinine \>200mmol/L)
* Neoplastic disease without documented remission within the past 5 years
* Weight\>140kg
* Subjects of childbearing potential
Minimum Eligible Age

18 Years

Maximum Eligible Age

80 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Royal Brompton & Harefield NHS Foundation Trust

OTHER

Sponsor Role collaborator

University College London Hospitals

OTHER

Sponsor Role collaborator

Barts & The London NHS Trust

OTHER

Sponsor Role lead

Responsible Party

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Anthony Mathur

Clinical and Research Lead (Cardiology)

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Anthony Mathur, MD FRCP FESC

Role: PRINCIPAL_INVESTIGATOR

Barts & The London NHS Trust

Locations

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London Chest Hospital

London, , United Kingdom

Site Status

Countries

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United Kingdom

References

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Arnous S, Mozid A, Mathur A. The Bone Marrow Derived Adult Stem Cells for Dilated Cardiomyopathy (REGENERATE-DCM) trial: study design. Regen Med. 2011 Jul;6(4):525-33. doi: 10.2217/rme.11.29.

Reference Type BACKGROUND
PMID: 21749209 (View on PubMed)

Other Identifiers

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2009-013112-12

Identifier Type: -

Identifier Source: org_study_id