Clinical Study to Assess the Efficacy, Safety and Tolerability of Macitentan in Subjects With Inoperable Chronic Thromboembolic Pulmonary Hypertension

NCT ID: NCT02021292

Last Updated: 2025-03-30

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

80 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-08-20

Study Completion Date

2016-09-28

Brief Summary

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Study to evaluate if macitentan is efficient, safe and tolerable enough to be used for treatment of inoperable chronic thromboembolic pulmonary hypertension (CTEPH).

Detailed Description

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Conditions

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Chronic Thromboembolic Pulmonary Hypertension

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Macitentan

Macitentan 10 mg, oral tablet, to be taken once daily.

Group Type EXPERIMENTAL

Macitentan

Intervention Type DRUG

Macitentan 10 mg, oral tablet, to be taken once daily.

Placebo

Matching placebo oral tablet, to be taken once daily.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Matching placebo oral tablet, to be taken once daily.

Interventions

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Macitentan

Macitentan 10 mg, oral tablet, to be taken once daily.

Intervention Type DRUG

Placebo

Matching placebo oral tablet, to be taken once daily.

Intervention Type DRUG

Other Intervention Names

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ACT-064992

Eligibility Criteria

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Inclusion Criteria

* Written informed consent
* Subject with CTEPH (WHO Group 4) judged as inoperable due to the localization of the obstruction being surgically inaccessible (i.e., distal disease).
* Female of childbearing potential must have a negative pre-treatment serum pregnancy test, be advised on appropriate methods of contraception, and agree to use 2 reliable methods of contraception.

Exclusion Criteria

* Previous pulmonary endarterectomy.
* Recurrent thromboembolism despite sufficient oral anticoagulants.
* Symptomatic acute pulmonary embolism in the 6-month period prior to randomization.
* Known moderate-to-severe restrictive lung disease (i.e., TLC \< 60% of predicted value) or obstructive lung disease (i.e., FEV1 \< 70% of predicted, with FEV1/FVC \< 65%) or known significant chronic lung disease diagnosed by chest imaging (e.g., interstitial lung disease, emphysema).
* Acute or chronic conditions (other than dyspnea) that limit the ability to comply with study requirements in the 3-month period prior to Screening visit or during the Screening period.
Minimum Eligible Age

18 Years

Maximum Eligible Age

84 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Actelion

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Kelly Papadakis, MD

Role: STUDY_CHAIR

Actelion

Locations

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University Hospital Gasthuisberg / Interne Geneeskunde - I.G. Pneumologie

Leuven, , Belgium

Site Status

Beijing Chao-Yang Hospital-Department of Respiration

Beijing, , China

Site Status

Cardiovascular institute & Fuwai Hospital- Thrombus Center

Beijing, , China

Site Status

The first affiliated hospital of guangzhou medical university-respiratory department

Guangzhou, , China

Site Status

ngShanghai Pulmonary Hospital, Department of Pulmonary Circulation

Shanghai, , China

Site Status

The General Hospital of Shenyang Military Region,Congenital Heart Disease Department

Shenyang, , China

Site Status

Wuhan Asia Heart Hospital

Wuhan, , China

Site Status

Centre for PPH, Charles University , II Interni klinika1.LF a VFN

Prague, , Czechia

Site Status

CHU de Bicêtre

Le Kremlin-Bicêtre, , France

Site Status

Hôpital Européen Georges Pompidou Service de Pneumologie, soins intensifs et endoscopies bronchiques

Paris, , France

Site Status

CHU de Toulouse Hopital Larrey

Toulouse, , France

Site Status

Justus-Liebig-Universität Gießen

Giessen, , Germany

Site Status

Thoraxklinik am Universitätsklinikum Heidelberg

Heidelberg, , Germany

Site Status

Missionsärztliche Klinik gGmbH Akademisches Lehrkrankenhaus der Julius-Maximilians-Universität

Würzburg, , Germany

Site Status

Semmelweis Egyetem

Budapest, , Hungary

Site Status

Debreceni Egyetem Orvos- és Egészségtudományi Centrum, Kardiológiai Klinika

Debrecen, , Hungary

Site Status

Lietuvos Sveikatos Mokslų Universiteto Ligoninės Kauno Klinikos Pulmonologijos-Imunologijos Klinika

Kaunas, , Lithuania

Site Status

Instituto Nacional de Cardiologia (INC) Ignacio Chavez

Mexico City, , Mexico

Site Status

Wojewódzki Szpital Specjalistyczny w Lublinie im. Stefana Kardynała Wyszyńskiego SPZOZ Oddział Kardiologii - Pododdział Intensywnego Nadzoru Kardiologicznego

Lublin, , Poland

Site Status

Wojewódzki Szpital Specjalistyczny we Wrocawiu

Wrocaw, , Poland

Site Status

Federal State Budgetary Institution "Scientific Research Institute of Systemic Problems of Cardiovascular Diseases", Siberian branch of RAMS

Kemerovo, , Russia

Site Status

Federal State Budgetary Institution "Russian Cardiology Scientific and Production Complex" of the Ministry of Health Care of the Russian Federation

Moscow, , Russia

Site Status

E.N.Meshalkin Novosibirsk State Research Institute Of Circulation Pathology Rosmedtechnology

Novosibirsk, , Russia

Site Status

Federal State Institution "Federal center of Heart, Blood and Endocrinology named after V.A.Almazov Rosmedtekhnologies"

Saint Petersburg, , Russia

Site Status

Federal State Budgetary Institution "Research Institute for Cardiology" of Siberian Branch under the Russian Academy of Medical Sciences / Cardiovascular Surgery Department

Tomsk, , Russia

Site Status

Severance Hospital, YonSei University Health System

Seoul, , South Korea

Site Status

University Hospital Zürich

Zurich, , Switzerland

Site Status

King Chulalongkorn Memorial Hospital, Division of Respiratory and Respiratory Critical Care Medicine

Bangkok, , Thailand

Site Status

Siriraj Hospital, Division of Respiratory Disease and Tuberculosis

Bangkok, , Thailand

Site Status

MAHARAJ NAKORN CHIANG MAI HOSPITAL, Department of Internal Medicine

Chiang Mai, , Thailand

Site Status

Istanbul University İstanbul Faculty Medicine Pulmonology Department

Capa_Istanbul, , Turkey (Türkiye)

Site Status

State Institute of Phthisiology and Pulmonology n.a. F.G. Yanovskiy of AMS Ukraine

Kyiv, , Ukraine

Site Status

Lviv Regional Clinical Hospital, Cardiosurgery Department

Lviv, , Ukraine

Site Status

Papworth Hospital NHS Trust, Pulmonary Vascular Diseases Unit

Cambridge, , United Kingdom

Site Status

Hammersmith Hospital

London, , United Kingdom

Site Status

Sheffield Teaching Hospitals NHS Foundation Trust Royal Hallamshire Hospital, Pulmonary Vascular Medicine

Sheffield, , United Kingdom

Site Status

Countries

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Belgium China Czechia France Germany Hungary Lithuania Mexico Poland Russia South Korea Switzerland Thailand Turkey (Türkiye) Ukraine United Kingdom

References

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Ghofrani HA, Simonneau G, D'Armini AM, Fedullo P, Howard LS, Jais X, Jenkins DP, Jing ZC, Madani MM, Martin N, Mayer E, Papadakis K, Richard D, Kim NH; MERIT study investigators. Macitentan for the treatment of inoperable chronic thromboembolic pulmonary hypertension (MERIT-1): results from the multicentre, phase 2, randomised, double-blind, placebo-controlled study. Lancet Respir Med. 2017 Oct;5(10):785-794. doi: 10.1016/S2213-2600(17)30305-3. Epub 2017 Sep 11.

Reference Type RESULT
PMID: 28919201 (View on PubMed)

Kim NH, D'Armini AM, Howard LS, Jenkins DP, Jing ZC, Mayer E, Chamitava L, Lack G, Rofael H, Solonets M, Ghofrani HA. Long-Term Safety and Efficacy of Macitentan in Inoperable Chronic Thromboembolic Pulmonary Hypertension: Results from MERIT and its Open-Label Extension. Pulm Ther. 2025 Mar;11(1):101-116. doi: 10.1007/s41030-024-00276-w. Epub 2024 Nov 9.

Reference Type DERIVED
PMID: 39520648 (View on PubMed)

Ghofrani HA, Simonneau G, D'Armini AM, Fedullo P, Howard LS, Jais X, Jenkins DP, Jing ZC, Madani MM, Martin N, Mayer E, Papadakis K, Richard D, Kim NH; MERIT study investigators. Macitentan for the treatment of inoperable chronic thromboembolic pulmonary hypertension (MERIT-1): results from the multicentre, phase 2, randomised, double-blind, placebo-controlled study. Lancet Respir Med. 2024 Apr;12(4):e21-e30. doi: 10.1016/S2213-2600(24)00027-4.

Reference Type DERIVED
PMID: 38548406 (View on PubMed)

Other Identifiers

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AC-055E201

Identifier Type: -

Identifier Source: org_study_id

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