L-citrulline and Metformin in Becker's Muscular Dystrophy

NCT ID: NCT02018731

Last Updated: 2016-05-16

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

20 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-06-30

Study Completion Date

2015-12-31

Brief Summary

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The purpose of the study is to compare the effects of L-citrulline and metformin and their combination therapy on muscle function and force in patients with Becker muscular dystrophy (BMD).

Detailed Description

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This is a single center, not-randomized open study. The study medication consists of L-citrulline and metformin administered orally; 5g citrulline and 500mg metformin tablets will be given 3 times daily.

Half of the patients will be treated with metformin during the first 6 weeks of the study. The other patients will receive initially L-citrulline for 6 weeks, before all patients will be treated with the combination therapy (metformin and L-citrulline) for another 6 week period.

The study lasts 12 weeks and includes the screening visit and 3 further visits at baseline, week 6 and week 12.

Conditions

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Becker's Muscular Dystrophy (BMD)

Study Design

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Allocation Method

NON_RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Metformin and Metformin & L-Citrulline

1500 mg/d metformin for 6 weeks, followed by 1500 mg/d metformin and 15 g/d L-citrulline for 6 further weeks

Group Type EXPERIMENTAL

Metformin and Metformin & L-Citrulline

Intervention Type DRUG

L-Citrulline and Metformin & L-Citrulline

15 g/d L-citrulline for 6 weeks, followed by 1500 mg/d metformin and 15 g/d L-citrulline for 6 further weeks

Group Type EXPERIMENTAL

L-Citrulline and Metformin & L-Citrulline

Intervention Type DRUG

Interventions

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Metformin and Metformin & L-Citrulline

Intervention Type DRUG

L-Citrulline and Metformin & L-Citrulline

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* 18 years or older
* Molecular or immunohistochemical diagnosis of BMD
* ambulant at the time point of screening

Exclusion Criteria

* Participation in another therapeutic BMD study within the last 3 months
* Use of L-Arginine, L-Citrulline or Metformin within the last 3 months
* Other chronic disease or relevant limitation of renal, liver, heart function according to discretion of investigator
* known hypersensitivity to L-citrulline or metformin
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University Hospital, Basel, Switzerland

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Dirk Fischer, MD

Role: PRINCIPAL_INVESTIGATOR

University Children's Hospital Basel

Locations

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University Children's Hospital

Basel, Canton of Basel-City, Switzerland

Site Status

Countries

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Switzerland

Other Identifiers

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BMD01

Identifier Type: -

Identifier Source: org_study_id

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