Study to Investigate Immunogenicity, Efficacy and Safety of Treatment With Human-cl rhFVIII

NCT ID: NCT01992549

Last Updated: 2021-01-19

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

48 participants

Study Classification

INTERVENTIONAL

Study Start Date

2014-04-30

Study Completion Date

2018-12-27

Brief Summary

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The purpose of the study is to collect long-term data on the inhibitor development rate of Human-cl rhFVIII in previously untreated patients with severe Hemophilia A.

Detailed Description

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Conditions

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Severe Hemophilia A

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Human-cl rhFVIII

Group Type EXPERIMENTAL

Human-cl rhFVIII

Intervention Type BIOLOGICAL

Interventions

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Human-cl rhFVIII

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

1\. Patients who completed GENA-05 in accordance with the study protocol

Exclusion Criteria

1. Severe liver or kidney disease
2. Concomitant treatment with any systemic immunosuppressive drug;
3. Other FVIII concentrate than Human-cl rhFVIII was received between completion visit of GENA-05 and start of GENA-15 (except emergency cases).
Eligible Sex

MALE

Accepts Healthy Volunteers

No

Sponsors

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Octapharma

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Sigurd Knaub, PhD

Role: STUDY_DIRECTOR

Octapharma

Locations

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UC Davis Medical Center

Sacramento, California, United States

Site Status

University of Alberta

Edmonton, Alberta, Canada

Site Status

BC Children's Hospital

Vancouver, British Columbia, Canada

Site Status

McMaster Children's Hospital

Hamilton, Ontario, Canada

Site Status

Hospital for Sick Children

Toronto, , Canada

Site Status

Hopital de la Timone

Marseille, , France

Site Status

Hôpital Kremlin Bicètre

Paris, , France

Site Status

Institute of Hematology and Transfusiology

Tbilisi, , Georgia

Site Status

Sahyadri Speciality Hospital

Pune, , India

Site Status

Christian Medical College

Vellore, , India

Site Status

IMSP Mother and Child Institute

Chisinau, , Moldova

Site Status

University Medical School

Warsaw, , Poland

Site Status

The National Children Specialized Hospital "OHMATDET"

Kiev, , Ukraine

Site Status

Danylo Halytsky Lviv National Medical University

Lviv, , Ukraine

Site Status

Great Ormond Street Hospital for Children

London, , United Kingdom

Site Status

Countries

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United States Canada France Georgia India Moldova Poland Ukraine United Kingdom

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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GENA-15

Identifier Type: -

Identifier Source: org_study_id

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