Open Label Study of Long Term Safety Evaluation of Alirocumab

NCT ID: NCT01954394

Last Updated: 2018-07-24

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

986 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-12-17

Study Completion Date

2017-06-30

Brief Summary

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Primary Objective:

To assess the long-term safety of alirocumab (SAR236553/REGN727) when added to lipid-lowering therapy in participants with heterozygous familial hypercholesterolemia (heFH) who had completed EFC12492 (NCT01623115), R727-CL-1112 (NCT01709500), EFC12732 (NCT01617655) and LTS11717 (NCT01507831).

Secondary Objectives:

* To evaluate the long-term efficacy of alirocumab on lipid parameters.
* To evaluate the long-term immunogenicity of alirocumab.

Detailed Description

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The maximum study duration will be 176 weeks per participant.

Conditions

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Hypercholesterolemia

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Alirocumab 75 or 150 mg Q2W

Alirocumab 75 mg or 150 mg every 2 weeks (Q2W) added to stable lipid-modifying therapy (LMT) for up to 168 additional weeks (or until the product was commercially available) in participants who completed the parent studies EFC12492, R727-CL-1112, EFC12732 and LTS11717.

Group Type EXPERIMENTAL

Alirocumab

Intervention Type DRUG

Solution for injection, one subcutaneous injection in the abdomen, thigh, or outer area of upper arm with a pre-filled syringe.

Lipid-Modifying Therapy (LMT)

Intervention Type DRUG

Statin (rosuvastatin, simvastatin or atorvastatin) at stable dose with or without other LMT as clinically indicated.

Interventions

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Alirocumab

Solution for injection, one subcutaneous injection in the abdomen, thigh, or outer area of upper arm with a pre-filled syringe.

Intervention Type DRUG

Lipid-Modifying Therapy (LMT)

Statin (rosuvastatin, simvastatin or atorvastatin) at stable dose with or without other LMT as clinically indicated.

Intervention Type DRUG

Other Intervention Names

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SAR236553 REGN727 Praluent

Eligibility Criteria

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Inclusion Criteria

Participants with heFH who had completed one of the four parent studies (EFC12492, R727-CL-1112, EFC12732 and LTS11717).

Exclusion Criteria

Significant protocol deviation in the parent study; Any permanent treatment discontinuation from the parent study.

The above information was not intended to contain all considerations relevant to a participant's potential participation in a clinical trial.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Regeneron Pharmaceuticals

INDUSTRY

Sponsor Role collaborator

Sanofi

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Clinical Sciences & Operations

Role: STUDY_DIRECTOR

Sanofi

Locations

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Investigational Site Number 840321

Huntsville, Alabama, United States

Site Status

Investigational Site Number 840341

Tempe, Arizona, United States

Site Status

Investigational Site Number 840334

Bell Gardens, California, United States

Site Status

Investigational Site Number 840319

Fountain Valley, California, United States

Site Status

Investigational Site Number 840336

Los Angeles, California, United States

Site Status

Investigational Site Number 840339

Mission Viejo, California, United States

Site Status

Investigational Site Number 840337

Newport Beach, California, United States

Site Status

Investigational Site Number 840306

Golden, Colorado, United States

Site Status

Investigational Site Number 840328

Washington D.C., District of Columbia, United States

Site Status

Investigational Site Number 840344

Atlantis, Florida, United States

Site Status

Investigational Site Number 840353

Clearwater, Florida, United States

Site Status

Investigational Site Number 840318

Fort Lauderdale, Florida, United States

Site Status

Investigational Site Number 840327

Jacksonville, Florida, United States

Site Status

Investigational Site Number 840309

Miami, Florida, United States

Site Status

Investigational Site Number 840351

Sarasota, Florida, United States

Site Status

Investigational Site Number 840315

Evanston, Illinois, United States

Site Status

Investigational Site Number 840305

Oakbrook Terrace, Illinois, United States

Site Status

Investigational Site Number 840333

Iowa City, Iowa, United States

Site Status

Investigational Site Number 840329

Kansas City, Kansas, United States

Site Status

Investigational Site Number 840345

Auburn, Maine, United States

Site Status

Investigational Site Number 840338

Biddeford, Maine, United States

Site Status

Investigational Site Number 840322

Boston, Massachusetts, United States

Site Status

Investigational Site Number 840346

Framingham, Massachusetts, United States

Site Status

Investigational Site Number 840317

St Louis, Missouri, United States

Site Status

Investigational Site Number 840349

St Louis, Missouri, United States

Site Status

Investigational Site Number 840314

Morristown, New Jersey, United States

Site Status

Investigational Site Number 840316

New York, New York, United States

Site Status

Investigational Site Number 840324

Poughkeepsie, New York, United States

Site Status

Investigational Site Number 840303

Charlotte, North Carolina, United States

Site Status

Investigational Site Number 840320

Durham, North Carolina, United States

Site Status

Investigational Site Number 840348

Raleigh, North Carolina, United States

Site Status

Investigational Site Number 840340

Cincinnati, Ohio, United States

Site Status

Investigational Site Number 840302

Marion, Ohio, United States

Site Status

Investigational Site Number 840330

Portland, Oregon, United States

Site Status

Investigational Site Number 840352

Beaver, Pennsylvania, United States

Site Status

Investigational Site Number 840308

Philadelphia, Pennsylvania, United States

Site Status

Investigational Site Number 840342

Scranton, Pennsylvania, United States

Site Status

Investigational Site Number 840304

Summerville, South Carolina, United States

Site Status

Investigational Site Number 840311

Dallas, Texas, United States

Site Status

Investigational Site Number 840312

Dallas, Texas, United States

Site Status

Investigational Site Number 840301

Fort Worth, Texas, United States

Site Status

Investigational Site Number 840343

Bountiful, Utah, United States

Site Status

Investigational Site Number 840354

Chesapeake, Virginia, United States

Site Status

Investigational Site Number 840350

Spokane, Washington, United States

Site Status

Investigational Site Number 032302

Caba, , Argentina

Site Status

Investigational Site Number 032301

Coronel Suárez, , Argentina

Site Status

Investigational Site Number 040302

Graz, , Austria

Site Status

Investigational Site Number 040303

Sankt Stefan, , Austria

Site Status

Investigational Site Number 040301

Vienna, , Austria

Site Status

Investigational Site Number 056301

Natoye, , Belgium

Site Status

Investigational Site Number 100302

Sofia, , Bulgaria

Site Status

Investigational Site Number 100301

Sofia, , Bulgaria

Site Status

Investigational Site Number 124303

Chicoutimi, , Canada

Site Status

Investigational Site Number 124302

Montreal, , Canada

Site Status

Investigational Site Number 124301

Québec, , Canada

Site Status

Investigational Site Number 124306

Sherbrooke, , Canada

Site Status

Investigational Site Number 124305

Toronto, , Canada

Site Status

Investigational Site Number 124304

Victoria, , Canada

Site Status

Investigational Site Number 203307

Hradec Králové, , Czechia

Site Status

Investigational Site Number 203305

Prague, , Czechia

Site Status

Investigational Site Number 203301

Prague, , Czechia

Site Status

Investigational Site Number 203303

Prague, , Czechia

Site Status

Investigational Site Number 203306

Praha 5 - Motol, , Czechia

Site Status

Investigational Site Number 203309

Trutnov, , Czechia

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Investigational Site Number 203304

Uherské Hradiště, , Czechia

Site Status

Investigational Site Number 203302

Zlín, , Czechia

Site Status

Investigational Site Number 208301

Aalborg, , Denmark

Site Status

Investigational Site Number 208306

Aarhus, , Denmark

Site Status

Investigational Site Number 208302

Esbjerg, , Denmark

Site Status

Investigational Site Number 208303

Roskilde, , Denmark

Site Status

Investigational Site Number 208304

Svendborg, , Denmark

Site Status

Investigational Site Number 246302

Joensuu, , Finland

Site Status

Investigational Site Number 246301

Kokkola, , Finland

Site Status

Investigational Site Number 246304

Vantaa, , Finland

Site Status

Investigational Site Number 250303

Dijon, , France

Site Status

Investigational Site Number 250304

Lille, , France

Site Status

Investigational Site Number 250302

Nantes, , France

Site Status

Investigational Site Number 250301

Paris, , France

Site Status

Investigational Site Number 250305

Pessac, , France

Site Status

Investigational Site Number 250306

Rennes, , France

Site Status

Investigational Site Number 276302

Berlin, , Germany

Site Status

Investigational Site Number 276305

Frankfurt A.M., , Germany

Site Status

Investigational Site Number 276306

Leipzig, , Germany

Site Status

Investigational Site Number 276301

Magdeburg, , Germany

Site Status

Investigational Site Number 276307

Witten, , Germany

Site Status

Investigational Site Number 348301

Baja, , Hungary

Site Status

Investigational Site Number 376302

Holon, , Israel

Site Status

Investigational Site Number 376304

Jerusalem, , Israel

Site Status

Investigational Site Number 376303

Safed, , Israel

Site Status

Investigational Site Number 376301

Tel Litwinsky, , Israel

Site Status

Investigational Site Number 380302

Chieti, , Italy

Site Status

Investigational Site Number 380304

Milan, , Italy

Site Status

Investigational Site Number 380303

Napoli, , Italy

Site Status

Investigational Site Number 380301

Palermo, , Italy

Site Status

Investigational Site Number 484301

México, , Mexico

Site Status

Investigational Site Number 528317

Alkmaar, , Netherlands

Site Status

Investigational Site Number 528301

Amsterdam-Zuidoost, , Netherlands

Site Status

Investigational Site Number 528320

Apeldoorn, , Netherlands

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Investigational Site Number 528309

Delfzijl, , Netherlands

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Investigational Site Number 528313

Eindhoven, , Netherlands

Site Status

Investigational Site Number 528319

Enschede, , Netherlands

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Investigational Site Number 528322

Goes, , Netherlands

Site Status

Investigational Site Number 528325

Groningen, , Netherlands

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Investigational Site Number 528302

Groningen, , Netherlands

Site Status

Investigational Site Number 528324

Hoogeveen, , Netherlands

Site Status

Investigational Site Number 528318

Hoorn, , Netherlands

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Investigational Site Number 528305

Leiden, , Netherlands

Site Status

Investigational Site Number 528311

Maastricht, , Netherlands

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Investigational Site Number 528312

Nijmegen, , Netherlands

Site Status

Investigational Site Number 528315

Rotterdam, , Netherlands

Site Status

Investigational Site Number 528326

Rotterdam, , Netherlands

Site Status

Investigational Site Number 528303

Utrecht, , Netherlands

Site Status

Investigational Site Number 528323

Utrecht, , Netherlands

Site Status

Investigational Site Number 528321

Venlo, , Netherlands

Site Status

Investigational Site Number 528316

Waalwijk, , Netherlands

Site Status

Investigational Site Number 578301

Bodø, , Norway

Site Status

Investigational Site Number 578305

Oslo, , Norway

Site Status

Investigational Site Number 578304

Oslo, , Norway

Site Status

Investigational Site Number 620302

Funchal, , Portugal

Site Status

Investigational Site Number 620301

Lisbon, , Portugal

Site Status

Investigational Site Number 642302

Timișoara, , Romania

Site Status

Investigational Site Number 643304

Arkhangelsk, , Russia

Site Status

Investigational Site Number 643303

Kazan', , Russia

Site Status

Investigational Site Number 643302

Moscow, , Russia

Site Status

Investigational Site Number 643308

Moscow, , Russia

Site Status

Investigational Site Number 643305

Moscow, , Russia

Site Status

Investigational Site Number 643310

Novosibirsk, , Russia

Site Status

Investigational Site Number 643301

Saint Petersburg, , Russia

Site Status

Investigational Site Number 643306

Saint Petersburg, , Russia

Site Status

Investigational Site Number 643312

Saint Petersburg, , Russia

Site Status

Investigational Site Number 710311

Bellville, , South Africa

Site Status

Investigational Site Number 710307

Bloemfontein, , South Africa

Site Status

Investigational Site Number 710306

Cape Town, , South Africa

Site Status

Investigational Site Number 710302

Cape Town, , South Africa

Site Status

Investigational Site Number 710309

Centurion, , South Africa

Site Status

Investigational Site Number 710312

Parktown, , South Africa

Site Status

Investigational Site Number 710304

Parow, , South Africa

Site Status

Investigational Site Number 710313

Pretoria, , South Africa

Site Status

Investigational Site Number 710303

Pretoria, , South Africa

Site Status

Investigational Site Number 710305

Pretoria, , South Africa

Site Status

Investigational Site Number 710314

Pretoria, , South Africa

Site Status

Investigational Site Number 710315

Roodepoort, , South Africa

Site Status

Investigational Site Number 710310

Somerset West, , South Africa

Site Status

Investigational Site Number 710308

Witbank, , South Africa

Site Status

Investigational Site Number 724303

A Coruña, , Spain

Site Status

Investigational Site Number 724308

Barcelona, , Spain

Site Status

Investigational Site Number 724306

Córdoba, , Spain

Site Status

Investigational Site Number 724312

Granada, , Spain

Site Status

Investigational Site Number 724307

L'Hospitalet de Llobregat, , Spain

Site Status

Investigational Site Number 724301

Madrid, , Spain

Site Status

Investigational Site Number 724309

Madrid, , Spain

Site Status

Investigational Site Number 724305

Madrid, , Spain

Site Status

Investigational Site Number 724311

Madrid, , Spain

Site Status

Investigational Site Number 724314

Málaga, , Spain

Site Status

Investigational Site Number 724315

Quart de Poblet, , Spain

Site Status

Investigational Site Number 724310

Sabadell, , Spain

Site Status

Investigational Site Number 724313

Seville, , Spain

Site Status

Investigational Site Number 724304

Tarragona, , Spain

Site Status

Investigational Site Number 724302

Zaragoza, , Spain

Site Status

Investigational Site Number 752302

Gothenburg, , Sweden

Site Status

Investigational Site Number 752301

Stockholm, , Sweden

Site Status

Investigational Site Number 752304

Stockholm, , Sweden

Site Status

Investigational Site Number 826318

Birmingham, , United Kingdom

Site Status

Investigational Site Number 826304

Brighton, , United Kingdom

Site Status

Investigational Site Number 826301

Bristol, , United Kingdom

Site Status

Investigational Site Number 826311

Cambridge, , United Kingdom

Site Status

Investigational Site Number 826310

Cardiff, , United Kingdom

Site Status

Investigational Site Number 826302

Dundee, , United Kingdom

Site Status

Investigational Site Number 826317

Liverpool, , United Kingdom

Site Status

Investigational Site Number 826306

Liverpool, , United Kingdom

Site Status

Investigational Site Number 826312

Manchester, , United Kingdom

Site Status

Investigational Site Number 826303

Manchester, , United Kingdom

Site Status

Investigational Site Number 826305

Middlesex, , United Kingdom

Site Status

Investigational Site Number 826313

Newcastle upon Tyne, , United Kingdom

Site Status

Investigational Site Number 826309

Reading, , United Kingdom

Site Status

Investigational Site Number 826315

West Bromwich, , United Kingdom

Site Status

Investigational Site Number 826316

West Bromwich, , United Kingdom

Site Status

Countries

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United States Argentina Austria Belgium Bulgaria Canada Czechia Denmark Finland France Germany Hungary Israel Italy Mexico Netherlands Norway Portugal Romania Russia South Africa Spain Sweden United Kingdom

References

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Dufour R, Hovingh GK, Guyton JR, Langslet G, Baccara-Dinet MT, Din-Bell C, Manvelian G, Farnier M. Individualized low-density lipoprotein cholesterol reduction with alirocumab titration strategy in heterozygous familial hypercholesterolemia: Results from an open-label extension of the ODYSSEY LONG TERM trial. J Clin Lipidol. 2019 Jan-Feb;13(1):138-147. doi: 10.1016/j.jacl.2018.11.007. Epub 2018 Nov 30.

Reference Type DERIVED
PMID: 30591415 (View on PubMed)

Farnier M, Hovingh GK, Langslet G, Dufour R, Baccara-Dinet MT, Din-Bell C, Manvelian G, Guyton JR. Long-term safety and efficacy of alirocumab in patients with heterozygous familial hypercholesterolemia: An open-label extension of the ODYSSEY program. Atherosclerosis. 2018 Nov;278:307-314. doi: 10.1016/j.atherosclerosis.2018.08.036. Epub 2018 Sep 1.

Reference Type DERIVED
PMID: 30293878 (View on PubMed)

Hovingh GK, Guyton JR, Langslet G, Dufour R, Baccara-Dinet MT, Din-Bell C, Manvelian G, Farnier M. Alirocumab dosing patterns during 40 months of open-label treatment in patients with heterozygous familial hypercholesterolemia. J Clin Lipidol. 2018 Nov-Dec;12(6):1463-1470. doi: 10.1016/j.jacl.2018.08.011. Epub 2018 Aug 30.

Reference Type DERIVED
PMID: 30287210 (View on PubMed)

Provided Documents

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Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Other Identifiers

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2013-002572-40

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

U1111-1143-3810

Identifier Type: OTHER

Identifier Source: secondary_id

LTS13463

Identifier Type: -

Identifier Source: org_study_id

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