A Study Of PF-05212384 In Combination With Other Anti-Tumor Agents and in Combination With Cisplatin in Patients With Triple Negative Breast Cancer in an Expansion Arm (TNBC)

NCT ID: NCT01920061

Last Updated: 2022-09-13

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE1

Total Enrollment

110 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-09-10

Study Completion Date

2020-01-08

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

This study will evaluate PF-05212384 (gedatolisib) PI3K/mTOR inhibitor)) in combination with either docetaxel, cisplatin or dacomitinib in select advanced solid tumors. The study will assess the safety, pharmacokinetics and pharmacodynamics of these combinations in patients with advanced cancer in order to determine the maximum tolerated dose in each combination. The cisplatin combination expansion portion will evaluate the anti tumor activity of PF 05212384 plus cisplatin in patients with TNBC in 2 separate Arms (Arm 1 and Arm 2).

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Neoplasm

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NON_RANDOMIZED

Intervention Model

SEQUENTIAL

Primary Study Purpose

BASIC_SCIENCE

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Arm A

Group Type EXPERIMENTAL

PF-05212384 (gedatolisib)

Intervention Type DRUG

PF-05212384 weekly intravenous infusions starting at 90 mg/wk as a 3 week cycle

Docetaxel

Intervention Type DRUG

Docetaxel intravenous infusions once every 3 weeks starting at 75 mg/m\^2

Arm B

Group Type EXPERIMENTAL

PF-05212384 (gedatolisib)

Intervention Type DRUG

PF-05212384 weekly intravenous infusions starting at 90 mg/wk as a 3 week cycle

Cisplatin

Intervention Type DRUG

Cisplatin intravenous infusions once every 3 weeks starting at 75 mg/m\^2

Arm C

Group Type EXPERIMENTAL

PF-05212384 (gedatolisib)

Intervention Type DRUG

PF-05212384 weekly intravenous infusions starting at 90 mg/wk as a 3 week cycle

Dacomitinib

Intervention Type DRUG

Dacomitinib to be taken orally as a continuous once daily regimen at a starting dose of 30 mg

Expansion Arm 1

Group Type EXPERIMENTAL

PF-05212384 (gedatolisib)

Intervention Type DRUG

PF-05212384 weekly intravenous infusions starting at 90 mg/wk as a 3 week cycle

Cisplatin

Intervention Type DRUG

Cisplatin intravenous infusions once every 3 weeks starting at 75 mg/m\^2

Expansion Arm 2

Group Type EXPERIMENTAL

PF-05212384 (gedatolisib)

Intervention Type DRUG

PF-05212384 weekly intravenous infusions starting at 90 mg/wk as a 3 week cycle

Cisplatin

Intervention Type DRUG

Cisplatin intravenous infusions once every 3 weeks starting at 75 mg/m\^2

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

PF-05212384 (gedatolisib)

PF-05212384 weekly intravenous infusions starting at 90 mg/wk as a 3 week cycle

Intervention Type DRUG

Docetaxel

Docetaxel intravenous infusions once every 3 weeks starting at 75 mg/m\^2

Intervention Type DRUG

Cisplatin

Cisplatin intravenous infusions once every 3 weeks starting at 75 mg/m\^2

Intervention Type DRUG

Dacomitinib

Dacomitinib to be taken orally as a continuous once daily regimen at a starting dose of 30 mg

Intervention Type DRUG

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

Cisplatin Combination Expansion:

Arm 1:Patients with TNBC with no prior cytotoxic chemotherapy therapy in the metastatic setting; Arm 2: Patients with TNBC and one or two prior cytotoxic therapies in the metastatic setting.

* Arm A: castrate resistant prostate cancer, advanced breast cancer, or non-small cell lunch cancer that are candidates for treatment with a docetaxel-based combination.
* Arm B: Urothelial transitional cell cancer, triple negative breast cancer, ovarian cancer or non small cell lunch cancer that are candidates for a cisplatin-based combination.
* Arm C: Her2+ breast cancer refractory to prior herceptin or lapatinib, her2+ esophagal-gastric cancer, head and neck squamous cell cancer, or non small cell lunch cancer that are candidates for treatment with a dacomitinib-based combination.
* Availability of archival tumor biopsy sample or willing to provide fresh biopsy if not available.
* Eastern Cooperative Oncology Group \[ECOG\] performance must be 0 or 1.
* Adequate bone marrow, renal and liver function.

Exclusion Criteria

* Prior therapy for Cisplatin Combination Expansion:

* Prior platinum (carboplatin or cisplatin) in either the adjuvant or metastatic setting;
* Prior radiation to \>25% bone marrow as estimated by the Investigator.
* Patients with known symptomatic brain metastases.
* Chemotherapy, radiotherapy, biologics or investigational agent within 4 weeks of the lead-in dose.
* Major surgery within 4 weeks of the baseline disease assessments.
* \>2 prior regimens containing cytotoxic chemotherapy in the metastatic setting.
* Active bacterial, fungal or viral infection.
* Uncontrolled or significant cardiovascular disease.
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Pfizer

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

University of Alabama at Birmingham

Birmingham, Alabama, United States

Site Status

Ronald Reagan UCLA Medical Center

Los Angeles, California, United States

Site Status

UCLA Hematology Oncology

Los Angeles, California, United States

Site Status

Westwood Bowyer Clinic

Los Angeles, California, United States

Site Status

UCSF Helen Diller Family Comprehensive Cancer Center

San Francisco, California, United States

Site Status

Santa Monica UCLA Medical Center & Orthopaedic Hospital

Santa Monica, California, United States

Site Status

UCLA Hematology Oncology

Santa Monica, California, United States

Site Status

University of Colorado Denver CTO (CTRC)

Aurora, Colorado, United States

Site Status

University of Colorado Hospital

Aurora, Colorado, United States

Site Status

Brigham and Women's Hospital

Boston, Massachusetts, United States

Site Status

Beth Israel Deaconess Medical Center

Boston, Massachusetts, United States

Site Status

Dana Farber Cancer Institute

Boston, Massachusetts, United States

Site Status

Harper Professional Building

Detroit, Michigan, United States

Site Status

Karmanos Cancer Institute

Detroit, Michigan, United States

Site Status

Fox Chase Cancer Center

Philadelphia, Pennsylvania, United States

Site Status

Medical University of South Carolina/ University Hospital

Charleston, South Carolina, United States

Site Status

Medical University of South Carolina

Charleston, South Carolina, United States

Site Status

MUSC SCTR Research

Charleston, South Carolina, United States

Site Status

MUSC Health East Cooper

Mt. Pleasant, South Carolina, United States

Site Status

MUSC Specialty Care-North

North Charleston, South Carolina, United States

Site Status

British Columbia Cancer Agency - Vancouver Centre

Vancouver, British Columbia, Canada

Site Status

Princess Margaret Cancer Center

Toronto, Ontario, Canada

Site Status

Istituto Europeo di Oncologia - Divisione Sviluppo di Nuovi Farmaci per Terapie Innovative

Milan, MI, Italy

Site Status

Istituto Regina Elena Struttura Complessa Oncologia Medica A

Roma, RM, Italy

Site Status

Hospital Universitari Vall d'Hebron

Barcelona, , Spain

Site Status

Hospital Universitario 12 de Octubre

Madrid, , Spain

Site Status

University College London Hospital, NIHR UCLH Clinical Research Facility

London, , United Kingdom

Site Status

Oxford Cancer Centre

Oxford, , United Kingdom

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Canada Italy Spain United Kingdom

References

Explore related publications, articles, or registry entries linked to this study.

Curigliano G, Shapiro GI, Kristeleit RS, Abdul Razak AR, Leong S, Alsina M, Giordano A, Gelmon KA, Stringer-Reasor E, Vaishampayan UN, Middleton M, Olszanski AJ, Rugo HS, Kern KA, Pathan N, Perea R, Pierce KJ, Mutka SC, Wainberg ZA. A Phase 1B open-label study of gedatolisib (PF-05212384) in combination with other anti-tumour agents for patients with advanced solid tumours and triple-negative breast cancer. Br J Cancer. 2023 Jan;128(1):30-41. doi: 10.1038/s41416-022-02025-9. Epub 2022 Nov 5.

Reference Type DERIVED
PMID: 36335217 (View on PubMed)

Provided Documents

Download supplemental materials such as informed consent forms, study protocols, or participant manuals.

Document Type: Study Protocol

View Document

Document Type: Statistical Analysis Plan

View Document

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2013-001390-24

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

B2151002

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.