Trial Outcomes & Findings for A Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of N-Rephasin® SAL200 in Healthy Male Volunteers (NCT NCT01855048)

NCT ID: NCT01855048

Last Updated: 2021-11-03

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE1

Target enrollment

36 participants

Primary outcome timeframe

Up to 50 days after administration

Results posted on

2021-11-03

Participant Flow

Enrollment have completed in a single center (Seoul National University Hospital) from Nov. 2013 and the completion date is Feb. 2014.

57 subjects were screened and 36 subjects met the eligibility criteria.

Participant milestones

Participant milestones
Measure
INT200-Placebo
Placebo INT200-Placebo: Formulation buffer for continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 0.1mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 0.3 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 1 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 3 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 10 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
Overall Study
STARTED
9
3
6
6
6
6
Overall Study
COMPLETED
9
2
6
6
5
6
Overall Study
NOT COMPLETED
0
1
0
0
1
0

Reasons for withdrawal

Reasons for withdrawal
Measure
INT200-Placebo
Placebo INT200-Placebo: Formulation buffer for continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 0.1mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 0.3 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 1 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 3 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 10 mg/kg
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
Overall Study
Withdrawal by Subject
0
1
0
0
1
0

Baseline Characteristics

A Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of N-Rephasin® SAL200 in Healthy Male Volunteers

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
N-Rephasin® SAL200 0.1(mg/kg)
n=3 Participants
N-Rephasin® SAL200, 0.1 mg/kg N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200 0.3(mg/kg)
n=6 Participants
N-Rephasin® SAL200, 0.3 mg/kg N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200 1(mg/kg)
n=6 Participants
N-Rephasin® SAL200, 1 mg/kg N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200 3(mg/kg)
n=6 Participants
N-Rephasin® SAL200, 3 mg/kg N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200 10(mg/kg)
n=6 Participants
N-Rephasin® SAL200, 10 mg/kg N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
INT200-Placebo
n=9 Participants
Placebo INT200-Placebo: Formulation buffer for continuous intravenous infusion over 60 minutes
Total
n=36 Participants
Total of all reporting groups
Age, Customized
25.3 Years
n=5 Participants
27.8 Years
n=7 Participants
29.8 Years
n=5 Participants
23.7 Years
n=4 Participants
30.5 Years
n=21 Participants
26.2 Years
n=10 Participants
27.4 Years
n=115 Participants
Sex/Gender, Customized
Male
3 Participants
n=5 Participants
6 Participants
n=7 Participants
6 Participants
n=5 Participants
6 Participants
n=4 Participants
6 Participants
n=21 Participants
9 Participants
n=10 Participants
36 Participants
n=115 Participants
Race/Ethnicity, Customized
Asian
3 Participants
n=5 Participants
6 Participants
n=7 Participants
6 Participants
n=5 Participants
6 Participants
n=4 Participants
6 Participants
n=21 Participants
9 Participants
n=10 Participants
36 Participants
n=115 Participants
Region of Enrollment
South Korea
3 participants
n=5 Participants
6 participants
n=7 Participants
6 participants
n=5 Participants
6 participants
n=4 Participants
6 participants
n=21 Participants
9 participants
n=10 Participants
36 participants
n=115 Participants
Body weight
67.1 kg
n=5 Participants
65.5 kg
n=7 Participants
74.0 kg
n=5 Participants
69.1 kg
n=4 Participants
68.7 kg
n=21 Participants
68.1 kg
n=10 Participants
68.9 kg
n=115 Participants
Height
176.8 cm
n=5 Participants
171.3 cm
n=7 Participants
175.1 cm
n=5 Participants
174.8 cm
n=4 Participants
170.5 cm
n=21 Participants
174.5 cm
n=10 Participants
173.6 cm
n=115 Participants

PRIMARY outcome

Timeframe: Up to 50 days after administration

Outcome measures

Outcome measures
Measure
Placebo
n=9 Participants
INT200-Placebo, IV administration
N-Rephasin® SAL200 (0.1 mg/kg)
n=3 Participants
Study drug 0.0056 mL/kg, IV administration
N-Rephasin® SAL200 (0.3 mg/kg)
n=6 Participants
Study drug 0.017 mL/kg, IV administration
N-Rephasin® SAL200 (1 mg/kg)
n=6 Participants
Study drug 0.056 mL/kg, IV administration
N-Rephasin® SAL200 (3 mg/kg)
n=6 Participants
Study drug 0.167 mL/kg, IV administration
N-Rephasin® SAL200 (10 mg/kg)
n=6 Participants
Study drug 0.556 mL/kg, IV administration
Evaluation of the Safety of N-Rephasin® SAL200 in Healthy Human Volunteers
Number of Subjects with at least one AE
1 Participants
0 Participants
2 Participants
1 Participants
2 Participants
6 Participants
Evaluation of the Safety of N-Rephasin® SAL200 in Healthy Human Volunteers
Number of Subjects with at least one drug-related AE
1 Participants
0 Participants
2 Participants
1 Participants
0 Participants
6 Participants

OTHER_PRE_SPECIFIED outcome

Timeframe: 0, 4, 8, 12, 16, 20, 24 hours post-dose

Outcome measures

Outcome measures
Measure
Placebo
n=3 Participants
INT200-Placebo, IV administration
N-Rephasin® SAL200 (0.1 mg/kg)
n=6 Participants
Study drug 0.0056 mL/kg, IV administration
N-Rephasin® SAL200 (0.3 mg/kg)
n=6 Participants
Study drug 0.017 mL/kg, IV administration
N-Rephasin® SAL200 (1 mg/kg)
n=6 Participants
Study drug 0.056 mL/kg, IV administration
N-Rephasin® SAL200 (3 mg/kg)
n=6 Participants
Study drug 0.167 mL/kg, IV administration
N-Rephasin® SAL200 (10 mg/kg)
Study drug 0.556 mL/kg, IV administration
Pharmacokinetic Parameters After Single IV Administration of N-Rephasin® SAL200 [Effective t1/2 (h)]
0.04 h
Standard Deviation 0.02
0.04 h
Standard Deviation 0.01
0.25 h
Standard Deviation 0.05
0.38 h
Standard Deviation 0.06
0.38 h
Standard Deviation 0.05

OTHER_PRE_SPECIFIED outcome

Timeframe: up to 2hours

Outcome measures

Outcome measures
Measure
Placebo
n=3 Participants
INT200-Placebo, IV administration
N-Rephasin® SAL200 (0.1 mg/kg)
n=6 Participants
Study drug 0.0056 mL/kg, IV administration
N-Rephasin® SAL200 (0.3 mg/kg)
n=6 Participants
Study drug 0.017 mL/kg, IV administration
N-Rephasin® SAL200 (1 mg/kg)
n=6 Participants
Study drug 0.056 mL/kg, IV administration
N-Rephasin® SAL200 (3 mg/kg)
n=6 Participants
Study drug 0.167 mL/kg, IV administration
N-Rephasin® SAL200 (10 mg/kg)
Study drug 0.556 mL/kg, IV administration
Pharmacodynamics Evaluation of N-Rephasin® SAL200 : Mean Concentration of Bactericidal Activity After Single Dose of N-Rephsin® SAL200 IV Administration
0h
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
Pharmacodynamics Evaluation of N-Rephasin® SAL200 : Mean Concentration of Bactericidal Activity After Single Dose of N-Rephsin® SAL200 IV Administration
2h
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0.04 μg/mL
Standard Deviation 0.05
Pharmacodynamics Evaluation of N-Rephasin® SAL200 : Mean Concentration of Bactericidal Activity After Single Dose of N-Rephsin® SAL200 IV Administration
1h
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0.13 μg/mL
Standard Deviation 0.05
0.22 μg/mL
Standard Deviation 0.10
0.40 μg/mL
Standard Deviation 0.13
Pharmacodynamics Evaluation of N-Rephasin® SAL200 : Mean Concentration of Bactericidal Activity After Single Dose of N-Rephsin® SAL200 IV Administration
1.5h
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0 μg/mL
Standard Deviation 0
0.15 μg/mL
Standard Deviation 0.06

OTHER_PRE_SPECIFIED outcome

Timeframe: Day 1 to 2

Outcome measures

Outcome measures
Measure
Placebo
n=3 Participants
INT200-Placebo, IV administration
N-Rephasin® SAL200 (0.1 mg/kg)
n=6 Participants
Study drug 0.0056 mL/kg, IV administration
N-Rephasin® SAL200 (0.3 mg/kg)
n=6 Participants
Study drug 0.017 mL/kg, IV administration
N-Rephasin® SAL200 (1 mg/kg)
n=6 Participants
Study drug 0.056 mL/kg, IV administration
N-Rephasin® SAL200 (3 mg/kg)
n=6 Participants
Study drug 0.167 mL/kg, IV administration
N-Rephasin® SAL200 (10 mg/kg)
Study drug 0.556 mL/kg, IV administration
Pharmacokinetic Evaluation of N-Rephasin® SAL200 at the Administered Doses by Analysis of Concentration of N-Rephasin® SAL200 in Serum [Cmax (µg/ml)]
0.04 µg/ml
Standard Deviation 0.01
0.09 µg/ml
Standard Deviation 0.04
0.82 µg/ml
Standard Deviation 0.50
7.10 µg/ml
Standard Deviation 5.39
55.99 µg/ml
Standard Deviation 10.37

OTHER_PRE_SPECIFIED outcome

Timeframe: Day 1 to 2

Outcome measures

Outcome measures
Measure
Placebo
n=3 Participants
INT200-Placebo, IV administration
N-Rephasin® SAL200 (0.1 mg/kg)
n=6 Participants
Study drug 0.0056 mL/kg, IV administration
N-Rephasin® SAL200 (0.3 mg/kg)
n=6 Participants
Study drug 0.017 mL/kg, IV administration
N-Rephasin® SAL200 (1 mg/kg)
n=6 Participants
Study drug 0.056 mL/kg, IV administration
N-Rephasin® SAL200 (3 mg/kg)
n=6 Participants
Study drug 0.167 mL/kg, IV administration
N-Rephasin® SAL200 (10 mg/kg)
Study drug 0.556 mL/kg, IV administration
Pharmacokinetic Evaluation of N-Rephasin® SAL200 at the Administered Doses by Analysis of Concentration of N-Rephasin® SAL200 in Serum [Cmax/D (µg/ml/mg)]
0.01 µg/ml/mg
Standard Deviation 0.001
0.005 µg/ml/mg
Standard Deviation 0.001
0.01 µg/ml/mg
Standard Deviation 0.01
0.03 µg/ml/mg
Standard Deviation 0.02
0.08 µg/ml/mg
Standard Deviation 0.01

OTHER_PRE_SPECIFIED outcome

Timeframe: Day 1 to 2

Outcome measures

Outcome measures
Measure
Placebo
n=3 Participants
INT200-Placebo, IV administration
N-Rephasin® SAL200 (0.1 mg/kg)
n=69 Participants
Study drug 0.0056 mL/kg, IV administration
N-Rephasin® SAL200 (0.3 mg/kg)
n=6 Participants
Study drug 0.017 mL/kg, IV administration
N-Rephasin® SAL200 (1 mg/kg)
n=6 Participants
Study drug 0.056 mL/kg, IV administration
N-Rephasin® SAL200 (3 mg/kg)
n=6 Participants
Study drug 0.167 mL/kg, IV administration
N-Rephasin® SAL200 (10 mg/kg)
Study drug 0.556 mL/kg, IV administration
Pharmacokinetic Evaluation of N-Rephasin® SAL200 at the Administered Doses by Analysis of Concentration of N-Rephasin® SAL200 in Serum [AUC Last (µg*h/ml)]
0.03 µg*h/ml
Standard Deviation 0.005
0.05 µg*h/ml
Standard Deviation 0.02
0.57 µg*h/ml
Standard Deviation 0.31
7.26 µg*h/ml
Standard Deviation 3.42
59.79 µg*h/ml
Standard Deviation 9.03

Adverse Events

INT200-Placebo

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

N-Rephasin® SAL200, 0.1mg/kg

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

N-Rephasin® SAL200, 0.3 mg/kg

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

N-Rephasin® SAL200, 1 mg/kg

Serious events: 0 serious events
Other events: 1 other events
Deaths: 0 deaths

N-Rephasin® SAL200, 3 mg/kg

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

N-Rephasin® SAL200, 10 mg/kg

Serious events: 0 serious events
Other events: 6 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
INT200-Placebo
n=9 participants at risk
Placebo INT200-Placebo: Formulation buffer for continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 0.1mg/kg
n=3 participants at risk
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 0.3 mg/kg
n=6 participants at risk
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 1 mg/kg
n=6 participants at risk
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 3 mg/kg
n=6 participants at risk
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
N-Rephasin® SAL200, 10 mg/kg
n=6 participants at risk
N-Rephasin® SAL200: continuous intravenous infusion over 60 minutes
General disorders
Fatigue
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
50.0%
3/6 • Number of events 3 • Up to 50 Days ± 7 Days
General disorders
Fever
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
General disorders
Rigors
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
33.3%
2/6 • Number of events 2 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
66.7%
4/6 • Number of events 4 • Up to 50 Days ± 7 Days
Respiratory, thoracic and mediastinal disorders
Coughing
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
Respiratory, thoracic and mediastinal disorders
Pharyngitis
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
Respiratory, thoracic and mediastinal disorders
Rhinitis
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
66.7%
4/6 • Number of events 4 • Up to 50 Days ± 7 Days
Nervous system disorders
Headache
11.1%
1/9 • Number of events 3 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
50.0%
3/6 • Number of events 3 • Up to 50 Days ± 7 Days
Nervous system disorders
Dizziness
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
33.3%
2/6 • Number of events 2 • Up to 50 Days ± 7 Days
Nervous system disorders
Syncope
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
Gastrointestinal disorders
Abdominal pain
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
Gastrointestinal disorders
Diarrhoea
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
Gastrointestinal disorders
Nausea
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
33.3%
2/6 • Number of events 2 • Up to 50 Days ± 7 Days
Gastrointestinal disorders
Dyspepsia
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
Musculoskeletal and connective tissue disorders
Back pain
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
Musculoskeletal and connective tissue disorders
Myalgia
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
33.3%
2/6 • Number of events 3 • Up to 50 Days ± 7 Days
Vascular disorders
Hypotension
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
Hepatobiliary disorders
Bilirubinaemia
0.00%
0/9 • Up to 50 Days ± 7 Days
0.00%
0/3 • Up to 50 Days ± 7 Days
16.7%
1/6 • Number of events 1 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days
0.00%
0/6 • Up to 50 Days ± 7 Days

Additional Information

Jun SooYoun, Ph.D. / Executive Director/ Principal researcher

Organization:Institute of iNtRON Biotechnology

Phone: +82-31-739-5332

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place