Pharmacokinetics, Efficacy and Safety of Abatacept Administered Subcutaneously (SC) in Children and Adolescents With Active Polyarticular Juvenile Idiopathic Arthritis (pJIA) and Inadequate Response (IR) to Biologic or Non Biologic Disease Modifying Anti-rheumatic Drugs (DMARDs)

NCT ID: NCT01844518

Last Updated: 2023-07-12

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

View full results

Basic Information

Get a concise snapshot of the trial, including recruitment status, study phase, enrollment targets, and key timeline milestones.

Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

219 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-08-30

Study Completion Date

2023-02-01

Brief Summary

Review the sponsor-provided synopsis that highlights what the study is about and why it is being conducted.

The purpose of this study is to estimate Abatacept steady-state trough concentration (Cmin) at Day 113 in children and adolescents with pJIA

Detailed Description

Dive into the extended narrative that explains the scientific background, objectives, and procedures in greater depth.

Conditions

See the medical conditions and disease areas that this research is targeting or investigating.

Active Polyarticular Juvenile Idiopathic Arthritis

Study Design

Understand how the trial is structured, including allocation methods, masking strategies, primary purpose, and other design elements.

Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

Review each arm or cohort in the study, along with the interventions and objectives associated with them.

Short and Long Terms: Orencia

Short Term: Orencia 50 mg/mL, 87.5 mg/mL, 125 mg/mL pre-filled syringes subcutaneously (0.4 mL/0.7 mL/1.0 mL) weekly for 4 months

Long term: Orencia 50 mg/mL, 87.5 mg/mL, 125 mg/mL pre-filled syringes subcutaneously (0.4 mL/0.7 mL/1.0 mL) weekly for 20 months

Group Type EXPERIMENTAL

Abatacept

Intervention Type BIOLOGICAL

Interventions

Learn about the drugs, procedures, or behavioral strategies being tested and how they are applied within this trial.

Abatacept

Intervention Type BIOLOGICAL

Other Intervention Names

Discover alternative or legacy names that may be used to describe the listed interventions across different sources.

Orencia

Eligibility Criteria

Check the participation requirements, including inclusion and exclusion rules, age limits, and whether healthy volunteers are accepted.

Inclusion Criteria

* JIA subjects (male or female), ages 2-17 years with active disease who had an insufficient therapeutic response or intolerance to at least one non biologic DMARD or Tumor Necrosis Factor (TNFα) antagonists for at least 3 months prior to screening
* Subjects with TNFα inadequate response (or prior biologic) will be restricted to 30% of the population
* Subjects must have a history of at least 5 joints with active disease and must have currently active articular disease with ≥2 active joints and ≥2 joints with limitation of motion.

Exclusion Criteria

* Subjects with other rheumatic diseases or major chronic inflammatory/immunologic diseases, active uveitis, systemic JIA with active systemic features (within a period of 6 months prior to enrollment), persistent Oligoarthritis JIA, or failed 3 or more TNFα antagonists or other biological DMARDs will be excluded.
* Active systemic disease: (ie, extra-articular features of systemic JIA including fever, rash, organomegaly) within a period of 6 months prior to randomization.
* Subjects who have failed more than two TNFα antagonists or other biologic DMARDs
Minimum Eligible Age

2 Years

Maximum Eligible Age

17 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

Meet the organizations funding or collaborating on the study and learn about their roles.

Bristol-Myers Squibb

INDUSTRY

Sponsor Role lead

Responsible Party

Identify the individual or organization who holds primary responsibility for the study information submitted to regulators.

Responsibility Role SPONSOR

Principal Investigators

Learn about the lead researchers overseeing the trial and their institutional affiliations.

Bristol-Myers Squibb

Role: STUDY_DIRECTOR

Bristol-Myers Squibb

Locations

Explore where the study is taking place and check the recruitment status at each participating site.

Local Institution - 0007

Birmingham, Alabama, United States

Site Status

Local Institution - 0003

Little Rock, Arkansas, United States

Site Status

Local Institution - 0011

Hartford, Connecticut, United States

Site Status

Local Institution - 0009

Chicago, Illinois, United States

Site Status

Riley Hospital For Children

Indianapolis, Indiana, United States

Site Status

University Of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Local Institution - 0001

Kansas City, Missouri, United States

Site Status

Local Institution - 0002

The Bronx, New York, United States

Site Status

Local Institution - 0008

Cincinnati, Ohio, United States

Site Status

Local Institution - 0005

Portland, Oregon, United States

Site Status

Local Institution - 0004

Salt Lake City, Utah, United States

Site Status

Seattle Children'S Hospital

Seattle, Washington, United States

Site Status

Local Institution - 0029

Rosario, Santa Fe Province, Argentina

Site Status

Local Institution - 0028

San Miguel de Tucumán, Tucumán Province, Argentina

Site Status

Local Institution - 0030

Buenos Aires, , Argentina

Site Status

Local Institution - 0064

CABA, , Argentina

Site Status

Local Institution - 0031

Córdoba, , Argentina

Site Status

Local Institution - 0037

Brussels, , Belgium

Site Status

Local Institution - 0036

Ghent, , Belgium

Site Status

Local Institution - 0049

Leuven, , Belgium

Site Status

Local Institution

Curitiba, Paraná, Brazil

Site Status

Local Institution - 0038

Porto Alegre, Rio Grande do Sul, Brazil

Site Status

Local Institution - 0042

São Paulo, , Brazil

Site Status

Local Institution - 0040

São Paulo, , Brazil

Site Status

Local Institution - 0041

São Paulo, , Brazil

Site Status

Local Institution - 0018

Bron, , France

Site Status

Local Institution - 0016

Le Kremlin-Bicêtre, , France

Site Status

Local Institution - 0014

Paris, , France

Site Status

Local Institution - 0017

Poitiers, , France

Site Status

Local Institution - 0015

Strasbourg, , France

Site Status

Local Institution - 0044

Bad Bramstedt, , Germany

Site Status

Local Institution - 0045

Berlin, , Germany

Site Status

Local Institution - 0046

Hamburg, , Germany

Site Status

Local Institution - 0048

Heidelberg, , Germany

Site Status

Local Institution - 0047

Sankt Augustin, , Germany

Site Status

Local Institution - 0061

Florence, , Italy

Site Status

Local Institution

Genova, , Italy

Site Status

Local Institution - 0022

Milan, , Italy

Site Status

Local Institution - 0062

Napoli, , Italy

Site Status

Local Institution - 0060

Guadalajara, Jalisco, Mexico

Site Status

Local Institution - 0059

Mexico City, Mexico City, Mexico

Site Status

Local Institution - 0057

Mexico City, Mexico City, Mexico

Site Status

Local Institution - 0056

Monterrey, Nuevo León, Mexico

Site Status

Local Institution - 0058

Mérida, Yucatán, Mexico

Site Status

Local Institution - 0027

Lima, , Peru

Site Status

Local Institution

Lima, , Peru

Site Status

Local Institution - 0025

Lima, , Peru

Site Status

Local Institution - 0026

Lima, , Peru

Site Status

Local Institution - 0068

Tolyatti, , Russia

Site Status

Local Institution - 0035

Park West, Bloemfontein, Free State, South Africa

Site Status

Local Institution - 0032

Pretoria, Gauteng, South Africa

Site Status

Local Institution - 0034

Pretoria, Gauteng, South Africa

Site Status

Local Institution - 0033

Cape Town, Western Cape, South Africa

Site Status

Local Institution - 0050

Barcelona, , Spain

Site Status

Local Institution - 0053

Madrid, , Spain

Site Status

Local Institution - 0055

Madrid, , Spain

Site Status

Local Institution - 0052

Valencia, , Spain

Site Status

Countries

Review the countries where the study has at least one active or historical site.

United States Argentina Belgium Brazil France Germany Italy Mexico Peru Russia South Africa Spain

References

Explore related publications, articles, or registry entries linked to this study.

Ruperto N, Lovell DJ, Berman A, Anton J, Viola DO, Lauwerys B, Rama ME, Bohnsack J, Breedt J, Fischbach M, Lutz T, Minden K, Ally M, Rubio-Perez N, Gervais E, Van Zyl R, Wong R, Askelson M, Martini A, Brunner HI; Pediatric Rheumatology Collaborative Study Group (PRCSG) and the Paediatric Rheumatology International Trials Organisation (PRINTO). Abatacept as Monotherapy and in Combination With Methotrexate in Patients With Juvenile Idiopathic Arthritis: Analysis of 2 Phase III Trials. J Rheumatol. 2023 Nov;50(11):1471-1480. doi: 10.3899/jrheum.2022-1320. Epub 2023 Jul 15.

Reference Type DERIVED
PMID: 37453737 (View on PubMed)

Brunner HI, Tzaribachev N, Louw I, Calvo Penades I, Avila-Zapata F, Horneff G, Foeldvari I, Kingsbury DJ, Paz Gastanaga ME, Wouters C, Breedt J, Wong R, Askelson M, Zhuo J, Martini A, Lovell DJ, Ruperto N; Paediatric Rheumatology International Trials Organisation (PRINTO) and the Pediatric Rheumatology Collaborative Study Group (PRCSG) investigators. Long-Term Maintenance of Clinical Responses by Individual Patients With Polyarticular-Course Juvenile Idiopathic Arthritis Treated With Abatacept. Arthritis Care Res (Hoboken). 2023 Nov;75(11):2259-2266. doi: 10.1002/acr.25156. Epub 2023 Jun 22.

Reference Type DERIVED
PMID: 37221146 (View on PubMed)

Ruperto N, Lovell DJ, Berman A, Avila-Zapata F, Horneff G, Alessio M, Becker ML, Belot A, Burgos-Vargas R, Gamir ML, Goldenstein-Schainberg C, Scheibel IM, Terreri MT, Zemel L, Zhuo J, Askelson M, Wong R, Martini A, Brunner HI; Pediatric Rheumatology Collaborative Study Group and the Paediatric Rheumatology International Trials Organisation. Patient-Reported Outcomes Among Patients Ages Two to Seventeen Years With Polyarticular-Course Juvenile Idiopathic Arthritis Treated With Subcutaneous Abatacept: Two-Year Results From an International Phase III Study. Arthritis Care Res (Hoboken). 2023 Aug;75(8):1804-1814. doi: 10.1002/acr.24989. Epub 2023 Jan 29.

Reference Type DERIVED
PMID: 36710243 (View on PubMed)

Ruperto N, Brunner HI, Tzaribachev N, Vega-Cornejo G, Louw I, Cimaz R, Dare J, Espada G, Faugier E, Ferrandiz M, Gerloni V, Quartier P, Silva CA, Wagner-Weiner L, Gandhi Y, Passarell J, Nys M, Wong R, Martini A, Lovell DJ; Pediatric Rheumatology Collaborative Study Group (PRCSG) and the Paediatric Rheumatology International Trials Organisation (PRINTO). Absence of Association Between Abatacept Exposure and Initial Infection in Patients With Juvenile Idiopathic Arthritis. J Rheumatol. 2021 Jul;48(7):1073-1081. doi: 10.3899/jrheum.200154. Epub 2021 Jan 15.

Reference Type DERIVED
PMID: 33452173 (View on PubMed)

Brunner HI, Tzaribachev N, Cornejo GV, Joos R, Gervais E, Cimaz R, Calvo Penades I, Cuttica R, Lutz T, Quartier P, Gandhi Y, Nys M, Wong R, Martini A, Lovell DJ, Ruperto N; Pediatric Rheumatology Collaborative Study Group and the Paediatric Rheumatology International Trials Organisation. Maintenance of antibody response to diphtheria/tetanus vaccine in patients aged 2-5 years with polyarticular-course juvenile idiopathic arthritis receiving subcutaneous abatacept. Pediatr Rheumatol Online J. 2020 Feb 22;18(1):19. doi: 10.1186/s12969-020-0410-x.

Reference Type DERIVED
PMID: 32087715 (View on PubMed)

Brunner HI, Tzaribachev N, Vega-Cornejo G, Louw I, Berman A, Calvo Penades I, Anton J, Avila-Zapata F, Cuttica R, Horneff G, Foeldvari I, Keltsev V, Kingsbury DJ, Viola DO, Joos R, Lauwerys B, Paz Gastanaga ME, Rama ME, Wouters C, Bohnsack J, Breedt J, Fischbach M, Lutz T, Minden K, Miraval T, Ally MMTM, Rubio-Perez N, Solau Gervais E, van Zyl R, Li X, Nys M, Wong R, Banerjee S, Lovell DJ, Martini A, Ruperto N; Paediatric Rheumatology International Trials Organisation (PRINTO) and the Pediatric Rheumatology Collaborative Study Group (PRCSG). Subcutaneous Abatacept in Patients With Polyarticular-Course Juvenile Idiopathic Arthritis: Results From a Phase III Open-Label Study. Arthritis Rheumatol. 2018 Jul;70(7):1144-1154. doi: 10.1002/art.40466. Epub 2018 May 20.

Reference Type DERIVED
PMID: 29481737 (View on PubMed)

Related Links

Access external resources that provide additional context or updates about the study.

Other Identifiers

Review additional registry numbers or institutional identifiers associated with this trial.

2012-003195-39

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

IM101-301

Identifier Type: -

Identifier Source: org_study_id

More Related Trials

Additional clinical trials that may be relevant based on similarity analysis.

Tofacitinib in Juvenile Idiopathic Arthritis
NCT07211932 NOT_YET_RECRUITING