Buphenyl Therapy for Byler's Disease

NCT ID: NCT01784718

Last Updated: 2013-02-06

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

NO_LONGER_AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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This is a single patient compassionate use protocol to determine whether Buphenyl (4-phenylbutyrate) will improve the poor bile flow associated with Byler Disease.

Detailed Description

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Conditions

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Byler Disease

Interventions

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Buphenyl

Intervention Type DRUG

Eligibility Criteria

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Inclusion Criteria

* Byler Disease
* Cholestasis unresponsive to pharmacologic therapy

Exclusion Criteria

* Allergy/Hypersensitivity to Buphenyl
Minimum Eligible Age

1 Year

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Pittsburgh

OTHER

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Other Identifiers

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PRO12070385

Identifier Type: -

Identifier Source: org_study_id

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