Transition From Buphenyl to RAVICTI for the Therapy of Byler Disease

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

NO_LONGER_AVAILABLE

Study Classification

EXPANDED_ACCESS

Brief Summary

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This is a single patient compassionate use protocol to determine whether RAVICTI will improve bile flow in a subject who previously tolerated therapy with Buphenyl.

Detailed Description

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Conditions

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Byler Disease

Interventions

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Glycerol phenylbutyrate

Intervention Type DRUG

Other Intervention Names

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RAVICTI

Eligibility Criteria

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Inclusion Criteria

* Byler Disease
* Cholestasis
* Tolerance of Buphenyl therapy

Exclusion Criteria

* Allergy/Hypersensitivity to RAVICTI

Minimum Eligible Age

6 Months

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Responsible Party

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Responsibility Role SPONSOR

Other Identifiers

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PRO12070385.2

Identifier Type: -

Identifier Source: org_study_id