A Safety, Efficacy and Tolerability Trial of Pregabalin as Add-On Treatment in Pediatric and Adult Subjects With Primary Generalized Tonic-Clonic (i.e., Grand Mal) Seizures.

NCT ID: NCT01747915

Last Updated: 2021-01-20

Study Results

Results available

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE3

Total Enrollment

219 participants

Study Classification

INTERVENTIONAL

Study Start Date

2013-04-03

Study Completion Date

2019-02-20

Brief Summary

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The study is designed to evaluate the safety, tolerability and efficacy of two doses of pregabalin as add-on treatment in pediatric and adult subjects with Primary Generalized Tonic-Clonic (PGTC) seizures as compared to placebo. It is hypothesized that both doses of pregabalin will demonstrated superior efficacy when compared to placebo by reducing PGTC seizure frequency and that pregabalin will be safe and well tolerated.

Detailed Description

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Conditions

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Generalized Tonic Clonic Seizures

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

TRIPLE

Participants Caregivers Investigators

Study Groups

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Study Drug Level 1

Group Type EXPERIMENTAL

Pregabalin Dose Level 1

Intervention Type DRUG

Pregabalin, either liquid or capsule, dosed twice daily, escalated up to a maximum of 300 mg/day beginning at Randomization to Taper Phase, then tapered down to a maximum dose of 150 mg/day during 1 week Taper Phase to End of Study/Early Termination.

Study Drug Level 2

Group Type EXPERIMENTAL

Pregabalin Dose Level 2

Intervention Type DRUG

Pregabalin, either liquid or capsule, dosed twice daily, escalated up to a maximum of 600 mg/day beginning at Randomization to Taper Phase, then tapered down to a maximum of 150 mg/day during 1 week Taper Phase to End of Study/Early Termination.

Placebo

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type DRUG

Placebo, either liquid or capsule, dosed twice daily beginning at Randomization to End of Study/Early Termination.

Interventions

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Pregabalin Dose Level 1

Pregabalin, either liquid or capsule, dosed twice daily, escalated up to a maximum of 300 mg/day beginning at Randomization to Taper Phase, then tapered down to a maximum dose of 150 mg/day during 1 week Taper Phase to End of Study/Early Termination.

Intervention Type DRUG

Pregabalin Dose Level 2

Pregabalin, either liquid or capsule, dosed twice daily, escalated up to a maximum of 600 mg/day beginning at Randomization to Taper Phase, then tapered down to a maximum of 150 mg/day during 1 week Taper Phase to End of Study/Early Termination.

Intervention Type DRUG

Placebo

Placebo, either liquid or capsule, dosed twice daily beginning at Randomization to End of Study/Early Termination.

Intervention Type DRUG

Other Intervention Names

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Lyrica Dose Level 1 Lyrica Dose Level 2

Eligibility Criteria

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Inclusion Criteria

* Seizures classified as Primary Generalized Tonic Clonic Seizures
* Must have at least 1 PGTC seizure in the 8 weeks prior to screening
* Must have a minimum of 3 PGTC seizures during the 8-week baseline phase and at least 1 PGTC in each 4-week period of the baseline phase
* Currently receiving adequate and stable dosage of 1 to 3 anti-epileptic treatments (stable within 28 days of screening)
* Signed informed consent and assent if a minor
* Ability to comply with daily seizure and dosing diary requirements and all study procedures

Exclusion Criteria

* A current diagnosis of febrile seizures, or seizures related to an ongoing acute medical illness
* Focal seizures (simple partial, complex partial, or partial becoming secondarily generalized)
* Status Epilepticus within 1 year prior to screening
* Lennox-Gastaut syndrome, infantile spasms, Benign Epilepsy with Centrotemporal Spikes (BECTS) and Dravet syndrome
* Seizures related to drugs, alcohol, or acute medical illness
* Any change in anti-epileptic treatment regimen (type of medication or dose; VNS alteration) within 28 days of the screening visit or during the baseline phase
* Progressive or potentially progressive structural CNS lesion or a progressive encephalopathy.
* Progressive inborn errors of metabolism.
Minimum Eligible Age

5 Years

Maximum Eligible Age

65 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Pfizer's Upjohn has merged with Mylan to form Viatris Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Pfizer CT.gov Call Center

Role: STUDY_DIRECTOR

Pfizer

Locations

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Axcess Medical Research

Loxahatchee Groves, Florida, United States

Site Status

Pediatric Epilepsy Center of Central Florida

Orlando, Florida, United States

Site Status

Pediatric Neurology, PA

Orlando, Florida, United States

Site Status

Medsol Clinical Research Center

Port Charlotte, Florida, United States

Site Status

Hawaii Pacific Neuroscience

Honolulu, Hawaii, United States

Site Status

Alexian Brothers Center for Psychiatric Research

Hoffman Estates, Illinois, United States

Site Status

Chinmay K. Patel, D.O.

Hoffman Estates, Illinois, United States

Site Status

St. Alexius Medical Center

Hoffman Estates, Illinois, United States

Site Status

Ohio Clinical Research Partners, LLC

Canton, Ohio, United States

Site Status

Road Runner Research, Ltd

San Antonio, Texas, United States

Site Status

Scott & White Memorial Hospital and Clinic

Temple, Texas, United States

Site Status

Rainier Clinical Research Center, Inc.

Renton, Washington, United States

Site Status

Medizinische Universitaet Innsbruck

Innsbruck, , Austria

Site Status

AKH Linz

Linz, , Austria

Site Status

UZ Vitebsk Regional Childrens Clinical Centre

Vitebsk, , Belarus

Site Status

UZ Vitebsk Regional Childrens Clinical Centre

Vitebsk, , Belarus

Site Status

University Clinical Center Sarajevo

Sarajevo, Canton Sarajevo, Bosnia and Herzegovina

Site Status

University Clinical Center Tuzla

Tuzla, Canton Tuzla, Bosnia and Herzegovina

Site Status

University Clinical Hospital Mostar

Mostar, Herzegovinaneretva Canton, Bosnia and Herzegovina

Site Status

Public Health Institution Hospital Dr Mladen Stojanovic

Prijedor, Republika Srpska, Bosnia and Herzegovina

Site Status

Multiprofile Hospital for Active Treatment Puls AD

Blagoevgrad, , Bulgaria

Site Status

DCC Sv. Pantaleimon OOD

Pleven, , Bulgaria

Site Status

Military Medical Academy - Multiprofile Hospital for Active Treatment

Pleven, , Bulgaria

Site Status

MHAT Central Onco Hospital OOD

Plovdiv, , Bulgaria

Site Status

Medical Center Teodora

Rousse, , Bulgaria

Site Status

MHATNP Sveti Naum EAD

Sofia, , Bulgaria

Site Status

UMHAT Aleksandrovska

Sofia, , Bulgaria

Site Status

DCC Sveta Anna - Sofia

Sofia, , Bulgaria

Site Status

The First Affiliated Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, China

Site Status

The First Bethune Hospital of Jilin University

Changchun, Jilin, China

Site Status

Shanghai Huashan Hospital, Neurology Department

Shanghai, Shanghai Municipality, China

Site Status

University Hospital Center Split, Clinic for Neurology

Split, , Croatia

Site Status

Aarhus University Hospital

Aarhus C, , Denmark

Site Status

Odense University Hospital

Odense C, , Denmark

Site Status

CHU d'Amiens - Picardie

Amiens, , France

Site Status

CHRU de Rennes - Hôpital Pontchaillou

Rennes, , France

Site Status

CHU d'Amiens Hopital Pontchaillou

Rennes, , France

Site Status

Eginition Hospital

Athens, , Greece

Site Status

Athens Medical Center

Athens, , Greece

Site Status

General Children's Hospital Penteli

Athens, , Greece

Site Status

University General Hospital of Thessaloniki "AHEPA"

Thessaloniki, , Greece

Site Status

Semmelweis Egyetem, I. Sz. Gyermekgyogyaszati Klinika

Budapest, , Hungary

Site Status

Csongrad Megyei Egeszsegugyi Ellato Kozpont Hodmezovasarhely-Mako

Hódmezővásárhely, , Hungary

Site Status

Pest Megyei Flór Ferenc Kórhaz

Kistarcsa, , Hungary

Site Status

St. John's Medical College Hospital

Bangalore, Karnataka, India

Site Status

Mangala Hospital & Mangala Kidney Foundation

Mangalore, Karnataka, India

Site Status

P D Hinduja National Hospital and Medical Research Centre

Mumbai, Maharashtra, India

Site Status

Getwell Hospital and Research Institute

Nagpur, Maharashtra, India

Site Status

Sahyadri Speciality Hospital

Pune, Maharashtra, India

Site Status

KEM Hospital Research Centre

Pune, Maharashtra, India

Site Status

Indraprastha Apollo Hospitals

New Delhi, National Capital Territory of Delhi, India

Site Status

Saint George Hospital - University Medical Center

Beirut, , Lebanon

Site Status

Ain Wazein Medical Village

El Chouf, , Lebanon

Site Status

Hospital Raja Permaisuri Bainun

Ipoh, Perak, Malaysia

Site Status

Pzu Neuron

Bijelo Polje, , Montenegro

Site Status

Cebu Doctors' University Hospital

Cebu City, CEBU, Philippines

Site Status

Perpetual Succour Hospital

Cebu City, CEBU, Philippines

Site Status

Cebu Doctors' University Hospital, Rm Ph 7

Cebu City, , Philippines

Site Status

Manila Doctors Hospital

Manila, , Philippines

Site Status

Metropolitan Medical Center

Manila, , Philippines

Site Status

University of Santo Tomas Hospital

Manila, , Philippines

Site Status

St. Luke's Medical Center Cathedral Heights Building

Quezon City, , Philippines

Site Status

COPERNICUS Podmiot Leczniczy Spzoo

Gdansk, , Poland

Site Status

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS

Katowice, , Poland

Site Status

NZOZ Novo Med

Katowice, , Poland

Site Status

Neuro-Care Gabriela Klodowska

Katowice, , Poland

Site Status

NZOZ "HIPOKRATES II" Sp. z o.o.

Krakow, , Poland

Site Status

Instytut Medycyny Wsi im. Witolda Chodzki w Lublinie

Lublin, , Poland

Site Status

Solumed Centrum Medyczne

Poznan, , Poland

Site Status

NZOZ IGNIS dr n. med. Alicja Lobinska

Świdnik, , Poland

Site Status

Lecznica Medyczna ''Zycie"

Warsaw, , Poland

Site Status

Centrul Medical de Diagnostic si Tratament Ambulator Neomed

Brasov, , Romania

Site Status

CMI Neurologie, Neurofiziologie (EEG, EMG, PEC) Roceanu Adina Maria

Bucharest, , Romania

Site Status

Sapiens Medical Center

Bucharest, , Romania

Site Status

Spitalul Clinic de Urgenta "Prof. Dr. Nicolae Oblu"

Iași, , Romania

Site Status

Spitalul Clinic de Urgente pentru Copii "Sf. Maria"

Iași, , Romania

Site Status

Spitalul de Psihiatrie "Dr. Gh. Preda"

Sibiu, , Romania

Site Status

SPHI Leningrad Regional Psychoneurological Dispensary

Pgt. Roshchino, Leningradskaya Oblast', Russia

Site Status

Nizhmedklinika

Nizhny Novgorod, Nizhny Novgorod Oblast, Russia

Site Status

Perm State Medical University n. a. acad. E.A. Vagner

Perm, Permskiy KRAY, Russia

Site Status

State Budgetary Healthcare Institution of Stavropol region

Pyatigorsk, Stavropol Kray, Russia

Site Status

GBOU VPO "Kazan State Medical University" of Roszdrav

Kazan', Tatarstan Republic, Russia

Site Status

Republican clinical hospital

Kazan', Tatarstan Republic, Russia

Site Status

TSBHI City Hospital No. 5 of Barnaul

Barnaul, , Russia

Site Status

MAHI of the Order of the Red Banner of Labor City Clinical Hospital No. 1

Chelyabinsk, , Russia

Site Status

Non-state Healthcare Institution

Moscow, , Russia

Site Status

LLC City Neurological Center "Sibneiromed"

Novosibirsk, , Russia

Site Status

Perm State Medical University n. a. acad. E.A. Vagner

Perm, , Russia

Site Status

SPHI Leningrad Regional Psychoneurological Dispensary

Saint Petersburg, , Russia

Site Status

FSBI V.M. Bekhterev National Research Medical Center for

Saint Petersburg, , Russia

Site Status

SBHI of Saint Petersburg Psychoneurological Dispensary #5

Saint Petersburg, , Russia

Site Status

SBHI of Saint Petersburg Psychoneurological Dispensary #5

Saint Petersburg, , Russia

Site Status

Regional State Budgetary Institution of Ministry of Health

Smolensk, , Russia

Site Status

RSBHI Smolensk Regional Clinical Hospital

Smolensk, , Russia

Site Status

GBOU VPO Smolensk State Medical University

Smolensk, , Russia

Site Status

SHI "Central Clinical Medical Unit

Ulyanovsk, , Russia

Site Status

SHI "Central Clinical Medical Unit

Ulyanovsk, , Russia

Site Status

Institute for Child and Youth Healthcare of Vojvodina

Novi Sad, Vojvodina, Serbia

Site Status

Institute for Mental Health

Belgrade, , Serbia

Site Status

University Children's Hospital

Belgrade, , Serbia

Site Status

Clinical Center Kragujevac

Kragujevac, , Serbia

Site Status

Nemocnica s poliklinikou Hlohovec, s.r.o.

Hlohovec, , Slovakia

Site Status

Neurologicka ambulancia MUDr. Eva Gasparova

Hlohovec, , Slovakia

Site Status

Keimyung University Dongsan Hospital

Daegu, Korea, South Korea

Site Status

Seoul National University Hospital

Seoul, , South Korea

Site Status

Konkuk University medical center

Seoul, , South Korea

Site Status

Samsung Medical Center

Seoul, , South Korea

Site Status

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Barcelona, Spain

Site Status

Marmara University Pendik Training and Research Hospital

Istanbul, UST Kaynarca/pendik, Turkey (Türkiye)

Site Status

Eskisehir Osmangazi University Medical Faculty Department Of Neurology

Eskişehir, , Turkey (Türkiye)

Site Status

Dokuz Eylul Ün. Tip Fakültesi İç Hastalıkları

Izmir, , Turkey (Türkiye)

Site Status

Celal Bayar University School of Medicine, Neurology Department

Manisa, , Turkey (Türkiye)

Site Status

Komunalna ustanova "Odeska oblasna psykhiatrychna likarnia 2"

S. Oleksandrivka, Komintern. R-N, Odeska OBL., Ukraine

Site Status

Komunalnyi zaklad "Dnipropetrovska dytiacha miska klinichna likarnia No. 5"

Dnipro, , Ukraine

Site Status

Komunalnyi zaklad "Dnipropetrovska oblasna dytiacha klinichna likarnia"

Dnipro, , Ukraine

Site Status

Ivano-Frankivska oblasna dytiacha klinichna likarnia

Ivano-Frankivsk, , Ukraine

Site Status

Derzhavna ustanova "Instytut nevrolohii, psykhiatrii ta narkolohii

Kharkiv, , Ukraine

Site Status

Komunalne nekomertsiine pidpryiemstvo Kharkivskoi oblasnoi rady "Oblasna klinichna psykhiatrychna li

Kharkiv, , Ukraine

Site Status

Derzhavnyi zaklad "Ukrainskyi medychnyi tsentr reabilitatsii ditei z

Kyiv, , Ukraine

Site Status

Komunalnyi zaklad Lvivskoi oblasnoi rady "Lvivska oblasna klinichna likarnia"

Lviv, , Ukraine

Site Status

Komunalne nekomertsiine pidpryiemstvo "Odeskyi oblasnyi

Odesa, , Ukraine

Site Status

Oblasnyi klinichnyi tsentr neirokhirurhii ta nevrolohii,

Uzhhorod, , Ukraine

Site Status

Komunalna ustanova "Miska klinichna likarnia #2", nevrolohichne viddilennia

Zaporizhzhia, , Ukraine

Site Status

The Barberry National Centre for Mental Health

Birmingham, WEST Midlands, United Kingdom

Site Status

Barts Health NHS Foundation Trust, The Royal London Hospital

London, , United Kingdom

Site Status

Salford Royal NHS Foundation Trust

Salford, , United Kingdom

Site Status

ABMU Local Health Board, Morriston Hospital

Swansea, , United Kingdom

Site Status

Countries

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United States Austria Belarus Bosnia and Herzegovina Bulgaria China Croatia Denmark France Greece Hungary India Lebanon Malaysia Montenegro Philippines Poland Romania Russia Serbia Slovakia South Korea Spain Turkey (Türkiye) Ukraine United Kingdom

References

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Driscoll J, Almas M, Gregorian G, Kyrychenko A, Makedonska I, Liu J, Patrick J, Scavone JM, Antinew J; 1105 Study Group. Pregabalin as adjunctive therapy in adult and pediatric patients with generalized tonic-clonic seizures: A randomized, placebo-controlled trial. Epilepsia Open. 2021 Jun;6(2):381-393. doi: 10.1002/epi4.12492. Epub 2021 May 16.

Reference Type DERIVED
PMID: 34033265 (View on PubMed)

Provided Documents

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Document Type: Statistical Analysis Plan

View Document

Document Type: Study Protocol

View Document

Related Links

Other Identifiers

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2010-023263-18

Identifier Type: EUDRACT_NUMBER

Identifier Source: secondary_id

A0081105

Identifier Type: -

Identifier Source: org_study_id

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