Pancreas Cancer: Molecular Profiling as a Guide to Therapy Before and After Surgery ("Personalized Medicine")

NCT ID: NCT01726582

Last Updated: 2023-08-14

Study Results

Results available

Outcome measurements, participant flow, baseline characteristics, and adverse events have been published for this study.

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Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

229 participants

Study Classification

INTERVENTIONAL

Study Start Date

2011-11-30

Study Completion Date

2022-04-11

Brief Summary

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In this clinical trial, if the doctor knows or suspects that a growth in the pancreas is cancer (adenocarcinoma), then a sample of the growth is tested (the test is called molecular profiling). The results of the test are used by the doctor to recommend therapy (chemotherapy and radiation therapy) that the patient will receive before having surgery to remove the adenocarcinoma. When the patient goes to surgery, the adenocarcinoma that is removed is tested again. The results of that test are used to guide the choice of therapy after surgery.

The chemotherapy drugs and the radiation therapy used in this clinical trial are already approved for treatment of pancreas cancer. This trial is intended to establish which treatment is best for a specific patient, based on test results from that patient's actual adenocarcinoma. In the past, the decision as to which treatment the patient will receive was not based on testing of the actual adenocarcinoma.

See treatment pathways at http://www.mcw.edu/surgery/patientinfo/Pancreatic-Cancer-Trial.htm.

Hypothesis: Resectability rate, overall survival rate and progression-free survival in subjects with adenocarcinoma of the pancreas will be superior for who receive targeted "personalized" therapy.

Detailed Description

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Conditions

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Pancreatic Adenocarcinoma

Study Design

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Allocation Method

NA

Intervention Model

SINGLE_GROUP

Primary Study Purpose

TREATMENT

Blinding Strategy

NONE

Study Groups

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Milestones related to therapy

Milestone 1: Targeted chemotherapy prior to surgery: 8 weeks targeted chemotherapy; restaging.

Milestone 2: Before surgery: Chemoradiotherapy (cRXT); restaging Milestone 3: Before surgery: 8 weeks targeted chemotherapy; restaging; chemoradiotherapy (cXRT); restaging.

Milestone 4: standard FOLFIRINOX chemotherapy prior to surgery: 8 weeks FOLFIRINOX (standard chemotherapy); restaging; standard chemoradiotherapy (cXRT); restaging.

Milestone 5: After surgery: 8 weeks targeted chemotherapy; restaging; chemoradiotherapy (cXRT); restaging.

Milestone 6: Gemcitabine after surgery: 8 weeks standard Gemcitabine (chemotherapy); restaging; chemoradiotherapy (cXRT); restaging.

Milestone 7: After surgery: chemoradiotherapy (cXRT); restaging. Milestone 8: Gemcitabine after surgery: 8 weeks Gemcitabine (chemotherapy); restaging; 8 weeks Gemcitabine (chemotherapy); restaging.

Milestone 9: No additional therapy after surgery. Milestone 10: After surgery no additional treatment.

Group Type EXPERIMENTAL

Milestone 1: Targeted chemotherapy prior to surgery

Intervention Type DRUG

The molecular profile from the biopsy before surgery will point to a particular chemotherapy treatment.

Milestone 2: Chemoradiotherapy (cXRT)

Intervention Type RADIATION

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or intensity-modulated radiation therapy (IMRT) techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Milestone 3: Targeted chemotherapy prior to surgery

Intervention Type DRUG

The molecular profile from the biopsy before surgery will point to a particular chemotherapy treatment.

Milestone 3: Chemoradiotherapy (cXRT)

Intervention Type RADIATION

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Milestone 4: standard FOLFIRINOX chemotherapy prior to surgery

Intervention Type DRUG

A biopsy of the borderline tumor does not provide a molecular profile that can be used to target treatment. The treatment will be standard FOLFIRINOX chemotherapy regimen.

Milestone 4: Chemoradiotherapy (cXRT)

Intervention Type RADIATION

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Milestone 5: Targeted chemotherapy after surgery

Intervention Type DRUG

The molecular profile from the surgical specimen will point to a particular chemotherapy treatment.

Milestone 5: Chemoradiotherapy (cXRT)

Intervention Type RADIATION

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Milestone 6: Gemcitabine after surgery

Intervention Type DRUG

Chemotherapy treatment with Gemcitabine.

Milestone 6: Chemoradiotherapy (cXRT)

Intervention Type RADIATION

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Milestone 7: Chemoradiotherapy (cXRT)

Intervention Type RADIATION

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Milestone 8: Targeted chemotherapy after surgery

Intervention Type DRUG

The molecular profile from the surgical specimen will point to a particular chemotherapy treatment.

Milestone 9: Gemcitabine after surgery

Intervention Type DRUG

Chemotherapy treatment with Gemcitabine.

Milestone 10: No additional therapy after surgery

Intervention Type OTHER

The molecular profile of the tumor that was removed during surgery points to a lack of treatment affect for available therapies. No additional therapy is recommended.

Interventions

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Milestone 1: Targeted chemotherapy prior to surgery

The molecular profile from the biopsy before surgery will point to a particular chemotherapy treatment.

Intervention Type DRUG

Milestone 2: Chemoradiotherapy (cXRT)

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or intensity-modulated radiation therapy (IMRT) techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Intervention Type RADIATION

Milestone 3: Targeted chemotherapy prior to surgery

The molecular profile from the biopsy before surgery will point to a particular chemotherapy treatment.

Intervention Type DRUG

Milestone 3: Chemoradiotherapy (cXRT)

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Intervention Type RADIATION

Milestone 4: standard FOLFIRINOX chemotherapy prior to surgery

A biopsy of the borderline tumor does not provide a molecular profile that can be used to target treatment. The treatment will be standard FOLFIRINOX chemotherapy regimen.

Intervention Type DRUG

Milestone 4: Chemoradiotherapy (cXRT)

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Intervention Type RADIATION

Milestone 5: Targeted chemotherapy after surgery

The molecular profile from the surgical specimen will point to a particular chemotherapy treatment.

Intervention Type DRUG

Milestone 5: Chemoradiotherapy (cXRT)

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Intervention Type RADIATION

Milestone 6: Gemcitabine after surgery

Chemotherapy treatment with Gemcitabine.

Intervention Type DRUG

Milestone 6: Chemoradiotherapy (cXRT)

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Intervention Type RADIATION

Milestone 7: Chemoradiotherapy (cXRT)

A radio-sensitizing chemotherapy agent (either Gemcitabine or Capecitabine) will be given. Using 3D conformal or IMRT techniques, patients will receive a total dose of 50.4 Gy prescribed to the 95% isodose at 1.8 Gy/fraction (28 fractions).

Intervention Type RADIATION

Milestone 8: Targeted chemotherapy after surgery

The molecular profile from the surgical specimen will point to a particular chemotherapy treatment.

Intervention Type DRUG

Milestone 9: Gemcitabine after surgery

Chemotherapy treatment with Gemcitabine.

Intervention Type DRUG

Milestone 10: No additional therapy after surgery

The molecular profile of the tumor that was removed during surgery points to a lack of treatment affect for available therapies. No additional therapy is recommended.

Intervention Type OTHER

Other Intervention Names

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FOLFIRINOX FOLFIRI Gemcitabine with irinotecan Gemcitabine / oxaliplatin Gemcitabine / cisplatinum Gemcitabine / capecitabine Gemcitabine / nab-paclitaxel Capecitabine / nab-paclitaxel Gemcitabine Capecitabine FOLFIRINOX FOLFIRI Gemcitabine with irinotecan Gemcitabine / oxaliplatin Gemcitabine / cisplatinum Gemcitabine / capecitabine Gemcitabine / nab-paclitaxel Capecitabine / nab-paclitaxel Gemcitabine Capecitabine FOLFIRINOX oxaliplatin irinotecan leucovorin 5 fluorouracil Gemcitabine Capecitabine FOLFIRINOX FOLFIRI Gemcitabine with irinotecan Gemcitabine / oxaliplatin Gemcitabine / cisplatinum Gemcitabine / capecitabine Gemcitabine / nab-paclitaxel Capecitabine / nab-paclitaxel Gemcitabine Capecitabine 5-Fluorouracil Gemcitabine Capecitabine Chemotherapy treatment with Gemcitabine. Gemzar Gemcitabine Capecitabine Gemcitabine Capecitabine FOLFIRINOX FOLFIRI Gemcitabine with irinotecan Gemcitabine / oxaliplatin Gemcitabine / cisplatinum Gemcitabine / capecitabine Gemcitabine / nab-paclitaxel Capecitabine / nab-paclitaxel Gemcitabine Capecitabine 5 fluorouracil Gemzar Restaged after surgery. No additional therapy.

Eligibility Criteria

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Inclusion Criteria

* 18 years of age or older
* Able to understand and provide written informed consent
* Diagnosis of adenocarcinoma of the pancreas or high suspicion of adenocarcinoma of the pancreas based on CT and MRI findings as detailed below by "Definition of...."

Treatment Eligibility Criteria:

* Have an Eastern Cooperative Oncology Group performance status less than or equal to 2
* Have biopsy-proven resectable or borderline resectable adenocarcinoma of the pancreas
* Have adequate organ and bone marrow function as defined by:

* total leukocytes greater than or equal to 3 x1000/μL
* absolute neutrophil count (ANC) \> or equal to 1.5x 1000/μL
* hemoglobin \> or equal to 9 g/dL
* platelets \> or equal to 100 x 1000/μL
* creatinine clearance \>60 mL/min or creatinine \< or equal to 1.5 mg/dL
* bilirubin \< or equal to 2 mg/dL or \>2 and declining as described in the protocol
* aspartate transaminases (AST/SGOT) \< or equal to3 x upper limit of normal (ULN)
* alanine transaminases (ALT/SGPT) \< or equal to 3 x ULN
* Female patients must be post menopausal for \> 1 year, surgically sterile, or have a negative pregnancy test and used at least one form of contraception for 4 weeks prior to Day 1 of the study, during study treatment and during the first 4 months after study treatment is discontinued. Male patients must be surgically sterile or use barrier contraception during the study and for 4 months after the last dose of any study drug.

Definition of Resectable Pancreatic Cancer includes:

* No evidence of extra-pancreatic disease
* No evidence of tumor-arterial abutment (celiac, superior mesenteric artery or hepatic artery)
* If tumor induced narrowing of the superior mesenteric vein, portal vein or superior mesenteric-portal vein confluence is present it must be \<50% of the diameter of the vessel
* Ca19-9 \<5000, when bilirubin is \<2 (or \>2 and declining as described in the protocol)

Definition of Borderline Resectable Pancreatic Cancer to include at least one of the following:

* Tumor abutment \< or equal to 180 degrees of the superior mesenteric artery or celiac axis
* Tumor abutment or encasement (\>180 degrees) of a short segment of the hepatic artery
* Tumor induced narrowing of superior mesenteric vein, portal vein or superior mesenteric-portal vein of \>50% of the diameter of the vessel.
* Short segment occlusion of the superior mesenteric vein, portal vein or superior mesenteric-portal vein confluence with a suitable portal vein above and superior mesenteric vein below, for reconstruction
* CT or MRI findings suspicious for, but not diagnostic of, metastatic disease (based on multidisciplinary assessment at the Medical College of Wisconsin weekly pancreatic cancer conference)
* Biopsy proven N1 disease (regional lymph nodes involved) from pre-referral biopsy or endoscopic ultrasound-guided fine needle aspirate
* Resectable tumor and cancer antigen 19-9 (CA19-9) \>5000

Exclusion Criteria

Any patient with one or more of the following will be excluded:

* Have received chemotherapy or chemoradiation within 5 years prior of study enrollment
* Have any previous history of another malignancy (other than cured basal or squamous cell carcinoma of the skin or cured in-situ carcinoma of the cervix) within 5 years of study enrollment
* Uncontrolled comorbidities including, but not limited to, ongoing or active serious infection, symptomatic congestive heart failure, unstable angina, unstable cardiac arrhythmias, psychiatric illness, excessive obesity, or situations that would limit compliance with the study requirements or the ability to willingly give written informed consent
* Known human immunodeficiency virus, hepatitis B virus, or hepatitis C virus infection
* Pregnant or breast-feeding patients or any patient with child-bearing potential not using contraception 4 weeks prior to, during and 4 months after study treatment is discontinued
Minimum Eligible Age

18 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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University of Cincinnati

OTHER

Sponsor Role collaborator

Medical College of Wisconsin

OTHER

Sponsor Role lead

Responsible Party

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Susan Tsai

Professor

Responsibility Role PRINCIPAL_INVESTIGATOR

Principal Investigators

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Douglas B. Evans, M.D., FACS

Role: PRINCIPAL_INVESTIGATOR

Medical College of Wisconsin

Kathleen Christians, M.D., FACS

Role: PRINCIPAL_INVESTIGATOR

Medical College of Wisconsin

Susan Tsai, M.D., M.H.S.

Role: PRINCIPAL_INVESTIGATOR

Medical College of Wisconsin

Paul Ritch, M.D.

Role: PRINCIPAL_INVESTIGATOR

Medical College of Wisconsin

Locations

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University of Cincinnati Cancer Center

Cincinnati, Ohio, United States

Site Status

Froedtert and The Medical College of Wisconsin

Milwaukee, Wisconsin, United States

Site Status

Countries

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United States

References

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Edge SB, Compton CC. The American Joint Committee on Cancer: the 7th edition of the AJCC cancer staging manual and the future of TNM. Ann Surg Oncol. 2010 Jun;17(6):1471-4. doi: 10.1245/s10434-010-0985-4.

Reference Type BACKGROUND
PMID: 20180029 (View on PubMed)

Tsai S, Christians KK, George B, Ritch PS, Dua K, Khan A, Mackinnon AC, Tolat P, Ahmad SA, Hall WA, Erickson BA, Evans DB. A Phase II Clinical Trial of Molecular Profiled Neoadjuvant Therapy for Localized Pancreatic Ductal Adenocarcinoma. Ann Surg. 2018 Oct;268(4):610-619. doi: 10.1097/SLA.0000000000002957.

Reference Type RESULT
PMID: 30080723 (View on PubMed)

Provided Documents

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Document Type: Study Protocol and Statistical Analysis Plan

View Document

Document Type: Informed Consent Form

View Document

Other Identifiers

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Advancing a Healthier WI

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

FP 7718

Identifier Type: OTHER_GRANT

Identifier Source: secondary_id

MCW 15565

Identifier Type: -

Identifier Source: org_study_id

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