Study of Tcelna (Imilecleucel-T) in Secondary Progressive Multiple Sclerosis

NCT ID: NCT01684761

Last Updated: 2017-01-10

Study Results

Results pending

The study team has not published outcome measurements, participant flow, or safety data for this trial yet. Check back later for updates.

Basic Information

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Recruitment Status

COMPLETED

Clinical Phase

PHASE2

Total Enrollment

183 participants

Study Classification

INTERVENTIONAL

Study Start Date

2012-08-31

Study Completion Date

2016-10-31

Brief Summary

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The purpose of this study is to determine whether Tcelna (imilecleucel-T, autologous T-Cell Immunotherapy) is effective in the treatment of secondary progressive multiple sclerosis (SPMS).

Detailed Description

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Subjects whose myelin reactive T-cell can be identified by EPA will are randomized and provide blood to manufacture Tcelna. Approximately 5 weeks after receipt of the subject's whole blood procurement, the subjects will receive either Tcelna or placebo and will complete baseline assessments and will receive study treatments at Weeks 0, 4, 8, 12, and 24 (Visits 3-7), totaling 5 doses in year one.

Approximately one month prior to the Week 52 visit a second blood procurement will be performed and the subject will receive the second series of treatments as received in the first year study schedule. Subjects will be evaluated for changes in disability and cognitive function every 3 months, and radiographic changes annually.

Conditions

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Autoimmune Diseases of the Nervous System Multiple Sclerosis Secondary Progressive Multiple Sclerosis Disease Progression Brain Atrophy

Study Design

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Allocation Method

RANDOMIZED

Intervention Model

PARALLEL

Primary Study Purpose

TREATMENT

Blinding Strategy

QUADRUPLE

Participants Caregivers Investigators Outcome Assessors

Study Groups

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Tcelna

30-45 x 10E6 total cells in 2 ml. Subjects receive two annual courses of 5 subcutaneous doses each year (at 0, 4, 8, 12 and 24 weeks).

Group Type EXPERIMENTAL

Tcelna

Intervention Type BIOLOGICAL

Autologous pool of myelin reactive T-cells (MRTC) expanded ex vivo with immunodominant epitopes selected from the three myelin antigens, MBP, PLP and MOG on a per subject basis. Attenuated by irradiation to prevent further proliferation before releasing product for administration.

Placebo

Tcelna inactive ingredients (without cells) totaling 2 ml per dose. Administered subcutaneously with same two year treatment regimen as experimental treatment arm.

Group Type PLACEBO_COMPARATOR

Placebo

Intervention Type BIOLOGICAL

2 ml of Tcelna excipients, prepared daily as individual doses and irradiated before releasing product for administration.

Interventions

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Tcelna

Autologous pool of myelin reactive T-cells (MRTC) expanded ex vivo with immunodominant epitopes selected from the three myelin antigens, MBP, PLP and MOG on a per subject basis. Attenuated by irradiation to prevent further proliferation before releasing product for administration.

Intervention Type BIOLOGICAL

Placebo

2 ml of Tcelna excipients, prepared daily as individual doses and irradiated before releasing product for administration.

Intervention Type BIOLOGICAL

Eligibility Criteria

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Inclusion Criteria

* Diagnosed with MS as defined by the modified McDonald criteria
* SPMS defined as relapsing-remitting disease with recent progression in MS-related neurological deficits
* EDSS score 3.0 - 6.0, inclusively
* Presence of myelin reactive T-cells

Exclusion Criteria

* Diagnosed with primary progressive MS
* Treatment with beta-interferon, glatiramer acetate or dimethyl fumarate 30 days prior to screening
* Treatment with ACTH, any over-the-counter or prescription corticosteroids 60 days prior to screening
* Treatment with IVIG, plasmapheresis or cytopheresis 90 days prior to screening
* Treatment with mitoxantrone, teriflunomide, fingolimod, natalizumab, azathioprine, cyclosporine, methotrexate or mycophenolate mofetil 1 year prior to baseline
* Any prior treatment with cladribine, cyclophosphamide, total lymphoid irradiation, T cell or T cell receptor products, or any therapeutic monoclonal antibody, except natalizumab
* Previous treatment with any other MS investigational drug 1 year prior to screening
* All non-MS investigational drugs must have a minimum washout of 30 days prior to screening or 5 half-lives, whatever is the longest period of time.
* HIV or hepatitis infection
* History of cancer
* Any other significant medical condition that, in the opinion of the investigator, could cause CNS tissue damage or limit its repair.
Minimum Eligible Age

18 Years

Maximum Eligible Age

60 Years

Eligible Sex

ALL

Accepts Healthy Volunteers

No

Sponsors

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Opexa Therapeutics, Inc.

INDUSTRY

Sponsor Role lead

Responsible Party

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Responsibility Role SPONSOR

Principal Investigators

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Jessica Jackson

Role: STUDY_DIRECTOR

Opexa Therapeutics, Inc.

Locations

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HOPE Research Institute

Phoenix, Arizona, United States

Site Status

Northwest NeuroSpecialists, LLC

Tucson, Arizona, United States

Site Status

Alta Bates Summit Medical Center, The Research and Education Development Institute

Berkeley, California, United States

Site Status

Neurology Associates, P.A.

Maitland, Florida, United States

Site Status

University of Miami

Miami, Florida, United States

Site Status

Collier Neurologic Specialists, LLC

Naples, Florida, United States

Site Status

Neurological Services of Orlando

Orlando, Florida, United States

Site Status

Meridien Research

Tampa, Florida, United States

Site Status

Vero Beach Neurology

Vero Beach, Florida, United States

Site Status

Shepherd Center

Atlanta, Georgia, United States

Site Status

Consultants In Neurology, Ltd.

Northbrook, Illinois, United States

Site Status

Fort Wayne Neurological Center

Fort Wayne, Indiana, United States

Site Status

Josephson Wallack Munshower Neurology, PC

Indianapolis, Indiana, United States

Site Status

University of Kansas Medical Center

Kansas City, Kansas, United States

Site Status

Associates in Neurology

Lexington, Kentucky, United States

Site Status

Saint Elizabeth's Medical Center

Boston, Massachusetts, United States

Site Status

Island Neurological Assoicates, PC

Plainview, New York, United States

Site Status

University Hospital and Medical Center Stony Brook New York

Stony Brook, New York, United States

Site Status

The Neurological Institute, PA

Charlotte, North Carolina, United States

Site Status

Carolinas Medical Center Neurology

Charlotte, North Carolina, United States

Site Status

PMG Research of Charlotte

Charlotte, North Carolina, United States

Site Status

Neurology Specialists, Inc

Dayton, Ohio, United States

Site Status

Providence Medical Group - Medford

Medford, Oregon, United States

Site Status

Providence St. Vincent Medical Center - Northwest MS Center

Portland, Oregon, United States

Site Status

University of Pennsylvania

Philadelphia, Pennsylvania, United States

Site Status

The Maxine Mesinger MS Clinic/Baylor College of Medicine

Houston, Texas, United States

Site Status

Central Texas Neurology

Round Rock, Texas, United States

Site Status

Integra Clinical Research, LLC

San Antonio, Texas, United States

Site Status

Fletcher Allen Health Care - Neurology Service

Burlington, Vermont, United States

Site Status

Hampton Roads Neurology

Newport News, Virginia, United States

Site Status

Neurological Associates, Inc

Richmond, Virginia, United States

Site Status

Swedish Neuroscience Institute

Issaquah, Washington, United States

Site Status

Swedish Neuroscience Institute

Seattle, Washington, United States

Site Status

University of Ottawa

Ottawa, Ontario, Canada

Site Status

Recherche Sepmus Inc.

Greenfield Park, Quebec, Canada

Site Status

Montreal Neurological Institute and Hospital

Montreal, Quebec, Canada

Site Status

Countries

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United States Canada

Related Links

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http://www.nationalmssociety.org

Click here for more information about MS and current research.

Other Identifiers

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Protocol Number 2012-00

Identifier Type: -

Identifier Source: org_study_id

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